EA202192158A1 - DELIVERY OF POLYNUCLEOTIDE CLN6 USING AN ADENO-ASSOCIATED VIRUS - Google Patents

DELIVERY OF POLYNUCLEOTIDE CLN6 USING AN ADENO-ASSOCIATED VIRUS

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Publication number
EA202192158A1
EA202192158A1 EA202192158A EA202192158A EA202192158A1 EA 202192158 A1 EA202192158 A1 EA 202192158A1 EA 202192158 A EA202192158 A EA 202192158A EA 202192158 A EA202192158 A EA 202192158A EA 202192158 A1 EA202192158 A1 EA 202192158A1
Authority
EA
Eurasian Patent Office
Prior art keywords
cln6
polynucleotide
delivery
associated virus
adeno
Prior art date
Application number
EA202192158A
Other languages
Russian (ru)
Inventor
Катрин Мейер
Брайан К. КАСПАР
Original Assignee
Рисерч Инститьют Эт Нэшнуайд Чилдрен'С Хоспитал
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Рисерч Инститьют Эт Нэшнуайд Чилдрен'С Хоспитал filed Critical Рисерч Инститьют Эт Нэшнуайд Чилдрен'С Хоспитал
Priority claimed from PCT/US2020/016541 external-priority patent/WO2020163299A1/en
Publication of EA202192158A1 publication Critical patent/EA202192158A1/en

Links

Abstract

Настоящее изобретение относится к доставке полинуклеотида восковидного липофусциноза нейронов-6 (CLN6) с применением рекомбинантного аденоассоциированного вируса (rAAV). В настоящем изобретении предложены rAAV и способы применения rAAV для генной терапии восковидного липофусциноза нейронов или CLN6-болезни Баттена с применением гена CLN6.The present invention relates to the delivery of a neuron-6 waxy lipofuscinosis (CLN6) polynucleotide using a recombinant adeno-associated virus (rAAV). The present invention provides rAAV and methods of using rAAV for gene therapy for neuronal waxy lipofuscinosis or CLN6 Batten's disease using the CLN6 gene.

EA202192158A 2019-10-18 2020-02-04 DELIVERY OF POLYNUCLEOTIDE CLN6 USING AN ADENO-ASSOCIATED VIRUS EA202192158A1 (en)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US201962923125P 2019-10-18 2019-10-18
PCT/US2020/016541 WO2020163299A1 (en) 2019-02-04 2020-02-04 Adeno-associated virus delivery of cln6 polynucleotide

Publications (1)

Publication Number Publication Date
EA202192158A1 true EA202192158A1 (en) 2021-11-10

Family

ID=78768122

Family Applications (1)

Application Number Title Priority Date Filing Date
EA202192158A EA202192158A1 (en) 2019-10-18 2020-02-04 DELIVERY OF POLYNUCLEOTIDE CLN6 USING AN ADENO-ASSOCIATED VIRUS

Country Status (1)

Country Link
EA (1) EA202192158A1 (en)

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