AR115647A1 -
PRODUCTS AND METHODS WITH RECOMBINANT ADENO-ASSOCIATED VIRUSES FOR THE TREATMENT OF TYPE 2A MUSCULAR LIMB AND WAIST DYSTROPHY
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PRODUCTS AND METHODS WITH RECOMBINANT ADENO-ASSOCIATED VIRUSES FOR THE TREATMENT OF TYPE 2A MUSCULAR LIMB AND WAIST DYSTROPHY
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Medicines That Contain Protein Lipid Enzymes And Other Medicines
(AREA)
Abstract
Se proporcionan productos y métodos para tratar la distrofia muscular de extremidades y cintura de tipo 2A. En los métodos, los virus adenoasociados recombinantes suministran ADN que codifica una proteína con actividad calpaína 3.Products and methods are provided for treating Type 2A limb and girdle muscular dystrophy. In the methods, recombinant adeno-associated viruses deliver DNA encoding a protein with calpain 3 activity.
ARP190101814A2018-06-292019-06-28
PRODUCTS AND METHODS WITH RECOMBINANT ADENO-ASSOCIATED VIRUSES FOR THE TREATMENT OF TYPE 2A MUSCULAR LIMB AND WAIST DYSTROPHY
AR115647A1
(en)