AU2019228448A1 - Methods and compositions for treating bile duct paucity-associated conditions - Google Patents
Methods and compositions for treating bile duct paucity-associated conditions Download PDFInfo
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- AU2019228448A1 AU2019228448A1 AU2019228448A AU2019228448A AU2019228448A1 AU 2019228448 A1 AU2019228448 A1 AU 2019228448A1 AU 2019228448 A AU2019228448 A AU 2019228448A AU 2019228448 A AU2019228448 A AU 2019228448A AU 2019228448 A1 AU2019228448 A1 AU 2019228448A1
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- C—CHEMISTRY; METALLURGY
- C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
- C12N—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
- C12N15/00—Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor
- C12N15/09—Recombinant DNA-technology
- C12N15/11—DNA or RNA fragments; Modified forms thereof; Non-coding nucleic acids having a biological activity
- C12N15/113—Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids, e.g. ribozymes; Nucleic acids used in co-suppression or gene silencing
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- C—CHEMISTRY; METALLURGY
- C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
- C12N—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
- C12N2310/00—Structure or type of the nucleic acid
- C12N2310/10—Type of nucleic acid
- C12N2310/14—Type of nucleic acid interfering nucleic acids [NA]
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- Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
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- Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
- Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
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Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201862637973P | 2018-03-02 | 2018-03-02 | |
| US62/637,973 | 2018-03-02 | ||
| PCT/US2019/018184 WO2019168686A1 (en) | 2018-03-02 | 2019-02-15 | Methods and compositions for treating bile duct paucity-associated conditions |
Publications (1)
| Publication Number | Publication Date |
|---|---|
| AU2019228448A1 true AU2019228448A1 (en) | 2020-09-10 |
Family
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Family Applications (1)
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| AU2019228448A Abandoned AU2019228448A1 (en) | 2018-03-02 | 2019-02-15 | Methods and compositions for treating bile duct paucity-associated conditions |
Country Status (10)
| Country | Link |
|---|---|
| US (1) | US11634715B2 (https=) |
| EP (1) | EP3740248A4 (https=) |
| JP (1) | JP2021517909A (https=) |
| KR (1) | KR20200127008A (https=) |
| CN (1) | CN112055597A (https=) |
| AU (1) | AU2019228448A1 (https=) |
| CA (1) | CA3092089A1 (https=) |
| IL (1) | IL277015A (https=) |
| MX (1) | MX2020009074A (https=) |
| WO (1) | WO2019168686A1 (https=) |
Families Citing this family (2)
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| CA3092089A1 (en) | 2018-03-02 | 2019-09-06 | Dicerna Pharmaceuticals, Inc. | Methods and compositions for treating bile duct paucity-associated conditions |
| WO2024262593A1 (ja) * | 2023-06-22 | 2024-12-26 | 公益財団法人川崎市産業振興財団 | 核酸の血中安定性を向上させ、標的化効率を向上させる方法 |
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| DK3037538T3 (da) | 2010-07-06 | 2019-06-24 | Dicerna Pharmaceuticals Inc | Fremgangsmåder og sammensætninger til specifik inhibering af beta-catenin ved hjælp af dobbeltstrenget rna |
| US9468670B2 (en) * | 2011-04-01 | 2016-10-18 | Texas A&M University System | Melatonin-based treatment and diagnosis of bile duct disease |
| IL316808A (en) * | 2014-08-20 | 2025-01-01 | Alnylam Pharmaceuticals Inc | Modified double-stranded RNA materials and their uses |
| AU2015330670B2 (en) * | 2014-10-10 | 2022-01-06 | Novo Nordisk Health Care Ag | Therapeutic inhibition of lactate dehydrogenase and agents therefor |
| CA3092089A1 (en) | 2018-03-02 | 2019-09-06 | Dicerna Pharmaceuticals, Inc. | Methods and compositions for treating bile duct paucity-associated conditions |
-
2019
- 2019-02-15 CA CA3092089A patent/CA3092089A1/en active Pending
- 2019-02-15 US US16/975,946 patent/US11634715B2/en active Active
- 2019-02-15 AU AU2019228448A patent/AU2019228448A1/en not_active Abandoned
- 2019-02-15 WO PCT/US2019/018184 patent/WO2019168686A1/en not_active Ceased
- 2019-02-15 JP JP2020568662A patent/JP2021517909A/ja active Pending
- 2019-02-15 MX MX2020009074A patent/MX2020009074A/es unknown
- 2019-02-15 KR KR1020207027733A patent/KR20200127008A/ko not_active Ceased
- 2019-02-15 CN CN201980029432.6A patent/CN112055597A/zh active Pending
- 2019-02-15 EP EP19761345.8A patent/EP3740248A4/en not_active Withdrawn
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2020
- 2020-08-31 IL IL277015A patent/IL277015A/en unknown
Also Published As
| Publication number | Publication date |
|---|---|
| EP3740248A1 (en) | 2020-11-25 |
| KR20200127008A (ko) | 2020-11-09 |
| EP3740248A4 (en) | 2022-01-26 |
| MX2020009074A (es) | 2020-10-08 |
| JP2021517909A (ja) | 2021-07-29 |
| US11634715B2 (en) | 2023-04-25 |
| CA3092089A1 (en) | 2019-09-06 |
| WO2019168686A1 (en) | 2019-09-06 |
| CN112055597A (zh) | 2020-12-08 |
| US20210010005A1 (en) | 2021-01-14 |
| IL277015A (en) | 2020-10-29 |
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