JP2023551874A5 - - Google Patents
Info
- Publication number
- JP2023551874A5 JP2023551874A5 JP2023533279A JP2023533279A JP2023551874A5 JP 2023551874 A5 JP2023551874 A5 JP 2023551874A5 JP 2023533279 A JP2023533279 A JP 2023533279A JP 2023533279 A JP2023533279 A JP 2023533279A JP 2023551874 A5 JP2023551874 A5 JP 2023551874A5
- Authority
- JP
- Japan
- Prior art keywords
- aav
- capsid protein
- sequence
- vector according
- protein
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (7)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202063119977P | 2020-12-01 | 2020-12-01 | |
| US63/119,977 | 2020-12-01 | ||
| US202063130092P | 2020-12-23 | 2020-12-23 | |
| US63/130,092 | 2020-12-23 | ||
| US202163278746P | 2021-11-12 | 2021-11-12 | |
| US63/278,746 | 2021-11-12 | ||
| PCT/US2021/061490 WO2022119979A1 (en) | 2020-12-01 | 2021-12-01 | Rna-targeting compositions and methods for treating myotonic dystrophy type 1 |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2023551874A JP2023551874A (ja) | 2023-12-13 |
| JP2023551874A5 true JP2023551874A5 (https=) | 2024-12-09 |
Family
ID=79731176
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023533279A Pending JP2023551874A (ja) | 2020-12-01 | 2021-12-01 | 筋強直性ジストロフィー１型を処置するためのｒｎａ標的化組成物および方法 |
Country Status (7)
| Country | Link |
|---|---|
| US (1) | US20240108751A1 (https=) |
| EP (1) | EP4255471A1 (https=) |
| JP (1) | JP2023551874A (https=) |
| KR (1) | KR20230129162A9 (https=) |
| AU (1) | AU2021391645A1 (https=) |
| CA (1) | CA3200588A1 (https=) |
| WO (1) | WO2022119979A1 (https=) |
Families Citing this family (8)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP3947700A4 (en) | 2019-04-01 | 2023-01-04 | Tenaya Therapeutics, Inc. | Adeno-associated virus with engineered capsid |
| BR112023006305A2 (pt) | 2020-10-09 | 2023-05-09 | Tenaya Therapeutics Inc | Métodos e composições de terapia gênica com placofilina-2 |
| WO2022119974A1 (en) * | 2020-12-01 | 2022-06-09 | Locanabio, Inc. | Rna-targeting compositions and methods for treating cag repeat diseases |
| WO2022221278A1 (en) * | 2021-04-12 | 2022-10-20 | Locanabio, Inc. | Compositions and methods comprising hybrid promoters |
| GB202207026D0 (en) * | 2022-05-13 | 2022-06-29 | Univ Oxford Innovation Ltd | Method |
| WO2025101968A1 (en) * | 2023-11-10 | 2025-05-15 | Repeat Therapeutics, Inc. | Treatment of neurodegenerative diseases caused by repeat expansion with nucleoside administration |
| TW202546236A (zh) | 2024-01-16 | 2025-12-01 | 美商安斯泰來基因治療股份有限公司 | 用於治療第1型肌強直性營養不良之肌肉選擇性混合調節組合及其使用方法 |
| WO2026015609A1 (en) * | 2024-07-10 | 2026-01-15 | The Johns Hopkins University | Vectors and methods for increased non-coding rna expression |
Family Cites Families (9)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US7056502B2 (en) | 2000-04-28 | 2006-06-06 | The Trustees Of The University Of Pennsylvania | Recombinant aav vectors with AAV5 capsids and AAV5 vectors pseudotyped in heterologous capsids |
| ES2714007T3 (es) | 2007-04-09 | 2019-05-24 | Univ Florida | Composiciones de vectores rAAV que tienen proteínas de la cápside modificadas en tirosina y métodos para su uso |
| CN101895633A (zh) | 2010-07-14 | 2010-11-24 | 中兴通讯股份有限公司 | 一种移动终端及其解锁方法 |
| WO2012068627A1 (en) | 2010-11-24 | 2012-05-31 | The University Of Western Australia | Peptides for the specific binding of rna targets |
| DK2784157T3 (da) | 2011-10-21 | 2019-10-21 | Univ Kyushu Nat Univ Corp | Designfremgangsmåde til et rna-bindende protein under anvendelse af ppr-motiv og anvendelse deraf |
| US10330674B2 (en) | 2015-01-13 | 2019-06-25 | Massachusetts Institute Of Technology | Pumilio domain-based modular protein architecture for RNA binding |
| US10476825B2 (en) | 2017-08-22 | 2019-11-12 | Salk Institue for Biological Studies | RNA targeting methods and compositions |
| KR20210058806A (ko) * | 2018-06-08 | 2021-05-24 | 로카나바이오 인크. | Rna 표적화 융합 단백질 조성물 및 사용 방법 |
| WO2022119974A1 (en) * | 2020-12-01 | 2022-06-09 | Locanabio, Inc. | Rna-targeting compositions and methods for treating cag repeat diseases |
-
2021
- 2021-12-01 JP JP2023533279A patent/JP2023551874A/ja active Pending
- 2021-12-01 AU AU2021391645A patent/AU2021391645A1/en active Pending
- 2021-12-01 EP EP21845129.2A patent/EP4255471A1/en active Pending
- 2021-12-01 US US18/039,812 patent/US20240108751A1/en active Pending
- 2021-12-01 WO PCT/US2021/061490 patent/WO2022119979A1/en not_active Ceased
- 2021-12-01 KR KR1020237021514A patent/KR20230129162A9/ko active Pending
- 2021-12-01 CA CA3200588A patent/CA3200588A1/en active Pending
Similar Documents
| Publication | Publication Date | Title |
|---|---|---|
| JP2023551874A5 (https=) | ||
| JP2023551873A5 (https=) | ||
| JP2022529631A5 (https=) | ||
| US20240197918A1 (en) | Tissue-targeted modified aav capsids and methods of use thereof | |
| JP2020019772A5 (https=) | ||
| JP2024009857A5 (https=) | ||
| JP2021516046A5 (https=) | ||
| JP2022507534A5 (https=) | ||
| JP2022529424A5 (https=) | ||
| JP2020519284A5 (https=) | ||
| JP2018522529A5 (https=) | ||
| JP2022547197A5 (https=) | ||
| JP2022542828A5 (https=) | ||
| JP2021523702A5 (https=) | ||
| JP2022524434A5 (https=) | ||
| JP2022525302A5 (https=) | ||
| JP2023520488A5 (https=) | ||
| JP2023515692A5 (https=) | ||
| JP2024508696A5 (https=) | ||
| JP2023520763A5 (https=) | ||
| KR20250115422A (ko) | 반복적 요소의 적절한 패키징을 위한 아데노 연관 바이러스 벡터 | |
| JP2023549124A5 (https=) | ||
| JP2023542131A5 (https=) | ||
| JP2023515795A5 (https=) | ||
| JP2025513785A5 (https=) |