JP2023516753A5 - - Google Patents
Info
- Publication number
- JP2023516753A5 JP2023516753A5 JP2022553583A JP2022553583A JP2023516753A5 JP 2023516753 A5 JP2023516753 A5 JP 2023516753A5 JP 2022553583 A JP2022553583 A JP 2022553583A JP 2022553583 A JP2022553583 A JP 2022553583A JP 2023516753 A5 JP2023516753 A5 JP 2023516753A5
- Authority
- JP
- Japan
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2025157586A JP2026016375A (ja) | 2020-03-06 | 2025-09-24 | Gla遺伝子の突然変異を有する患者におけるファブリー病を治療する方法 |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202062986297P | 2020-03-06 | 2020-03-06 | |
| US62/986,297 | 2020-03-06 | ||
| PCT/US2021/020984 WO2021178737A1 (en) | 2020-03-06 | 2021-03-05 | Methods of treating fabry disease in patients having a mutation in the gla gene |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025157586A Division JP2026016375A (ja) | 2020-03-06 | 2025-09-24 | Gla遺伝子の突然変異を有する患者におけるファブリー病を治療する方法 |
Publications (4)
| Publication Number | Publication Date |
|---|---|
| JP2023516753A JP2023516753A (ja) | 2023-04-20 |
| JP2023516753A5 true JP2023516753A5 (https=) | 2024-03-14 |
| JPWO2021178737A5 JPWO2021178737A5 (https=) | 2024-03-14 |
| JP7749572B2 JP7749572B2 (ja) | 2025-10-06 |
Family
ID=75267607
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022553583A Active JP7749572B2 (ja) | 2020-03-06 | 2021-03-05 | Gla遺伝子の突然変異を有する患者におけるファブリー病を治療する方法 |
| JP2025157586A Pending JP2026016375A (ja) | 2020-03-06 | 2025-09-24 | Gla遺伝子の突然変異を有する患者におけるファブリー病を治療する方法 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025157586A Pending JP2026016375A (ja) | 2020-03-06 | 2025-09-24 | Gla遺伝子の突然変異を有する患者におけるファブリー病を治療する方法 |
Country Status (25)
| Country | Link |
|---|---|
| US (1) | US20230136297A1 (https=) |
| EP (2) | EP4114390B1 (https=) |
| JP (2) | JP7749572B2 (https=) |
| KR (1) | KR20220152547A (https=) |
| CN (1) | CN115427040A (https=) |
| AR (1) | AR122390A1 (https=) |
| AU (1) | AU2021230371A1 (https=) |
| BR (1) | BR112022017881A2 (https=) |
| CA (1) | CA3170718A1 (https=) |
| CL (1) | CL2022002423A1 (https=) |
| DK (1) | DK4114390T3 (https=) |
| ES (1) | ES3013813T3 (https=) |
| FI (1) | FI4114390T3 (https=) |
| HR (1) | HRP20250179T1 (https=) |
| HU (1) | HUE070116T2 (https=) |
| IL (1) | IL296221A (https=) |
| LT (1) | LT4114390T (https=) |
| MX (1) | MX2022011030A (https=) |
| PL (1) | PL4114390T3 (https=) |
| PT (1) | PT4114390T (https=) |
| RS (1) | RS66530B1 (https=) |
| SI (1) | SI4114390T1 (https=) |
| SM (1) | SMT202500072T1 (https=) |
| TW (1) | TW202146020A (https=) |
| WO (1) | WO2021178737A1 (https=) |
Families Citing this family (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP4282472A3 (en) * | 2018-08-20 | 2024-02-21 | Amicus Therapeutics, Inc. | Methods of treating fabry disease in patients having a mutation in the gla gene |
| EP3851105B1 (en) | 2019-08-07 | 2026-03-04 | Amicus Therapeutics, Inc. | Migalastat for use in treating fabry disease in patients having a mutation in the gla gene |
Family Cites Families (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US6274597B1 (en) | 1998-06-01 | 2001-08-14 | Mount Sinai School Of Medicine Of New York University | Method of enhancing lysosomal α-Galactosidase A |
| AU2008232614A1 (en) | 2007-03-30 | 2008-10-09 | Amicus Therapeutics, Inc. | Method for the treatment of Fabry disease using pharmacological chaperones |
| SI3470077T1 (sl) | 2008-02-12 | 2020-12-31 | Amicus Therapeutics, Inc. | Postopek za napovedovanje odgovora na zdravljenje bolezni s farmakološkim spremljevalcem |
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2021
- 2021-03-05 EP EP21715035.8A patent/EP4114390B1/en active Active
- 2021-03-05 AU AU2021230371A patent/AU2021230371A1/en active Pending
- 2021-03-05 EP EP24217104.9A patent/EP4527454A3/en active Pending
- 2021-03-05 JP JP2022553583A patent/JP7749572B2/ja active Active
- 2021-03-05 FI FIEP21715035.8T patent/FI4114390T3/fi active
- 2021-03-05 US US17/909,450 patent/US20230136297A1/en active Pending
- 2021-03-05 SI SI202130266T patent/SI4114390T1/sl unknown
- 2021-03-05 PT PT217150358T patent/PT4114390T/pt unknown
- 2021-03-05 AR ARP210100575A patent/AR122390A1/es unknown
- 2021-03-05 ES ES21715035T patent/ES3013813T3/es active Active
- 2021-03-05 DK DK21715035.8T patent/DK4114390T3/da active
- 2021-03-05 TW TW110107854A patent/TW202146020A/zh unknown
- 2021-03-05 CN CN202180028403.5A patent/CN115427040A/zh active Pending
- 2021-03-05 RS RS20250171A patent/RS66530B1/sr unknown
- 2021-03-05 BR BR112022017881A patent/BR112022017881A2/pt unknown
- 2021-03-05 HR HRP20250179TT patent/HRP20250179T1/hr unknown
- 2021-03-05 MX MX2022011030A patent/MX2022011030A/es unknown
- 2021-03-05 SM SM20250072T patent/SMT202500072T1/it unknown
- 2021-03-05 IL IL296221A patent/IL296221A/en unknown
- 2021-03-05 LT LTEPPCT/US2021/020984T patent/LT4114390T/lt unknown
- 2021-03-05 WO PCT/US2021/020984 patent/WO2021178737A1/en not_active Ceased
- 2021-03-05 CA CA3170718A patent/CA3170718A1/en active Pending
- 2021-03-05 PL PL21715035.8T patent/PL4114390T3/pl unknown
- 2021-03-05 KR KR1020227034499A patent/KR20220152547A/ko active Pending
- 2021-03-05 HU HUE21715035A patent/HUE070116T2/hu unknown
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2022
- 2022-09-06 CL CL2022002423A patent/CL2022002423A1/es unknown
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2025
- 2025-09-24 JP JP2025157586A patent/JP2026016375A/ja active Pending