JP2025510339A5 - - Google Patents

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Publication number
JP2025510339A5
JP2025510339A5 JP2024557582A JP2024557582A JP2025510339A5 JP 2025510339 A5 JP2025510339 A5 JP 2025510339A5 JP 2024557582 A JP2024557582 A JP 2024557582A JP 2024557582 A JP2024557582 A JP 2024557582A JP 2025510339 A5 JP2025510339 A5 JP 2025510339A5
Authority
JP
Japan
Prior art keywords
nucleic acid
composition
use according
modified
weeks
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024557582A
Other languages
English (en)
Japanese (ja)
Other versions
JP2025510339A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2023/065074 external-priority patent/WO2023192885A2/en
Publication of JP2025510339A publication Critical patent/JP2025510339A/ja
Publication of JP2025510339A5 publication Critical patent/JP2025510339A5/ja
Pending legal-status Critical Current

Links

JP2024557582A 2022-03-28 2023-03-28 オリゴマー化合物を使用してscn2a関連障害を治療する方法 Pending JP2025510339A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202263324531P 2022-03-28 2022-03-28
US63/324,531 2022-03-28
US202263335152P 2022-04-26 2022-04-26
US63/335,152 2022-04-26
PCT/US2023/065074 WO2023192885A2 (en) 2022-03-28 2023-03-28 Methods of using oligomeric compounds to treat scn2a-related disorders

Publications (2)

Publication Number Publication Date
JP2025510339A JP2025510339A (ja) 2025-04-14
JP2025510339A5 true JP2025510339A5 (enExample) 2026-04-06

Family

ID=88203426

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024557582A Pending JP2025510339A (ja) 2022-03-28 2023-03-28 オリゴマー化合物を使用してscn2a関連障害を治療する方法

Country Status (6)

Country Link
US (1) US20250179503A1 (enExample)
EP (1) EP4499835A2 (enExample)
JP (1) JP2025510339A (enExample)
AU (1) AU2023244348A1 (enExample)
CA (1) CA3246834A1 (enExample)
WO (1) WO2023192885A2 (enExample)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
AU2024343201A1 (en) * 2023-09-15 2026-03-26 Praxis Precision Medicines, Inc. Elsunersen / prax-222 for use in the treatment of scn2a-related disorders

Family Cites Families (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US8138201B2 (en) * 2007-07-11 2012-03-20 Medicinova, Inc. Treatment of progressive neurodegenerative disease with ibudilast
IL297642A (en) * 2020-04-29 2022-12-01 Praxis Prec Medicines Inc Methods for using t-type calcium channel modulators
IL300258A (en) * 2020-08-07 2023-03-01 Ionis Pharmaceuticals Inc Compounds and methods for modulating SCN2A

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