BR112023016943A2 - Métodos para tratamento da síndrome de quilomicronemia familiar - Google Patents
Métodos para tratamento da síndrome de quilomicronemia familiarInfo
- Publication number
- BR112023016943A2 BR112023016943A2 BR112023016943A BR112023016943A BR112023016943A2 BR 112023016943 A2 BR112023016943 A2 BR 112023016943A2 BR 112023016943 A BR112023016943 A BR 112023016943A BR 112023016943 A BR112023016943 A BR 112023016943A BR 112023016943 A2 BR112023016943 A2 BR 112023016943A2
- Authority
- BR
- Brazil
- Prior art keywords
- methods
- familiar
- treatment
- chylomicronemia syndrome
- syndrome
- Prior art date
Links
- 208000011580 syndromic disease Diseases 0.000 title 1
- 208000016667 Familial chylomicronemia syndrome Diseases 0.000 abstract 2
- MBBCVAKAJPKAKM-UHFFFAOYSA-N lomitapide Chemical compound C12=CC=CC=C2C2=CC=CC=C2C1(C(=O)NCC(F)(F)F)CCCCN(CC1)CCC1NC(=O)C1=CC=CC=C1C1=CC=C(C(F)(F)F)C=C1 MBBCVAKAJPKAKM-UHFFFAOYSA-N 0.000 abstract 1
- 229960003566 lomitapide Drugs 0.000 abstract 1
- 239000000203 mixture Substances 0.000 abstract 1
- 150000003839 salts Chemical class 0.000 abstract 1
Classifications
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K31/00—Medicinal preparations containing organic active ingredients
- A61K31/33—Heterocyclic compounds
- A61K31/395—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins
- A61K31/435—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having six-membered rings with one nitrogen as the only ring hetero atom
- A61K31/44—Non condensed pyridines; Hydrogenated derivatives thereof
- A61K31/445—Non condensed piperidines, e.g. piperocaine
- A61K31/4468—Non condensed piperidines, e.g. piperocaine having a nitrogen directly attached in position 4, e.g. clebopride, fentanyl
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K9/00—Medicinal preparations characterised by special physical form
- A61K9/0012—Galenical forms characterised by the site of application
- A61K9/0053—Mouth and digestive tract, i.e. intraoral and peroral administration
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P3/00—Drugs for disorders of the metabolism
- A61P3/06—Antihyperlipidemics
Landscapes
- Health & Medical Sciences (AREA)
- Chemical & Material Sciences (AREA)
- Medicinal Chemistry (AREA)
- Pharmacology & Pharmacy (AREA)
- Life Sciences & Earth Sciences (AREA)
- Animal Behavior & Ethology (AREA)
- General Health & Medical Sciences (AREA)
- Public Health (AREA)
- Veterinary Medicine (AREA)
- Epidemiology (AREA)
- Diabetes (AREA)
- Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
- Engineering & Computer Science (AREA)
- Hematology (AREA)
- Obesity (AREA)
- Chemical Kinetics & Catalysis (AREA)
- General Chemical & Material Sciences (AREA)
- Bioinformatics & Cheminformatics (AREA)
- Organic Chemistry (AREA)
- Nutrition Science (AREA)
- Physiology (AREA)
- Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
- Acyclic And Carbocyclic Compounds In Medicinal Compositions (AREA)
- Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163155960P | 2021-03-03 | 2021-03-03 | |
| US202163165457P | 2021-03-24 | 2021-03-24 | |
| PCT/US2022/018672 WO2022187463A1 (en) | 2021-03-03 | 2022-03-03 | Methods for treating familial chylomicronemia syndrome |
Publications (1)
| Publication Number | Publication Date |
|---|---|
| BR112023016943A2 true BR112023016943A2 (pt) | 2023-10-31 |
Family
ID=80819670
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| BR112023016943A BR112023016943A2 (pt) | 2021-03-03 | 2022-03-03 | Métodos para tratamento da síndrome de quilomicronemia familiar |
Country Status (10)
| Country | Link |
|---|---|
| US (1) | US20240165093A1 (https=) |
| EP (1) | EP4301361A1 (https=) |
| JP (1) | JP2024508334A (https=) |
| KR (1) | KR20230153375A (https=) |
| AU (1) | AU2022231007A1 (https=) |
| BR (1) | BR112023016943A2 (https=) |
| CA (1) | CA3208189A1 (https=) |
| IL (1) | IL305191A (https=) |
| MX (1) | MX2023010297A (https=) |
| WO (1) | WO2022187463A1 (https=) |
Families Citing this family (1)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CA3186856A1 (en) | 2020-07-29 | 2022-02-03 | Ruth NALLEN | Lomitapide for use in methods of treating hyperlipidemia and hypercholesterolemia in pediatric patients |
Family Cites Families (5)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US5595872A (en) | 1992-03-06 | 1997-01-21 | Bristol-Myers Squibb Company | Nucleic acids encoding microsomal trigyceride transfer protein |
| US5883109A (en) | 1996-07-24 | 1999-03-16 | Bristol-Myers Squibb Company | Method for lowering serum lipid levels employing an MTP inhibitor in combination with another cholesterol lowering drug |
| US6066653A (en) | 1997-01-17 | 2000-05-23 | Bristol-Myers Squibb Co. | Method of treating acid lipase deficiency diseases with an MTP inhibitor and cholesterol lowering drugs |
| KR101494067B1 (ko) | 2004-03-05 | 2015-02-16 | 더 트러스티스 오브 더 유니버시티 오브 펜실바니아 | 부작용을 최소화하면서 과지질혈증 및 과콜레스테롤혈증과 연관된 질환 또는 질병의 치료 방법 |
| BR102015025502B1 (pt) | 2015-04-30 | 2022-06-21 | Aegerion Pharmaceuticals, Inc | Composição de lomitapida, tablete, produto de lomitapida, métodos para analisar uma composição de amostra de lomitapida e para determinar uma quantidade de uma impureza em uma amostra da composição |
-
2022
- 2022-03-03 CA CA3208189A patent/CA3208189A1/en active Pending
- 2022-03-03 AU AU2022231007A patent/AU2022231007A1/en active Pending
- 2022-03-03 MX MX2023010297A patent/MX2023010297A/es unknown
- 2022-03-03 BR BR112023016943A patent/BR112023016943A2/pt unknown
- 2022-03-03 JP JP2023553354A patent/JP2024508334A/ja active Pending
- 2022-03-03 IL IL305191A patent/IL305191A/en unknown
- 2022-03-03 EP EP22711788.4A patent/EP4301361A1/en active Pending
- 2022-03-03 US US18/548,798 patent/US20240165093A1/en active Pending
- 2022-03-03 WO PCT/US2022/018672 patent/WO2022187463A1/en not_active Ceased
- 2022-03-03 KR KR1020237028890A patent/KR20230153375A/ko active Pending
Also Published As
| Publication number | Publication date |
|---|---|
| IL305191A (en) | 2023-10-01 |
| US20240165093A1 (en) | 2024-05-23 |
| AU2022231007A9 (en) | 2024-09-19 |
| AU2022231007A1 (en) | 2023-08-17 |
| KR20230153375A (ko) | 2023-11-06 |
| MX2023010297A (es) | 2023-09-12 |
| CA3208189A1 (en) | 2022-09-09 |
| JP2024508334A (ja) | 2024-02-26 |
| EP4301361A1 (en) | 2024-01-10 |
| WO2022187463A1 (en) | 2022-09-09 |
Similar Documents
| Publication | Publication Date | Title |
|---|---|---|
| BR112022000019A2 (pt) | Composto da fórmula, composição farmacêutica e método de tratamento de câncer | |
| BR112021024999A2 (pt) | Inibidores de prmt5 | |
| BR112022017393A2 (pt) | Composto, composição farmacêutica, método para tratar um transtorno mediado por brd9, e, uso de um composto | |
| JOP20230277A1 (ar) | مثبطات الكرومينون الألستيرية للفوسفونوسيتيد 3-كيناز (pi3k) لعلاج الأمراض | |
| BR112022012594A2 (pt) | Dosagem de gama-hidroxibutirato (ghb) | |
| EA201792214A1 (ru) | Соединения замещенного хиназолина | |
| BR112019008431A2 (pt) | aplicação de (s)-norcetamina e sal da mesma como fármaco | |
| BR112021021284A2 (pt) | Composto, composição farmacêutica, e, métodos para o tratamento ou profilaxia de doenças inflamatórias da pele, doenças respiratórias, doenças gastrointestinais, doenças oculares, cânceres, doenças reumáticas, doenças desmielinizantes e doenças fibróticas e de inibição da atividade de proteínas de bromodomínio e domínio terminal extra | |
| BR112021018687A2 (pt) | Combinação de dose fixa de canabinoides e cogumelos medicinais para prevenção e tratamento de câncer, doenças inflamatórias ou inflamatórias imunomediadas | |
| BR112023001615A2 (pt) | Tratamento para enxaqueca | |
| BR112021017550A2 (pt) | Métodos de tratamento da amiloidose al | |
| BR112016024176A2 (pt) | composições para tratamento bucal tendo estabilidade aprimorada | |
| BR112021025732A2 (pt) | Inibidores macrocíclicos de mcl-1 | |
| BR112019018615A2 (pt) | compostos antimicrobianos, composições e usos dos mesmos | |
| BR112018073553A2 (pt) | medicamento e composição farmacêutica para a prevenção ou tratamento de fibromialgia ou sintomas funcionais associados com fibromialgia, método para prevenir ou tratar fibromialgia ou sintomas funcionais associados com fibromialgia em um indivíduo, e, uso de um composto carbamato. | |
| BR112023015590A2 (pt) | Antagonistas de gpr84 e usos dos mesmos | |
| MX2019011908A (es) | Macrociclos de peptidos anti-bacterianos y uso de los mismos. | |
| BR112022007616A2 (pt) | Métodos e composições para tratar doença falciforme com um inibidor de ferroportina (vit-2763) | |
| BR112022008938A2 (pt) | Derivados de 1-aminossulfonil-2-carboxipirrol como inibidores de metalo-beta-lactamase | |
| BR112023016943A2 (pt) | Métodos para tratamento da síndrome de quilomicronemia familiar | |
| BR112023015584A2 (pt) | Antagonistas de gpr84 e usos dos mesmos | |
| BR112023019795A2 (pt) | Composições nasais compreendendo alcaftadina | |
| BR112017021589A2 (pt) | métodos para o tratamento de transtornos cardiovasculares | |
| BR112023025789A2 (pt) | Nitroxolina para uso no tratamento de neurofibroma cutâneo | |
| BR112019004791A2 (pt) | tratamento de esclerose múltipla com chs-131 |