JP2024502304A5 - - Google Patents
Info
- Publication number
- JP2024502304A5 JP2024502304A5 JP2023539080A JP2023539080A JP2024502304A5 JP 2024502304 A5 JP2024502304 A5 JP 2024502304A5 JP 2023539080 A JP2023539080 A JP 2023539080A JP 2023539080 A JP2023539080 A JP 2023539080A JP 2024502304 A5 JP2024502304 A5 JP 2024502304A5
- Authority
- JP
- Japan
- Prior art keywords
- ingredient
- day
- subject
- piperidinyl
- propoxy
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (7)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202063130438P | 2020-12-24 | 2020-12-24 | |
| US63/130,438 | 2020-12-24 | ||
| EP21155579 | 2021-02-05 | ||
| EP21155579.2 | 2021-02-05 | ||
| US202163185111P | 2021-05-06 | 2021-05-06 | |
| US63/185,111 | 2021-05-06 | ||
| PCT/EP2021/087483 WO2022136640A1 (en) | 2020-12-24 | 2021-12-23 | Arimoclomol for the treatment of niemann pick disease, type c, in patients with er type missense mutations |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024502304A JP2024502304A (ja) | 2024-01-18 |
| JP2024502304A5 true JP2024502304A5 (https=) | 2025-01-06 |
Family
ID=79830856
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023539080A Pending JP2024502304A (ja) | 2020-12-24 | 2021-12-23 | Ｅｒ型ミスセンス変異を有する患者におけるニーマンピック病ｃ型の治療用アリモクロモル |
Country Status (9)
| Country | Link |
|---|---|
| US (1) | US20240115558A1 (https=) |
| EP (1) | EP4267139A1 (https=) |
| JP (1) | JP2024502304A (https=) |
| KR (1) | KR20230128037A (https=) |
| AU (1) | AU2021405780A1 (https=) |
| CA (1) | CA3205873A1 (https=) |
| IL (1) | IL303968A (https=) |
| MX (1) | MX2023007551A (https=) |
| WO (1) | WO2022136640A1 (https=) |
Families Citing this family (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| AU2023366474A1 (en) * | 2022-10-27 | 2025-05-15 | Zevra Denmark A/S | Arimoclomol compositions for use in treating niemann pick disease type c (npc) |
| WO2026010894A1 (en) * | 2024-06-30 | 2026-01-08 | Zevra Therapeutics, Inc. | Arimoclomol in combination with miglustat for use in the treatment of lysosomal storage disorders |
| US20260000661A1 (en) * | 2024-07-01 | 2026-01-01 | Zevra Therapeutics, Inc. | Use of arimoclomol in activating clear gene expression as treatment for lysosomal storage disorders |
| WO2026010893A1 (en) * | 2024-07-01 | 2026-01-08 | Zevra Therapeutics, Inc. | Arimoclomol in combination with miglustat for use in the treatment of lysosomal storage disorders such as niemann-pick disease, type-c |
Family Cites Families (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| HU222994B1 (hu) | 1995-11-02 | 2004-01-28 | BIOREX Kutató és Fejlesztő Rt. | Hidroxilaminszármazékok és azok alkalmazása sejtek molekuláris chaperon-termelésének fokozására alkalmas gyógyszerkészítmények előállítására |
| HUP9900475D0 (en) | 1999-02-26 | 1999-04-28 | Biorex Kutato Fejlesztoe Kft | O-(3-piperidino-2-hydroxy-1-propyl)-hiyroximic acid-halogenid derivative, it's use for treating insulin resistance, and pharmaceutical compositions containing them as active component |
| HUP0001583A2 (hu) | 2000-04-18 | 2002-11-28 | BIOREX Kutató és Fejlesztő Rt. | Egy piridin-1-oxid-származék és eljárás annak átalakítására gyógyászati hatású vegyületekké |
| RU2013125923A (ru) * | 2010-11-30 | 2015-01-10 | Орфазиме Апс | СПОСОБЫ УВЕЛИЧЕНИЯ ВНУТРИКЛЕТОЧНОЙ АКТИВНОСТИ Hsp70 |
-
2021
- 2021-12-23 WO PCT/EP2021/087483 patent/WO2022136640A1/en not_active Ceased
- 2021-12-23 CA CA3205873A patent/CA3205873A1/en active Pending
- 2021-12-23 MX MX2023007551A patent/MX2023007551A/es unknown
- 2021-12-23 EP EP21847473.2A patent/EP4267139A1/en active Pending
- 2021-12-23 US US18/267,591 patent/US20240115558A1/en active Pending
- 2021-12-23 JP JP2023539080A patent/JP2024502304A/ja active Pending
- 2021-12-23 KR KR1020237024972A patent/KR20230128037A/ko active Pending
- 2021-12-23 AU AU2021405780A patent/AU2021405780A1/en active Pending
- 2021-12-23 IL IL303968A patent/IL303968A/en unknown
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| Agent | PrJAMP-KETOTIFEN |