HK1214269A1 - 肌萎縮側索硬化症 治療 - Google Patents

肌萎縮側索硬化症 治療

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Publication number
HK1214269A1
HK1214269A1 HK16101846.6A HK16101846A HK1214269A1 HK 1214269 A1 HK1214269 A1 HK 1214269A1 HK 16101846 A HK16101846 A HK 16101846A HK 1214269 A1 HK1214269 A1 HK 1214269A1
Authority
HK
Hong Kong
Prior art keywords
als
treatment
lateral sclerosis
amyotrophic lateral
amyotrophic
Prior art date
Application number
HK16101846.6A
Other languages
English (en)
Inventor
Grey Petsko
Dagmar Ringe
Shulin Ju
Original Assignee
Univ Brandeis
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Univ Brandeis filed Critical Univ Brandeis
Publication of HK1214269A1 publication Critical patent/HK1214269A1/zh

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HK16101846.6A 2012-10-11 2016-02-18 肌萎縮側索硬化症 治療 HK1214269A1 (zh)

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Application Number Priority Date Filing Date Title
US201261712322P 2012-10-11 2012-10-11
PCT/US2013/063858 WO2014058866A2 (en) 2012-10-11 2013-10-08 Treatment of amyotrophic lateral sclerosis

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HK1214269A1 true HK1214269A1 (zh) 2016-07-22

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US (3) US10533038B2 (zh)
EP (2) EP2906580B1 (zh)
AU (1) AU2013204200B2 (zh)
CA (1) CA2887569A1 (zh)
DK (1) DK2906580T3 (zh)
ES (1) ES2792151T3 (zh)
HK (1) HK1214269A1 (zh)
WO (1) WO2014058866A2 (zh)

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Publication number Priority date Publication date Assignee Title
AU2013204200B2 (en) 2012-10-11 2016-10-20 Brandeis University Treatment of amyotrophic lateral sclerosis
US10597660B2 (en) 2014-11-14 2020-03-24 Voyager Therapeutics, Inc. Compositions and methods of treating amyotrophic lateral sclerosis (ALS)
KR20240056729A (ko) 2016-05-18 2024-04-30 보이저 테라퓨틱스, 인크. 조절성 폴리뉴클레오티드
JPWO2018012497A1 (ja) * 2016-07-14 2019-04-25 国立大学法人名古屋大学 疾患モデル動物および疾患治療剤
US11603542B2 (en) 2017-05-05 2023-03-14 Voyager Therapeutics, Inc. Compositions and methods of treating amyotrophic lateral sclerosis (ALS)
JP7457505B2 (ja) 2017-05-10 2024-03-28 ユニバーシティー オブ ロチェスター 神経精神障害を処置する方法
EP3661509A4 (en) 2017-08-04 2021-01-13 Skyhawk Therapeutics, Inc. METHODS AND COMPOSITIONS FOR MODULATING THE SPLICE
US20200237799A1 (en) 2017-10-16 2020-07-30 Voyager Therapeutics, Inc. Treatment of amyotrophic lateral sclerosis (als)
AU2018352236A1 (en) 2017-10-16 2020-04-23 The Curators Of The University Of Missouri Treatment of amyotrophic lateral sclerosis (ALS)
KR20210135241A (ko) 2019-02-05 2021-11-12 스카이호크 테라퓨틱스, 인코포레이티드 스플라이싱을 조절하는 방법 및 조성물
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