JP2023517929A5 - - Google Patents

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Publication number
JP2023517929A5
JP2023517929A5 JP2022554440A JP2022554440A JP2023517929A5 JP 2023517929 A5 JP2023517929 A5 JP 2023517929A5 JP 2022554440 A JP2022554440 A JP 2022554440A JP 2022554440 A JP2022554440 A JP 2022554440A JP 2023517929 A5 JP2023517929 A5 JP 2023517929A5
Authority
JP
Japan
Application number
JP2022554440A
Other languages
Japanese (ja)
Other versions
JPWO2021183779A5 (https=
JP2023517929A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/021936 external-priority patent/WO2021183779A1/en
Publication of JP2023517929A publication Critical patent/JP2023517929A/ja
Publication of JPWO2021183779A5 publication Critical patent/JPWO2021183779A5/ja
Publication of JP2023517929A5 publication Critical patent/JP2023517929A5/ja
Pending legal-status Critical Current

Links

JP2022554440A 2020-03-11 2021-03-11 Nmnat1関連網膜変性に対する遺伝子療法 Pending JP2023517929A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202062988260P 2020-03-11 2020-03-11
US62/988,260 2020-03-11
PCT/US2021/021936 WO2021183779A1 (en) 2020-03-11 2021-03-11 Gene therapy for nmnat1-associated retinal degeneration

Publications (3)

Publication Number Publication Date
JP2023517929A JP2023517929A (ja) 2023-04-27
JPWO2021183779A5 JPWO2021183779A5 (https=) 2024-03-19
JP2023517929A5 true JP2023517929A5 (https=) 2024-03-19

Family

ID=77672442

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2022554440A Pending JP2023517929A (ja) 2020-03-11 2021-03-11 Nmnat1関連網膜変性に対する遺伝子療法

Country Status (11)

Country Link
US (2) US12257320B2 (https=)
EP (1) EP4117644A4 (https=)
JP (1) JP2023517929A (https=)
KR (1) KR20220152550A (https=)
CN (1) CN115379834A (https=)
AU (1) AU2021236233A1 (https=)
BR (1) BR112022017970A2 (https=)
CA (1) CA3174781A1 (https=)
IL (1) IL296262A (https=)
MX (1) MX2022011177A (https=)
WO (1) WO2021183779A1 (https=)

Family Cites Families (10)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JP2008501343A (ja) * 2004-06-04 2008-01-24 ワシントン・ユニバーシティ 神経障害を治療するための方法および組成物
EP3030665B9 (en) 2013-08-05 2023-10-04 Academisch Ziekenhuis Leiden H.O.D.N. Leids Universitair Medisch Centrum Recombinant aav-crumbs homologue composition and methods for treating lca-8 and progressive rp
KR102537394B1 (ko) * 2014-03-17 2023-05-30 애드베룸 바이오테크놀로지스, 인코포레이티드 원추세포에서 증강된 유전자 발현을 위한 조성물 및 방법
IL248102B (en) 2014-05-02 2022-07-01 Genzyme Corp aav vectors for gene therapy of the central nervous system and retina
PT3191139T (pt) 2014-07-24 2020-11-05 Massachusetts Eye & Ear Infirmary Terapia do gene rpgr para retinite pigmentosa
PL3265568T3 (pl) * 2015-03-06 2020-11-30 Massachusetts Eye & Ear Infirmary Terapie augmentacji genów w przypadku wrodzonego zwyrodnienia siatkówki spowodowanego mutacjami genu prpf31
EP3364973A1 (en) * 2015-10-23 2018-08-29 The Jackson Laboratory Nicotinamide for use in the treatment and prevention of ocular neurodegenerative disorder (e.g. glaucoma)
US11260081B2 (en) 2016-06-29 2022-03-01 Ramot At Tel-Aviv University Ltd. Engineered parasites for delivering protein to the central nervous system (CNS)
CN116509885A (zh) 2016-12-21 2023-08-01 新南创新私人有限公司 增加血管密度的方法
KR20200036912A (ko) * 2017-07-31 2020-04-07 리플렉션 바이오테크놀러지스 리미티드 안과 질환을 위한 세포 모델 및 치료요법

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