AU2019253700B2 - Rescuing voltage-gated sodium channel function in inhibitory neurons - Google Patents

Rescuing voltage-gated sodium channel function in inhibitory neurons

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Publication number
AU2019253700B2
AU2019253700B2 AU2019253700A AU2019253700A AU2019253700B2 AU 2019253700 B2 AU2019253700 B2 AU 2019253700B2 AU 2019253700 A AU2019253700 A AU 2019253700A AU 2019253700 A AU2019253700 A AU 2019253700A AU 2019253700 B2 AU2019253700 B2 AU 2019253700B2
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seq
vector
expression
scn1a
protein
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AU2019253700A2 (en
AU2019253700A1 (en
Inventor
Erik HESS
Franck KALUME
Edward Sebastian LEIN
Boaz P. LEVI
John K. Mich
Jonathan Ting
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Seattle Childrens Hospital
Allen Institute
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Seattle Childrens Hospital
Allen Institute
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    • A—HUMAN NECESSITIES
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    • C07K14/4702—Regulators; Modulating activity
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    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
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    • A61K48/00—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy
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    • C12N2750/14011—Parvoviridae
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AU2019253700A 2018-04-09 2019-04-09 Rescuing voltage-gated sodium channel function in inhibitory neurons Active AU2019253700B2 (en)

Priority Applications (1)

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AU2025263840A AU2025263840A1 (en) 2018-04-09 2025-11-07 Rescuing voltage-gated sodium channel function in inhibitory neurons

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US201862655043P 2018-04-09 2018-04-09
US62/655,043 2018-04-09
US201862742835P 2018-10-08 2018-10-08
US62/742,835 2018-10-08
US201962810281P 2019-02-25 2019-02-25
US62/810,281 2019-02-25
PCT/US2019/026638 WO2019199867A1 (en) 2018-04-09 2019-04-09 Rescuing voltage-gated sodium channel function in inhibitory neurons

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JP7793675B2 (ja) 2026-01-05
AU2025263840A1 (en) 2026-01-15
AU2019253700A2 (en) 2020-12-03
CA3096407A1 (en) 2019-10-17
JP2024095779A (ja) 2024-07-10
JP7472036B2 (ja) 2024-04-22
EP3781174A4 (en) 2022-01-26
WO2019199867A1 (en) 2019-10-17
AU2019253700A1 (en) 2020-11-26
US12121563B2 (en) 2024-10-22
JP2021521152A (ja) 2021-08-26
US20250041384A1 (en) 2025-02-06
EP3781174A1 (en) 2021-02-24
US20210015898A1 (en) 2021-01-21

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