AR115647A1 - PRODUCTS AND METHODS WITH RECOMBINANT ADENO-ASSOCIATED VIRUSES FOR THE TREATMENT OF TYPE 2A MUSCULAR LIMB AND WAIST DYSTROPHY - Google Patents

PRODUCTS AND METHODS WITH RECOMBINANT ADENO-ASSOCIATED VIRUSES FOR THE TREATMENT OF TYPE 2A MUSCULAR LIMB AND WAIST DYSTROPHY

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Publication number
AR115647A1
AR115647A1 ARP190101814A ARP190101814A AR115647A1 AR 115647 A1 AR115647 A1 AR 115647A1 AR P190101814 A ARP190101814 A AR P190101814A AR P190101814 A ARP190101814 A AR P190101814A AR 115647 A1 AR115647 A1 AR 115647A1
Authority
AR
Argentina
Prior art keywords
methods
limb
products
dystrophy
muscular
Prior art date
Application number
ARP190101814A
Other languages
Spanish (es)
Inventor
Zarife Sahenk
Original Assignee
Res Institute At Nationwide Children’S Hospital
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Res Institute At Nationwide Children’S Hospital filed Critical Res Institute At Nationwide Children’S Hospital
Publication of AR115647A1 publication Critical patent/AR115647A1/en

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  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)

Abstract

Se proporcionan productos y métodos para tratar la distrofia muscular de extremidades y cintura de tipo 2A. En los métodos, los virus adenoasociados recombinantes suministran ADN que codifica una proteína con actividad calpaína 3.Products and methods are provided for treating Type 2A limb and girdle muscular dystrophy. In the methods, recombinant adeno-associated viruses deliver DNA encoding a protein with calpain 3 activity.

ARP190101814A 2018-06-29 2019-06-28 PRODUCTS AND METHODS WITH RECOMBINANT ADENO-ASSOCIATED VIRUSES FOR THE TREATMENT OF TYPE 2A MUSCULAR LIMB AND WAIST DYSTROPHY AR115647A1 (en)

Applications Claiming Priority (1)

Application Number Priority Date Filing Date Title
US201862691934P 2018-06-29 2018-06-29

Publications (1)

Publication Number Publication Date
AR115647A1 true AR115647A1 (en) 2021-02-10

Family

ID=74672498

Family Applications (1)

Application Number Title Priority Date Filing Date
ARP190101814A AR115647A1 (en) 2018-06-29 2019-06-28 PRODUCTS AND METHODS WITH RECOMBINANT ADENO-ASSOCIATED VIRUSES FOR THE TREATMENT OF TYPE 2A MUSCULAR LIMB AND WAIST DYSTROPHY

Country Status (1)

Country Link
AR (1) AR115647A1 (en)

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