JP2022525888A - リソソーム蓄積症のための、経鼻遺伝子送達と経口の桂皮酸、オレアミド、またはゲムフィブロジルとの組合せ - Google Patents

リソソーム蓄積症のための、経鼻遺伝子送達と経口の桂皮酸、オレアミド、またはゲムフィブロジルとの組合せ Download PDF

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JP2022525888A
JP2022525888A JP2021555592A JP2021555592A JP2022525888A JP 2022525888 A JP2022525888 A JP 2022525888A JP 2021555592 A JP2021555592 A JP 2021555592A JP 2021555592 A JP2021555592 A JP 2021555592A JP 2022525888 A JP2022525888 A JP 2022525888A
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カリパーダ パハン，
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ラッシュ・ユニバーシティ・メディカル・センター
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JP2021555592A 2019-03-22 2020-03-20 リソソーム蓄積症のための、経鼻遺伝子送達と経口の桂皮酸、オレアミド、またはゲムフィブロジルとの組合せ Pending JP2022525888A (ja)

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US201962822310P 2019-03-22 2019-03-22
US62/822,310 2019-03-22
PCT/US2020/023768 WO2020197967A1 (en) 2019-03-22 2020-03-20 Combination of nasal gene delivery and oral cinnamic acid, oleamide or gemfibrozil for lysosomal stoarge disorders

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JP2022525888A true JP2022525888A (ja) 2022-05-20
JPWO2020197967A5 JPWO2020197967A5 (enExample) 2023-03-28

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US (1) US20220152165A1 (enExample)
EP (1) EP3941584A4 (enExample)
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KR (1) KR20210143848A (enExample)
CN (1) CN113811359A (enExample)
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WO2022159086A1 (en) * 2021-01-20 2022-07-28 Rush University Medical Center Improved treatment for globoid cell leukodsytrophy or krabbe disease
WO2024155759A1 (en) * 2023-01-18 2024-07-25 Rush University Medical Center Oral gemfibrozil for the treatment of cln3-related juvenile neuronal ceroid lipofuscinosis

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