SG11201706767RA - Materials and methods for treatment of hemoglobinopathies - Google Patents

Materials and methods for treatment of hemoglobinopathies

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Publication number
SG11201706767RA
SG11201706767RA SG11201706767RA SG11201706767RA SG11201706767RA SG 11201706767R A SG11201706767R A SG 11201706767RA SG 11201706767R A SG11201706767R A SG 11201706767RA SG 11201706767R A SG11201706767R A SG 11201706767RA SG 11201706767R A SG11201706767R A SG 11201706767RA
Authority
SG
Singapore
Prior art keywords
hemoglobinopathies
treatment
materials
methods
Prior art date
Application number
SG11201706767RA
Inventor
Matthew Hebden Porteus
Thomas James Cradick
Gang Bao
Ciaran M Lee
Original Assignee
Crispr Therapeutics Ag
Georgia Tech Res Inst
Univ Rice William M
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Crispr Therapeutics Ag, Georgia Tech Res Inst, Univ Rice William M filed Critical Crispr Therapeutics Ag
Publication of SG11201706767RA publication Critical patent/SG11201706767RA/en

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    • C12N15/113—Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids, e.g. ribozymes; Nucleic acids used in co-suppression or gene silencing
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
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    • A—HUMAN NECESSITIES
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    • A61K38/41—Porphyrin- or corrin-ring-containing peptides
    • A61K38/42—Haemoglobins; Myoglobins
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
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    • C12N15/09—Recombinant DNA-technology
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    • C12N2310/00—Structure or type of the nucleic acid
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    • C12N2310/20—Type of nucleic acid involving clustered regularly interspaced short palindromic repeats [CRISPRs]
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SG11201706767RA 2015-02-23 2016-02-23 Materials and methods for treatment of hemoglobinopathies SG11201706767RA (en)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US201562119754P 2015-02-23 2015-02-23
PCT/IB2016/000282 WO2016135558A2 (en) 2015-02-23 2016-02-23 Materials and methods for treatment of hemoglobinopathies

Publications (1)

Publication Number Publication Date
SG11201706767RA true SG11201706767RA (en) 2017-09-28

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SG11201706767RA SG11201706767RA (en) 2015-02-23 2016-02-23 Materials and methods for treatment of hemoglobinopathies
SG11201706766WA SG11201706766WA (en) 2015-02-23 2016-02-23 Materials and methods for treatment of hemoglobinopathies

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Country Status (8)

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US (3) US20180030438A1 (en)
EP (2) EP3262171A2 (en)
CN (2) CN107532168A (en)
AU (2) AU2016225178B2 (en)
BR (2) BR112017017812A2 (en)
CA (2) CA2977447A1 (en)
SG (2) SG11201706767RA (en)
WO (2) WO2016135558A2 (en)

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