KR102758180B1 - 합성 가이드 분자, 그와 관련된 조성물 및 방법 - Google Patents

합성 가이드 분자, 그와 관련된 조성물 및 방법 Download PDF

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KR102758180B1
KR102758180B1 KR1020237043357A KR20237043357A KR102758180B1 KR 102758180 B1 KR102758180 B1 KR 102758180B1 KR 1020237043357 A KR1020237043357 A KR 1020237043357A KR 20237043357 A KR20237043357 A KR 20237043357A KR 102758180 B1 KR102758180 B1 KR 102758180B1
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guide molecule
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KR20230175330A (ko
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짐 하일
스테파니 킹
샘 사코마노
스테이시 케이프하트
세실리아 페르난데스
하리하란 자야람
브루스 이튼
카린 젬스키 베리
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에디타스 메디신, 인코포레이티드
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    • C12N15/09—Recombinant DNA-technology
    • C12N15/11—DNA or RNA fragments; Modified forms thereof; Non-coding nucleic acids having a biological activity
    • C12N15/113—Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids, e.g. ribozymes; Nucleic acids used in co-suppression or gene silencing
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    • A61K31/712—Nucleic acids or oligonucleotides having modified sugars, i.e. other than ribose or 2'-deoxyribose
    • A—HUMAN NECESSITIES
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    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
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    • C12N9/14—Hydrolases (3)
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    • C12N2310/00—Structure or type of the nucleic acid
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  • Micro-Organisms Or Cultivation Processes Thereof (AREA)
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KR1020237043357A 2016-12-30 2017-12-29 합성 가이드 분자, 그와 관련된 조성물 및 방법 Active KR102758180B1 (ko)

Applications Claiming Priority (6)

Application Number Priority Date Filing Date Title
US201662441046P 2016-12-30 2016-12-30
US62/441,046 2016-12-30
US201762492001P 2017-04-28 2017-04-28
US62/492,001 2017-04-28
PCT/US2017/069019 WO2018126176A1 (en) 2016-12-30 2017-12-29 Synthetic guide molecules, compositions and methods relating thereto
KR1020197022278A KR102618864B1 (ko) 2016-12-30 2017-12-29 합성 가이드 분자, 그와 관련된 조성물 및 방법

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KR20230175330A KR20230175330A (ko) 2023-12-29
KR102758180B1 true KR102758180B1 (ko) 2025-01-23

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KR1020197022278A Active KR102618864B1 (ko) 2016-12-30 2017-12-29 합성 가이드 분자, 그와 관련된 조성물 및 방법

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US (1) US20230111575A1 (enExample)
EP (1) EP3565895A1 (enExample)
JP (3) JP7167029B2 (enExample)
KR (2) KR102758180B1 (enExample)
CN (2) CN118345072A (enExample)
AU (2) AU2017388753A1 (enExample)
CA (1) CA3048434A1 (enExample)
MX (1) MX420023B (enExample)
WO (1) WO2018126176A1 (enExample)

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JP2025016776A (ja) 2025-02-04
CN110249052A (zh) 2019-09-17
US20230111575A1 (en) 2023-04-13
KR102618864B1 (ko) 2024-01-02
CN110249052B (zh) 2024-04-12
JP2022173349A (ja) 2022-11-18
JP7167029B2 (ja) 2022-11-08
MX420023B (es) 2025-01-14
AU2017388753A1 (en) 2019-07-11
AU2024205204A1 (en) 2024-09-05
WO2018126176A1 (en) 2018-07-05
MX2019007750A (es) 2019-10-15
CN118345072A (zh) 2024-07-16
CA3048434A1 (en) 2018-07-05
KR20190110554A (ko) 2019-09-30
KR20230175330A (ko) 2023-12-29
JP2020503049A (ja) 2020-01-30
EP3565895A1 (en) 2019-11-13
JP7610559B2 (ja) 2025-01-08

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