JP7558929B2 - プログラム可能塩基エディターシステムを用いて病原性変異を抑制する方法 - Google Patents

プログラム可能塩基エディターシステムを用いて病原性変異を抑制する方法 Download PDF

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JP7558929B2
JP7558929B2 JP2021513762A JP2021513762A JP7558929B2 JP 7558929 B2 JP7558929 B2 JP 7558929B2 JP 2021513762 A JP2021513762 A JP 2021513762A JP 2021513762 A JP2021513762 A JP 2021513762A JP 7558929 B2 JP7558929 B2 JP 7558929B2
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polynucleotide
protein
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ジョン エヴァンス、
ヤンファン フ、
マイケル パッカー、
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ビーム セラピューティクス インク．
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JP2021513762A 2018-05-11 2019-05-11 プログラム可能塩基エディターシステムを用いて病原性変異を抑制する方法 Active JP7558929B2 (ja)

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US201862670498P 2018-05-11 2018-05-11
US62/670,498 2018-05-11
US201862780864P 2018-12-17 2018-12-17
US62/780,864 2018-12-17
PCT/US2019/031896 WO2019217941A1 (en) 2018-05-11 2019-05-11 Methods of suppressing pathogenic mutations using programmable base editor systems

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