JP2021514956A5 - - Google Patents

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Publication number
JP2021514956A5
JP2021514956A5 JP2020544456A JP2020544456A JP2021514956A5 JP 2021514956 A5 JP2021514956 A5 JP 2021514956A5 JP 2020544456 A JP2020544456 A JP 2020544456A JP 2020544456 A JP2020544456 A JP 2020544456A JP 2021514956 A5 JP2021514956 A5 JP 2021514956A5
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JP
Japan
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composition according
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administered
composition
trin
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Pending
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JP2020544456A
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English (en)
Japanese (ja)
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JP2021514956A (ja
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Priority claimed from PCT/US2019/017623 external-priority patent/WO2019164703A1/en
Publication of JP2021514956A publication Critical patent/JP2021514956A/ja
Publication of JP2021514956A5 publication Critical patent/JP2021514956A5/ja
Priority to JP2023139463A priority Critical patent/JP2023162344A/ja
Pending legal-status Critical Current

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JP2020544456A 2018-02-22 2019-02-12 コハク酸セミアルデヒドデヒドロゲナーゼ欠損症(ssadhd)を処置するための組成物および方法 Pending JP2021514956A (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2023139463A JP2023162344A (ja) 2018-02-22 2023-08-30 コハク酸セミアルデヒドデヒドロゲナーゼ欠損症(ssadhd)を処置するための組成物および方法

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862634092P 2018-02-22 2018-02-22
US62/634,092 2018-02-22
PCT/US2019/017623 WO2019164703A1 (en) 2018-02-22 2019-02-12 Compositions and methods for treating succinic semialdehyde dehydrogenase deficiency (ssadhd)

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2023139463A Division JP2023162344A (ja) 2018-02-22 2023-08-30 コハク酸セミアルデヒドデヒドロゲナーゼ欠損症(ssadhd)を処置するための組成物および方法

Publications (2)

Publication Number Publication Date
JP2021514956A JP2021514956A (ja) 2021-06-17
JP2021514956A5 true JP2021514956A5 (enExample) 2022-03-31

Family

ID=67688295

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2020544456A Pending JP2021514956A (ja) 2018-02-22 2019-02-12 コハク酸セミアルデヒドデヒドロゲナーゼ欠損症(ssadhd)を処置するための組成物および方法
JP2023139463A Pending JP2023162344A (ja) 2018-02-22 2023-08-30 コハク酸セミアルデヒドデヒドロゲナーゼ欠損症(ssadhd)を処置するための組成物および方法

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2023139463A Pending JP2023162344A (ja) 2018-02-22 2023-08-30 コハク酸セミアルデヒドデヒドロゲナーゼ欠損症(ssadhd)を処置するための組成物および方法

Country Status (6)

Country Link
US (2) US20210008225A1 (enExample)
JP (2) JP2021514956A (enExample)
KR (1) KR20200140255A (enExample)
AU (1) AU2019225729A1 (enExample)
CA (1) CA3092035A1 (enExample)
WO (1) WO2019164703A1 (enExample)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP4440626A4 (en) * 2021-12-02 2025-09-17 Childrens Medical Ct Corp GENE THERAPY FOR SUCCINIC SEMIALDEHYDE DEHYDROGENASE DEFICIENCY (SSADHD)
CN116478961B (zh) * 2023-04-27 2023-09-15 北京因诺惟康医药科技有限公司 CRISPR/SprCas9基因编辑系统的开发及应用
WO2025042900A1 (en) * 2023-08-21 2025-02-27 Washington State University Messenger rna treatment for succinic semialdehyde dehydrogenase deficiency

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