JPWO2019243574A5 - - Google Patents

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Publication number
JPWO2019243574A5
JPWO2019243574A5 JP2020570467A JP2020570467A JPWO2019243574A5 JP WO2019243574 A5 JPWO2019243574 A5 JP WO2019243574A5 JP 2020570467 A JP2020570467 A JP 2020570467A JP 2020570467 A JP2020570467 A JP 2020570467A JP WO2019243574 A5 JPWO2019243574 A5 JP WO2019243574A5
Authority
JP
Japan
Prior art keywords
therapeutic agent
transgene
based vector
combination therapeutic
use according
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2020570467A
Other languages
English (en)
Japanese (ja)
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JP2021528407A5 (https=
JP2021528407A (ja
Publication date
Priority claimed from GBGB1810301.0A external-priority patent/GB201810301D0/en
Application filed filed Critical
Publication of JP2021528407A publication Critical patent/JP2021528407A/ja
Publication of JP2021528407A5 publication Critical patent/JP2021528407A5/ja
Publication of JPWO2019243574A5 publication Critical patent/JPWO2019243574A5/ja
Pending legal-status Critical Current

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JP2020570467A 2018-06-22 2019-06-21 組合せ遺伝子治療薬 Pending JP2021528407A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
GB1810301.0 2018-06-22
GBGB1810301.0A GB201810301D0 (en) 2018-06-22 2018-06-22 Combinatorial gene therapy
PCT/EP2019/066471 WO2019243574A1 (en) 2018-06-22 2019-06-21 Combinatorial gene therapy

Publications (3)

Publication Number Publication Date
JP2021528407A JP2021528407A (ja) 2021-10-21
JP2021528407A5 JP2021528407A5 (https=) 2022-06-24
JPWO2019243574A5 true JPWO2019243574A5 (https=) 2022-06-24

Family

ID=63042788

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2020570467A Pending JP2021528407A (ja) 2018-06-22 2019-06-21 組合せ遺伝子治療薬

Country Status (14)

Country Link
US (1) US20210252164A1 (https=)
EP (1) EP3810206B1 (https=)
JP (1) JP2021528407A (https=)
KR (1) KR20210024040A (https=)
CN (1) CN112955185A (https=)
AU (1) AU2019289998A1 (https=)
BR (1) BR112020026260A2 (https=)
CA (1) CA3104432A1 (https=)
GB (1) GB201810301D0 (https=)
IL (1) IL279584A (https=)
MX (1) MX2020013865A (https=)
SG (1) SG11202012727SA (https=)
WO (1) WO2019243574A1 (https=)
ZA (1) ZA202100244B (https=)

Families Citing this family (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CA3226019A1 (en) 2021-07-20 2023-01-26 Ags Therapeutics Sas Extracellular vesicles from microalgae, their preparation, and uses
WO2023144127A1 (en) 2022-01-31 2023-08-03 Ags Therapeutics Sas Extracellular vesicles from microalgae, their biodistribution upon administration, and uses
WO2023232976A1 (en) 2022-06-03 2023-12-07 Ags Therapeutics Sas Extracellular vesicles from genetically-modified microalgae containing endogenously-loaded cargo, their preparation, and uses
CN121038801A (zh) 2022-10-24 2025-11-28 Ags治疗简易股份公司 来自微藻的细胞外囊泡、它们在鼻内施用时的生物分布及其用途
WO2025176847A1 (en) 2024-02-21 2025-08-28 Ags Therapeutics Sas Ocular delivery of active agents via microalgae extracellular vesicles

Family Cites Families (9)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
AU2001273150A1 (en) * 2000-07-20 2002-02-05 Genentech Inc. Secreted and transmembrane polypeptides and nucleic acids encoding the same
EP2500434A1 (en) * 2011-03-12 2012-09-19 Association Institut de Myologie Capsid-free AAV vectors, compositions, and methods for vector production and gene delivery
CN102813942A (zh) * 2012-08-15 2012-12-12 钟志容 脂质超声微泡介导的腺相关病毒基因转染制剂及制备工艺
WO2015002956A1 (en) * 2013-07-01 2015-01-08 Ohio State Innovation Foundation Exosome delivery system
EP3495486B1 (en) * 2013-12-30 2020-12-16 CureVac AG Artificial nucleic acid molecules
WO2016033695A1 (en) * 2014-09-05 2016-03-10 Exerkine Corporation Exosome isolation
CA2962081A1 (en) * 2014-09-26 2016-03-31 Exerkine Corporation Exosomes useful to treat lysosomal storage disease
AU2017241534A1 (en) * 2016-03-28 2018-10-04 The Regents Of The University Of California Method and composition for treating neuronal hyper-excitability
GB2568255A (en) * 2017-11-08 2019-05-15 Evox Therapeutics Ltd Exosomes comprising RNA therapeutics

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