JPWO2020237130A5 - - Google Patents
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- Publication number
- JPWO2020237130A5 JPWO2020237130A5 JP2021569494A JP2021569494A JPWO2020237130A5 JP WO2020237130 A5 JPWO2020237130 A5 JP WO2020237130A5 JP 2021569494 A JP2021569494 A JP 2021569494A JP 2021569494 A JP2021569494 A JP 2021569494A JP WO2020237130 A5 JPWO2020237130 A5 JP WO2020237130A5
- Authority
- JP
- Japan
- Prior art keywords
- polynucleotide
- expression cassette
- vector
- expression
- human
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962851411P | 2019-05-22 | 2019-05-22 | |
| US62/851,411 | 2019-05-22 | ||
| PCT/US2020/034171 WO2020237130A1 (en) | 2019-05-22 | 2020-05-22 | Ube3a genes and expression cassettes and their use |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2022533448A JP2022533448A (ja) | 2022-07-22 |
| JPWO2020237130A5 true JPWO2020237130A5 (ru) | 2023-10-31 |
Family
ID=73458642
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021569494A Pending JP2022533448A (ja) | 2019-05-22 | 2020-05-22 | Ｕｂｅ３ａ遺伝子および発現カセットならびにそれらの使用 |
Country Status (12)
| Country | Link |
|---|---|
| US (1) | US20220241434A1 (ru) |
| EP (1) | EP3973059A4 (ru) |
| JP (1) | JP2022533448A (ru) |
| KR (1) | KR20210158859A (ru) |
| CN (1) | CN114127296A (ru) |
| AU (1) | AU2020279387A1 (ru) |
| CA (1) | CA3139678A1 (ru) |
| EA (1) | EA202193214A1 (ru) |
| IL (1) | IL287943A (ru) |
| MX (1) | MX2021014248A (ru) |
| SG (1) | SG11202112470YA (ru) |
| WO (1) | WO2020237130A1 (ru) |
Families Citing this family (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CA3200192A1 (en) * | 2020-12-01 | 2022-06-09 | Justin PERCIVAL | Compositions and uses thereof for treatment of angelman syndrome |
| WO2023239782A2 (en) * | 2022-06-07 | 2023-12-14 | Kicho Inc. | Agents for modulating expression |
Family Cites Families (8)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2014004572A2 (en) * | 2012-06-25 | 2014-01-03 | Isis Pharmaceuticals, Inc. | Modulation of ube3a-ats expression |
| RU2716421C2 (ru) * | 2013-06-17 | 2020-03-11 | Те Брод Инститьют Инк. | Доставка, применение и применения в терапии систем crispr-cas и композиций для целенаправленного воздействия на нарушения и заболевания с использованием вирусных компонентов |
| CA2984629A1 (en) * | 2015-05-07 | 2016-11-10 | University Of South Florida | Modified ube3a gene for a gene therapy approach for angelman syndrome |
| WO2017048466A1 (en) * | 2015-09-15 | 2017-03-23 | The Regents Of The University Of California | Compositions and methods for delivering biotherapeutics |
| WO2017081250A1 (en) * | 2015-11-12 | 2017-05-18 | F. Hoffmann-La Roche Ag | Standardized neuronal cell assays from primate species |
| CN110869031A (zh) * | 2017-06-28 | 2020-03-06 | 南佛罗里达大学 | 用于天使人综合征的基因治疗方法的修饰的ube3a基因 |
| WO2020191366A1 (en) * | 2019-03-21 | 2020-09-24 | Ptc Therapeutics, Inc. | Vector and method for treating angelman syndrome |
| MX2022002139A (es) * | 2019-08-22 | 2022-03-17 | Univ California | Ube3a para el tratamiento del sindrome de angelman. |
-
2020
- 2020-05-22 CA CA3139678A patent/CA3139678A1/en active Pending
- 2020-05-22 AU AU2020279387A patent/AU2020279387A1/en active Pending
- 2020-05-22 MX MX2021014248A patent/MX2021014248A/es unknown
- 2020-05-22 WO PCT/US2020/034171 patent/WO2020237130A1/en unknown
- 2020-05-22 CN CN202080050918.0A patent/CN114127296A/zh active Pending
- 2020-05-22 EA EA202193214A patent/EA202193214A1/ru unknown
- 2020-05-22 US US17/612,833 patent/US20220241434A1/en active Pending
- 2020-05-22 JP JP2021569494A patent/JP2022533448A/ja active Pending
- 2020-05-22 KR KR1020217041626A patent/KR20210158859A/ko unknown
- 2020-05-22 SG SG11202112470YA patent/SG11202112470YA/en unknown
- 2020-05-22 EP EP20809370.8A patent/EP3973059A4/en active Pending
-
2021
- 2021-11-09 IL IL287943A patent/IL287943A/en unknown
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