JP2025512501A5 - - Google Patents

Info

Publication number
JP2025512501A5
JP2025512501A5 JP2024560756A JP2024560756A JP2025512501A5 JP 2025512501 A5 JP2025512501 A5 JP 2025512501A5 JP 2024560756 A JP2024560756 A JP 2024560756A JP 2024560756 A JP2024560756 A JP 2024560756A JP 2025512501 A5 JP2025512501 A5 JP 2025512501A5
Authority
JP
Japan
Prior art keywords
seq
exon
pmp22
shc
mer
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024560756A
Other languages
English (en)
Japanese (ja)
Other versions
JP2025512501A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2023/065728 external-priority patent/WO2023201300A2/en
Publication of JP2025512501A publication Critical patent/JP2025512501A/ja
Publication of JP2025512501A5 publication Critical patent/JP2025512501A5/ja
Pending legal-status Critical Current

Links

JP2024560756A 2022-04-14 2023-04-13 シャルコー・マリー・トゥース病に対するポリヌクレオチド治療 Pending JP2025512501A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202263331045P 2022-04-14 2022-04-14
US202263331044P 2022-04-14 2022-04-14
US63/331,045 2022-04-14
US63/331,044 2022-04-14
PCT/US2023/065728 WO2023201300A2 (en) 2022-04-14 2023-04-13 Polynucleotide treatments for charcot-marie-tooth disease

Publications (2)

Publication Number Publication Date
JP2025512501A JP2025512501A (ja) 2025-04-17
JP2025512501A5 true JP2025512501A5 (https=) 2026-04-03

Family

ID=88330382

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024560756A Pending JP2025512501A (ja) 2022-04-14 2023-04-13 シャルコー・マリー・トゥース病に対するポリヌクレオチド治療

Country Status (7)

Country Link
US (2) US20250333744A1 (https=)
EP (1) EP4508219A2 (https=)
JP (1) JP2025512501A (https=)
KR (1) KR20250005287A (https=)
AU (1) AU2023254106A1 (https=)
CA (1) CA3248302A1 (https=)
WO (2) WO2023201300A2 (https=)

Family Cites Families (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JP2009538603A (ja) * 2006-06-02 2009-11-12 ヒューマン ジェネティック シグネチャーズ ピーティーワイ リミテッド 微生物の検出および分析に使用するための微生物改変核酸
US20150086982A1 (en) * 2011-08-19 2015-03-26 Roka Bioscience, Inc. Compositions and methods for detecting and discriminating between yeast or mold
EP3174981B1 (en) * 2014-07-31 2020-03-25 Association Institut de Myologie Treatment of amyotrophic lateral sclerosis
WO2017156242A1 (en) * 2016-03-09 2017-09-14 Ionis Pharmaceuticals, Inc. Methods and compositions for inhibiting pmp22 expression
WO2021113390A1 (en) * 2019-12-02 2021-06-10 Shape Therapeutics Inc. Compositions for treatment of diseases
AU2021244774A1 (en) * 2020-03-23 2022-09-29 Monash University Antisense oligomers for treatment of disease

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