CA3164055A1 - Cellules modifiees et methodes pour le traitement d'hemoglobinopathies - Google Patents
Cellules modifiees et methodes pour le traitement d'hemoglobinopathiesInfo
- Publication number
- CA3164055A1 CA3164055A1 CA3164055A CA3164055A CA3164055A1 CA 3164055 A1 CA3164055 A1 CA 3164055A1 CA 3164055 A CA3164055 A CA 3164055A CA 3164055 A CA3164055 A CA 3164055A CA 3164055 A1 CA3164055 A1 CA 3164055A1
- Authority
- CA
- Canada
- Prior art keywords
- cells
- population
- modified
- hbg1
- certain embodiments
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Landscapes
- Micro-Organisms Or Cultivation Processes Thereof (AREA)
- Medicines Containing Material From Animals Or Micro-Organisms (AREA)
Abstract
L'invention concerne des systèmes d'édition du génome, des ARN guides et des procédés à médiation par CRISPR pour modifier des parties des loci des gènes HBG1 et HBG2 dans des cellules et augmenter l'expression de l'hémoglobine ftale.
Applications Claiming Priority (4)
Application Number | Priority Date | Filing Date | Title |
---|---|---|---|
US62/945,190 | 2019-12-08 | ||
US202063115518P | 2020-11-18 | 2020-11-18 | |
US63/115,518 | 2020-11-18 | ||
PCT/US2020/063854 WO2021119040A1 (fr) | 2019-12-08 | 2020-12-09 | Cellules modifiées et méthodes pour le traitement d'hémoglobinopathies |
Publications (1)
Publication Number | Publication Date |
---|---|
CA3164055A1 true CA3164055A1 (fr) | 2021-06-17 |
Family
ID=82309508
Family Applications (1)
Application Number | Title | Priority Date | Filing Date |
---|---|---|---|
CA3164055A Pending CA3164055A1 (fr) | 2019-12-08 | 2020-12-09 | Cellules modifiees et methodes pour le traitement d'hemoglobinopathies |
Country Status (3)
Country | Link |
---|---|
JP (1) | JP2023521524A (fr) |
CN (1) | CN115175990A (fr) |
CA (1) | CA3164055A1 (fr) |
-
2020
- 2020-12-09 CN CN202080095711.5A patent/CN115175990A/zh active Pending
- 2020-12-09 JP JP2022534449A patent/JP2023521524A/ja active Pending
- 2020-12-09 CA CA3164055A patent/CA3164055A1/fr active Pending
Also Published As
Publication number | Publication date |
---|---|
JP2023521524A (ja) | 2023-05-25 |
CN115175990A (zh) | 2022-10-11 |
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