AU2022419588A1 - Fitusiran for use in improving patient-reported outcome in hemophilia patients - Google Patents
Fitusiran for use in improving patient-reported outcome in hemophilia patients Download PDFInfo
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- AU2022419588A1 AU2022419588A1 AU2022419588A AU2022419588A AU2022419588A1 AU 2022419588 A1 AU2022419588 A1 AU 2022419588A1 AU 2022419588 A AU2022419588 A AU 2022419588A AU 2022419588 A AU2022419588 A AU 2022419588A AU 2022419588 A1 AU2022419588 A1 AU 2022419588A1
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- hemophilia
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- A—HUMAN NECESSITIES
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- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K31/00—Medicinal preparations containing organic active ingredients
- A61K31/70—Carbohydrates; Sugars; Derivatives thereof
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- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K31/00—Medicinal preparations containing organic active ingredients
- A61K31/70—Carbohydrates; Sugars; Derivatives thereof
- A61K31/7042—Compounds having saccharide radicals and heterocyclic rings
- A61K31/7052—Compounds having saccharide radicals and heterocyclic rings having nitrogen as a ring hetero atom, e.g. nucleosides, nucleotides
- A61K31/7056—Compounds having saccharide radicals and heterocyclic rings having nitrogen as a ring hetero atom, e.g. nucleosides, nucleotides containing five-membered rings with nitrogen as a ring hetero atom
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- A—HUMAN NECESSITIES
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- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P7/00—Drugs for disorders of the blood or the extracellular fluid
- A61P7/04—Antihaemorrhagics; Procoagulants; Haemostatic agents; Antifibrinolytic agents
Landscapes
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Applications Claiming Priority (13)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163293070P | 2021-12-22 | 2021-12-22 | |
| US63/293,070 | 2021-12-22 | ||
| US202263305550P | 2022-02-01 | 2022-02-01 | |
| US63/305,550 | 2022-02-01 | ||
| US202263335535P | 2022-04-27 | 2022-04-27 | |
| US63/335,535 | 2022-04-27 | ||
| US202263359717P | 2022-07-08 | 2022-07-08 | |
| US63/359,717 | 2022-07-08 | ||
| US202263382223P | 2022-11-03 | 2022-11-03 | |
| US63/382,223 | 2022-11-03 | ||
| US202263386489P | 2022-12-07 | 2022-12-07 | |
| US63/386,489 | 2022-12-07 | ||
| PCT/US2022/082213 WO2023122713A1 (en) | 2021-12-22 | 2022-12-22 | Fitusiran for use in improving patient-reported outcome in hemophilia patients |
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| AU2022419588A1 true AU2022419588A1 (en) | 2024-08-01 |
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| AU2022419588A Pending AU2022419588A1 (en) | 2021-12-22 | 2022-12-22 | Fitusiran for use in improving patient-reported outcome in hemophilia patients |
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| US (1) | US20250064842A1 (https=) |
| EP (1) | EP4452280A1 (https=) |
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| KR (1) | KR20240138572A (https=) |
| AU (1) | AU2022419588A1 (https=) |
| CA (1) | CA3243297A1 (https=) |
| IL (1) | IL313677A (https=) |
| MX (1) | MX2024007894A (https=) |
| TW (1) | TW202342065A (https=) |
| WO (1) | WO2023122713A1 (https=) |
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| WO2025171279A1 (en) * | 2024-02-09 | 2025-08-14 | Genzyme Corporation | Treatment of hemophilia with fitusiran |
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| US9127274B2 (en) | 2012-04-26 | 2015-09-08 | Alnylam Pharmaceuticals, Inc. | Serpinc1 iRNA compositions and methods of use thereof |
| KR20180095843A (ko) | 2015-12-07 | 2018-08-28 | 젠자임 코포레이션 | Serpinc1-연관 장애의 치료를 위한 방법 및 조성물 |
| TW202434265A (zh) | 2017-07-10 | 2024-09-01 | 美商健贊公司 | 於患有血友病之個體中治療出血事件之方法及組成物 |
| WO2022120291A1 (en) * | 2020-12-06 | 2022-06-09 | Genzyme Corporation | Treatment of hemophilia with fitusiran |
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2022
- 2022-12-21 TW TW111149131A patent/TW202342065A/zh unknown
- 2022-12-22 KR KR1020247024462A patent/KR20240138572A/ko active Pending
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- 2022-12-22 MX MX2024007894A patent/MX2024007894A/es unknown
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- 2022-12-22 US US18/723,352 patent/US20250064842A1/en active Pending
- 2022-12-22 WO PCT/US2022/082213 patent/WO2023122713A1/en not_active Ceased
- 2022-12-22 JP JP2024537896A patent/JP2025500412A/ja active Pending
- 2022-12-22 IL IL313677A patent/IL313677A/en unknown
Also Published As
| Publication number | Publication date |
|---|---|
| TW202342065A (zh) | 2023-11-01 |
| JP2025500412A (ja) | 2025-01-09 |
| MX2024007894A (es) | 2024-08-20 |
| US20250064842A1 (en) | 2025-02-27 |
| EP4452280A1 (en) | 2024-10-30 |
| WO2023122713A1 (en) | 2023-06-29 |
| KR20240138572A (ko) | 2024-09-20 |
| IL313677A (en) | 2024-08-01 |
| CA3243297A1 (en) | 2023-06-29 |
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