JP2025507279A5 - - Google Patents
Info
- Publication number
- JP2025507279A5 JP2025507279A5 JP2024545792A JP2024545792A JP2025507279A5 JP 2025507279 A5 JP2025507279 A5 JP 2025507279A5 JP 2024545792 A JP2024545792 A JP 2024545792A JP 2024545792 A JP2024545792 A JP 2024545792A JP 2025507279 A5 JP2025507279 A5 JP 2025507279A5
- Authority
- JP
- Japan
- Prior art keywords
- fus
- antisense oligonucleotide
- disease
- pharmaceutical composition
- oligonucleotide according
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| AU2022900200A AU2022900200A0 (en) | 2022-02-02 | Compositions and Methods for Treating Diseases Associated with Pathogenic FUS Variants | |
| AU2022900200 | 2022-02-02 | ||
| PCT/AU2023/050067 WO2023147630A1 (en) | 2022-02-02 | 2023-02-02 | Compositions and methods for treating diseases associated with pathogenic fus variants |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2025507279A JP2025507279A (ja) | 2025-03-18 |
| JP2025507279A5 true JP2025507279A5 (https=) | 2025-12-17 |
Family
ID=87553059
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024545792A Pending JP2025507279A (ja) | 2022-02-02 | 2023-02-02 | 病原性ｆｕｓバリアントに関連する疾患を処置するための組成物および方法 |
Country Status (8)
| Country | Link |
|---|---|
| US (1) | US20250382612A1 (https=) |
| EP (1) | EP4473111A1 (https=) |
| JP (1) | JP2025507279A (https=) |
| KR (1) | KR20240141197A (https=) |
| CN (1) | CN118871584A (https=) |
| AU (1) | AU2023215555A1 (https=) |
| CA (1) | CA3243618A1 (https=) |
| WO (1) | WO2023147630A1 (https=) |
Family Cites Families (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US20050244851A1 (en) * | 2004-01-13 | 2005-11-03 | Affymetrix, Inc. | Methods of analysis of alternative splicing in human |
| US20140349938A1 (en) * | 2011-06-03 | 2014-11-27 | President And Fellows Of Harvard College | Methods of diagnosing and treating amyotrophic lateral sclerosis |
| HRP20250468T1 (hr) * | 2019-05-28 | 2025-07-18 | Ionis Pharmaceuticals. Inc. | SPOJEVI I METODE ZA SMANJENJE POKAZATELJA FUS-a |
-
2023
- 2023-02-02 CA CA3243618A patent/CA3243618A1/en active Pending
- 2023-02-02 KR KR1020247028814A patent/KR20240141197A/ko active Pending
- 2023-02-02 CN CN202380027775.5A patent/CN118871584A/zh active Pending
- 2023-02-02 JP JP2024545792A patent/JP2025507279A/ja active Pending
- 2023-02-02 WO PCT/AU2023/050067 patent/WO2023147630A1/en not_active Ceased
- 2023-02-02 AU AU2023215555A patent/AU2023215555A1/en active Pending
- 2023-02-02 US US18/835,212 patent/US20250382612A1/en active Pending
- 2023-02-02 EP EP23749291.3A patent/EP4473111A1/en active Pending
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