EA202190155A1 - PRODUCTS BASED ON RECOMBINANT ADENO-ASSOCIATED VIRUSES AND METHODS FOR TREATMENT OF PELVIC-SHOULDER MUSCULAR DYSTROPHY TYPE 2A - Google Patents

PRODUCTS BASED ON RECOMBINANT ADENO-ASSOCIATED VIRUSES AND METHODS FOR TREATMENT OF PELVIC-SHOULDER MUSCULAR DYSTROPHY TYPE 2A

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Publication number
EA202190155A1
EA202190155A1 EA202190155A EA202190155A EA202190155A1 EA 202190155 A1 EA202190155 A1 EA 202190155A1 EA 202190155 A EA202190155 A EA 202190155A EA 202190155 A EA202190155 A EA 202190155A EA 202190155 A1 EA202190155 A1 EA 202190155A1
Authority
EA
Eurasian Patent Office
Prior art keywords
methods
pelvic
treatment
muscular dystrophy
associated viruses
Prior art date
Application number
EA202190155A
Other languages
Russian (ru)
Inventor
Зариф Саенк
Original Assignee
Рисерч Инститьют Эт Нэшнуайд Чилдрен'С Хоспитал
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Рисерч Инститьют Эт Нэшнуайд Чилдрен'С Хоспитал filed Critical Рисерч Инститьют Эт Нэшнуайд Чилдрен'С Хоспитал
Priority claimed from PCT/US2019/039893 external-priority patent/WO2020006458A1/en
Publication of EA202190155A1 publication Critical patent/EA202190155A1/en

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  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)

Abstract

Изобретение относится к продуктам и способам для лечения тазово-плечевой мышечной дистрофии типа 2А. В этих способах рекомбинантные аденоассоциированные вирусы доставляют ДНК, кодирующую белок, имеющий активность кальпаина-3.The invention relates to products and methods for the treatment of type 2A pelvic-brachial muscular dystrophy. In these methods, recombinant adeno-associated viruses deliver DNA encoding a protein having calpain-3 activity.

EA202190155A 2019-06-21 2019-06-28 PRODUCTS BASED ON RECOMBINANT ADENO-ASSOCIATED VIRUSES AND METHODS FOR TREATMENT OF PELVIC-SHOULDER MUSCULAR DYSTROPHY TYPE 2A EA202190155A1 (en)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US201962865081P 2019-06-21 2019-06-21
PCT/US2019/039893 WO2020006458A1 (en) 2018-06-29 2019-06-28 Recombinant adeno-associated virus products and methods for treating limb girdle muscular dystrophy 2a

Publications (1)

Publication Number Publication Date
EA202190155A1 true EA202190155A1 (en) 2021-05-04

Family

ID=76160108

Family Applications (1)

Application Number Title Priority Date Filing Date
EA202190155A EA202190155A1 (en) 2019-06-21 2019-06-28 PRODUCTS BASED ON RECOMBINANT ADENO-ASSOCIATED VIRUSES AND METHODS FOR TREATMENT OF PELVIC-SHOULDER MUSCULAR DYSTROPHY TYPE 2A

Country Status (1)

Country Link
EA (1) EA202190155A1 (en)

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