JP2022526429A - Amdの処置のためのhtra1調節 - Google Patents

Amdの処置のためのhtra1調節 Download PDF

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JP2022526429A
JP2022526429A JP2021559892A JP2021559892A JP2022526429A JP 2022526429 A JP2022526429 A JP 2022526429A JP 2021559892 A JP2021559892 A JP 2021559892A JP 2021559892 A JP2021559892 A JP 2021559892A JP 2022526429 A JP2022526429 A JP 2022526429A
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htra1
sequence
risk
protein
amd
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JPWO2020210724A5 (https=
JP2022526429A5 (https=
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ウィリアムズ,ブランディ
ハーグマン,グレゴリー
ティモシー リチャーズ,バート
ユセフ,オサマ
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ザ ユニバーシティ オブ ユタ リサーチ ファウンデイション
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    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
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    • A61K48/005Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'active' part of the composition delivered, i.e. the nucleic acid delivered
    • A61K48/0066Manipulation of the nucleic acid to modify its expression pattern, e.g. enhance its duration of expression, achieved by the presence of particular introns in the delivered nucleic acid
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JP2021559892A 2019-04-10 2020-04-10 Amdの処置のためのhtra1調節 Pending JP2022526429A (ja)

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JP2025093119A JP2025175283A (ja) 2019-04-10 2025-06-04 Amdの処置のためのhtra1調節

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US201962832182P 2019-04-10 2019-04-10
US62/832,182 2019-04-10
PCT/US2020/027802 WO2020210724A1 (en) 2019-04-10 2020-04-10 Htra1 modulation for treatment of amd

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JPWO2020210724A5 JPWO2020210724A5 (https=) 2023-04-17
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US (1) US20230165976A1 (https=)
EP (1) EP3953485A4 (https=)
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CN (1) CN113966401A (https=)
CA (1) CA3136119A1 (https=)
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US20240358855A1 (en) * 2021-08-18 2024-10-31 University Of Utah Research Foundation Multigene constructs for treatment of age-related macular degeneration and other complement dysregulation-related conditions
US20250003989A1 (en) * 2021-11-15 2025-01-02 The Children`S Medical Center Corporation Methods for tauopathy diagnosis and treatment

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EP3953485A1 (en) 2022-02-16
US20230165976A1 (en) 2023-06-01
EP3953485A4 (en) 2023-05-17
CN113966401A (zh) 2022-01-21
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JP2025175283A (ja) 2025-12-01

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