JP2024532261A5 - - Google Patents

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Publication number
JP2024532261A5
JP2024532261A5 JP2024512004A JP2024512004A JP2024532261A5 JP 2024532261 A5 JP2024532261 A5 JP 2024532261A5 JP 2024512004 A JP2024512004 A JP 2024512004A JP 2024512004 A JP2024512004 A JP 2024512004A JP 2024532261 A5 JP2024532261 A5 JP 2024532261A5
Authority
JP
Japan
Prior art keywords
seq
nucleic acid
acid molecule
molecule according
nucleotides
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024512004A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024532261A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/075187 external-priority patent/WO2023028441A1/en
Publication of JP2024532261A publication Critical patent/JP2024532261A/ja
Publication of JP2024532261A5 publication Critical patent/JP2024532261A5/ja
Pending legal-status Critical Current

Links

JP2024512004A 2021-08-23 2022-08-19 操作ｉｔｒ配列および使用方法 Pending JP2024532261A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
USPCT/US2021/047207 2021-08-23
USPCT/US2021/047207 2021-08-23
US202263310042P 2022-02-14 2022-02-14
US63/310,042 2022-02-14
PCT/US2022/075187 WO2023028441A1 (en) 2021-08-23 2022-08-19 Engineered itr sequences and methods of use

Publications (2)

Publication Number Publication Date
JP2024532261A JP2024532261A (ja) 2024-09-05
JP2024532261A5 true JP2024532261A5 (https=) 2025-08-26

Family

ID=83598638

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024512004A Pending JP2024532261A (ja) 2021-08-23 2022-08-19 操作ｉｔｒ配列および使用方法

Country Status (4)

Country Link
US (1) US20240350671A1 (https=)
EP (1) EP4392444A1 (https=)
JP (1) JP2024532261A (https=)
WO (1) WO2023028441A1 (https=)

Families Citing this family (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
NZ762100A (en) 2017-08-09 2025-12-19 Bioverativ Therapeutics Inc Nucleic acid molecules and uses thereof
EP3833766A1 (en) 2018-08-09 2021-06-16 Bioverativ Therapeutics Inc. Nucleic acid molecules and uses thereof for non-viral gene therapy
CA3262218A1 (en) 2022-07-19 2024-01-25 Rampart Bioscience, Inc. CIRCULAR NON-IMMUNOGENEOUS NON-VIRAL DNA VECTORS
EP4692314A1 (en) * 2023-03-24 2026-02-11 Nanjing GenScript Biotech Co., Ltd. Host cell for improving stability of plasmid

Family Cites Families (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2014168953A1 (en) * 2013-04-08 2014-10-16 University Of Iowa Research Foundation Chimeric adeno-associated virus/ bocavirus parvovirus vector
CA3012695A1 (en) 2016-02-01 2017-08-10 Bioverativ Therapeutics Inc. Optimized factor viii genes
US11142775B2 (en) * 2017-01-13 2021-10-12 University Of Iowa Research Foundation Bocaparvovirus small noncoding RNA and uses thereof
NZ762100A (en) * 2017-08-09 2025-12-19 Bioverativ Therapeutics Inc Nucleic acid molecules and uses thereof
EP3833766A1 (en) 2018-08-09 2021-06-16 Bioverativ Therapeutics Inc. Nucleic acid molecules and uses thereof for non-viral gene therapy

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