JP2024543782A5 - - Google Patents

Info

Publication number
JP2024543782A5
JP2024543782A5 JP2024521180A JP2024521180A JP2024543782A5 JP 2024543782 A5 JP2024543782 A5 JP 2024543782A5 JP 2024521180 A JP2024521180 A JP 2024521180A JP 2024521180 A JP2024521180 A JP 2024521180A JP 2024543782 A5 JP2024543782 A5 JP 2024543782A5
Authority
JP
Japan
Prior art keywords
drawings
invention described
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024521180A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024543782A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/077572 external-priority patent/WO2023060104A1/en
Publication of JP2024543782A publication Critical patent/JP2024543782A/ja
Publication of JP2024543782A5 publication Critical patent/JP2024543782A5/ja
Pending legal-status Critical Current

Links

JP2024521180A 2021-10-06 2022-10-05 Cagリピート疾患を治療するための組成物および方法 Pending JP2024543782A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202163253070P 2021-10-06 2021-10-06
US63/253,070 2021-10-06
US202263339363P 2022-05-06 2022-05-06
US63/339,363 2022-05-06
PCT/US2022/077572 WO2023060104A1 (en) 2021-10-06 2022-10-05 Compositions and methods for treating cag repeat diseases

Publications (2)

Publication Number Publication Date
JP2024543782A JP2024543782A (ja) 2024-11-26
JP2024543782A5 true JP2024543782A5 (https=) 2025-10-14

Family

ID=85804745

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024521180A Pending JP2024543782A (ja) 2021-10-06 2022-10-05 Cagリピート疾患を治療するための組成物および方法

Country Status (9)

Country Link
US (1) US20240425856A1 (https=)
EP (1) EP4413137A4 (https=)
JP (1) JP2024543782A (https=)
AU (1) AU2022358732A1 (https=)
CA (1) CA3232737A1 (https=)
IL (1) IL311638A (https=)
MX (1) MX2024004119A (https=)
TW (1) TW202329985A (https=)
WO (1) WO2023060104A1 (https=)

Families Citing this family (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
AU2024253981A1 (en) * 2023-04-05 2025-11-06 Board Of Trustees Of Southern Illinois University Compositions and methods for treating cag repeat diseases
US20240360443A1 (en) * 2023-04-09 2024-10-31 Dystrogen Gene Therapies Inc. Nucleic acid molecule and use of the nucleic acid molecule in therapy of diseases induced by expansion of trinucleotide cag repeats
AU2024332679A1 (en) * 2023-08-31 2026-04-16 Iris Medicine, Inc. Methods and compositions for treating ggggcc repeat expansion diseases
WO2025137623A1 (en) * 2023-12-22 2025-06-26 Iris Medicine, Inc. Methods and compositions for treating ctg repeat expansion diseases
WO2025213123A1 (en) * 2024-04-05 2025-10-09 Encoded Therapeutics, Inc. Methods and compositions for increasing expression of ube3a

Family Cites Families (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
PL243776B1 (pl) * 2013-09-02 2023-10-09 Inst Chemii Bioorganicznej Polskiej Akademii Nauk Cząsteczka kwasu nukleinowego, kaseta ekspresyjna, wektor ekspresyjny, komórka eukariotycznego gospodarza i zastosowanie cząsteczki kwasu nukleinowego w terapii chorób wywoływanych ekspansją trójnukleotydowych powtórzeń typu CAG
EP3359667A1 (en) * 2015-10-05 2018-08-15 ProQR Therapeutics II B.V. Use of single-stranded antisense oligonucleotide in prevention or treatment of genetic diseases involving a trinucleotide repeat expansion
WO2018152523A1 (en) * 2017-02-20 2018-08-23 Northwestern University Use of trinucleotide repeat rnas to treat cancer

Similar Documents

Publication Publication Date Title
JP2024023385A5 (https=)
JP2022068302A5 (https=)
JP2022028828A5 (https=)
JP2022025124A5 (https=)
JP2021169491A5 (https=)
JP2021185136A5 (https=)
JP2024059739A5 (https=)
JP2020127428A5 (https=)
JP2023022224A5 (https=)
JP2021038271A5 (https=)
JP2022523200A5 (https=)
JP2024016014A5 (https=)
JP2022538797A5 (https=)
JP2022060295A5 (https=)
JP2023100643A5 (https=)
JP2025506484A5 (https=)
JP2023085551A5 (https=)
JP2020171301A5 (https=)
JP2022537813A5 (https=)
JP2020120660A5 (https=)
JP2024534771A5 (https=)
JP2023011759A5 (https=)
JP2025084837A5 (https=)
JP2022022379A5 (https=)
JP2022172276A5 (https=)