JPWO2023069754A5 - - Google Patents

Info

Publication number
JPWO2023069754A5
JPWO2023069754A5 JP2024523434A JP2024523434A JPWO2023069754A5 JP WO2023069754 A5 JPWO2023069754 A5 JP WO2023069754A5 JP 2024523434 A JP2024523434 A JP 2024523434A JP 2024523434 A JP2024523434 A JP 2024523434A JP WO2023069754 A5 JPWO2023069754 A5 JP WO2023069754A5
Authority
JP
Japan
Prior art keywords
rnai construct
nucleotides
gpam
sense strand
length
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024523434A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024539097A (ja
JP2024539097A5 (https=
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/047491 external-priority patent/WO2023069754A2/en
Publication of JP2024539097A publication Critical patent/JP2024539097A/ja
Publication of JPWO2023069754A5 publication Critical patent/JPWO2023069754A5/ja
Publication of JP2024539097A5 publication Critical patent/JP2024539097A5/ja
Pending legal-status Critical Current

Links

JP2024523434A 2021-10-22 2022-10-21 Gpam発現を阻害するためのrnaiコンストラクト及びその使用方法 Pending JP2024539097A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163270813P 2021-10-22 2021-10-22
US63/270,813 2021-10-22
PCT/US2022/047491 WO2023069754A2 (en) 2021-10-22 2022-10-21 Rnai constructs for inhibiting gpam expression and methods of use thereof

Publications (3)

Publication Number Publication Date
JP2024539097A JP2024539097A (ja) 2024-10-28
JPWO2023069754A5 true JPWO2023069754A5 (https=) 2025-11-12
JP2024539097A5 JP2024539097A5 (https=) 2025-11-12

Family

ID=84360886

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024523434A Pending JP2024539097A (ja) 2021-10-22 2022-10-21 Gpam発現を阻害するためのrnaiコンストラクト及びその使用方法

Country Status (10)

Country Link
EP (1) EP4419682A2 (https=)
JP (1) JP2024539097A (https=)
KR (1) KR20240090496A (https=)
CN (1) CN118525091A (https=)
AU (1) AU2022370883A1 (https=)
CA (1) CA3235262A1 (https=)
CL (1) CL2024001214A1 (https=)
IL (1) IL311839A (https=)
MX (1) MX2024004913A (https=)
WO (1) WO2023069754A2 (https=)

Family Cites Families (37)

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US5981505A (en) 1993-01-26 1999-11-09 The Trustees Of The University Of Pennsylvania Compositions and methods for delivery of genetic material
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ATE285477T1 (de) 1995-06-07 2005-01-15 Inex Pharmaceutical Corp Herstellung von lipid-nukleinsäure partikeln duch ein hydrophobische lipid-nukleinsäuree komplexe zwischenprodukt und zur verwendung in der gentransfer
US7422902B1 (en) 1995-06-07 2008-09-09 The University Of British Columbia Lipid-nucleic acid particles prepared via a hydrophobic lipid-nucleic acid complex intermediate and use for gene transfer
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