JP2023544702A5 - - Google Patents

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Publication number
JP2023544702A5
JP2023544702A5 JP2023519419A JP2023519419A JP2023544702A5 JP 2023544702 A5 JP2023544702 A5 JP 2023544702A5 JP 2023519419 A JP2023519419 A JP 2023519419A JP 2023519419 A JP2023519419 A JP 2023519419A JP 2023544702 A5 JP2023544702 A5 JP 2023544702A5
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JP
Japan
Prior art keywords
nucleic acid
recombinant nucleic
acid according
vector
tcf4
Prior art date
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Application number
JP2023519419A
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English (en)
Japanese (ja)
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JP7786750B2 (ja
JP2023544702A (ja
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Priority claimed from PCT/US2021/052987 external-priority patent/WO2022072709A1/en
Publication of JP2023544702A publication Critical patent/JP2023544702A/ja
Publication of JP2023544702A5 publication Critical patent/JP2023544702A5/ja
Application granted granted Critical
Publication of JP7786750B2 publication Critical patent/JP7786750B2/ja
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JP2023519419A 2020-09-30 2021-09-30 Ｔｃｆ４遺伝子発現を調節するため、およびピット・ホプキンス症候群を治療するための組成物および方法 Active JP7786750B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063085878P 2020-09-30 2020-09-30
US63/085,878 2020-09-30
PCT/US2021/052987 WO2022072709A1 (en) 2020-09-30 2021-09-30 Compositions and methods for modulating tcf4 gene expression and treating pitt hopkins syndrome

Publications (3)

Publication Number Publication Date
JP2023544702A JP2023544702A (ja) 2023-10-25
JP2023544702A5 true JP2023544702A5 (cg-RX-API-DMAC7.html) 2024-08-13
JP7786750B2 JP7786750B2 (ja) 2025-12-16

Family

ID=80951835

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023519419A Active JP7786750B2 (ja) 2020-09-30 2021-09-30 Ｔｃｆ４遺伝子発現を調節するため、およびピット・ホプキンス症候群を治療するための組成物および方法

Country Status (9)

Country Link
US (1) US20230372542A1 (cg-RX-API-DMAC7.html)
EP (1) EP4222268A4 (cg-RX-API-DMAC7.html)
JP (1) JP7786750B2 (cg-RX-API-DMAC7.html)
KR (1) KR20230079190A (cg-RX-API-DMAC7.html)
CN (1) CN116670769A (cg-RX-API-DMAC7.html)
AU (1) AU2021351512A1 (cg-RX-API-DMAC7.html)
CA (1) CA3194085A1 (cg-RX-API-DMAC7.html)
IL (1) IL301610A (cg-RX-API-DMAC7.html)
WO (1) WO2022072709A1 (cg-RX-API-DMAC7.html)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN117298153B (zh) * 2023-08-30 2024-03-08 济宁市第一人民医院 脑内皮细胞来源的细胞外囊泡在神经炎症中的应用
CN117476101B (zh) * 2023-11-22 2025-10-10 浙江大学 一种多组学单细胞测序数据区分恶性细胞的方法、系统、设备和介质
WO2025213093A1 (en) * 2024-04-04 2025-10-09 Lundquist Institute For Biomedical Innovation At Harbor-Ucla Medical Center Antisense oligonucleotides for treating pitt hopkin syndrome

Family Cites Families (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US4683195A (en) 1986-01-30 1987-07-28 Cetus Corporation Process for amplifying, detecting, and/or-cloning nucleic acid sequences
US20180305689A1 (en) * 2015-04-22 2018-10-25 Mina Therapeutics Limited Sarna compositions and methods of use

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