JP2024510972A5 - - Google Patents

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Publication number
JP2024510972A5
JP2024510972A5 JP2023555441A JP2023555441A JP2024510972A5 JP 2024510972 A5 JP2024510972 A5 JP 2024510972A5 JP 2023555441 A JP2023555441 A JP 2023555441A JP 2023555441 A JP2023555441 A JP 2023555441A JP 2024510972 A5 JP2024510972 A5 JP 2024510972A5
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JP
Japan
Prior art keywords
patient
approximately
mmhg
respiratory
assessed
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023555441A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024510972A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/019876 external-priority patent/WO2022192622A1/en
Publication of JP2024510972A publication Critical patent/JP2024510972A/ja
Publication of JP2024510972A5 publication Critical patent/JP2024510972A5/ja
Pending legal-status Critical Current

Links

JP2023555441A 2021-03-11 2022-03-11 X連鎖性ミオチュブラーミオパチーを処置するための組成物及び方法 Pending JP2024510972A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163159898P 2021-03-11 2021-03-11
US63/159,898 2021-03-11
PCT/US2022/019876 WO2022192622A1 (en) 2021-03-11 2022-03-11 Compositions and methods for treating x-linked myotubular myopathy

Publications (2)

Publication Number Publication Date
JP2024510972A JP2024510972A (ja) 2024-03-12
JP2024510972A5 true JP2024510972A5 (https=) 2025-03-19

Family

ID=83227148

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023555441A Pending JP2024510972A (ja) 2021-03-11 2022-03-11 X連鎖性ミオチュブラーミオパチーを処置するための組成物及び方法

Country Status (7)

Country Link
US (1) US20240148906A1 (https=)
EP (1) EP4304664A4 (https=)
JP (1) JP2024510972A (https=)
CN (1) CN117255698A (https=)
AR (1) AR125077A1 (https=)
TW (1) TW202302156A (https=)
WO (1) WO2022192622A1 (https=)

Family Cites Families (23)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
SE9502543D0 (sv) * 1995-07-10 1995-07-10 Lachmann Burkhardt Artificial ventilation system
US6148814A (en) * 1996-02-08 2000-11-21 Ihc Health Services, Inc Method and system for patient monitoring and respiratory assistance control through mechanical ventilation by the use of deterministic protocols
US6804656B1 (en) * 1999-06-23 2004-10-12 Visicu, Inc. System and method for providing continuous, expert network critical care services from a remote location(s)
US7246618B2 (en) * 2001-06-21 2007-07-24 Nader Maher Habashi Ventilation method and control of a ventilator based on same
WO2010150264A1 (en) * 2009-06-24 2010-12-29 Oridion Medical 1987 Ltd. Integrated pulmonary index for weaning from mechanical ventilation
US8695593B2 (en) * 2007-03-31 2014-04-15 Fleur T. Tehrani Weaning and decision support system for mechanical ventilation
US20080295839A1 (en) * 2007-06-01 2008-12-04 Habashi Nader M Ventilator Apparatus and System of Ventilation
US8789529B2 (en) * 2009-08-20 2014-07-29 Covidien Lp Method for ventilation
US20160199608A1 (en) * 2010-02-18 2016-07-14 Orlando Morejon System and method of expediting weaning from ventilator support including an artificial airway cleaning apparatus
US20110213215A1 (en) * 2010-02-26 2011-09-01 Nellcor Puritan Bennett Llc Spontaneous Breathing Trial Manager
US20180280646A1 (en) * 2010-08-13 2018-10-04 Respiratory Motion, Inc. Respiratory volume monitor and ventilator
US9327090B2 (en) * 2012-06-29 2016-05-03 Carefusion 303, Inc. Respiratory knowledge portal
US20140060540A1 (en) * 2012-09-06 2014-03-06 Nellcor Puritan Bennett Llc Method and system for automated spontaneous breathing trial
US20140150796A1 (en) * 2012-11-30 2014-06-05 Covidien Lp System and method for detecting minimal ventilation support with proportional assist ventilation plus software and remote monitoring
US20140235959A1 (en) * 2013-02-15 2014-08-21 Covidien Lp Methods and algorithms for supervisory closed-loop determination of optimized scheduling of ventilator weaning trials
US8957044B2 (en) * 2013-03-01 2015-02-17 Wake Forest University Health Sciences Systemic gene replacement therapy for treatment of X-linked myotubular myopathy (XLMTM)
WO2018035311A1 (en) * 2016-08-19 2018-02-22 Gray John T Compositions and methods for modulating gene expression using reading frame surveillance
FI128346B (en) * 2018-11-19 2020-03-31 Hapella Oy A device for taking care of respiratory well-being and for practicing and improving respiratory function
US11166862B2 (en) * 2018-12-06 2021-11-09 General Electric Company System and method for a thermoregulated environment
WO2021110576A1 (en) * 2019-12-02 2021-06-10 Koninklijke Philips N.V. Providing information for assisting in the treatment of a ventilated and sedated patient
AU2020397171A1 (en) * 2019-12-05 2022-07-07 Disati Medical, Inc Systems and methods for determining a degree of respiratory effort exerted by a patient while breathing
US20230157955A1 (en) * 2020-01-08 2023-05-25 Puretech Lyt, Inc. Vesicle compositions for oral delivery
PH12023553216A1 (en) * 2021-05-24 2024-04-29 Astellas Gene Therapies Inc Compositions and methods for improved treatment of x-linked myotubular myopathy

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