JP2023512242A5 - - Google Patents
Info
- Publication number
- JP2023512242A5 JP2023512242A5 JP2022546049A JP2022546049A JP2023512242A5 JP 2023512242 A5 JP2023512242 A5 JP 2023512242A5 JP 2022546049 A JP2022546049 A JP 2022546049A JP 2022546049 A JP2022546049 A JP 2022546049A JP 2023512242 A5 JP2023512242 A5 JP 2023512242A5
- Authority
- JP
- Japan
- Prior art keywords
- human
- ids
- paragraphs
- cells
- brain
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (7)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202062967494P | 2020-01-29 | 2020-01-29 | |
| US62/967,494 | 2020-01-29 | ||
| US202063066625P | 2020-08-17 | 2020-08-17 | |
| US63/066,625 | 2020-08-17 | ||
| US202063088305P | 2020-10-06 | 2020-10-06 | |
| US63/088,305 | 2020-10-06 | ||
| PCT/US2021/015446 WO2021154963A1 (en) | 2020-01-29 | 2021-01-28 | Treatment of mucopolysaccharidosis ii with recombinant human iduronate-2-sulfatase (ids) produced by human neural or glial cells |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2023512242A JP2023512242A (ja) | 2023-03-24 |
| JP2023512242A5 true JP2023512242A5 (https=) | 2024-02-28 |
Family
ID=74859506
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022546049A Pending JP2023512242A (ja) | 2020-01-29 | 2021-01-28 | ヒト神経細胞またはヒトグリア細胞が産生した組換えヒトイズロン酸－２－スルファターゼ（ｉｄｓ）によるムコ多糖症ｉｉの治療 |
Country Status (10)
| Country | Link |
|---|---|
| US (1) | US20230088992A1 (https=) |
| EP (1) | EP4096631A1 (https=) |
| JP (1) | JP2023512242A (https=) |
| KR (1) | KR20220148162A (https=) |
| AU (1) | AU2021214174A1 (https=) |
| BR (1) | BR112022015183A2 (https=) |
| CA (1) | CA3167741A1 (https=) |
| IL (1) | IL294636A (https=) |
| TW (1) | TW202142695A (https=) |
| WO (1) | WO2021154963A1 (https=) |
Families Citing this family (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| KR20190139951A (ko) | 2017-04-14 | 2019-12-18 | 리젠엑스바이오 인크. | 인간 뉴런 또는 신경교 세포에 의해 생성된 재조합 인간 이두로네이트-2 설파타제(ids)를 이용한 뮤코다당증 ii형의 치료 |
| US11822232B2 (en) * | 2020-07-28 | 2023-11-21 | Synopsys, Inc. | Dose information generation and communication for lithography manufacturing systems |
| EP4291249A2 (en) | 2021-02-10 | 2023-12-20 | RegenxBio Inc. | Treatment of mucopolysaccharidosis ii with recombinant human iduronate-2-sulfatase (ids) |
| CN120550109B (zh) * | 2025-05-29 | 2026-04-17 | 普大生物科技(泰州)有限公司 | 一种包含多价肺炎球菌多糖-蛋白结合物的组合物及其制备方法和应用 |
Family Cites Families (22)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CA2379166C (en) | 1999-08-09 | 2013-03-26 | Targeted Genetics Corporation | Enhancement of expression of a single-stranded, heterologous nucleotide sequence from recombinant viral vectors by designing the sequence such that it forms instrastrand base pairs |
| MX359371B (es) | 2001-11-13 | 2018-09-25 | Univ Pennsylvania | Un metodo para detectar y/o identificar secuencias del virus adeno-asociado y aislamiento de secuencias novedosas identificadas de ese modo. |
| PT1453547T (pt) | 2001-12-17 | 2016-12-28 | Univ Pennsylvania | Sequências do vírus adeno-associado (aav) do serotipo 8, vetores contendo as mesmas, e utilizações destas |
| EP2345731B1 (en) | 2003-09-30 | 2015-10-21 | The Trustees of the University of Pennsylvania | Adeno-associated virus (AAV) clades, sequences, vectors containing same, and uses thereof |
| ES2525067T3 (es) | 2005-04-07 | 2014-12-17 | The Trustees Of The University Of Pennsylvania | Método de incremento de la función de un vector de AAV |
| JP4495210B2 (ja) | 2005-06-09 | 2010-06-30 | パナソニック株式会社 | 振幅誤差補償装置及び直交度誤差補償装置 |
| US8734809B2 (en) | 2009-05-28 | 2014-05-27 | University Of Massachusetts | AAV's and uses thereof |
| US8927514B2 (en) | 2010-04-30 | 2015-01-06 | City Of Hope | Recombinant adeno-associated vectors for targeted treatment |
| US8628966B2 (en) | 2010-04-30 | 2014-01-14 | City Of Hope | CD34-derived recombinant adeno-associated vectors for stem cell transduction and systemic therapeutic gene transfer |
| KR20230159646A (ko) * | 2010-06-25 | 2023-11-21 | 샤이어 휴먼 지네틱 테라피즈 인크. | 이듀로네이트-2-설파타제의 cns 전달을 위한 방법들 및 조성물들 |
| WO2012057363A1 (ja) | 2010-10-27 | 2012-05-03 | 学校法人自治医科大学 | 神経系細胞への遺伝子導入のためのアデノ随伴ウイルスビリオン |
| WO2012109570A1 (en) | 2011-02-10 | 2012-08-16 | The University Of North Carolina At Chapel Hill | Viral vectors with modified transduction profiles and methods of making and using the same |
| CN105755044A (zh) | 2011-04-22 | 2016-07-13 | 加利福尼亚大学董事会 | 具有变异衣壳的腺相关病毒病毒体及其使用方法 |
| ES2857773T5 (es) | 2011-08-24 | 2024-06-04 | Univ Leland Stanford Junior | Nuevas proteínas de la cápside de AAV para la transferencia de ácidos nucleicos |
| WO2013170078A1 (en) | 2012-05-09 | 2013-11-14 | Oregon Health & Science University | Adeno associated virus plasmids and vectors |
| CA2905952A1 (en) | 2013-03-13 | 2014-10-02 | The Children's Hospital Of Philadelphia | Adeno-associated virus vectors and methods of use thereof |
| ES2739288T3 (es) | 2013-09-13 | 2020-01-30 | California Inst Of Techn | Recuperación selectiva |
| CN106232618A (zh) | 2013-10-11 | 2016-12-14 | 马萨诸塞眼科耳科诊所 | 预测祖先病毒序列的方法及其用途 |
| WO2015164757A1 (en) | 2014-04-25 | 2015-10-29 | Oregon Health & Science University | Methods of viral neutralizing antibody epitope mapping |
| SG10201912761UA (en) | 2016-04-15 | 2020-02-27 | The Trustees Of The Univ Of Pennsyvania | Gene therapy for treating mucopolysaccharidosis type ii |
| KR20190139951A (ko) * | 2017-04-14 | 2019-12-18 | 리젠엑스바이오 인크. | 인간 뉴런 또는 신경교 세포에 의해 생성된 재조합 인간 이두로네이트-2 설파타제(ids)를 이용한 뮤코다당증 ii형의 치료 |
| KR20220131522A (ko) * | 2020-01-22 | 2022-09-28 | 리젠엑스바이오 인크. | 완전-인간 글리코실화된 인간 알파-l-이두로니다아제 (idua)를 사용한 점액다당류증 i의 치료 |
-
2021
- 2021-01-28 BR BR112022015183A patent/BR112022015183A2/pt unknown
- 2021-01-28 JP JP2022546049A patent/JP2023512242A/ja active Pending
- 2021-01-28 AU AU2021214174A patent/AU2021214174A1/en active Pending
- 2021-01-28 US US17/792,961 patent/US20230088992A1/en active Pending
- 2021-01-28 KR KR1020227027253A patent/KR20220148162A/ko active Pending
- 2021-01-28 CA CA3167741A patent/CA3167741A1/en active Pending
- 2021-01-28 WO PCT/US2021/015446 patent/WO2021154963A1/en not_active Ceased
- 2021-01-28 TW TW110103276A patent/TW202142695A/zh unknown
- 2021-01-28 EP EP21710357.1A patent/EP4096631A1/en not_active Withdrawn
- 2021-01-28 IL IL294636A patent/IL294636A/en unknown
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| JP2023512242A5 (https=) | ||
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