JP2023517326A - フォークヘッドボックスｐ３（ｆｏｘｐ３）遺伝子発現をモジュレートするための組成物および方法 - Google Patents

フォークヘッドボックスｐ３（ｆｏｘｐ３）遺伝子発現をモジュレートするための組成物および方法 Download PDF

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JP2023517326A
JP2023517326A JP2022554320A JP2022554320A JP2023517326A JP 2023517326 A JP2023517326 A JP 2023517326A JP 2022554320 A JP2022554320 A JP 2022554320A JP 2022554320 A JP2022554320 A JP 2022554320A JP 2023517326 A JP2023517326 A JP 2023517326A
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foxp3
site
disruptor
specific
cells
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ティムシ ラオ，
ジョディ ケネディ，
パンカジ マンダル，
ジェレミア ディー． ファレリ，
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オメガ セラピューティクス， インコーポレイテッド
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JP2022554320A 2020-03-11 2021-03-11 フォークヘッドボックスｐ３（ｆｏｘｐ３）遺伝子発現をモジュレートするための組成物および方法 Withdrawn JP2023517326A (ja)

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US202062988044P 2020-03-11 2020-03-11
US62/988,044 2020-03-11
PCT/US2021/021825 WO2021183720A1 (en) 2020-03-11 2021-03-11 Compositions and methods for modulating forkhead box p3 (foxp3) gene expression

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JP2023517326A5 JP2023517326A5 (https=) 2024-03-18

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EP (1) EP4118207A1 (https=)
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CN114729376A (zh) 2019-09-23 2022-07-08 欧米茄治疗公司 用于调节肝细胞核因子4α(HNF4α)基因表达的组合物和方法
WO2023081787A2 (en) * 2021-11-04 2023-05-11 Prime Medicine, Inc. Genome editing compositions and methods for treatment of fanconi anemia
AU2024240582A1 (en) * 2023-03-21 2025-11-06 Lung Biotechnology Pbc Methods for creating regulatory t cells (tregs) using genome engineering
WO2025019742A1 (en) * 2023-07-19 2025-01-23 Omega Therapeutics, Inc. Methods and compositions for modulating ctnnb1 expression

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