KR20230117731A - 청력 상실의 치료를 위한 변이체 아데노-연관된 바이러스(aav) 캡시드 폴리펩티드 및 이의 유전자 치료제 - Google Patents
청력 상실의 치료를 위한 변이체 아데노-연관된 바이러스(aav) 캡시드 폴리펩티드 및 이의 유전자 치료제 Download PDFInfo
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| WO2020148458A1 (en) * | 2019-01-18 | 2020-07-23 | Institut Pasteur | Aav-mediated gene therapy restoring the otoferlin gene |
| CA3153133A1 (en) * | 2019-09-30 | 2021-04-08 | Chris Bartolome | Adeno-associated virus (aav) systems for treatment of genetic hearing loss |
| CN111349148A (zh) * | 2020-03-13 | 2020-06-30 | 辉大(上海)生物科技有限公司 | 一种腺相关病毒载体及其用途 |
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| CA3197592A1 (en) | 2022-05-12 |
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| MX2023005344A (es) | 2023-12-07 |
| AU2021376225A1 (en) | 2023-06-22 |
| WO2022099007A1 (en) | 2022-05-12 |
| IL302653A (en) | 2023-07-01 |
| JP2023549124A (ja) | 2023-11-22 |
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