MX2010009874A - Tratamiento para la enfermedad de pompe con chaperonas farmacologicas especificas y monitoreo del tratamiento usando marcadores subrogados. - Google Patents
Tratamiento para la enfermedad de pompe con chaperonas farmacologicas especificas y monitoreo del tratamiento usando marcadores subrogados.Info
- Publication number
- MX2010009874A MX2010009874A MX2010009874A MX2010009874A MX2010009874A MX 2010009874 A MX2010009874 A MX 2010009874A MX 2010009874 A MX2010009874 A MX 2010009874A MX 2010009874 A MX2010009874 A MX 2010009874A MX 2010009874 A MX2010009874 A MX 2010009874A
- Authority
- MX
- Mexico
- Prior art keywords
- pompe
- dnj
- gaa
- glucosidase
- treatment
- Prior art date
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- G01N33/48—Biological material, e.g. blood, urine; Haemocytometers
- G01N33/50—Chemical analysis of biological material, e.g. blood, urine; Testing involving biospecific ligand binding methods; Immunological testing
- G01N33/68—Chemical analysis of biological material, e.g. blood, urine; Testing involving biospecific ligand binding methods; Immunological testing involving proteins, peptides or amino acids
- G01N33/6893—Chemical analysis of biological material, e.g. blood, urine; Testing involving biospecific ligand binding methods; Immunological testing involving proteins, peptides or amino acids related to diseases not provided for elsewhere
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- G—PHYSICS
- G01—MEASURING; TESTING
- G01N—INVESTIGATING OR ANALYSING MATERIALS BY DETERMINING THEIR CHEMICAL OR PHYSICAL PROPERTIES
- G01N33/00—Investigating or analysing materials by specific methods not covered by groups G01N1/00 - G01N31/00
- G01N33/48—Biological material, e.g. blood, urine; Haemocytometers
- G01N33/50—Chemical analysis of biological material, e.g. blood, urine; Testing involving biospecific ligand binding methods; Immunological testing
- G01N33/5005—Chemical analysis of biological material, e.g. blood, urine; Testing involving biospecific ligand binding methods; Immunological testing involving human or animal cells
- G01N33/5091—Chemical analysis of biological material, e.g. blood, urine; Testing involving biospecific ligand binding methods; Immunological testing involving human or animal cells for testing the pathological state of an organism
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- G—PHYSICS
- G01—MEASURING; TESTING
- G01N—INVESTIGATING OR ANALYSING MATERIALS BY DETERMINING THEIR CHEMICAL OR PHYSICAL PROPERTIES
- G01N2333/00—Assays involving biological materials from specific organisms or of a specific nature
- G01N2333/435—Assays involving biological materials from specific organisms or of a specific nature from animals; from humans
- G01N2333/475—Assays involving growth factors
- G01N2333/49—Platelet-derived growth factor [PDGF]
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- G—PHYSICS
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- G01N—INVESTIGATING OR ANALYSING MATERIALS BY DETERMINING THEIR CHEMICAL OR PHYSICAL PROPERTIES
- G01N2333/00—Assays involving biological materials from specific organisms or of a specific nature
- G01N2333/435—Assays involving biological materials from specific organisms or of a specific nature from animals; from humans
- G01N2333/475—Assays involving growth factors
- G01N2333/515—Angiogenesic factors; Angiogenin
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- G—PHYSICS
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- G01N2333/435—Assays involving biological materials from specific organisms or of a specific nature from animals; from humans
- G01N2333/52—Assays involving cytokines
- G01N2333/54—Interleukins [IL]
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- G—PHYSICS
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- G01N—INVESTIGATING OR ANALYSING MATERIALS BY DETERMINING THEIR CHEMICAL OR PHYSICAL PROPERTIES
- G01N2333/00—Assays involving biological materials from specific organisms or of a specific nature
- G01N2333/435—Assays involving biological materials from specific organisms or of a specific nature from animals; from humans
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- G—PHYSICS
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- G01N2333/435—Assays involving biological materials from specific organisms or of a specific nature from animals; from humans
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Applications Claiming Priority (2)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US3586908P | 2008-03-12 | 2008-03-12 | |
| PCT/US2009/036936 WO2009114679A2 (fr) | 2008-03-12 | 2009-03-12 | Traitement de la maladie de pompe au moyen de chaperones pharmacologiques spécifiques, et traitement de surveillance utilisant des critères de substitution |
Publications (1)
| Publication Number | Publication Date |
|---|---|
| MX2010009874A true MX2010009874A (es) | 2010-11-30 |
Family
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Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| MX2010009874A MX2010009874A (es) | 2008-03-12 | 2009-03-12 | Tratamiento para la enfermedad de pompe con chaperonas farmacologicas especificas y monitoreo del tratamiento usando marcadores subrogados. |
Country Status (7)
| Country | Link |
|---|---|
| US (1) | US20110189710A1 (fr) |
| EP (1) | EP2252325A4 (fr) |
| JP (1) | JP2011512876A (fr) |
| AU (1) | AU2009223092A1 (fr) |
| CA (1) | CA2718182A1 (fr) |
| MX (1) | MX2010009874A (fr) |
| WO (1) | WO2009114679A2 (fr) |
Families Citing this family (7)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US20150258081A1 (en) * | 2011-12-22 | 2015-09-17 | Centogene Ip Gmbh | Combination of a compound having the ability to rearrange a lysosomal enzyme and ambroxol and/or a derivative of ambroxol |
| WO2013134530A1 (fr) * | 2012-03-07 | 2013-09-12 | Amicus Therapeutics, Inc. | Compositions d'alpha-glucosidase à haute concentration pour le traitement de la maladie de pompe |
| JP6024953B2 (ja) * | 2012-07-25 | 2016-11-16 | 国立大学法人 岡山大学 | Ｐｉｎｋ１のユビキチン化アッセイ及びスクリーニングへの利用 |
| BR112017005810A2 (pt) | 2014-09-30 | 2018-02-27 | Amicus Therapeutics Inc | alfa-glucosidase ácida altamente potente com carboidratos melhorados |
| KR102510941B1 (ko) | 2015-12-30 | 2023-03-20 | 아미쿠스 세라퓨틱스, 인코포레이티드 | 폼페병 치료용의 강화된 산 알파-글루코시다제 |
| BR112018070189A2 (pt) | 2016-03-30 | 2019-02-19 | Amicus Therapeutics, Inc. | método para seleção de proteínas recombinantes ricas em m6p |
| SG11201808455VA (en) | 2016-03-30 | 2018-10-30 | Amicus Therapeutics Inc | Formulations comprising recombinant acid alpha-glucosidase |
Family Cites Families (6)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US5869262A (en) * | 1992-01-27 | 1999-02-09 | Icos Corporation | Method for monitoring an inflammatory disease state by detecting circulating ICAM-R |
| AUPN991796A0 (en) * | 1996-05-17 | 1996-06-13 | Women's And Children's Hospital | Early detection of lysosomal storage disorders |
| AU2001269923A1 (en) * | 2000-06-19 | 2002-01-02 | Genzyme Corporation | Combination enzyme replacement, gene therapy and small molecule therapy for lysosomal storage diseases |
| US6900016B1 (en) * | 2000-09-08 | 2005-05-31 | Applera Corporation | Polymorphisms in known genes associated with inflammatory autoimmune disease, methods of detection and uses thereof |
| EP3441090A1 (fr) * | 2005-05-17 | 2019-02-13 | Amicus Therapeutics, Inc. | Procédé pour le traitement de la maladie de pompe au moyen de 1-désoxynojirimycine et de ses dérivés |
| EP1888068B1 (fr) * | 2005-06-08 | 2014-05-21 | Amicus Therapeutics, Inc. | Traitement de troubles du snc associes a des mutations dans des genes codant pour des enzymes lysosomales |
-
2009
- 2009-03-12 CA CA2718182A patent/CA2718182A1/fr not_active Abandoned
- 2009-03-12 US US12/920,864 patent/US20110189710A1/en not_active Abandoned
- 2009-03-12 EP EP09720946A patent/EP2252325A4/fr not_active Withdrawn
- 2009-03-12 WO PCT/US2009/036936 patent/WO2009114679A2/fr active Application Filing
- 2009-03-12 AU AU2009223092A patent/AU2009223092A1/en not_active Abandoned
- 2009-03-12 JP JP2010550860A patent/JP2011512876A/ja not_active Ceased
- 2009-03-12 MX MX2010009874A patent/MX2010009874A/es unknown
Also Published As
| Publication number | Publication date |
|---|---|
| JP2011512876A (ja) | 2011-04-28 |
| US20110189710A1 (en) | 2011-08-04 |
| CA2718182A1 (fr) | 2009-09-17 |
| WO2009114679A3 (fr) | 2010-02-18 |
| AU2009223092A1 (en) | 2009-09-17 |
| EP2252325A2 (fr) | 2010-11-24 |
| EP2252325A4 (fr) | 2012-07-11 |
| WO2009114679A2 (fr) | 2009-09-17 |
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