JP2023516753A5 - - Google Patents

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Publication number
JP2023516753A5
JP2023516753A5 JP2022553583A JP2022553583A JP2023516753A5 JP 2023516753 A5 JP2023516753 A5 JP 2023516753A5 JP 2022553583 A JP2022553583 A JP 2022553583A JP 2022553583 A JP2022553583 A JP 2022553583A JP 2023516753 A5 JP2023516753 A5 JP 2023516753A5
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JP
Japan
Prior art keywords
pharmaceutical product
patient
product according
salt
day
Prior art date
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Granted
Application number
JP2022553583A
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English (en)
Japanese (ja)
Other versions
JP7749572B2 (ja
JP2023516753A (ja
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Priority claimed from PCT/US2021/020984 external-priority patent/WO2021178737A1/en
Publication of JP2023516753A publication Critical patent/JP2023516753A/ja
Publication of JP2023516753A5 publication Critical patent/JP2023516753A5/ja
Priority to JP2025157586A priority Critical patent/JP2026016375A/ja
Application granted granted Critical
Publication of JP7749572B2 publication Critical patent/JP7749572B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

Links

JP2022553583A 2020-03-06 2021-03-05 Gla遺伝子の突然変異を有する患者におけるファブリー病を治療する方法 Active JP7749572B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2025157586A JP2026016375A (ja) 2020-03-06 2025-09-24 Gla遺伝子の突然変異を有する患者におけるファブリー病を治療する方法

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202062986297P 2020-03-06 2020-03-06
US62/986,297 2020-03-06
PCT/US2021/020984 WO2021178737A1 (en) 2020-03-06 2021-03-05 Methods of treating fabry disease in patients having a mutation in the gla gene

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2025157586A Division JP2026016375A (ja) 2020-03-06 2025-09-24 Gla遺伝子の突然変異を有する患者におけるファブリー病を治療する方法

Publications (3)

Publication Number Publication Date
JP2023516753A JP2023516753A (ja) 2023-04-20
JP2023516753A5 true JP2023516753A5 (https=) 2024-03-14
JP7749572B2 JP7749572B2 (ja) 2025-10-06

Family

ID=75267607

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2022553583A Active JP7749572B2 (ja) 2020-03-06 2021-03-05 Gla遺伝子の突然変異を有する患者におけるファブリー病を治療する方法
JP2025157586A Pending JP2026016375A (ja) 2020-03-06 2025-09-24 Gla遺伝子の突然変異を有する患者におけるファブリー病を治療する方法

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2025157586A Pending JP2026016375A (ja) 2020-03-06 2025-09-24 Gla遺伝子の突然変異を有する患者におけるファブリー病を治療する方法

Country Status (25)

Country Link
US (1) US20230136297A1 (https=)
EP (2) EP4114390B1 (https=)
JP (2) JP7749572B2 (https=)
KR (1) KR20220152547A (https=)
CN (1) CN115427040A (https=)
AR (1) AR122390A1 (https=)
AU (1) AU2021230371A1 (https=)
BR (1) BR112022017881A2 (https=)
CA (1) CA3170718A1 (https=)
CL (1) CL2022002423A1 (https=)
DK (1) DK4114390T3 (https=)
ES (1) ES3013813T3 (https=)
FI (1) FI4114390T3 (https=)
HR (1) HRP20250179T1 (https=)
HU (1) HUE070116T2 (https=)
IL (1) IL296221A (https=)
LT (1) LT4114390T (https=)
MX (1) MX2022011030A (https=)
PL (1) PL4114390T3 (https=)
PT (1) PT4114390T (https=)
RS (1) RS66530B1 (https=)
SI (1) SI4114390T1 (https=)
SM (1) SMT202500072T1 (https=)
TW (1) TW202146020A (https=)
WO (1) WO2021178737A1 (https=)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US12594268B2 (en) * 2018-08-20 2026-04-07 Amicus Therapeutics, Inc. Methods of treating Fabry disease in patients having a mutation in the GLA gene
KR20220044560A (ko) 2019-08-07 2022-04-08 아미쿠스 세라퓨틱스, 인코포레이티드 Gla 유전자에 돌연변이를 갖는 환자에서 파브리 질병을 치료하는 방법

Family Cites Families (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6274597B1 (en) 1998-06-01 2001-08-14 Mount Sinai School Of Medicine Of New York University Method of enhancing lysosomal α-Galactosidase A
MX2009010557A (es) 2007-03-30 2009-11-19 Amicus Therapeutics Inc Metodo para el tratamiento de la enfermedad de fabry que utiliza chaperonas farmacologicas.
EP2946785B1 (en) 2008-02-12 2018-10-24 Amicus Therapeutics, Inc. Method to predict response to pharmacological chaperone treatment of diseases

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