JP2019534890A5 - - Google Patents

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Publication number
JP2019534890A5
JP2019534890A5 JP2019520628A JP2019520628A JP2019534890A5 JP 2019534890 A5 JP2019534890 A5 JP 2019534890A5 JP 2019520628 A JP2019520628 A JP 2019520628A JP 2019520628 A JP2019520628 A JP 2019520628A JP 2019534890 A5 JP2019534890 A5 JP 2019534890A5
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JP
Japan
Prior art keywords
nucleic acid
composition
nanoparticles
composition according
acid sequence
Prior art date
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Pending
Application number
JP2019520628A
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English (en)
Japanese (ja)
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JP2019534890A (ja
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Priority claimed from PCT/US2017/056188 external-priority patent/WO2018071572A1/en
Publication of JP2019534890A publication Critical patent/JP2019534890A/ja
Publication of JP2019534890A5 publication Critical patent/JP2019534890A5/ja
Pending legal-status Critical Current

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JP2019520628A 2016-10-11 2017-10-11 遺伝子編集ツールによって機能化されたナノ粒子および関連する方法 Pending JP2019534890A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201662406542P 2016-10-11 2016-10-11
US62/406,542 2016-10-11
PCT/US2017/056188 WO2018071572A1 (en) 2016-10-11 2017-10-11 Nanoparticles functionalized with gene editing tools and related methods

Publications (2)

Publication Number Publication Date
JP2019534890A JP2019534890A (ja) 2019-12-05
JP2019534890A5 true JP2019534890A5 (https=) 2020-10-15

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Family Applications (1)

Application Number Title Priority Date Filing Date
JP2019520628A Pending JP2019534890A (ja) 2016-10-11 2017-10-11 遺伝子編集ツールによって機能化されたナノ粒子および関連する方法

Country Status (5)

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US (2) US20190233820A1 (https=)
EP (1) EP3525831A4 (https=)
JP (1) JP2019534890A (https=)
CA (1) CA3039924A1 (https=)
WO (1) WO2018071572A1 (https=)

Families Citing this family (7)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CA2986310A1 (en) 2015-05-11 2016-11-17 Editas Medicine, Inc. Optimized crispr/cas9 systems and methods for gene editing in stem cells
CN108026526B (zh) 2015-06-09 2023-05-12 爱迪塔斯医药公司 用于改善移植的crispr/cas相关方法和组合物
US11866726B2 (en) 2017-07-14 2024-01-09 Editas Medicine, Inc. Systems and methods for targeted integration and genome editing and detection thereof using integrated priming sites
KR20220146437A (ko) * 2020-01-10 2022-11-01 안드라닉 앤드류 아프리키안 목적 유전자의 발현 및/또는 신호전달 경로의 조절을 위한 나노입자
US20220162601A1 (en) * 2020-11-23 2022-05-26 Recursion Pharmaceuticals, Inc. High throughput gene editing system and method
WO2022210822A1 (ja) * 2021-04-02 2022-10-06 キヤノン株式会社 試薬、及びそれを用いた標的核酸の検出方法
JP2022158921A (ja) * 2021-04-02 2022-10-17 キヤノン株式会社 試薬、及びそれを用いた標的核酸の検出方法

Family Cites Families (11)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US10022457B2 (en) * 2005-08-05 2018-07-17 Gholam A. Peyman Methods to regulate polarization and enhance function of cells
TWI576432B (zh) * 2009-04-07 2017-04-01 陶氏農業科學公司 序列特異性核酸酶之奈米粒子媒介式遞送技術
CA2938661A1 (en) * 2011-10-21 2013-04-25 Stemgenics, Inc Functionalized nanoparticles for intracellular delivery of biologically active molecules
PL3360964T3 (pl) * 2012-12-06 2020-03-31 Sigma-Aldrich Co. Llc Modyfikacja i regulacja genomu oparta na crispr
RU2716420C2 (ru) * 2013-06-17 2020-03-11 Те Брод Инститьют Инк. Доставка и применение систем crispr-cas, векторов и композиций для целенаправленного воздействия и терапии в печени
JP6455912B2 (ja) * 2014-03-24 2019-01-23 国立研究開発法人産業技術総合研究所 人工ヌクレアーゼの細胞への導入方法
WO2016028682A1 (en) * 2014-08-17 2016-02-25 The Broad Institute Inc. Genome editing using cas9 nickases
WO2016094874A1 (en) * 2014-12-12 2016-06-16 The Broad Institute Inc. Escorted and functionalized guides for crispr-cas systems
WO2016124765A1 (en) * 2015-02-06 2016-08-11 Cellectis Primary hematopoietic cells genetically engineered by slow release of nucleic acids using nanoparticles
WO2016197133A1 (en) * 2015-06-04 2016-12-08 Protiva Biotherapeutics, Inc. Delivering crispr therapeutics with lipid nanoparticles
US20180237800A1 (en) * 2015-09-21 2018-08-23 The Regents Of The University Of California Compositions and methods for target nucleic acid modification

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