JP2021526818A5 - - Google Patents
Info
- Publication number
- JP2021526818A5 JP2021526818A5 JP2020568431A JP2020568431A JP2021526818A5 JP 2021526818 A5 JP2021526818 A5 JP 2021526818A5 JP 2020568431 A JP2020568431 A JP 2020568431A JP 2020568431 A JP2020568431 A JP 2020568431A JP 2021526818 A5 JP2021526818 A5 JP 2021526818A5
- Authority
- JP
- Japan
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2024062211A JP2024097779A (ja) | 2018-06-08 | 2024-04-08 | 心筋症のためのaav心臓遺伝子治療 |
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201862682772P | 2018-06-08 | 2018-06-08 | |
| US62/682,772 | 2018-06-08 | ||
| US201962822015P | 2019-03-21 | 2019-03-21 | |
| US62/822,015 | 2019-03-21 | ||
| PCT/US2019/036157 WO2019237067A1 (en) | 2018-06-08 | 2019-06-07 | Aav cardiac gene therapy for cardiomyopathy |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024062211A Division JP2024097779A (ja) | 2018-06-08 | 2024-04-08 | 心筋症のためのaav心臓遺伝子治療 |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2021526818A JP2021526818A (ja) | 2021-10-11 |
| JP2021526818A5 true JP2021526818A5 (https=) | 2024-05-15 |
| JPWO2019237067A5 JPWO2019237067A5 (https=) | 2024-05-15 |
Family
ID=68770676
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2020568431A Pending JP2021526818A (ja) | 2018-06-08 | 2019-06-07 | 心筋症のためのaav心臓遺伝子治療 |
| JP2024062211A Pending JP2024097779A (ja) | 2018-06-08 | 2024-04-08 | 心筋症のためのaav心臓遺伝子治療 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024062211A Pending JP2024097779A (ja) | 2018-06-08 | 2024-04-08 | 心筋症のためのaav心臓遺伝子治療 |
Country Status (14)
| Country | Link |
|---|---|
| US (1) | US20210260215A1 (https=) |
| EP (1) | EP3814512A4 (https=) |
| JP (2) | JP2021526818A (https=) |
| KR (1) | KR20210018902A (https=) |
| CN (1) | CN112272705A (https=) |
| AU (1) | AU2019282822B2 (https=) |
| BR (1) | BR112020024935A2 (https=) |
| CA (1) | CA3100280A1 (https=) |
| CL (1) | CL2020003190A1 (https=) |
| CO (1) | CO2020016718A2 (https=) |
| IL (1) | IL279225B2 (https=) |
| MX (1) | MX421375B (https=) |
| SG (1) | SG11202011061SA (https=) |
| WO (1) | WO2019237067A1 (https=) |
Families Citing this family (5)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| BR112022000898A2 (pt) * | 2019-07-19 | 2022-06-07 | Univ Florida | Terapia de gene cardíaco aav para cardiomiopatia em seres humanos |
| BR112023001336A2 (pt) * | 2020-08-05 | 2023-02-14 | Spacecraft Seven Llc | Terapia gênica de csrp3 (proteína 3 rica em cisteína e glicina) |
| MX2023007602A (es) * | 2020-12-23 | 2023-09-21 | Univ Florida | Mayor eficiencia del empaquetamiento de vectores para terapia genica cardiaca. |
| CA3252359A1 (en) * | 2022-03-02 | 2023-09-07 | Cevec Pharmaceuticals Gmbh | IMPROVED CELL LINES AND PROCESSES FOR THE PRODUCTION OF ADENO-ASSOCIATED VECTORS |
| EP4239063A1 (en) * | 2022-03-02 | 2023-09-06 | CEVEC Pharmaceuticals GmbH | Improved cell lines and methods for the production of adeno-associated vectors |
Family Cites Families (7)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US5139941A (en) | 1985-10-31 | 1992-08-18 | University Of Florida Research Foundation, Inc. | AAV transduction vectors |
| US5962313A (en) | 1996-01-18 | 1999-10-05 | Avigen, Inc. | Adeno-associated virus vectors comprising a gene encoding a lyosomal enzyme |
| AU2003274397A1 (en) | 2002-06-05 | 2003-12-22 | University Of Florida | Production of pseudotyped recombinant aav virions |
| US20120322861A1 (en) | 2007-02-23 | 2012-12-20 | Barry John Byrne | Compositions and Methods for Treating Diseases |
| CN105452458A (zh) * | 2013-06-07 | 2016-03-30 | 加利福尼亚大学董事会 | 用于治疗心力衰竭和增加心脏功能的不能产生环腺苷酸的腺苷酸环化酶和组合物和方法 |
| DK3405215T3 (da) * | 2016-01-19 | 2022-09-19 | Univ California | Fremgangsmåder til behandling af danon-sygdom og andre autofagilidelser |
| US20170348387A1 (en) * | 2016-02-29 | 2017-12-07 | The Trustees Of The University Of Pennsylvania | Aav-mediated gene therapy for nphp5 lca-ciliopathy |
-
2019
- 2019-06-07 US US16/972,740 patent/US20210260215A1/en active Pending
- 2019-06-07 WO PCT/US2019/036157 patent/WO2019237067A1/en not_active Ceased
- 2019-06-07 CN CN201980038176.7A patent/CN112272705A/zh active Pending
- 2019-06-07 MX MX2020013313A patent/MX421375B/es unknown
- 2019-06-07 BR BR112020024935-1A patent/BR112020024935A2/pt unknown
- 2019-06-07 CA CA3100280A patent/CA3100280A1/en active Pending
- 2019-06-07 IL IL279225A patent/IL279225B2/en unknown
- 2019-06-07 SG SG11202011061SA patent/SG11202011061SA/en unknown
- 2019-06-07 AU AU2019282822A patent/AU2019282822B2/en active Active
- 2019-06-07 JP JP2020568431A patent/JP2021526818A/ja active Pending
- 2019-06-07 EP EP19815084.9A patent/EP3814512A4/en active Pending
- 2019-06-07 KR KR1020217000163A patent/KR20210018902A/ko not_active Ceased
-
2020
- 2020-12-07 CL CL2020003190A patent/CL2020003190A1/es unknown
- 2020-12-31 CO CONC2020/0016718A patent/CO2020016718A2/es unknown
-
2024
- 2024-04-08 JP JP2024062211A patent/JP2024097779A/ja active Pending