JP2023526449A5 - - Google Patents

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Publication number
JP2023526449A5
JP2023526449A5 JP2022570566A JP2022570566A JP2023526449A5 JP 2023526449 A5 JP2023526449 A5 JP 2023526449A5 JP 2022570566 A JP2022570566 A JP 2022570566A JP 2022570566 A JP2022570566 A JP 2022570566A JP 2023526449 A5 JP2023526449 A5 JP 2023526449A5
Authority
JP
Japan
Prior art keywords
pharmaceutical composition
composition according
sequence
park2
gene
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2022570566A
Other languages
English (en)
Japanese (ja)
Other versions
JP2023526449A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/033758 external-priority patent/WO2021237158A1/en
Publication of JP2023526449A publication Critical patent/JP2023526449A/ja
Publication of JP2023526449A5 publication Critical patent/JP2023526449A5/ja
Pending legal-status Critical Current

Links

JP2022570566A 2020-05-21 2021-05-21 パーキンソン病を治療するための、増加した活性を有するパーキン変異体の遺伝子治療送達 Pending JP2023526449A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063028335P 2020-05-21 2020-05-21
US63/028,335 2020-05-21
PCT/US2021/033758 WO2021237158A1 (en) 2020-05-21 2021-05-21 Gene therapy delivery of parkin mutants having increased activity to treat parkinson's disease

Publications (2)

Publication Number Publication Date
JP2023526449A JP2023526449A (ja) 2023-06-21
JP2023526449A5 true JP2023526449A5 (https=) 2024-04-23

Family

ID=78707645

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2022570566A Pending JP2023526449A (ja) 2020-05-21 2021-05-21 パーキンソン病を治療するための、増加した活性を有するパーキン変異体の遺伝子治療送達

Country Status (6)

Country Link
US (2) US12133897B2 (https=)
EP (1) EP4153760A4 (https=)
JP (1) JP2023526449A (https=)
AU (1) AU2021273979A1 (https=)
CA (1) CA3179402A1 (https=)
WO (1) WO2021237158A1 (https=)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
MX2020011386A (es) 2018-04-27 2021-01-29 Spacecraft Seven Llc Terapia genica para la degeneracion del snc.
EP4153760A4 (en) 2020-05-21 2024-08-21 Nysnobio GT, LLC GENE THERAPY ADMINISTRATION OF PARKIN MUTANTS WITH ENHANCED ACTIVITY FOR THE TREATMENT OF PARKINSON'S DISEASE

Family Cites Families (11)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP1131424B1 (fr) * 1998-11-19 2009-08-19 Aventis Pharma S.A. Mutations du gene de la parkine, compositions, methodes et utilisations
US7998667B1 (en) * 1998-11-19 2011-08-16 Aventis Pharma S.A. Mutations of the parkin gene, compositions, methods and uses
US6855314B1 (en) 2000-03-22 2005-02-15 The United States Of America As Represented By The Department Of Health And Human Services AAV5 vector for transducing brain cells and lung cells
WO2009026116A2 (en) * 2007-08-16 2009-02-26 Genizon Biosciences, Inc. Genemap of the human genes associated with longevity
EP2524037B1 (en) * 2010-01-12 2018-05-16 The University Of North Carolina At Chapel Hill Restrictive inverted terminal repeats for viral vectors
US8603994B2 (en) * 2010-11-11 2013-12-10 Valted, Llc Transcriptional repression leading to Parkinson's disease
US9464311B2 (en) 2013-05-02 2016-10-11 E3X Bio, Inc. Method for identifying modulators of ubiquitin ligases
WO2017191274A2 (en) * 2016-05-04 2017-11-09 Curevac Ag Rna encoding a therapeutic protein
MX2020011386A (es) * 2018-04-27 2021-01-29 Spacecraft Seven Llc Terapia genica para la degeneracion del snc.
US12448629B2 (en) * 2018-10-05 2025-10-21 University Of Massachusetts rAAV vectors for the treatment of GM1 and GM2 gangliosidosis
EP4153760A4 (en) 2020-05-21 2024-08-21 Nysnobio GT, LLC GENE THERAPY ADMINISTRATION OF PARKIN MUTANTS WITH ENHANCED ACTIVITY FOR THE TREATMENT OF PARKINSON'S DISEASE

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