JP2024511767A - 筋萎縮性側索硬化症の治療 - Google Patents
筋萎縮性側索硬化症の治療 Download PDFInfo
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- C12N15/09—Recombinant DNA-technology
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- C12N15/113—Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids, e.g. ribozymes; Nucleic acids used in co-suppression or gene silencing
- C12N15/1137—Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids, e.g. ribozymes; Nucleic acids used in co-suppression or gene silencing against enzymes
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- Investigating Or Analysing Biological Materials (AREA)
Applications Claiming Priority (3)
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| US202163168972P | 2021-03-31 | 2021-03-31 | |
| US63/168,972 | 2021-03-31 | ||
| PCT/US2022/022485 WO2022212459A1 (en) | 2021-03-31 | 2022-03-30 | Treatment of amyotrophic lateral sclerosis |
Publications (2)
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| JP2024511767A true JP2024511767A (ja) | 2024-03-15 |
| JP2024511767A5 JP2024511767A5 (https=) | 2025-04-08 |
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| EP (1) | EP4314294A1 (https=) |
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| CA2452458A1 (en) | 2001-07-03 | 2003-01-16 | Isis Pharmaceuticals, Inc. | Nuclease resistant chimeric oligonucleotides |
| HUE050704T2 (hu) | 2014-04-01 | 2020-12-28 | Biogen Ma Inc | Összetételek a SOD-1 expressziójának modulálására |
| TWI906204B (zh) * | 2018-12-14 | 2025-12-01 | 美商百健Ｍａ公司 | 用於治療及預防肌肉萎縮性脊髓側索硬化症之組合物及方法 |
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Also Published As
| Publication number | Publication date |
|---|---|
| KR20230172502A (ko) | 2023-12-22 |
| WO2022212459A1 (en) | 2022-10-06 |
| US20240182903A1 (en) | 2024-06-06 |
| AU2022252236A1 (en) | 2023-10-12 |
| TW202304471A (zh) | 2023-02-01 |
| CN117062911A (zh) | 2023-11-14 |
| EP4314294A1 (en) | 2024-02-07 |
| AU2022252236A9 (en) | 2023-10-19 |
| BR112023019877A2 (pt) | 2023-11-07 |
| CA3214585A1 (en) | 2022-10-06 |
| MX2023011214A (es) | 2023-12-08 |
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