AR100771A1 - Métodos de tratamiento que utilizan el ácido 1,2,4-oxadiazolbenzoico - Google Patents
Métodos de tratamiento que utilizan el ácido 1,2,4-oxadiazolbenzoicoInfo
- Publication number
- AR100771A1 AR100771A1 ARP150101807A ARP150101807A AR100771A1 AR 100771 A1 AR100771 A1 AR 100771A1 AR P150101807 A ARP150101807 A AR P150101807A AR P150101807 A ARP150101807 A AR P150101807A AR 100771 A1 AR100771 A1 AR 100771A1
- Authority
- AR
- Argentina
- Prior art keywords
- acid
- oxadiazolbenzoic
- treatment methods
- nmmps
- disease
- Prior art date
Links
Classifications
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K31/00—Medicinal preparations containing organic active ingredients
- A61K31/33—Heterocyclic compounds
- A61K31/395—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins
- A61K31/41—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having five-membered rings with two or more ring hetero atoms, at least one of which being nitrogen, e.g. tetrazole
- A61K31/4245—Oxadiazoles
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P3/00—Drugs for disorders of the metabolism
-
- C—CHEMISTRY; METALLURGY
- C07—ORGANIC CHEMISTRY
- C07D—HETEROCYCLIC COMPOUNDS
- C07D271/00—Heterocyclic compounds containing five-membered rings having two nitrogen atoms and one oxygen atom as the only ring hetero atoms
- C07D271/02—Heterocyclic compounds containing five-membered rings having two nitrogen atoms and one oxygen atom as the only ring hetero atoms not condensed with other rings
- C07D271/06—1,2,4-Oxadiazoles; Hydrogenated 1,2,4-oxadiazoles
Abstract
Reivindicación 1: Un método para el tratamiento, prevención, recuperación o control de una enfermedad de mucopolisacaridosis con mediación de mutación interruptora (nmMPS) asociada con una mutación interruptora o un codón de terminación prematura, que comprende la administración de una cantidad efectiva de ácido 3-[5-(2-fluoro-fenil)-[1,2,4]oxadiazol-3-il]benzoico o una sal farmacéuticamente aceptable de este a un paciente que tiene la enfermedad de nmMPS.
Applications Claiming Priority (1)
Application Number | Priority Date | Filing Date | Title |
---|---|---|---|
US201462009100P | 2014-06-06 | 2014-06-06 |
Publications (1)
Publication Number | Publication Date |
---|---|
AR100771A1 true AR100771A1 (es) | 2016-11-02 |
Family
ID=54767414
Family Applications (1)
Application Number | Title | Priority Date | Filing Date |
---|---|---|---|
ARP150101807A AR100771A1 (es) | 2014-06-06 | 2015-06-05 | Métodos de tratamiento que utilizan el ácido 1,2,4-oxadiazolbenzoico |
Country Status (4)
Country | Link |
---|---|
US (1) | US20170196842A1 (es) |
AR (1) | AR100771A1 (es) |
TW (1) | TW201625241A (es) |
WO (1) | WO2015188037A1 (es) |
Families Citing this family (3)
Publication number | Priority date | Publication date | Assignee | Title |
---|---|---|---|---|
KR102497273B1 (ko) | 2014-03-06 | 2023-02-07 | 피티씨 테라퓨틱스, 인크. | 1,2,4-옥사디아졸 벤조산의 약학 조성물 및 염 |
CA3003132A1 (en) | 2015-10-30 | 2017-05-04 | Ptc Therapeutics, Inc. | Methods for treating epilepsy |
US11203578B2 (en) | 2017-11-23 | 2021-12-21 | Universita'degli Studi Dipalermo | Oxadiazole derivatives for the treatment of genetic diseases due to nonsense mutations |
Family Cites Families (2)
Publication number | Priority date | Publication date | Assignee | Title |
---|---|---|---|---|
MX2007012206A (es) * | 2005-04-08 | 2007-12-05 | Ptc Therapeutics Inc | Composiciones de 1,2,4-oxadiazol activo por via oral para terapia de supresion de mutacion interruptora. |
ES2710854T3 (es) * | 2010-08-05 | 2019-04-29 | Univ Lille | Compuesto útil para el tratamiento de enfermedades mediadas por una mutación sin sentido y composición farmacéutica que comprende dicho compuesto |
-
2015
- 2015-06-05 US US15/316,415 patent/US20170196842A1/en not_active Abandoned
- 2015-06-05 TW TW104118395A patent/TW201625241A/zh unknown
- 2015-06-05 AR ARP150101807A patent/AR100771A1/es unknown
- 2015-06-05 WO PCT/US2015/034350 patent/WO2015188037A1/en active Application Filing
Also Published As
Publication number | Publication date |
---|---|
TW201625241A (zh) | 2016-07-16 |
WO2015188037A1 (en) | 2015-12-10 |
US20170196842A1 (en) | 2017-07-13 |
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Legal Events
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