SG11202107844UA - Methods for treating symptoms and disorders associated with lysosomal storage diseases - Google Patents

Methods for treating symptoms and disorders associated with lysosomal storage diseases

Info

Publication number
SG11202107844UA
SG11202107844UA SG11202107844UA SG11202107844UA SG11202107844UA SG 11202107844U A SG11202107844U A SG 11202107844UA SG 11202107844U A SG11202107844U A SG 11202107844UA SG 11202107844U A SG11202107844U A SG 11202107844UA SG 11202107844U A SG11202107844U A SG 11202107844UA
Authority
SG
Singapore
Prior art keywords
methods
disorders associated
lysosomal storage
storage diseases
treating symptoms
Prior art date
Application number
SG11202107844UA
Inventor
Nigel Patrick Somerville Crawford
Tanya Zaremba Fischer
Original Assignee
Genzyme Corp
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Genzyme Corp filed Critical Genzyme Corp
Publication of SG11202107844UA publication Critical patent/SG11202107844UA/en

Links

Classifications

    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K31/00Medicinal preparations containing organic active ingredients
    • A61K31/33Heterocyclic compounds
    • A61K31/395Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins
    • A61K31/435Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having six-membered rings with one nitrogen as the only ring hetero atom
    • A61K31/439Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having six-membered rings with one nitrogen as the only ring hetero atom the ring forming part of a bridged ring system, e.g. quinuclidine
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K38/00Medicinal preparations containing peptides
    • A61K38/16Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof
    • A61K38/43Enzymes; Proenzymes; Derivatives thereof
    • A61K38/46Hydrolases (3)
    • A61K38/47Hydrolases (3) acting on glycosyl compounds (3.2), e.g. cellulases, lactases
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K45/00Medicinal preparations containing active ingredients not provided for in groups A61K31/00 - A61K41/00
    • A61K45/06Mixtures of active ingredients without chemical characterisation, e.g. antiphlogistics and cardiaca
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P17/00Drugs for dermatological disorders
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P25/00Drugs for disorders of the nervous system
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P25/00Drugs for disorders of the nervous system
    • A61P25/02Drugs for disorders of the nervous system for peripheral neuropathies
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P3/00Drugs for disorders of the metabolism
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P43/00Drugs for specific purposes, not provided for in groups A61P1/00-A61P41/00
    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12YENZYMES
    • C12Y302/00Hydrolases acting on glycosyl compounds, i.e. glycosylases (3.2)
    • C12Y302/01Glycosidases, i.e. enzymes hydrolysing O- and S-glycosyl compounds (3.2.1)
    • C12Y302/01045Glucosylceramidase (3.2.1.45), i.e. beta-glucocerebrosidase
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K2300/00Mixtures or combinations of active ingredients, wherein at least one active ingredient is fully defined in groups A61K31/00 - A61K41/00

Landscapes

  • Health & Medical Sciences (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • Chemical & Material Sciences (AREA)
  • General Health & Medical Sciences (AREA)
  • Veterinary Medicine (AREA)
  • Animal Behavior & Ethology (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Medicinal Chemistry (AREA)
  • Public Health (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • Engineering & Computer Science (AREA)
  • Organic Chemistry (AREA)
  • Epidemiology (AREA)
  • General Chemical & Material Sciences (AREA)
  • Chemical Kinetics & Catalysis (AREA)
  • Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
  • Gastroenterology & Hepatology (AREA)
  • Immunology (AREA)
  • Proteomics, Peptides & Aminoacids (AREA)
  • Genetics & Genomics (AREA)
  • Zoology (AREA)
  • Wood Science & Technology (AREA)
  • General Engineering & Computer Science (AREA)
  • Biochemistry (AREA)
  • Biomedical Technology (AREA)
  • Neurology (AREA)
  • Neurosurgery (AREA)
  • Diabetes (AREA)
  • Hematology (AREA)
  • Obesity (AREA)
  • Dermatology (AREA)
  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
SG11202107844UA 2019-02-04 2020-02-03 Methods for treating symptoms and disorders associated with lysosomal storage diseases SG11202107844UA (en)

Applications Claiming Priority (6)

Application Number Priority Date Filing Date Title
US201962800996P 2019-02-04 2019-02-04
US201962851433P 2019-05-22 2019-05-22
US201962894167P 2019-08-30 2019-08-30
US201962937618P 2019-11-19 2019-11-19
US202062962647P 2020-01-17 2020-01-17
PCT/US2020/016441 WO2020163245A1 (en) 2019-02-04 2020-02-03 Methods for treating symptoms and disorders associated with lysosomal storage diseases

Publications (1)

Publication Number Publication Date
SG11202107844UA true SG11202107844UA (en) 2021-08-30

Family

ID=69743942

Family Applications (2)

Application Number Title Priority Date Filing Date
SG11202107842QA SG11202107842QA (en) 2019-02-04 2020-02-03 Methods for treating symptoms and disorders associated with lysosomal storage diseases
SG11202107844UA SG11202107844UA (en) 2019-02-04 2020-02-03 Methods for treating symptoms and disorders associated with lysosomal storage diseases

Family Applications Before (1)

Application Number Title Priority Date Filing Date
SG11202107842QA SG11202107842QA (en) 2019-02-04 2020-02-03 Methods for treating symptoms and disorders associated with lysosomal storage diseases

Country Status (13)

Country Link
US (2) US20220023273A1 (en)
EP (2) EP3920913A1 (en)
JP (2) JP2022520747A (en)
KR (2) KR20210123353A (en)
CN (2) CN113645969A (en)
AU (2) AU2020218496A1 (en)
BR (2) BR112021015099A2 (en)
CA (2) CA3128039A1 (en)
IL (2) IL285187A (en)
MX (2) MX2021009383A (en)
SG (2) SG11202107842QA (en)
TW (2) TW202045167A (en)
WO (2) WO2020163245A1 (en)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CA3186766A1 (en) 2020-07-24 2022-01-27 Danielle Combessis Pharmaceutical compositions comprising venglustat

Family Cites Families (9)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
BE640616A (en) 1962-12-19
US3492397A (en) 1967-04-07 1970-01-27 Warner Lambert Pharmaceutical Sustained release dosage in the pellet form and process thereof
US4060598A (en) 1967-06-28 1977-11-29 Boehringer Mannheim G.M.B.H. Tablets coated with aqueous resin dispersions
US3538214A (en) 1969-04-22 1970-11-03 Merck & Co Inc Controlled release medicinal tablets
US4173626A (en) 1978-12-11 1979-11-06 Merck & Co., Inc. Sustained release indomethacin
GB0400812D0 (en) 2004-01-14 2004-02-18 Celltech R&D Ltd Novel compounds
CR20190034A (en) * 2011-03-18 2019-05-20 Genzyme Corp GLUCOSILCERAMIDE SINTASA INHIBITORS (Divisional 2013-0471)
CN105979945A (en) 2013-12-11 2016-09-28 建新公司 Glucosylceramide synthase inhibitors
TW201642855A (en) * 2015-03-10 2016-12-16 健臻公司 Methods for treating proteinopathies

Also Published As

Publication number Publication date
US20220023273A1 (en) 2022-01-27
KR20210123352A (en) 2021-10-13
AU2020217659A1 (en) 2021-08-26
WO2020163244A1 (en) 2020-08-13
EP3920913A1 (en) 2021-12-15
AU2020218496A1 (en) 2021-08-26
CA3128041A1 (en) 2020-08-13
EP3920914A1 (en) 2021-12-15
BR112021015172A2 (en) 2021-09-28
JP2022520747A (en) 2022-04-01
BR112021015099A2 (en) 2021-10-05
JP2022519274A (en) 2022-03-22
WO2020163245A1 (en) 2020-08-13
CN113645969A (en) 2021-11-12
KR20210123353A (en) 2021-10-13
CN113710249A (en) 2021-11-26
MX2021009384A (en) 2021-09-10
CA3128039A1 (en) 2020-08-13
IL285187A (en) 2021-09-30
TW202045168A (en) 2020-12-16
US20220016092A1 (en) 2022-01-20
SG11202107842QA (en) 2021-08-30
IL285304A (en) 2021-09-30
TW202045167A (en) 2020-12-16
MX2021009383A (en) 2021-09-10

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