AU2013248197B2 - Compounds and compositions for the detection and treatment of Alzheimer's disease and related disorders - Google Patents
Compounds and compositions for the detection and treatment of Alzheimer's disease and related disorders Download PDFInfo
- Publication number
- AU2013248197B2 AU2013248197B2 AU2013248197A AU2013248197A AU2013248197B2 AU 2013248197 B2 AU2013248197 B2 AU 2013248197B2 AU 2013248197 A AU2013248197 A AU 2013248197A AU 2013248197 A AU2013248197 A AU 2013248197A AU 2013248197 B2 AU2013248197 B2 AU 2013248197B2
- Authority
- AU
- Australia
- Prior art keywords
- compound
- certain embodiments
- present
- attendant definitions
- relates
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Ceased
Links
- 150000001875 compounds Chemical class 0.000 title claims abstract description 300
- 239000000203 mixture Substances 0.000 title claims abstract description 72
- 238000011282 treatment Methods 0.000 title claims abstract description 12
- 208000024827 Alzheimer disease Diseases 0.000 title claims description 58
- 208000037265 diseases, disorders, signs and symptoms Diseases 0.000 title description 11
- 238000001514 detection method Methods 0.000 title description 6
- 238000000034 method Methods 0.000 claims abstract description 57
- 239000003795 chemical substances by application Substances 0.000 claims abstract description 36
- 230000001575 pathological effect Effects 0.000 claims abstract description 28
- 238000003384 imaging method Methods 0.000 claims abstract description 26
- 206010002022 amyloidosis Diseases 0.000 claims abstract description 24
- 125000000217 alkyl group Chemical group 0.000 claims description 78
- 229910052739 hydrogen Inorganic materials 0.000 claims description 55
- 239000001257 hydrogen Substances 0.000 claims description 55
- 229960000367 inositol Drugs 0.000 claims description 42
- CDAISMWEOUEBRE-UHFFFAOYSA-N scyllo-inosotol Natural products OC1C(O)C(O)C(O)C(O)C1O CDAISMWEOUEBRE-UHFFFAOYSA-N 0.000 claims description 38
- 125000004435 hydrogen atom Chemical class [H]* 0.000 claims description 37
- 125000003118 aryl group Chemical group 0.000 claims description 31
- 150000003839 salts Chemical class 0.000 claims description 27
- 239000003937 drug carrier Substances 0.000 claims description 22
- 125000000753 cycloalkyl group Chemical group 0.000 claims description 21
- 125000003545 alkoxy group Chemical group 0.000 claims description 20
- 125000003710 aryl alkyl group Chemical group 0.000 claims description 20
- WQZGKKKJIJFFOK-GASJEMHNSA-N Glucose Natural products OC[C@H]1OC(O)[C@H](O)[C@@H](O)[C@@H]1O WQZGKKKJIJFFOK-GASJEMHNSA-N 0.000 claims description 16
- WQZGKKKJIJFFOK-VFUOTHLCSA-N beta-D-glucose Chemical compound OC[C@H]1O[C@@H](O)[C@H](O)[C@@H](O)[C@@H]1O WQZGKKKJIJFFOK-VFUOTHLCSA-N 0.000 claims description 16
- 125000001072 heteroaryl group Chemical group 0.000 claims description 16
- 125000004104 aryloxy group Chemical group 0.000 claims description 15
- 125000005553 heteroaryloxy group Chemical group 0.000 claims description 15
- CDAISMWEOUEBRE-GPIVLXJGSA-N inositol Chemical compound O[C@H]1[C@H](O)[C@@H](O)[C@H](O)[C@H](O)[C@@H]1O CDAISMWEOUEBRE-GPIVLXJGSA-N 0.000 claims description 14
- 125000002102 aryl alkyloxo group Chemical group 0.000 claims description 11
- SQUHHTBVTRBESD-UHFFFAOYSA-N Hexa-Ac-myo-Inositol Natural products CC(=O)OC1C(OC(C)=O)C(OC(C)=O)C(OC(C)=O)C(OC(C)=O)C1OC(C)=O SQUHHTBVTRBESD-UHFFFAOYSA-N 0.000 claims description 10
- 239000008103 glucose Substances 0.000 claims description 9
- 125000004475 heteroaralkyl group Chemical group 0.000 claims description 9
- 229910052794 bromium Inorganic materials 0.000 claims description 7
- 239000008194 pharmaceutical composition Substances 0.000 claims description 7
- 230000007505 plaque formation Effects 0.000 claims description 6
- 125000004404 heteroalkyl group Chemical group 0.000 claims description 5
- 125000000592 heterocycloalkyl group Chemical group 0.000 claims description 5
- 150000002016 disaccharides Chemical class 0.000 claims description 2
- 125000001475 halogen functional group Chemical group 0.000 claims 2
- 125000004356 hydroxy functional group Chemical group O* 0.000 claims 2
- 239000000470 constituent Substances 0.000 claims 1
- 239000012216 imaging agent Substances 0.000 abstract description 40
- 208000037259 Amyloid Plaque Diseases 0.000 abstract description 23
- 238000003745 diagnosis Methods 0.000 abstract description 9
- 238000009825 accumulation Methods 0.000 abstract description 8
- 238000009826 distribution Methods 0.000 abstract description 7
- 239000003814 drug Substances 0.000 abstract description 3
- 229940124597 therapeutic agent Drugs 0.000 abstract description 3
- 238000002603 single-photon emission computed tomography Methods 0.000 abstract 1
- 230000015572 biosynthetic process Effects 0.000 description 57
- 239000000243 solution Substances 0.000 description 57
- 238000003786 synthesis reaction Methods 0.000 description 57
- -1 amino, nitro, sulfhydryl Chemical group 0.000 description 46
- OKKJLVBELUTLKV-UHFFFAOYSA-N Methanol Chemical compound OC OKKJLVBELUTLKV-UHFFFAOYSA-N 0.000 description 43
- YMWUJEATGCHHMB-UHFFFAOYSA-N Dichloromethane Chemical compound ClCCl YMWUJEATGCHHMB-UHFFFAOYSA-N 0.000 description 36
- LFQSCWFLJHTTHZ-UHFFFAOYSA-N Ethanol Chemical compound CCO LFQSCWFLJHTTHZ-UHFFFAOYSA-N 0.000 description 30
- XLYOFNOQVPJJNP-UHFFFAOYSA-N water Substances O XLYOFNOQVPJJNP-UHFFFAOYSA-N 0.000 description 27
- RTZKZFJDLAIYFH-UHFFFAOYSA-N Diethyl ether Chemical compound CCOCC RTZKZFJDLAIYFH-UHFFFAOYSA-N 0.000 description 25
- ZMANZCXQSJIPKH-UHFFFAOYSA-N Triethylamine Chemical compound CCN(CC)CC ZMANZCXQSJIPKH-UHFFFAOYSA-N 0.000 description 24
- 125000001797 benzyl group Chemical group [H]C1=C([H])C([H])=C(C([H])=C1[H])C([H])([H])* 0.000 description 23
- 210000004556 brain Anatomy 0.000 description 23
- 230000008685 targeting Effects 0.000 description 23
- UFHFLCQGNIYNRP-UHFFFAOYSA-N Hydrogen Chemical compound [H][H] UFHFLCQGNIYNRP-UHFFFAOYSA-N 0.000 description 22
- WODIALSWFWKWMM-UHFFFAOYSA-N 2,8-diazaspiro[4.5]decane-1,3-dione Chemical compound O=C1NC(=O)CC11CCNCC1 WODIALSWFWKWMM-UHFFFAOYSA-N 0.000 description 21
- 125000000623 heterocyclic group Chemical group 0.000 description 19
- UHOVQNZJYSORNB-UHFFFAOYSA-N Benzene Chemical compound C1=CC=CC=C1 UHOVQNZJYSORNB-UHFFFAOYSA-N 0.000 description 18
- 125000003342 alkenyl group Chemical group 0.000 description 18
- VYPSYNLAJGMNEJ-UHFFFAOYSA-N Silicium dioxide Chemical compound O=[Si]=O VYPSYNLAJGMNEJ-UHFFFAOYSA-N 0.000 description 17
- JUJWROOIHBZHMG-UHFFFAOYSA-N Pyridine Chemical compound C1=CC=NC=C1 JUJWROOIHBZHMG-UHFFFAOYSA-N 0.000 description 16
- 239000002904 solvent Substances 0.000 description 16
- 125000001424 substituent group Chemical group 0.000 description 16
- 239000011541 reaction mixture Substances 0.000 description 15
- HEDRZPFGACZZDS-UHFFFAOYSA-N Chloroform Chemical compound ClC(Cl)Cl HEDRZPFGACZZDS-UHFFFAOYSA-N 0.000 description 14
- 125000000304 alkynyl group Chemical group 0.000 description 14
- 238000006243 chemical reaction Methods 0.000 description 14
- 239000000047 product Substances 0.000 description 14
- QTBSBXVTEAMEQO-UHFFFAOYSA-N Acetic acid Chemical compound CC(O)=O QTBSBXVTEAMEQO-UHFFFAOYSA-N 0.000 description 13
- 230000032683 aging Effects 0.000 description 13
- 239000000741 silica gel Substances 0.000 description 13
- 229910002027 silica gel Inorganic materials 0.000 description 13
- 239000007787 solid Substances 0.000 description 13
- 125000000472 sulfonyl group Chemical group *S(*)(=O)=O 0.000 description 13
- WEVYAHXRMPXWCK-UHFFFAOYSA-N Acetonitrile Chemical compound CC#N WEVYAHXRMPXWCK-UHFFFAOYSA-N 0.000 description 12
- IJGRMHOSHXDMSA-UHFFFAOYSA-N Atomic nitrogen Chemical compound N#N IJGRMHOSHXDMSA-UHFFFAOYSA-N 0.000 description 12
- 238000013459 approach Methods 0.000 description 12
- 125000005843 halogen group Chemical group 0.000 description 12
- 125000002887 hydroxy group Chemical group [H]O* 0.000 description 12
- VLKZOEOYAKHREP-UHFFFAOYSA-N n-Hexane Chemical class CCCCCC VLKZOEOYAKHREP-UHFFFAOYSA-N 0.000 description 12
- 238000002360 preparation method Methods 0.000 description 12
- 125000002924 primary amino group Chemical group [H]N([H])* 0.000 description 12
- JOXIMZWYDAKGHI-UHFFFAOYSA-N toluene-4-sulfonic acid Chemical compound CC1=CC=C(S(O)(=O)=O)C=C1 JOXIMZWYDAKGHI-UHFFFAOYSA-N 0.000 description 12
- 239000012267 brine Substances 0.000 description 11
- 125000004093 cyano group Chemical group *C#N 0.000 description 11
- 230000000694 effects Effects 0.000 description 11
- 239000000706 filtrate Substances 0.000 description 11
- 125000001181 organosilyl group Chemical group [SiH3]* 0.000 description 11
- ACVYVLVWPXVTIT-UHFFFAOYSA-M phosphinate Chemical compound [O-][PH2]=O ACVYVLVWPXVTIT-UHFFFAOYSA-M 0.000 description 11
- 229910000104 sodium hydride Inorganic materials 0.000 description 11
- HPALAKNZSZLMCH-UHFFFAOYSA-M sodium;chloride;hydrate Chemical compound O.[Na+].[Cl-] HPALAKNZSZLMCH-UHFFFAOYSA-M 0.000 description 11
- KBHCPIJKJQNHPN-UHFFFAOYSA-N N=NP(O)=O Chemical compound N=NP(O)=O KBHCPIJKJQNHPN-UHFFFAOYSA-N 0.000 description 10
- KRHYYFGTRYWZRS-BJUDXGSMSA-N ac1l2y5h Chemical compound [18FH] KRHYYFGTRYWZRS-BJUDXGSMSA-N 0.000 description 10
- 125000004442 acylamino group Chemical group 0.000 description 10
- 125000003282 alkyl amino group Chemical group 0.000 description 10
- 125000003178 carboxy group Chemical group [H]OC(*)=O 0.000 description 10
- 238000003818 flash chromatography Methods 0.000 description 10
- 108090000623 proteins and genes Proteins 0.000 description 10
- 125000005420 sulfonamido group Chemical group S(=O)(=O)(N*)* 0.000 description 10
- 125000004423 acyloxy group Chemical group 0.000 description 9
- 125000001769 aryl amino group Chemical group 0.000 description 9
- OAYLNYINCPYISS-UHFFFAOYSA-N ethyl acetate;hexane Chemical compound CCCCCC.CCOC(C)=O OAYLNYINCPYISS-UHFFFAOYSA-N 0.000 description 9
- 125000002485 formyl group Chemical group [H]C(*)=O 0.000 description 9
- 125000005241 heteroarylamino group Chemical group 0.000 description 9
- 125000002462 isocyano group Chemical group *[N+]#[C-] 0.000 description 9
- 125000005740 oxycarbonyl group Chemical group [*:1]OC([*:2])=O 0.000 description 9
- 102000004169 proteins and genes Human genes 0.000 description 9
- 150000003568 thioethers Chemical group 0.000 description 9
- UIHKDOBBVHGTAQ-UHFFFAOYSA-N 2-ethyl-8-methyl-2,8-diazaspiro[4.5]decane-1,3-dione Chemical class O=C1N(CC)C(=O)CC11CCN(C)CC1 UIHKDOBBVHGTAQ-UHFFFAOYSA-N 0.000 description 8
- 201000010099 disease Diseases 0.000 description 8
- 229910052757 nitrogen Inorganic materials 0.000 description 8
- 238000012636 positron electron tomography Methods 0.000 description 8
- UMJSCPRVCHMLSP-UHFFFAOYSA-N pyridine Natural products COC1=CC=CN=C1 UMJSCPRVCHMLSP-UHFFFAOYSA-N 0.000 description 8
- 239000011734 sodium Substances 0.000 description 8
- 239000000126 substance Substances 0.000 description 8
- 229910052717 sulfur Inorganic materials 0.000 description 8
- 208000014644 Brain disease Diseases 0.000 description 7
- 238000005481 NMR spectroscopy Methods 0.000 description 7
- 206010039966 Senile dementia Diseases 0.000 description 7
- FAPWRFPIFSIZLT-UHFFFAOYSA-M Sodium chloride Chemical compound [Na+].[Cl-] FAPWRFPIFSIZLT-UHFFFAOYSA-M 0.000 description 7
- 125000002252 acyl group Chemical group 0.000 description 7
- 229910052799 carbon Inorganic materials 0.000 description 7
- RMGVZKRVHHSUIM-UHFFFAOYSA-N dithionic acid Chemical group OS(=O)(=O)S(O)(=O)=O RMGVZKRVHHSUIM-UHFFFAOYSA-N 0.000 description 7
- 125000005842 heteroatom Chemical group 0.000 description 7
- 239000010410 layer Substances 0.000 description 7
- 210000000056 organ Anatomy 0.000 description 7
- 229910052760 oxygen Inorganic materials 0.000 description 7
- 239000001301 oxygen Substances 0.000 description 7
- 229920006395 saturated elastomer Polymers 0.000 description 7
- CDAISMWEOUEBRE-CDRYSYESSA-N scyllo-inositol Chemical compound O[C@H]1[C@H](O)[C@@H](O)[C@H](O)[C@@H](O)[C@@H]1O CDAISMWEOUEBRE-CDRYSYESSA-N 0.000 description 7
- 239000011593 sulfur Substances 0.000 description 7
- 230000001225 therapeutic effect Effects 0.000 description 7
- VHYFNPMBLIVWCW-UHFFFAOYSA-N 4-Dimethylaminopyridine Chemical compound CN(C)C1=CC=NC=C1 VHYFNPMBLIVWCW-UHFFFAOYSA-N 0.000 description 6
- CSCPPACGZOOCGX-UHFFFAOYSA-N Acetone Chemical compound CC(C)=O CSCPPACGZOOCGX-UHFFFAOYSA-N 0.000 description 6
- OKTJSMMVPCPJKN-UHFFFAOYSA-N Carbon Chemical compound [C] OKTJSMMVPCPJKN-UHFFFAOYSA-N 0.000 description 6
- VEXZGXHMUGYJMC-UHFFFAOYSA-N Hydrochloric acid Chemical compound Cl VEXZGXHMUGYJMC-UHFFFAOYSA-N 0.000 description 6
- KFZMGEQAYNKOFK-UHFFFAOYSA-N Isopropanol Chemical compound CC(C)O KFZMGEQAYNKOFK-UHFFFAOYSA-N 0.000 description 6
- HEMHJVSKTPXQMS-UHFFFAOYSA-M Sodium hydroxide Chemical compound [OH-].[Na+] HEMHJVSKTPXQMS-UHFFFAOYSA-M 0.000 description 6
- NINIDFKCEFEMDL-UHFFFAOYSA-N Sulfur Chemical compound [S] NINIDFKCEFEMDL-UHFFFAOYSA-N 0.000 description 6
- 125000004429 atom Chemical group 0.000 description 6
- QVGXLLKOCUKJST-UHFFFAOYSA-N atomic oxygen Chemical compound [O] QVGXLLKOCUKJST-UHFFFAOYSA-N 0.000 description 6
- 125000001153 fluoro group Chemical group F* 0.000 description 6
- 125000003709 fluoroalkyl group Chemical group 0.000 description 6
- 238000004128 high performance liquid chromatography Methods 0.000 description 6
- RAXXELZNTBOGNW-UHFFFAOYSA-N imidazole Natural products C1=CNC=N1 RAXXELZNTBOGNW-UHFFFAOYSA-N 0.000 description 6
- 239000007924 injection Substances 0.000 description 6
- 238000002347 injection Methods 0.000 description 6
- 231100000252 nontoxic Toxicity 0.000 description 6
- 230000003000 nontoxic effect Effects 0.000 description 6
- 239000011780 sodium chloride Substances 0.000 description 6
- 210000001519 tissue Anatomy 0.000 description 6
- 208000023761 AL amyloidosis Diseases 0.000 description 5
- FEWJPZIEWOKRBE-JCYAYHJZSA-L L-tartrate(2-) Chemical compound [O-]C(=O)[C@H](O)[C@@H](O)C([O-])=O FEWJPZIEWOKRBE-JCYAYHJZSA-L 0.000 description 5
- 241000700159 Rattus Species 0.000 description 5
- WYURNTSHIVDZCO-UHFFFAOYSA-N Tetrahydrofuran Chemical compound C1CCOC1 WYURNTSHIVDZCO-UHFFFAOYSA-N 0.000 description 5
- 229960000583 acetic acid Drugs 0.000 description 5
- 125000004414 alkyl thio group Chemical group 0.000 description 5
- 125000000852 azido group Chemical group *N=[N+]=[N-] 0.000 description 5
- 239000002585 base Substances 0.000 description 5
- FATUQANACHZLRT-KMRXSBRUSA-L calcium glucoheptonate Chemical compound [Ca+2].OC[C@@H](O)[C@@H](O)[C@H](O)[C@@H](O)C(O)C([O-])=O.OC[C@@H](O)[C@@H](O)[C@H](O)[C@@H](O)C(O)C([O-])=O FATUQANACHZLRT-KMRXSBRUSA-L 0.000 description 5
- 239000003610 charcoal Substances 0.000 description 5
- 238000001816 cooling Methods 0.000 description 5
- 239000012043 crude product Substances 0.000 description 5
- 238000001914 filtration Methods 0.000 description 5
- 125000001188 haloalkyl group Chemical group 0.000 description 5
- 210000002216 heart Anatomy 0.000 description 5
- 210000003734 kidney Anatomy 0.000 description 5
- 239000002502 liposome Substances 0.000 description 5
- 239000003921 oil Substances 0.000 description 5
- 235000019198 oils Nutrition 0.000 description 5
- 150000002894 organic compounds Chemical class 0.000 description 5
- 125000005010 perfluoroalkyl group Chemical group 0.000 description 5
- 239000000843 powder Substances 0.000 description 5
- 238000000746 purification Methods 0.000 description 5
- 239000000700 radioactive tracer Substances 0.000 description 5
- 238000006467 substitution reaction Methods 0.000 description 5
- 229940095064 tartrate Drugs 0.000 description 5
- 238000004809 thin layer chromatography Methods 0.000 description 5
- NERNEXMEYQFFHU-UHFFFAOYSA-N 1,3-diazaspiro[4.5]decane-2,4-dione Chemical class N1C(=O)NC(=O)C11CCCCC1 NERNEXMEYQFFHU-UHFFFAOYSA-N 0.000 description 4
- CURLTUGMZLYLDI-UHFFFAOYSA-N Carbon dioxide Chemical compound O=C=O CURLTUGMZLYLDI-UHFFFAOYSA-N 0.000 description 4
- FBPFZTCFMRRESA-KVTDHHQDSA-N D-Mannitol Chemical compound OC[C@@H](O)[C@@H](O)[C@H](O)[C@H](O)CO FBPFZTCFMRRESA-KVTDHHQDSA-N 0.000 description 4
- RGHNJXZEOKUKBD-SQOUGZDYSA-M D-gluconate Chemical compound OC[C@@H](O)[C@@H](O)[C@H](O)[C@@H](O)C([O-])=O RGHNJXZEOKUKBD-SQOUGZDYSA-M 0.000 description 4
- XEKOWRVHYACXOJ-UHFFFAOYSA-N Ethyl acetate Chemical compound CCOC(C)=O XEKOWRVHYACXOJ-UHFFFAOYSA-N 0.000 description 4
- YLQBMQCUIZJEEH-UHFFFAOYSA-N Furan Chemical compound C=1C=COC=1 YLQBMQCUIZJEEH-UHFFFAOYSA-N 0.000 description 4
- 102000008100 Human Serum Albumin Human genes 0.000 description 4
- 108091006905 Human Serum Albumin Proteins 0.000 description 4
- 208000005531 Immunoglobulin Light-chain Amyloidosis Diseases 0.000 description 4
- 229930195725 Mannitol Natural products 0.000 description 4
- AFVFQIVMOAPDHO-UHFFFAOYSA-N Methanesulfonic acid Chemical compound CS(O)(=O)=O AFVFQIVMOAPDHO-UHFFFAOYSA-N 0.000 description 4
- 206010028980 Neoplasm Diseases 0.000 description 4
- GLUUGHFHXGJENI-UHFFFAOYSA-N Piperazine Chemical compound C1CNCCN1 GLUUGHFHXGJENI-UHFFFAOYSA-N 0.000 description 4
- 206010036673 Primary amyloidosis Diseases 0.000 description 4
- KYQCOXFCLRTKLS-UHFFFAOYSA-N Pyrazine Chemical compound C1=CN=CC=N1 KYQCOXFCLRTKLS-UHFFFAOYSA-N 0.000 description 4
- KAESVJOAVNADME-UHFFFAOYSA-N Pyrrole Chemical compound C=1C=CNC=1 KAESVJOAVNADME-UHFFFAOYSA-N 0.000 description 4
- YTPLMLYBLZKORZ-UHFFFAOYSA-N Thiophene Chemical compound C=1C=CSC=1 YTPLMLYBLZKORZ-UHFFFAOYSA-N 0.000 description 4
- 125000002723 alicyclic group Chemical group 0.000 description 4
- 125000001931 aliphatic group Chemical group 0.000 description 4
- 230000027455 binding Effects 0.000 description 4
- 210000004369 blood Anatomy 0.000 description 4
- 239000008280 blood Substances 0.000 description 4
- 125000004432 carbon atom Chemical group C* 0.000 description 4
- 238000004587 chromatography analysis Methods 0.000 description 4
- 238000002425 crystallisation Methods 0.000 description 4
- 230000008025 crystallization Effects 0.000 description 4
- JHIVVAPYMSGYDF-UHFFFAOYSA-N cyclohexanone Chemical compound O=C1CCCCC1 JHIVVAPYMSGYDF-UHFFFAOYSA-N 0.000 description 4
- 238000000921 elemental analysis Methods 0.000 description 4
- 150000002148 esters Chemical group 0.000 description 4
- 239000000284 extract Substances 0.000 description 4
- 125000000524 functional group Chemical group 0.000 description 4
- 229940050410 gluconate Drugs 0.000 description 4
- 239000005457 ice water Substances 0.000 description 4
- 210000004185 liver Anatomy 0.000 description 4
- 239000000594 mannitol Substances 0.000 description 4
- 235000010355 mannitol Nutrition 0.000 description 4
- 239000000463 material Substances 0.000 description 4
- 229910052751 metal Inorganic materials 0.000 description 4
- 239000002184 metal Substances 0.000 description 4
- 239000002480 mineral oil Substances 0.000 description 4
- 235000010446 mineral oil Nutrition 0.000 description 4
- 150000007522 mineralic acids Chemical class 0.000 description 4
- 230000007935 neutral effect Effects 0.000 description 4
- 150000007524 organic acids Chemical class 0.000 description 4
- 108020003175 receptors Proteins 0.000 description 4
- 102000005962 receptors Human genes 0.000 description 4
- 238000003756 stirring Methods 0.000 description 4
- 239000000725 suspension Substances 0.000 description 4
- 239000006188 syrup Substances 0.000 description 4
- 235000020357 syrup Nutrition 0.000 description 4
- FPGGTKZVZWFYPV-UHFFFAOYSA-M tetrabutylammonium fluoride Chemical compound [F-].CCCC[N+](CCCC)(CCCC)CCCC FPGGTKZVZWFYPV-UHFFFAOYSA-M 0.000 description 4
- 239000003981 vehicle Substances 0.000 description 4
- NSYOUQLPFSKISU-UHFFFAOYSA-N 1-benzyl-4-(cyanomethyl)piperidine-4-carbonitrile Chemical compound C1CC(CC#N)(C#N)CCN1CC1=CC=CC=C1 NSYOUQLPFSKISU-UHFFFAOYSA-N 0.000 description 3
- FJCPWUDGNYOGQR-RUDMXATFSA-N 4-[(e)-2-[6-(2-fluoroethoxy)-1,3-benzoxazol-2-yl]ethenyl]-n-methylaniline Chemical compound C1=CC(NC)=CC=C1\C=C\C1=NC2=CC=C(OCCF)C=C2O1 FJCPWUDGNYOGQR-RUDMXATFSA-N 0.000 description 3
- ZGADWVQZLQNWHP-UHFFFAOYSA-N 8-benzyl-3-oxo-2-aza-8-azoniaspiro[4.5]dec-1-en-1-olate Chemical compound O=C1NC(=O)CC11CCN(CC=2C=CC=CC=2)CC1 ZGADWVQZLQNWHP-UHFFFAOYSA-N 0.000 description 3
- CQYQMFBCMFXOAS-UHFFFAOYSA-N 8-ethyl-2,8-diazaspiro[4.5]decane-1,3-dione Chemical compound C1CN(CC)CCC11C(=O)NC(=O)C1 CQYQMFBCMFXOAS-UHFFFAOYSA-N 0.000 description 3
- 208000023769 AA amyloidosis Diseases 0.000 description 3
- WFDIJRYMOXRFFG-UHFFFAOYSA-N Acetic anhydride Chemical compound CC(=O)OC(C)=O WFDIJRYMOXRFFG-UHFFFAOYSA-N 0.000 description 3
- WVDDGKGOMKODPV-UHFFFAOYSA-N Benzyl alcohol Chemical compound OCC1=CC=CC=C1 WVDDGKGOMKODPV-UHFFFAOYSA-N 0.000 description 3
- 239000004971 Cross linker Substances 0.000 description 3
- 206010012289 Dementia Diseases 0.000 description 3
- 206010016202 Familial Amyloidosis Diseases 0.000 description 3
- WMFOQBRAJBCJND-UHFFFAOYSA-M Lithium hydroxide Chemical compound [Li+].[OH-] WMFOQBRAJBCJND-UHFFFAOYSA-M 0.000 description 3
- 241000124008 Mammalia Species 0.000 description 3
- 239000012359 Methanesulfonyl chloride Substances 0.000 description 3
- 238000012879 PET imaging Methods 0.000 description 3
- KDLHZDBZIXYQEI-UHFFFAOYSA-N Palladium on carbon Substances [Pd] KDLHZDBZIXYQEI-UHFFFAOYSA-N 0.000 description 3
- PCNDJXKNXGMECE-UHFFFAOYSA-N Phenazine Natural products C1=CC=CC2=NC3=CC=CC=C3N=C21 PCNDJXKNXGMECE-UHFFFAOYSA-N 0.000 description 3
- CZPWVGJYEJSRLH-UHFFFAOYSA-N Pyrimidine Chemical compound C1=CN=CN=C1 CZPWVGJYEJSRLH-UHFFFAOYSA-N 0.000 description 3
- RWRDLPDLKQPQOW-UHFFFAOYSA-N Pyrrolidine Chemical compound C1CCNC1 RWRDLPDLKQPQOW-UHFFFAOYSA-N 0.000 description 3
- 206010039811 Secondary amyloidosis Diseases 0.000 description 3
- KEAYESYHFKHZAL-UHFFFAOYSA-N Sodium Chemical compound [Na] KEAYESYHFKHZAL-UHFFFAOYSA-N 0.000 description 3
- YXFVVABEGXRONW-UHFFFAOYSA-N Toluene Chemical compound CC1=CC=CC=C1 YXFVVABEGXRONW-UHFFFAOYSA-N 0.000 description 3
- 239000002253 acid Substances 0.000 description 3
- 230000002378 acidificating effect Effects 0.000 description 3
- 239000002671 adjuvant Substances 0.000 description 3
- 150000001412 amines Chemical class 0.000 description 3
- XSCHRSMBECNVNS-UHFFFAOYSA-N benzopyrazine Natural products N1=CC=NC2=CC=CC=C21 XSCHRSMBECNVNS-UHFFFAOYSA-N 0.000 description 3
- AGEZXYOZHKGVCM-UHFFFAOYSA-N benzyl bromide Chemical compound BrCC1=CC=CC=C1 AGEZXYOZHKGVCM-UHFFFAOYSA-N 0.000 description 3
- 210000005013 brain tissue Anatomy 0.000 description 3
- 125000003917 carbamoyl group Chemical group [H]N([H])C(*)=O 0.000 description 3
- 229960004424 carbon dioxide Drugs 0.000 description 3
- 235000011089 carbon dioxide Nutrition 0.000 description 3
- 150000007942 carboxylates Chemical group 0.000 description 3
- 125000004122 cyclic group Chemical group 0.000 description 3
- 239000002552 dosage form Substances 0.000 description 3
- 238000001035 drying Methods 0.000 description 3
- 238000010828 elution Methods 0.000 description 3
- 229910052736 halogen Inorganic materials 0.000 description 3
- 150000002367 halogens Chemical class 0.000 description 3
- 208000017105 hereditary amyloidosis Diseases 0.000 description 3
- 238000001727 in vivo Methods 0.000 description 3
- 238000002372 labelling Methods 0.000 description 3
- 238000004519 manufacturing process Methods 0.000 description 3
- QARBMVPHQWIHKH-UHFFFAOYSA-N methanesulfonyl chloride Chemical compound CS(Cl)(=O)=O QARBMVPHQWIHKH-UHFFFAOYSA-N 0.000 description 3
- 125000001570 methylene group Chemical group [H]C([H])([*:1])[*:2] 0.000 description 3
- 125000004170 methylsulfonyl group Chemical group [H]C([H])([H])S(*)(=O)=O 0.000 description 3
- 239000000472 muscarinic agonist Substances 0.000 description 3
- SAVQQRYWWAGSQW-UHFFFAOYSA-N n-methyl-n-(trifluoro-$l^{4}-sulfanyl)methanamine Chemical compound CN(C)S(F)(F)F SAVQQRYWWAGSQW-UHFFFAOYSA-N 0.000 description 3
- 238000009206 nuclear medicine Methods 0.000 description 3
- 238000011160 research Methods 0.000 description 3
- 230000004044 response Effects 0.000 description 3
- 239000000523 sample Substances 0.000 description 3
- 239000012312 sodium hydride Substances 0.000 description 3
- BDHFUVZGWQCTTF-UHFFFAOYSA-M sulfonate Chemical compound [O-]S(=O)=O BDHFUVZGWQCTTF-UHFFFAOYSA-M 0.000 description 3
- 238000012360 testing method Methods 0.000 description 3
- 125000001889 triflyl group Chemical group FC(F)(F)S(*)(=O)=O 0.000 description 3
- JTLAIKFGRHDNQM-UHFFFAOYSA-N 1-bromo-2-fluoroethane Chemical compound FCCBr JTLAIKFGRHDNQM-UHFFFAOYSA-N 0.000 description 2
- DFMOYZCKOYEADZ-UHFFFAOYSA-N 1-bromo-2-fluoropropane Chemical compound CC(F)CBr DFMOYZCKOYEADZ-UHFFFAOYSA-N 0.000 description 2
- WEGOLYBUWCMMMY-UHFFFAOYSA-N 1-bromo-2-propanol Chemical compound CC(O)CBr WEGOLYBUWCMMMY-UHFFFAOYSA-N 0.000 description 2
- HZAXFHJVJLSVMW-UHFFFAOYSA-N 2-Aminoethan-1-ol Chemical compound NCCO HZAXFHJVJLSVMW-UHFFFAOYSA-N 0.000 description 2
- IZCVLYJVVCABBV-UHFFFAOYSA-N 2-hydrazinylpyridine-3-carboxylic acid Chemical group NNC1=NC=CC=C1C(O)=O IZCVLYJVVCABBV-UHFFFAOYSA-N 0.000 description 2
- VQNWAWRYJQHLAV-UHFFFAOYSA-N 3,4,5,6-tetrakis(phenylmethoxy)cyclohexane-1,2-diol Chemical compound C=1C=CC=CC=1COC1C(OCC=2C=CC=CC=2)C(OCC=2C=CC=CC=2)C(O)C(O)C1OCC1=CC=CC=C1 VQNWAWRYJQHLAV-UHFFFAOYSA-N 0.000 description 2
- 125000004080 3-carboxypropanoyl group Chemical group O=C([*])C([H])([H])C([H])([H])C(O[H])=O 0.000 description 2
- 229960000549 4-dimethylaminophenol Drugs 0.000 description 2
- KDCGOANMDULRCW-UHFFFAOYSA-N 7H-purine Chemical compound N1=CNC2=NC=NC2=C1 KDCGOANMDULRCW-UHFFFAOYSA-N 0.000 description 2
- HBAQYPYDRFILMT-UHFFFAOYSA-N 8-[3-(1-cyclopropylpyrazol-4-yl)-1H-pyrazolo[4,3-d]pyrimidin-5-yl]-3-methyl-3,8-diazabicyclo[3.2.1]octan-2-one Chemical class C1(CC1)N1N=CC(=C1)C1=NNC2=C1N=C(N=C2)N1C2C(N(CC1CC2)C)=O HBAQYPYDRFILMT-UHFFFAOYSA-N 0.000 description 2
- UJOBWOGCFQCDNV-UHFFFAOYSA-N 9H-carbazole Chemical compound C1=CC=C2C3=CC=CC=C3NC2=C1 UJOBWOGCFQCDNV-UHFFFAOYSA-N 0.000 description 2
- QGZKDVFQNNGYKY-UHFFFAOYSA-N Ammonia Chemical compound N QGZKDVFQNNGYKY-UHFFFAOYSA-N 0.000 description 2
- 208000003808 Amyloid Neuropathies Diseases 0.000 description 2
- 102000009091 Amyloidogenic Proteins Human genes 0.000 description 2
- 108010048112 Amyloidogenic Proteins Proteins 0.000 description 2
- IAZDPXIOMUYVGZ-WFGJKAKNSA-N Dimethyl sulfoxide Chemical compound [2H]C([2H])([2H])S(=O)C([2H])([2H])[2H] IAZDPXIOMUYVGZ-WFGJKAKNSA-N 0.000 description 2
- IAZDPXIOMUYVGZ-UHFFFAOYSA-N Dimethylsulphoxide Chemical compound CS(C)=O IAZDPXIOMUYVGZ-UHFFFAOYSA-N 0.000 description 2
- QUSNBJAOOMFDIB-UHFFFAOYSA-N Ethylamine Chemical compound CCN QUSNBJAOOMFDIB-UHFFFAOYSA-N 0.000 description 2
- 208000002339 Frontotemporal Lobar Degeneration Diseases 0.000 description 2
- 201000011240 Frontotemporal dementia Diseases 0.000 description 2
- PEDCQBHIVMGVHV-UHFFFAOYSA-N Glycerine Chemical compound OCC(O)CO PEDCQBHIVMGVHV-UHFFFAOYSA-N 0.000 description 2
- OAKJQQAXSVQMHS-UHFFFAOYSA-N Hydrazine Chemical compound NN OAKJQQAXSVQMHS-UHFFFAOYSA-N 0.000 description 2
- SIKJAQJRHWYJAI-UHFFFAOYSA-N Indole Chemical compound C1=CC=C2NC=CC2=C1 SIKJAQJRHWYJAI-UHFFFAOYSA-N 0.000 description 2
- YNAVUWVOSKDBBP-UHFFFAOYSA-N Morpholine Chemical compound C1COCCN1 YNAVUWVOSKDBBP-UHFFFAOYSA-N 0.000 description 2
- UFWIBTONFRDIAS-UHFFFAOYSA-N Naphthalene Chemical compound C1=CC=CC2=CC=CC=C21 UFWIBTONFRDIAS-UHFFFAOYSA-N 0.000 description 2
- CTQNGGLPUBDAKN-UHFFFAOYSA-N O-Xylene Chemical compound CC1=CC=CC=C1C CTQNGGLPUBDAKN-UHFFFAOYSA-N 0.000 description 2
- ZCQWOFVYLHDMMC-UHFFFAOYSA-N Oxazole Chemical compound C1=COC=N1 ZCQWOFVYLHDMMC-UHFFFAOYSA-N 0.000 description 2
- 229910019142 PO4 Inorganic materials 0.000 description 2
- ISWSIDIOOBJBQZ-UHFFFAOYSA-N Phenol Chemical compound OC1=CC=CC=C1 ISWSIDIOOBJBQZ-UHFFFAOYSA-N 0.000 description 2
- NQRYJNQNLNOLGT-UHFFFAOYSA-N Piperidine Chemical compound C1CCNCC1 NQRYJNQNLNOLGT-UHFFFAOYSA-N 0.000 description 2
- 206010035226 Plasma cell myeloma Diseases 0.000 description 2
- WTKZEGDFNFYCGP-UHFFFAOYSA-N Pyrazole Chemical compound C=1C=NNC=1 WTKZEGDFNFYCGP-UHFFFAOYSA-N 0.000 description 2
- SMWDFEZZVXVKRB-UHFFFAOYSA-N Quinoline Chemical compound N1=CC=CC2=CC=CC=C21 SMWDFEZZVXVKRB-UHFFFAOYSA-N 0.000 description 2
- 239000008156 Ringer's lactate solution Substances 0.000 description 2
- UIIMBOGNXHQVGW-UHFFFAOYSA-M Sodium bicarbonate Chemical compound [Na+].OC([O-])=O UIIMBOGNXHQVGW-UHFFFAOYSA-M 0.000 description 2
- QAOWNCQODCNURD-UHFFFAOYSA-L Sulfate Chemical compound [O-]S([O-])(=O)=O QAOWNCQODCNURD-UHFFFAOYSA-L 0.000 description 2
- QAOWNCQODCNURD-UHFFFAOYSA-N Sulfuric acid Chemical compound OS(O)(=O)=O QAOWNCQODCNURD-UHFFFAOYSA-N 0.000 description 2
- DZBUGLKDJFMEHC-UHFFFAOYSA-N acridine Chemical compound C1=CC=CC2=CC3=CC=CC=C3N=C21 DZBUGLKDJFMEHC-UHFFFAOYSA-N 0.000 description 2
- 210000004100 adrenal gland Anatomy 0.000 description 2
- 150000001299 aldehydes Chemical group 0.000 description 2
- 125000002947 alkylene group Chemical group 0.000 description 2
- 125000003368 amide group Chemical group 0.000 description 2
- 150000001408 amides Chemical class 0.000 description 2
- MWPLVEDNUUSJAV-UHFFFAOYSA-N anthracene Chemical compound C1=CC=CC2=CC3=CC=CC=C3C=C21 MWPLVEDNUUSJAV-UHFFFAOYSA-N 0.000 description 2
- 230000000844 anti-bacterial effect Effects 0.000 description 2
- 229940121375 antifungal agent Drugs 0.000 description 2
- 239000003429 antifungal agent Substances 0.000 description 2
- 230000008901 benefit Effects 0.000 description 2
- WPYMKLBDIGXBTP-UHFFFAOYSA-N benzoic acid Chemical compound OC(=O)C1=CC=CC=C1 WPYMKLBDIGXBTP-UHFFFAOYSA-N 0.000 description 2
- 210000004204 blood vessel Anatomy 0.000 description 2
- 210000000988 bone and bone Anatomy 0.000 description 2
- 239000000872 buffer Substances 0.000 description 2
- 239000006227 byproduct Substances 0.000 description 2
- 201000011510 cancer Diseases 0.000 description 2
- 150000001720 carbohydrates Chemical class 0.000 description 2
- 235000014633 carbohydrates Nutrition 0.000 description 2
- 125000002915 carbonyl group Chemical group [*:2]C([*:1])=O 0.000 description 2
- 239000000969 carrier Substances 0.000 description 2
- OSASVXMJTNOKOY-UHFFFAOYSA-N chlorobutanol Chemical compound CC(C)(O)C(Cl)(Cl)Cl OSASVXMJTNOKOY-UHFFFAOYSA-N 0.000 description 2
- 229960001231 choline Drugs 0.000 description 2
- 229940125898 compound 5 Drugs 0.000 description 2
- 125000000392 cycloalkenyl group Chemical group 0.000 description 2
- 239000003599 detergent Substances 0.000 description 2
- 238000011161 development Methods 0.000 description 2
- 230000018109 developmental process Effects 0.000 description 2
- CSJLBAMHHLJAAS-UHFFFAOYSA-N diethylaminosulfur trifluoride Chemical compound CCN(CC)S(F)(F)F CSJLBAMHHLJAAS-UHFFFAOYSA-N 0.000 description 2
- 239000003085 diluting agent Substances 0.000 description 2
- 239000000839 emulsion Substances 0.000 description 2
- 239000002532 enzyme inhibitor Substances 0.000 description 2
- ZIUSEGSNTOUIPT-UHFFFAOYSA-N ethyl 2-cyanoacetate Chemical compound CCOC(=O)CC#N ZIUSEGSNTOUIPT-UHFFFAOYSA-N 0.000 description 2
- 239000007850 fluorescent dye Substances 0.000 description 2
- 235000019000 fluorine Nutrition 0.000 description 2
- 229910052731 fluorine Inorganic materials 0.000 description 2
- 238000009472 formulation Methods 0.000 description 2
- 239000012362 glacial acetic acid Substances 0.000 description 2
- 150000002430 hydrocarbons Chemical class 0.000 description 2
- 238000011065 in-situ storage Methods 0.000 description 2
- 239000003112 inhibitor Substances 0.000 description 2
- 239000002198 insoluble material Substances 0.000 description 2
- 238000010253 intravenous injection Methods 0.000 description 2
- 229910052740 iodine Inorganic materials 0.000 description 2
- AWJUIBRHMBBTKR-UHFFFAOYSA-N isoquinoline Chemical compound C1=NC=CC2=CC=CC=C21 AWJUIBRHMBBTKR-UHFFFAOYSA-N 0.000 description 2
- 239000007951 isotonicity adjuster Substances 0.000 description 2
- 150000002576 ketones Chemical class 0.000 description 2
- 239000007788 liquid Substances 0.000 description 2
- 210000004072 lung Anatomy 0.000 description 2
- 239000003550 marker Substances 0.000 description 2
- 230000004048 modification Effects 0.000 description 2
- 238000012986 modification Methods 0.000 description 2
- 239000002808 molecular sieve Substances 0.000 description 2
- SQDFHQJTAWCFIB-UHFFFAOYSA-N n-methylidenehydroxylamine Chemical compound ON=C SQDFHQJTAWCFIB-UHFFFAOYSA-N 0.000 description 2
- 230000004770 neurodegeneration Effects 0.000 description 2
- 125000005151 nonafluorobutanesulfonyl group Chemical group FC(C(C(S(=O)(=O)*)(F)F)(F)F)(C(F)(F)F)F 0.000 description 2
- 239000012044 organic layer Substances 0.000 description 2
- 150000002923 oximes Chemical class 0.000 description 2
- 125000004430 oxygen atom Chemical group O* 0.000 description 2
- 239000003208 petroleum Substances 0.000 description 2
- RDOWQLZANAYVLL-UHFFFAOYSA-N phenanthridine Chemical compound C1=CC=C2C3=CC=CC=C3C=NC2=C1 RDOWQLZANAYVLL-UHFFFAOYSA-N 0.000 description 2
- NBIIXXVUZAFLBC-UHFFFAOYSA-K phosphate Chemical compound [O-]P([O-])([O-])=O NBIIXXVUZAFLBC-UHFFFAOYSA-K 0.000 description 2
- 239000010452 phosphate Substances 0.000 description 2
- 125000002467 phosphate group Chemical group [H]OP(=O)(O[H])O[*] 0.000 description 2
- 210000004180 plasmocyte Anatomy 0.000 description 2
- BWHMMNNQKKPAPP-UHFFFAOYSA-L potassium carbonate Chemical compound [K+].[K+].[O-]C([O-])=O BWHMMNNQKKPAPP-UHFFFAOYSA-L 0.000 description 2
- NNFCIKHAZHQZJG-UHFFFAOYSA-N potassium cyanide Chemical compound [K+].N#[C-] NNFCIKHAZHQZJG-UHFFFAOYSA-N 0.000 description 2
- 239000003755 preservative agent Substances 0.000 description 2
- 230000008569 process Effects 0.000 description 2
- BBEAQIROQSPTKN-UHFFFAOYSA-N pyrene Chemical compound C1=CC=C2C=CC3=CC=CC4=CC=C1C2=C43 BBEAQIROQSPTKN-UHFFFAOYSA-N 0.000 description 2
- PBMFSQRYOILNGV-UHFFFAOYSA-N pyridazine Chemical compound C1=CC=NN=C1 PBMFSQRYOILNGV-UHFFFAOYSA-N 0.000 description 2
- 230000002285 radioactive effect Effects 0.000 description 2
- 238000010992 reflux Methods 0.000 description 2
- 230000002441 reversible effect Effects 0.000 description 2
- URGAHOPLAPQHLN-UHFFFAOYSA-N sodium aluminosilicate Chemical compound [Na+].[Al+3].[O-][Si]([O-])=O.[O-][Si]([O-])=O URGAHOPLAPQHLN-UHFFFAOYSA-N 0.000 description 2
- 210000000952 spleen Anatomy 0.000 description 2
- 239000003381 stabilizer Substances 0.000 description 2
- 210000002784 stomach Anatomy 0.000 description 2
- 125000000020 sulfo group Chemical group O=S(=O)([*])O[H] 0.000 description 2
- 208000024891 symptom Diseases 0.000 description 2
- 230000009885 systemic effect Effects 0.000 description 2
- 238000002560 therapeutic procedure Methods 0.000 description 2
- 229930192474 thiophene Natural products 0.000 description 2
- 238000003325 tomography Methods 0.000 description 2
- VZCYOOQTPOCHFL-UHFFFAOYSA-N trans-butenedioic acid Natural products OC(=O)C=CC(O)=O VZCYOOQTPOCHFL-UHFFFAOYSA-N 0.000 description 2
- 125000002023 trifluoromethyl group Chemical group FC(F)(F)* 0.000 description 2
- QZZYPHBVOQMBAT-LRAGLOQXSA-N (2s)-2-amino-3-[4-(2-fluoranylethoxy)phenyl]propanoic acid Chemical compound OC(=O)[C@@H](N)CC1=CC=C(OCC[18F])C=C1 QZZYPHBVOQMBAT-LRAGLOQXSA-N 0.000 description 1
- CEGXZKXILQSJHO-KODRXGBYSA-N (3r,4s,5r)-3,4,5,6-tetrahydroxyhexanoyl fluoride Chemical compound OC[C@@H](O)[C@@H](O)[C@H](O)CC(F)=O CEGXZKXILQSJHO-KODRXGBYSA-N 0.000 description 1
- FFJCNSLCJOQHKM-CLFAGFIQSA-N (z)-1-[(z)-octadec-9-enoxy]octadec-9-ene Chemical compound CCCCCCCC\C=C/CCCCCCCCOCCCCCCCC\C=C/CCCCCCCC FFJCNSLCJOQHKM-CLFAGFIQSA-N 0.000 description 1
- 150000005207 1,3-dihydroxybenzenes Chemical class 0.000 description 1
- BDNKZNFMNDZQMI-UHFFFAOYSA-N 1,3-diisopropylcarbodiimide Chemical compound CC(C)N=C=NC(C)C BDNKZNFMNDZQMI-UHFFFAOYSA-N 0.000 description 1
- RYHBNJHYFVUHQT-UHFFFAOYSA-N 1,4-Dioxane Chemical compound C1COCCO1 RYHBNJHYFVUHQT-UHFFFAOYSA-N 0.000 description 1
- FLBAYUMRQUHISI-UHFFFAOYSA-N 1,8-naphthyridine Chemical compound N1=CC=CC2=CC=CN=C21 FLBAYUMRQUHISI-UHFFFAOYSA-N 0.000 description 1
- SJZKULRDWHPHGG-UHFFFAOYSA-N 1-benzylpiperidin-4-one Chemical compound C1CC(=O)CCN1CC1=CC=CC=C1 SJZKULRDWHPHGG-UHFFFAOYSA-N 0.000 description 1
- ZLGXEEAGBLFFTB-UHFFFAOYSA-N 1-bromoethanol Chemical compound CC(O)Br ZLGXEEAGBLFFTB-UHFFFAOYSA-N 0.000 description 1
- LDMOEFOXLIZJOW-UHFFFAOYSA-N 1-dodecanesulfonic acid Chemical class CCCCCCCCCCCCS(O)(=O)=O LDMOEFOXLIZJOW-UHFFFAOYSA-N 0.000 description 1
- HUUPVABNAQUEJW-UHFFFAOYSA-N 1-methylpiperidin-4-one Chemical compound CN1CCC(=O)CC1 HUUPVABNAQUEJW-UHFFFAOYSA-N 0.000 description 1
- WJFKNYWRSNBZNX-UHFFFAOYSA-N 10H-phenothiazine Chemical compound C1=CC=C2NC3=CC=CC=C3SC2=C1 WJFKNYWRSNBZNX-UHFFFAOYSA-N 0.000 description 1
- TZMSYXZUNZXBOL-UHFFFAOYSA-N 10H-phenoxazine Chemical compound C1=CC=C2NC3=CC=CC=C3OC2=C1 TZMSYXZUNZXBOL-UHFFFAOYSA-N 0.000 description 1
- 238000005160 1H NMR spectroscopy Methods 0.000 description 1
- BAXOFTOLAUCFNW-UHFFFAOYSA-N 1H-indazole Chemical compound C1=CC=C2C=NNC2=C1 BAXOFTOLAUCFNW-UHFFFAOYSA-N 0.000 description 1
- VEPOHXYIFQMVHW-XOZOLZJESA-N 2,3-dihydroxybutanedioic acid (2S,3S)-3,4-dimethyl-2-phenylmorpholine Chemical compound OC(C(O)C(O)=O)C(O)=O.C[C@H]1[C@@H](OCCN1C)c1ccccc1 VEPOHXYIFQMVHW-XOZOLZJESA-N 0.000 description 1
- PIQNVMHJTZPSSL-UHFFFAOYSA-N 2-(1-benzylpiperidin-4-ylidene)-2-cyanoacetic acid Chemical compound C1CC(=C(C#N)C(=O)O)CCN1CC1=CC=CC=C1 PIQNVMHJTZPSSL-UHFFFAOYSA-N 0.000 description 1
- IPRAKAXWBDSOCW-UHFFFAOYSA-N 2-(2-fluoroethyl)-8-methyl-2,8-diazaspiro[4.5]decane-1,3-dione Chemical compound C1CN(C)CCC11C(=O)N(CCF)C(=O)C1 IPRAKAXWBDSOCW-UHFFFAOYSA-N 0.000 description 1
- YZTFTTLKACESRX-UHFFFAOYSA-N 2-(2-fluoropropyl)-8-methyl-2,8-diazaspiro[4.5]decane-1,3-dione Chemical compound O=C1N(CC(F)C)C(=O)CC11CCN(C)CC1 YZTFTTLKACESRX-UHFFFAOYSA-N 0.000 description 1
- KPQJUKCKUBVSCI-UHFFFAOYSA-N 2-(2-hydroxyethyl)-8-methyl-2,8-diazaspiro[4.5]decane-1,3-dione Chemical compound C1CN(C)CCC11C(=O)N(CCO)C(=O)C1 KPQJUKCKUBVSCI-UHFFFAOYSA-N 0.000 description 1
- SALHQNSBMLVDCA-UHFFFAOYSA-N 2-(2-hydroxypropyl)-8-methyl-2,8-diazaspiro[4.5]decane-1,3-dione Chemical compound O=C1N(CC(O)C)C(=O)CC11CCN(C)CC1 SALHQNSBMLVDCA-UHFFFAOYSA-N 0.000 description 1
- FALRKNHUBBKYCC-UHFFFAOYSA-N 2-(chloromethyl)pyridine-3-carbonitrile Chemical compound ClCC1=NC=CC=C1C#N FALRKNHUBBKYCC-UHFFFAOYSA-N 0.000 description 1
- ZQAQXZBSGZUUNL-BJUDXGSMSA-N 2-[4-(methylamino)phenyl]-1,3-benzothiazol-6-ol Chemical compound C1=CC(N[11CH3])=CC=C1C1=NC2=CC=C(O)C=C2S1 ZQAQXZBSGZUUNL-BJUDXGSMSA-N 0.000 description 1
- 125000005273 2-acetoxybenzoic acid group Chemical group 0.000 description 1
- UXGVMFHEKMGWMA-UHFFFAOYSA-N 2-benzofuran Chemical compound C1=CC=CC2=COC=C21 UXGVMFHEKMGWMA-UHFFFAOYSA-N 0.000 description 1
- ZYTYMYLZMSCSKF-UHFFFAOYSA-N 2-benzyl-8-ethyl-2,8-diazaspiro[4.5]decane-1,3-dione Chemical compound C1CN(CC)CCC11C(=O)N(CC=2C=CC=CC=2)C(=O)C1 ZYTYMYLZMSCSKF-UHFFFAOYSA-N 0.000 description 1
- LDLCZOVUSADOIV-UHFFFAOYSA-N 2-bromoethanol Chemical compound OCCBr LDLCZOVUSADOIV-UHFFFAOYSA-N 0.000 description 1
- DBTWOTKWIVISQR-UHFFFAOYSA-N 2-bromopropan-1-ol Chemical compound CC(Br)CO DBTWOTKWIVISQR-UHFFFAOYSA-N 0.000 description 1
- AOYNUTHNTBLRMT-SLPGGIOYSA-N 2-deoxy-2-fluoro-aldehydo-D-glucose Chemical compound OC[C@@H](O)[C@@H](O)[C@H](O)[C@@H](F)C=O AOYNUTHNTBLRMT-SLPGGIOYSA-N 0.000 description 1
- OODAUJSHKGCQSF-UHFFFAOYSA-N 2-ethyl-2,8-diazaspiro[4.5]decane-1,3-dione Chemical compound O=C1N(CC)C(=O)CC11CCNCC1 OODAUJSHKGCQSF-UHFFFAOYSA-N 0.000 description 1
- VHMICKWLTGFITH-UHFFFAOYSA-N 2H-isoindole Chemical compound C1=CC=CC2=CNC=C21 VHMICKWLTGFITH-UHFFFAOYSA-N 0.000 description 1
- MGADZUXDNSDTHW-UHFFFAOYSA-N 2H-pyran Chemical compound C1OC=CC=C1 MGADZUXDNSDTHW-UHFFFAOYSA-N 0.000 description 1
- UXWSZFYLVAFLRT-UHFFFAOYSA-N 4-(2-methyl-3h-thiophen-2-yl)pyridine-3-carboxylic acid Chemical group C=1C=NC=C(C(O)=O)C=1C1(C)CC=CS1 UXWSZFYLVAFLRT-UHFFFAOYSA-N 0.000 description 1
- CUDJETOPBQFVER-UHFFFAOYSA-N 4-(3-methylthiophen-2-yl)pyridine-3-carboxylic acid Chemical compound C1=CSC(C=2C(=CN=CC=2)C(O)=O)=C1C CUDJETOPBQFVER-UHFFFAOYSA-N 0.000 description 1
- SKKVBJZDIJEKQV-UHFFFAOYSA-N 4-(carboxymethyl)-1-methylpiperidine-4-carboxylic acid Chemical compound CN1CCC(CC(O)=O)(C(O)=O)CC1 SKKVBJZDIJEKQV-UHFFFAOYSA-N 0.000 description 1
- HVMQILAWPNLEET-UHFFFAOYSA-N 4-(cyanomethyl)-1-methylpiperidine-4-carbonitrile Chemical compound CN1CCC(CC#N)(C#N)CC1 HVMQILAWPNLEET-UHFFFAOYSA-N 0.000 description 1
- QCQCHGYLTSGIGX-GHXANHINSA-N 4-[[(3ar,5ar,5br,7ar,9s,11ar,11br,13as)-5a,5b,8,8,11a-pentamethyl-3a-[(5-methylpyridine-3-carbonyl)amino]-2-oxo-1-propan-2-yl-4,5,6,7,7a,9,10,11,11b,12,13,13a-dodecahydro-3h-cyclopenta[a]chrysen-9-yl]oxy]-2,2-dimethyl-4-oxobutanoic acid Chemical compound N([C@@]12CC[C@@]3(C)[C@]4(C)CC[C@H]5C(C)(C)[C@@H](OC(=O)CC(C)(C)C(O)=O)CC[C@]5(C)[C@H]4CC[C@@H]3C1=C(C(C2)=O)C(C)C)C(=O)C1=CN=CC(C)=C1 QCQCHGYLTSGIGX-GHXANHINSA-N 0.000 description 1
- FJKROLUGYXJWQN-UHFFFAOYSA-N 4-hydroxybenzoic acid Chemical compound OC(=O)C1=CC=C(O)C=C1 FJKROLUGYXJWQN-UHFFFAOYSA-N 0.000 description 1
- GDRVFDDBLLKWRI-UHFFFAOYSA-N 4H-quinolizine Chemical compound C1=CC=CN2CC=CC=C21 GDRVFDDBLLKWRI-UHFFFAOYSA-N 0.000 description 1
- ZCYVEMRRCGMTRW-UHFFFAOYSA-N 7553-56-2 Chemical compound [I] ZCYVEMRRCGMTRW-UHFFFAOYSA-N 0.000 description 1
- IEEGEXBHUQYKQZ-UHFFFAOYSA-N 8-methyl-2,8-diazaspiro[4.5]decane-1,3-dione Chemical compound C1CN(C)CCC11C(=O)NC(=O)C1 IEEGEXBHUQYKQZ-UHFFFAOYSA-N 0.000 description 1
- LEYFYQRCPYQNMR-UHFFFAOYSA-N 8-methyl-2-(2-methylsulfonylethyl)-2,8-diazaspiro[4.5]decane Chemical compound CS(=O)(=O)CCN1CC2(CC1)CCN(CC2)C LEYFYQRCPYQNMR-UHFFFAOYSA-N 0.000 description 1
- JPPRAJKKRRYGDC-UHFFFAOYSA-N 8-methyl-2-(2-methylsulfonylethyl)-2,8-diazaspiro[4.5]decane-1,3-dione Chemical compound C1CN(C)CCC11C(=O)N(CCS(C)(=O)=O)C(=O)C1 JPPRAJKKRRYGDC-UHFFFAOYSA-N 0.000 description 1
- OWKWPVZGKAYIST-UHFFFAOYSA-N 8-methyl-2-(2-methylsulfonylpropyl)-2,8-diazaspiro[4.5]decane Chemical compound CS(=O)(=O)C(CN1CC2(CC1)CCN(CC2)C)C OWKWPVZGKAYIST-UHFFFAOYSA-N 0.000 description 1
- GJCOSYZMQJWQCA-UHFFFAOYSA-N 9H-xanthene Chemical compound C1=CC=C2CC3=CC=CC=C3OC2=C1 GJCOSYZMQJWQCA-UHFFFAOYSA-N 0.000 description 1
- 208000018282 ACys amyloidosis Diseases 0.000 description 1
- QTBSBXVTEAMEQO-UHFFFAOYSA-M Acetate Chemical compound CC([O-])=O QTBSBXVTEAMEQO-UHFFFAOYSA-M 0.000 description 1
- 229940100578 Acetylcholinesterase inhibitor Drugs 0.000 description 1
- 102000009027 Albumins Human genes 0.000 description 1
- 108010088751 Albumins Proteins 0.000 description 1
- GUBGYTABKSRVRQ-XLOQQCSPSA-N Alpha-Lactose Chemical compound O[C@@H]1[C@@H](O)[C@@H](O)[C@@H](CO)O[C@H]1O[C@@H]1[C@@H](CO)O[C@H](O)[C@H](O)[C@H]1O GUBGYTABKSRVRQ-XLOQQCSPSA-N 0.000 description 1
- 208000000044 Amnesia Diseases 0.000 description 1
- 244000144725 Amygdalus communis Species 0.000 description 1
- 235000011437 Amygdalus communis Nutrition 0.000 description 1
- 102000001049 Amyloid Human genes 0.000 description 1
- 108010094108 Amyloid Proteins 0.000 description 1
- 206010002025 Amyloidosis senile Diseases 0.000 description 1
- 108010039627 Aprotinin Proteins 0.000 description 1
- BVKZGUZCCUSVTD-UHFFFAOYSA-M Bicarbonate Chemical compound OC([O-])=O BVKZGUZCCUSVTD-UHFFFAOYSA-M 0.000 description 1
- ZOXJGFHDIHLPTG-UHFFFAOYSA-N Boron Chemical compound [B] ZOXJGFHDIHLPTG-UHFFFAOYSA-N 0.000 description 1
- COVZYZSDYWQREU-UHFFFAOYSA-N Busulfan Chemical compound CS(=O)(=O)OCCCCOS(C)(=O)=O COVZYZSDYWQREU-UHFFFAOYSA-N 0.000 description 1
- FAIFRACTBXWXGY-JTTXIWGLSA-N COc1ccc2C[C@H]3N(C)CC[C@@]45[C@@H](Oc1c24)[C@@]1(OC)C=C[C@@]35C[C@@H]1[C@](C)(O)CCc1ccccc1 Chemical compound COc1ccc2C[C@H]3N(C)CC[C@@]45[C@@H](Oc1c24)[C@@]1(OC)C=C[C@@]35C[C@@H]1[C@](C)(O)CCc1ccccc1 FAIFRACTBXWXGY-JTTXIWGLSA-N 0.000 description 1
- OYPRJOBELJOOCE-UHFFFAOYSA-N Calcium Chemical compound [Ca] OYPRJOBELJOOCE-UHFFFAOYSA-N 0.000 description 1
- BVKZGUZCCUSVTD-UHFFFAOYSA-L Carbonate Chemical compound [O-]C([O-])=O BVKZGUZCCUSVTD-UHFFFAOYSA-L 0.000 description 1
- 206010007509 Cardiac amyloidosis Diseases 0.000 description 1
- 208000005145 Cerebral amyloid angiopathy Diseases 0.000 description 1
- 108010058699 Choline O-acetyltransferase Proteins 0.000 description 1
- 102100023460 Choline O-acetyltransferase Human genes 0.000 description 1
- KRKNYBCHXYNGOX-UHFFFAOYSA-K Citrate Chemical compound [O-]C(=O)CC(O)(CC([O-])=O)C([O-])=O KRKNYBCHXYNGOX-UHFFFAOYSA-K 0.000 description 1
- 208000020406 Creutzfeldt Jacob disease Diseases 0.000 description 1
- 208000003407 Creutzfeldt-Jakob Syndrome Diseases 0.000 description 1
- 208000010859 Creutzfeldt-Jakob disease Diseases 0.000 description 1
- 229920000858 Cyclodextrin Polymers 0.000 description 1
- 201000010374 Down Syndrome Diseases 0.000 description 1
- OTMSDBZUPAUEDD-UHFFFAOYSA-N Ethane Chemical compound CC OTMSDBZUPAUEDD-UHFFFAOYSA-N 0.000 description 1
- VGGSQFUCUMXWEO-UHFFFAOYSA-N Ethene Chemical compound C=C VGGSQFUCUMXWEO-UHFFFAOYSA-N 0.000 description 1
- 239000005977 Ethylene Substances 0.000 description 1
- PIICEJLVQHRZGT-UHFFFAOYSA-N Ethylenediamine Chemical compound NCCN PIICEJLVQHRZGT-UHFFFAOYSA-N 0.000 description 1
- 208000007487 Familial Cerebral Amyloid Angiopathy Diseases 0.000 description 1
- 206010016207 Familial Mediterranean fever Diseases 0.000 description 1
- KRHYYFGTRYWZRS-UHFFFAOYSA-M Fluoride anion Chemical compound [F-] KRHYYFGTRYWZRS-UHFFFAOYSA-M 0.000 description 1
- BDAGIHXWWSANSR-UHFFFAOYSA-M Formate Chemical compound [O-]C=O BDAGIHXWWSANSR-UHFFFAOYSA-M 0.000 description 1
- 208000032849 Hereditary cerebral hemorrhage with amyloidosis Diseases 0.000 description 1
- CPELXLSAUQHCOX-UHFFFAOYSA-N Hydrogen bromide Chemical compound Br CPELXLSAUQHCOX-UHFFFAOYSA-N 0.000 description 1
- DGAQECJNVWCQMB-PUAWFVPOSA-M Ilexoside XXIX Chemical compound C[C@@H]1CC[C@@]2(CC[C@@]3(C(=CC[C@H]4[C@]3(CC[C@@H]5[C@@]4(CC[C@@H](C5(C)C)OS(=O)(=O)[O-])C)C)[C@@H]2[C@]1(C)O)C)C(=O)O[C@H]6[C@@H]([C@H]([C@@H]([C@H](O6)CO)O)O)O.[Na+] DGAQECJNVWCQMB-PUAWFVPOSA-M 0.000 description 1
- 206010061218 Inflammation Diseases 0.000 description 1
- JVTAAEKCZFNVCJ-UHFFFAOYSA-M Lactate Chemical compound CC(O)C([O-])=O JVTAAEKCZFNVCJ-UHFFFAOYSA-M 0.000 description 1
- GUBGYTABKSRVRQ-QKKXKWKRSA-N Lactose Natural products OC[C@H]1O[C@@H](O[C@H]2[C@H](O)[C@@H](O)C(O)O[C@@H]2CO)[C@H](O)[C@@H](O)[C@H]1O GUBGYTABKSRVRQ-QKKXKWKRSA-N 0.000 description 1
- 201000002832 Lewy body dementia Diseases 0.000 description 1
- WHXSMMKQMYFTQS-UHFFFAOYSA-N Lithium Chemical compound [Li] WHXSMMKQMYFTQS-UHFFFAOYSA-N 0.000 description 1
- FYYHWMGAXLPEAU-UHFFFAOYSA-N Magnesium Chemical compound [Mg] FYYHWMGAXLPEAU-UHFFFAOYSA-N 0.000 description 1
- 208000026139 Memory disease Diseases 0.000 description 1
- 241001465754 Metazoa Species 0.000 description 1
- 201000002795 Muckle-Wells syndrome Diseases 0.000 description 1
- 208000034578 Multiple myelomas Diseases 0.000 description 1
- 241000699660 Mus musculus Species 0.000 description 1
- 241000699670 Mus sp. Species 0.000 description 1
- 102000014415 Muscarinic acetylcholine receptor Human genes 0.000 description 1
- 108050003473 Muscarinic acetylcholine receptor Proteins 0.000 description 1
- 229940121743 Muscarinic receptor agonist Drugs 0.000 description 1
- 206010028289 Muscle atrophy Diseases 0.000 description 1
- FXHOOIRPVKKKFG-UHFFFAOYSA-N N,N-Dimethylacetamide Chemical compound CN(C)C(C)=O FXHOOIRPVKKKFG-UHFFFAOYSA-N 0.000 description 1
- 229910002651 NO3 Inorganic materials 0.000 description 1
- 239000007832 Na2SO4 Substances 0.000 description 1
- NHNBFGGVMKEFGY-UHFFFAOYSA-N Nitrate Chemical compound [O-][N+]([O-])=O NHNBFGGVMKEFGY-UHFFFAOYSA-N 0.000 description 1
- XFFSCOOTVXBLCK-QAVVBOBSSA-N OC(=O)c1cc(ccc1O)\N=N\c1ccc(cc1)-c1ccc(cc1)\N=N\c1ccc(O)c(c1)C(O)=O Chemical compound OC(=O)c1cc(ccc1O)\N=N\c1ccc(cc1)-c1ccc(cc1)\N=N\c1ccc(O)c(c1)C(O)=O XFFSCOOTVXBLCK-QAVVBOBSSA-N 0.000 description 1
- 102100034574 P protein Human genes 0.000 description 1
- 101710126321 Pancreatic trypsin inhibitor Proteins 0.000 description 1
- 241000282320 Panthera leo Species 0.000 description 1
- 208000037581 Persistent Infection Diseases 0.000 description 1
- OAICVXFJPJFONN-UHFFFAOYSA-N Phosphorus Chemical compound [P] OAICVXFJPJFONN-UHFFFAOYSA-N 0.000 description 1
- 229920003171 Poly (ethylene oxide) Polymers 0.000 description 1
- 239000004698 Polyethylene Substances 0.000 description 1
- 239000002202 Polyethylene glycol Substances 0.000 description 1
- ZLMJMSJWJFRBEC-UHFFFAOYSA-N Potassium Chemical compound [K] ZLMJMSJWJFRBEC-UHFFFAOYSA-N 0.000 description 1
- 108010015724 Prephenate Dehydratase Proteins 0.000 description 1
- GOOHAUXETOMSMM-UHFFFAOYSA-N Propylene oxide Chemical compound CC1CO1 GOOHAUXETOMSMM-UHFFFAOYSA-N 0.000 description 1
- 208000000236 Prostatic Neoplasms Diseases 0.000 description 1
- 206010037660 Pyrexia Diseases 0.000 description 1
- WBTCZXYOKNRFQX-UHFFFAOYSA-N S1(=O)(=O)NC1=O Chemical group S1(=O)(=O)NC1=O WBTCZXYOKNRFQX-UHFFFAOYSA-N 0.000 description 1
- BUGBHKTXTAQXES-UHFFFAOYSA-N Selenium Chemical compound [Se] BUGBHKTXTAQXES-UHFFFAOYSA-N 0.000 description 1
- PMZURENOXWZQFD-UHFFFAOYSA-L Sodium Sulfate Chemical compound [Na+].[Na+].[O-]S([O-])(=O)=O PMZURENOXWZQFD-UHFFFAOYSA-L 0.000 description 1
- 229920002472 Starch Polymers 0.000 description 1
- 239000004809 Teflon Substances 0.000 description 1
- 229920006362 Teflon® Polymers 0.000 description 1
- FZWLAAWBMGSTSO-UHFFFAOYSA-N Thiazole Chemical compound C1=CSC=N1 FZWLAAWBMGSTSO-UHFFFAOYSA-N 0.000 description 1
- ATJFFYVFTNAWJD-UHFFFAOYSA-N Tin Chemical compound [Sn] ATJFFYVFTNAWJD-UHFFFAOYSA-N 0.000 description 1
- 206010044688 Trisomy 21 Diseases 0.000 description 1
- 241000251539 Vertebrata <Metazoa> Species 0.000 description 1
- HYWPIYGUZWWMDH-BKJHVTENSA-N [(2r,3r,4s,5r)-3,4,5,6-tetrakis(phenylmethoxy)oxan-2-yl]methanol Chemical compound O([C@@H]([C@H]([C@H](OCC=1C=CC=CC=1)[C@H]1OCC=2C=CC=CC=2)OCC=2C=CC=CC=2)CO)C1OCC1=CC=CC=C1 HYWPIYGUZWWMDH-BKJHVTENSA-N 0.000 description 1
- DGEZNRSVGBDHLK-UHFFFAOYSA-N [1,10]phenanthroline Chemical compound C1=CN=C2C3=NC=CC=C3C=CC2=C1 DGEZNRSVGBDHLK-UHFFFAOYSA-N 0.000 description 1
- 230000002159 abnormal effect Effects 0.000 description 1
- 230000005856 abnormality Effects 0.000 description 1
- 239000006096 absorbing agent Substances 0.000 description 1
- 239000003070 absorption delaying agent Substances 0.000 description 1
- 238000010521 absorption reaction Methods 0.000 description 1
- 229940022663 acetate Drugs 0.000 description 1
- WETWJCDKMRHUPV-UHFFFAOYSA-N acetyl chloride Chemical compound CC(Cl)=O WETWJCDKMRHUPV-UHFFFAOYSA-N 0.000 description 1
- 239000012346 acetyl chloride Substances 0.000 description 1
- OIPILFWXSMYKGL-UHFFFAOYSA-N acetylcholine Chemical compound CC(=O)OCC[N+](C)(C)C OIPILFWXSMYKGL-UHFFFAOYSA-N 0.000 description 1
- 229960004373 acetylcholine Drugs 0.000 description 1
- 150000007513 acids Chemical class 0.000 description 1
- 230000009471 action Effects 0.000 description 1
- 230000004913 activation Effects 0.000 description 1
- 239000013543 active substance Substances 0.000 description 1
- 125000002015 acyclic group Chemical group 0.000 description 1
- 239000000654 additive Substances 0.000 description 1
- 230000002776 aggregation Effects 0.000 description 1
- 238000004220 aggregation Methods 0.000 description 1
- 239000000556 agonist Substances 0.000 description 1
- 150000001298 alcohols Chemical class 0.000 description 1
- 239000003513 alkali Substances 0.000 description 1
- 150000003973 alkyl amines Chemical class 0.000 description 1
- 235000020224 almond Nutrition 0.000 description 1
- AZDRQVAHHNSJOQ-UHFFFAOYSA-N alumane Chemical class [AlH3] AZDRQVAHHNSJOQ-UHFFFAOYSA-N 0.000 description 1
- 125000003277 amino group Chemical group 0.000 description 1
- 125000005021 aminoalkenyl group Chemical group 0.000 description 1
- 125000005014 aminoalkynyl group Chemical group 0.000 description 1
- 125000004397 aminosulfonyl group Chemical group NS(=O)(=O)* 0.000 description 1
- 229910021529 ammonia Inorganic materials 0.000 description 1
- 230000003941 amyloidogenesis Effects 0.000 description 1
- 230000000202 analgesic effect Effects 0.000 description 1
- 238000004458 analytical method Methods 0.000 description 1
- 239000003242 anti bacterial agent Substances 0.000 description 1
- 239000003963 antioxidant agent Substances 0.000 description 1
- 239000012062 aqueous buffer Substances 0.000 description 1
- 239000007864 aqueous solution Substances 0.000 description 1
- 239000008135 aqueous vehicle Substances 0.000 description 1
- 238000011914 asymmetric synthesis Methods 0.000 description 1
- 230000001746 atrial effect Effects 0.000 description 1
- 238000011888 autopsy Methods 0.000 description 1
- 238000000211 autoradiogram Methods 0.000 description 1
- MNFORVFSTILPAW-UHFFFAOYSA-N azetidin-2-one Chemical class O=C1CCN1 MNFORVFSTILPAW-UHFFFAOYSA-N 0.000 description 1
- 150000001540 azides Chemical class 0.000 description 1
- IOJUPLGTWVMSFF-UHFFFAOYSA-N benzothiazole Chemical class C1=CC=C2SC=NC2=C1 IOJUPLGTWVMSFF-UHFFFAOYSA-N 0.000 description 1
- 235000019445 benzyl alcohol Nutrition 0.000 description 1
- 230000005540 biological transmission Effects 0.000 description 1
- 238000001574 biopsy Methods 0.000 description 1
- 229910052796 boron Inorganic materials 0.000 description 1
- 230000007177 brain activity Effects 0.000 description 1
- 239000007975 buffered saline Substances 0.000 description 1
- 239000011575 calcium Substances 0.000 description 1
- 229910052791 calcium Inorganic materials 0.000 description 1
- BPKIGYQJPYCAOW-FFJTTWKXSA-I calcium;potassium;disodium;(2s)-2-hydroxypropanoate;dichloride;dihydroxide;hydrate Chemical compound O.[OH-].[OH-].[Na+].[Na+].[Cl-].[Cl-].[K+].[Ca+2].C[C@H](O)C([O-])=O BPKIGYQJPYCAOW-FFJTTWKXSA-I 0.000 description 1
- BMLSTPRTEKLIPM-UHFFFAOYSA-I calcium;potassium;disodium;hydrogen carbonate;dichloride;dihydroxide;hydrate Chemical compound O.[OH-].[OH-].[Na+].[Na+].[Cl-].[Cl-].[K+].[Ca+2].OC([O-])=O BMLSTPRTEKLIPM-UHFFFAOYSA-I 0.000 description 1
- 125000002837 carbocyclic group Chemical group 0.000 description 1
- 150000001721 carbon Chemical group 0.000 description 1
- 150000001732 carboxylic acid derivatives Chemical class 0.000 description 1
- 239000003054 catalyst Substances 0.000 description 1
- 150000001768 cations Chemical class 0.000 description 1
- 210000004027 cell Anatomy 0.000 description 1
- 230000008859 change Effects 0.000 description 1
- 230000009920 chelation Effects 0.000 description 1
- 229910052729 chemical element Inorganic materials 0.000 description 1
- 239000003638 chemical reducing agent Substances 0.000 description 1
- 229960004926 chlorobutanol Drugs 0.000 description 1
- OEYIOHPDSNJKLS-UHFFFAOYSA-N choline Chemical compound C[N+](C)(C)CCO OEYIOHPDSNJKLS-UHFFFAOYSA-N 0.000 description 1
- 238000013375 chromatographic separation Methods 0.000 description 1
- QZHPTGXQGDFGEN-UHFFFAOYSA-N chromene Chemical compound C1=CC=C2C=C[CH]OC2=C1 QZHPTGXQGDFGEN-UHFFFAOYSA-N 0.000 description 1
- WCZVZNOTHYJIEI-UHFFFAOYSA-N cinnoline Chemical compound N1=NC=CC2=CC=CC=C21 WCZVZNOTHYJIEI-UHFFFAOYSA-N 0.000 description 1
- 238000000576 coating method Methods 0.000 description 1
- 230000007278 cognition impairment Effects 0.000 description 1
- 239000012230 colorless oil Substances 0.000 description 1
- 229940125773 compound 10 Drugs 0.000 description 1
- 238000002591 computed tomography Methods 0.000 description 1
- 230000021615 conjugation Effects 0.000 description 1
- 239000002285 corn oil Substances 0.000 description 1
- 235000005687 corn oil Nutrition 0.000 description 1
- 230000008878 coupling Effects 0.000 description 1
- 238000010168 coupling process Methods 0.000 description 1
- 238000005859 coupling reaction Methods 0.000 description 1
- 239000006071 cream Substances 0.000 description 1
- 239000003431 cross linking reagent Substances 0.000 description 1
- 208000022993 cryopyrin-associated periodic syndrome Diseases 0.000 description 1
- 239000013078 crystal Substances 0.000 description 1
- 229940097362 cyclodextrins Drugs 0.000 description 1
- 125000005725 cyclohexenylene group Chemical group 0.000 description 1
- 125000004956 cyclohexylene group Chemical group 0.000 description 1
- 125000004979 cyclopentylene group Chemical group 0.000 description 1
- 230000007547 defect Effects 0.000 description 1
- 238000006115 defluorination reaction Methods 0.000 description 1
- 230000018044 dehydration Effects 0.000 description 1
- 238000006297 dehydration reaction Methods 0.000 description 1
- 230000008021 deposition Effects 0.000 description 1
- 238000009795 derivation Methods 0.000 description 1
- 239000002274 desiccant Substances 0.000 description 1
- 239000008356 dextrose and sodium chloride injection Substances 0.000 description 1
- 239000008355 dextrose injection Substances 0.000 description 1
- 206010012601 diabetes mellitus Diseases 0.000 description 1
- 238000002059 diagnostic imaging Methods 0.000 description 1
- 238000002405 diagnostic procedure Methods 0.000 description 1
- 238000000502 dialysis Methods 0.000 description 1
- 239000002027 dichloromethane extract Substances 0.000 description 1
- ZBCBWPMODOFKDW-UHFFFAOYSA-N diethanolamine Chemical compound OCCNCCO ZBCBWPMODOFKDW-UHFFFAOYSA-N 0.000 description 1
- FFYPMLJYZAEMQB-UHFFFAOYSA-N diethyl pyrocarbonate Chemical compound CCOC(=O)OC(=O)OCC FFYPMLJYZAEMQB-UHFFFAOYSA-N 0.000 description 1
- HPNMFZURTQLUMO-UHFFFAOYSA-N diethylamine Chemical compound CCNCC HPNMFZURTQLUMO-UHFFFAOYSA-N 0.000 description 1
- SBZXBUIDTXKZTM-UHFFFAOYSA-N diglyme Chemical compound COCCOCCOC SBZXBUIDTXKZTM-UHFFFAOYSA-N 0.000 description 1
- 229910001873 dinitrogen Inorganic materials 0.000 description 1
- AASUFOVSZUIILF-UHFFFAOYSA-N diphenylmethanone;sodium Chemical compound [Na].C=1C=CC=CC=1C(=O)C1=CC=CC=C1 AASUFOVSZUIILF-UHFFFAOYSA-N 0.000 description 1
- 208000035475 disorder Diseases 0.000 description 1
- 239000002270 dispersing agent Substances 0.000 description 1
- 239000002612 dispersion medium Substances 0.000 description 1
- POULHZVOKOAJMA-UHFFFAOYSA-M dodecanoate Chemical compound CCCCCCCCCCCC([O-])=O POULHZVOKOAJMA-UHFFFAOYSA-M 0.000 description 1
- 238000004980 dosimetry Methods 0.000 description 1
- 239000000975 dye Substances 0.000 description 1
- 229920001971 elastomer Polymers 0.000 description 1
- 230000008030 elimination Effects 0.000 description 1
- 238000003379 elimination reaction Methods 0.000 description 1
- 239000002329 esterase inhibitor Substances 0.000 description 1
- BEFDCLMNVWHSGT-UHFFFAOYSA-N ethenylcyclopentane Chemical compound C=CC1CCCC1 BEFDCLMNVWHSGT-UHFFFAOYSA-N 0.000 description 1
- 125000005678 ethenylene group Chemical group [H]C([*:1])=C([H])[*:2] 0.000 description 1
- 239000012259 ether extract Substances 0.000 description 1
- HSTSIRUENGPGSB-UHFFFAOYSA-N ethyl 2-(1-benzylpiperidin-4-ylidene)-2-cyanoacetate Chemical compound C1CC(=C(C#N)C(=O)OCC)CCN1CC1=CC=CC=C1 HSTSIRUENGPGSB-UHFFFAOYSA-N 0.000 description 1
- NDOFFNWLZSYDQP-UHFFFAOYSA-N ethyl 2-cyano-2-(1-methylpiperidin-4-ylidene)acetate Chemical compound CCOC(=O)C(C#N)=C1CCN(C)CC1 NDOFFNWLZSYDQP-UHFFFAOYSA-N 0.000 description 1
- 235000019439 ethyl acetate Nutrition 0.000 description 1
- UREBWPXBXRYXRJ-UHFFFAOYSA-N ethyl acetate;methanol Chemical compound OC.CCOC(C)=O UREBWPXBXRYXRJ-UHFFFAOYSA-N 0.000 description 1
- 125000004494 ethyl ester group Chemical group 0.000 description 1
- 125000001495 ethyl group Chemical group [H]C([H])([H])C([H])([H])* 0.000 description 1
- 238000001704 evaporation Methods 0.000 description 1
- 230000008020 evaporation Effects 0.000 description 1
- 230000007717 exclusion Effects 0.000 description 1
- 238000010265 fast atom bombardment Methods 0.000 description 1
- 239000012530 fluid Substances 0.000 description 1
- GVEPBJHOBDJJJI-UHFFFAOYSA-N fluoranthrene Natural products C1=CC(C2=CC=CC=C22)=C3C2=CC=CC3=C1 GVEPBJHOBDJJJI-UHFFFAOYSA-N 0.000 description 1
- 238000000799 fluorescence microscopy Methods 0.000 description 1
- 239000003269 fluorescent indicator Substances 0.000 description 1
- 238000003682 fluorination reaction Methods 0.000 description 1
- 125000004005 formimidoyl group Chemical group [H]\N=C(/[H])* 0.000 description 1
- 238000001640 fractional crystallisation Methods 0.000 description 1
- 239000012458 free base Substances 0.000 description 1
- VZCYOOQTPOCHFL-OWOJBTEDSA-L fumarate(2-) Chemical compound [O-]C(=O)\C=C\C([O-])=O VZCYOOQTPOCHFL-OWOJBTEDSA-L 0.000 description 1
- 230000006870 function Effects 0.000 description 1
- JKFAIQOWCVVSKC-UHFFFAOYSA-N furazan Chemical compound C=1C=NON=1 JKFAIQOWCVVSKC-UHFFFAOYSA-N 0.000 description 1
- 239000007789 gas Substances 0.000 description 1
- 239000000499 gel Substances 0.000 description 1
- 239000011521 glass Substances 0.000 description 1
- 230000004153 glucose metabolism Effects 0.000 description 1
- 230000004190 glucose uptake Effects 0.000 description 1
- 235000011187 glycerol Nutrition 0.000 description 1
- 238000005858 glycosidation reaction Methods 0.000 description 1
- 210000002149 gonad Anatomy 0.000 description 1
- 208000035474 group of disease Diseases 0.000 description 1
- 229940093915 gynecological organic acid Drugs 0.000 description 1
- 230000036541 health Effects 0.000 description 1
- 150000002390 heteroarenes Chemical class 0.000 description 1
- IPCSVZSSVZVIGE-UHFFFAOYSA-M hexadecanoate Chemical compound CCCCCCCCCCCCCCCC([O-])=O IPCSVZSSVZVIGE-UHFFFAOYSA-M 0.000 description 1
- 125000004836 hexamethylene group Chemical group [H]C([H])([*:2])C([H])([H])C([H])([H])C([H])([H])C([H])([H])C([H])([H])[*:1] 0.000 description 1
- 229930195733 hydrocarbon Natural products 0.000 description 1
- QAOWNCQODCNURD-UHFFFAOYSA-M hydrogensulfate Chemical compound OS([O-])(=O)=O QAOWNCQODCNURD-UHFFFAOYSA-M 0.000 description 1
- XLYOFNOQVPJJNP-UHFFFAOYSA-M hydroxide Chemical compound [OH-] XLYOFNOQVPJJNP-UHFFFAOYSA-M 0.000 description 1
- UWYVPFMHMJIBHE-OWOJBTEDSA-N hydroxymaleic acid group Chemical group O/C(/C(=O)O)=C/C(=O)O UWYVPFMHMJIBHE-OWOJBTEDSA-N 0.000 description 1
- 150000003949 imides Chemical class 0.000 description 1
- 125000001841 imino group Chemical group [H]N=* 0.000 description 1
- 201000008319 inclusion body myositis Diseases 0.000 description 1
- 238000010348 incorporation Methods 0.000 description 1
- PZOUSPYUWWUPPK-UHFFFAOYSA-N indole Natural products CC1=CC=CC2=C1C=CN2 PZOUSPYUWWUPPK-UHFFFAOYSA-N 0.000 description 1
- RKJUIXBNRJVNHR-UHFFFAOYSA-N indolenine Natural products C1=CC=C2CC=NC2=C1 RKJUIXBNRJVNHR-UHFFFAOYSA-N 0.000 description 1
- HOBCFUWDNJPFHB-UHFFFAOYSA-N indolizine Chemical compound C1=CC=CN2C=CC=C21 HOBCFUWDNJPFHB-UHFFFAOYSA-N 0.000 description 1
- 230000004054 inflammatory process Effects 0.000 description 1
- 150000007529 inorganic bases Chemical class 0.000 description 1
- 150000004001 inositols Chemical class 0.000 description 1
- 206010022498 insulinoma Diseases 0.000 description 1
- 230000003993 interaction Effects 0.000 description 1
- 210000000936 intestine Anatomy 0.000 description 1
- 238000001990 intravenous administration Methods 0.000 description 1
- 239000011630 iodine Substances 0.000 description 1
- 210000004153 islets of langerhan Anatomy 0.000 description 1
- ZLTPDFXIESTBQG-UHFFFAOYSA-N isothiazole Chemical compound C=1C=NSC=1 ZLTPDFXIESTBQG-UHFFFAOYSA-N 0.000 description 1
- CTAPFRYPJLPFDF-UHFFFAOYSA-N isoxazole Chemical compound C=1C=NOC=1 CTAPFRYPJLPFDF-UHFFFAOYSA-N 0.000 description 1
- ZLVXBBHTMQJRSX-VMGNSXQWSA-N jdtic Chemical compound C1([C@]2(C)CCN(C[C@@H]2C)C[C@H](C(C)C)NC(=O)[C@@H]2NCC3=CC(O)=CC=C3C2)=CC=CC(O)=C1 ZLVXBBHTMQJRSX-VMGNSXQWSA-N 0.000 description 1
- 150000003951 lactams Chemical class 0.000 description 1
- JYTUSYBCFIZPBE-AMTLMPIISA-M lactobionate Chemical compound [O-]C(=O)[C@H](O)[C@@H](O)[C@@H]([C@H](O)CO)O[C@@H]1O[C@H](CO)[C@H](O)[C@H](O)[C@H]1O JYTUSYBCFIZPBE-AMTLMPIISA-M 0.000 description 1
- 229940099584 lactobionate Drugs 0.000 description 1
- 150000002596 lactones Chemical class 0.000 description 1
- 239000008101 lactose Substances 0.000 description 1
- 229940070765 laurate Drugs 0.000 description 1
- QDLAGTHXVHQKRE-UHFFFAOYSA-N lichenxanthone Natural products COC1=CC(O)=C2C(=O)C3=C(C)C=C(OC)C=C3OC2=C1 QDLAGTHXVHQKRE-UHFFFAOYSA-N 0.000 description 1
- 239000003446 ligand Substances 0.000 description 1
- 229910052744 lithium Inorganic materials 0.000 description 1
- 230000004807 localization Effects 0.000 description 1
- 208000037841 lung tumor Diseases 0.000 description 1
- 210000001165 lymph node Anatomy 0.000 description 1
- 239000011777 magnesium Substances 0.000 description 1
- 229910052749 magnesium Inorganic materials 0.000 description 1
- VZCYOOQTPOCHFL-UPHRSURJSA-N maleic acid Chemical compound OC(=O)\C=C/C(O)=O VZCYOOQTPOCHFL-UPHRSURJSA-N 0.000 description 1
- 230000007257 malfunction Effects 0.000 description 1
- 239000011159 matrix material Substances 0.000 description 1
- 238000010339 medical test Methods 0.000 description 1
- 239000002609 medium Substances 0.000 description 1
- 208000023356 medullary thyroid gland carcinoma Diseases 0.000 description 1
- 230000006984 memory degeneration Effects 0.000 description 1
- 208000023060 memory loss Diseases 0.000 description 1
- QSHDDOUJBYECFT-UHFFFAOYSA-N mercury Chemical compound [Hg] QSHDDOUJBYECFT-UHFFFAOYSA-N 0.000 description 1
- 229910052753 mercury Inorganic materials 0.000 description 1
- 125000002496 methyl group Chemical group [H]C([H])([H])* 0.000 description 1
- 239000000693 micelle Substances 0.000 description 1
- 239000004005 microsphere Substances 0.000 description 1
- 125000000896 monocarboxylic acid group Chemical group 0.000 description 1
- 150000004682 monohydrates Chemical class 0.000 description 1
- 201000000585 muscular atrophy Diseases 0.000 description 1
- 230000035772 mutation Effects 0.000 description 1
- 201000000050 myeloid neoplasm Diseases 0.000 description 1
- 210000005036 nerve Anatomy 0.000 description 1
- 210000002241 neurite Anatomy 0.000 description 1
- 208000015122 neurodegenerative disease Diseases 0.000 description 1
- 210000002682 neurofibrillary tangle Anatomy 0.000 description 1
- 125000000449 nitro group Chemical group [O-][N+](*)=O 0.000 description 1
- 125000004433 nitrogen atom Chemical group N* 0.000 description 1
- QJGQUHMNIGDVPM-UHFFFAOYSA-N nitrogen group Chemical group [N] QJGQUHMNIGDVPM-UHFFFAOYSA-N 0.000 description 1
- 239000002736 nonionic surfactant Substances 0.000 description 1
- 230000009871 nonspecific binding Effects 0.000 description 1
- 238000000655 nuclear magnetic resonance spectrum Methods 0.000 description 1
- QIQXTHQIDYTFRH-UHFFFAOYSA-N octadecanoic acid Chemical compound CCCCCCCCCCCCCCCCCC(O)=O QIQXTHQIDYTFRH-UHFFFAOYSA-N 0.000 description 1
- 239000002674 ointment Substances 0.000 description 1
- ZQPPMHVWECSIRJ-KTKRTIGZSA-M oleate Chemical compound CCCCCCCC\C=C/CCCCCCCC([O-])=O ZQPPMHVWECSIRJ-KTKRTIGZSA-M 0.000 description 1
- 229940049964 oleate Drugs 0.000 description 1
- 238000012634 optical imaging Methods 0.000 description 1
- 238000005457 optimization Methods 0.000 description 1
- 235000005985 organic acids Nutrition 0.000 description 1
- 150000007530 organic bases Chemical class 0.000 description 1
- IPCSVZSSVZVIGE-UHFFFAOYSA-N palmitic acid group Chemical group C(CCCCCCCCCCCCCCC)(=O)O IPCSVZSSVZVIGE-UHFFFAOYSA-N 0.000 description 1
- 208000021255 pancreatic insulinoma Diseases 0.000 description 1
- 239000002245 particle Substances 0.000 description 1
- 230000036285 pathological change Effects 0.000 description 1
- 125000004817 pentamethylene group Chemical group [H]C([H])([*:2])C([H])([H])C([H])([H])C([H])([H])C([H])([H])[*:1] 0.000 description 1
- 230000000737 periodic effect Effects 0.000 description 1
- 229960003742 phenol Drugs 0.000 description 1
- 229950000688 phenothiazine Drugs 0.000 description 1
- 125000001997 phenyl group Chemical group [H]C1=C([H])C([H])=C(*)C([H])=C1[H] 0.000 description 1
- WLJVXDMOQOGPHL-UHFFFAOYSA-N phenylacetic acid Chemical compound OC(=O)CC1=CC=CC=C1 WLJVXDMOQOGPHL-UHFFFAOYSA-N 0.000 description 1
- 239000002953 phosphate buffered saline Substances 0.000 description 1
- UEZVMMHDMIWARA-UHFFFAOYSA-M phosphonate Chemical compound [O-]P(=O)=O UEZVMMHDMIWARA-UHFFFAOYSA-M 0.000 description 1
- 150000008300 phosphoramidites Chemical class 0.000 description 1
- DHRLEVQXOMLTIM-UHFFFAOYSA-N phosphoric acid;trioxomolybdenum Chemical compound O=[Mo](=O)=O.O=[Mo](=O)=O.O=[Mo](=O)=O.O=[Mo](=O)=O.O=[Mo](=O)=O.O=[Mo](=O)=O.O=[Mo](=O)=O.O=[Mo](=O)=O.O=[Mo](=O)=O.O=[Mo](=O)=O.O=[Mo](=O)=O.O=[Mo](=O)=O.OP(O)(O)=O DHRLEVQXOMLTIM-UHFFFAOYSA-N 0.000 description 1
- 229910052698 phosphorus Inorganic materials 0.000 description 1
- 239000011574 phosphorus Substances 0.000 description 1
- LFGREXWGYUGZLY-UHFFFAOYSA-N phosphoryl Chemical group [P]=O LFGREXWGYUGZLY-UHFFFAOYSA-N 0.000 description 1
- LFSXCDWNBUNEEM-UHFFFAOYSA-N phthalazine Chemical compound C1=NN=CC2=CC=CC=C21 LFSXCDWNBUNEEM-UHFFFAOYSA-N 0.000 description 1
- 229920000728 polyester Polymers 0.000 description 1
- 229920000573 polyethylene Polymers 0.000 description 1
- 229920001223 polyethylene glycol Polymers 0.000 description 1
- 229920000642 polymer Polymers 0.000 description 1
- 235000010482 polyoxyethylene sorbitan monooleate Nutrition 0.000 description 1
- 229920001451 polypropylene glycol Polymers 0.000 description 1
- 229920000053 polysorbate 80 Polymers 0.000 description 1
- 239000011148 porous material Substances 0.000 description 1
- 238000002600 positron emission tomography Methods 0.000 description 1
- 230000001242 postsynaptic effect Effects 0.000 description 1
- 229910052700 potassium Inorganic materials 0.000 description 1
- 239000011591 potassium Substances 0.000 description 1
- 229910000027 potassium carbonate Inorganic materials 0.000 description 1
- 238000012746 preparative thin layer chromatography Methods 0.000 description 1
- 230000002335 preservative effect Effects 0.000 description 1
- 230000003518 presynaptic effect Effects 0.000 description 1
- 150000003141 primary amines Chemical class 0.000 description 1
- 230000000750 progressive effect Effects 0.000 description 1
- BDERNNFJNOPAEC-UHFFFAOYSA-N propan-1-ol Chemical compound CCCO BDERNNFJNOPAEC-UHFFFAOYSA-N 0.000 description 1
- QQONPFPTGQHPMA-UHFFFAOYSA-N propylene Natural products CC=C QQONPFPTGQHPMA-UHFFFAOYSA-N 0.000 description 1
- 125000004805 propylene group Chemical group [H]C([H])([H])C([H])([*:1])C([H])([H])[*:2] 0.000 description 1
- 230000012846 protein folding Effects 0.000 description 1
- CPNGPNLZQNNVQM-UHFFFAOYSA-N pteridine Chemical compound N1=CN=CC2=NC=CN=C21 CPNGPNLZQNNVQM-UHFFFAOYSA-N 0.000 description 1
- 210000002637 putamen Anatomy 0.000 description 1
- 150000004040 pyrrolidinones Chemical class 0.000 description 1
- 150000003242 quaternary ammonium salts Chemical class 0.000 description 1
- JWVCLYRUEFBMGU-UHFFFAOYSA-N quinazoline Chemical compound N1=CN=CC2=CC=CC=C21 JWVCLYRUEFBMGU-UHFFFAOYSA-N 0.000 description 1
- 239000002287 radioligand Substances 0.000 description 1
- 230000008707 rearrangement Effects 0.000 description 1
- 238000003259 recombinant expression Methods 0.000 description 1
- 238000011084 recovery Methods 0.000 description 1
- 230000009467 reduction Effects 0.000 description 1
- 206010039073 rheumatoid arthritis Diseases 0.000 description 1
- 238000007363 ring formation reaction Methods 0.000 description 1
- 208000008864 scrapie Diseases 0.000 description 1
- 150000003335 secondary amines Chemical class 0.000 description 1
- 230000001624 sedative effect Effects 0.000 description 1
- 229910052711 selenium Inorganic materials 0.000 description 1
- 239000011669 selenium Substances 0.000 description 1
- 150000003346 selenoethers Chemical class 0.000 description 1
- 238000000926 separation method Methods 0.000 description 1
- 210000002966 serum Anatomy 0.000 description 1
- 210000002027 skeletal muscle Anatomy 0.000 description 1
- 210000003491 skin Anatomy 0.000 description 1
- 239000002002 slurry Substances 0.000 description 1
- 229910052708 sodium Inorganic materials 0.000 description 1
- 229910000030 sodium bicarbonate Inorganic materials 0.000 description 1
- 235000017557 sodium bicarbonate Nutrition 0.000 description 1
- 239000008354 sodium chloride injection Substances 0.000 description 1
- 229910052938 sodium sulfate Inorganic materials 0.000 description 1
- 235000011152 sodium sulphate Nutrition 0.000 description 1
- 210000004872 soft tissue Anatomy 0.000 description 1
- 239000012453 solvate Substances 0.000 description 1
- 239000004334 sorbic acid Substances 0.000 description 1
- 229940075582 sorbic acid Drugs 0.000 description 1
- 235000010199 sorbic acid Nutrition 0.000 description 1
- 150000003413 spiro compounds Chemical class 0.000 description 1
- 230000000087 stabilizing effect Effects 0.000 description 1
- 239000008107 starch Substances 0.000 description 1
- 235000019698 starch Nutrition 0.000 description 1
- 239000007858 starting material Substances 0.000 description 1
- 230000001954 sterilising effect Effects 0.000 description 1
- 238000004659 sterilization and disinfection Methods 0.000 description 1
- 125000000547 substituted alkyl group Chemical group 0.000 description 1
- 125000005346 substituted cycloalkyl group Chemical group 0.000 description 1
- KDYFGRWQOYBRFD-UHFFFAOYSA-M succinate(1-) Chemical compound OC(=O)CCC([O-])=O KDYFGRWQOYBRFD-UHFFFAOYSA-M 0.000 description 1
- KDYFGRWQOYBRFD-UHFFFAOYSA-L succinate(2-) Chemical compound [O-]C(=O)CCC([O-])=O KDYFGRWQOYBRFD-UHFFFAOYSA-L 0.000 description 1
- 229940014800 succinic anhydride Drugs 0.000 description 1
- 125000003375 sulfoxide group Chemical group 0.000 description 1
- 150000008053 sultones Chemical class 0.000 description 1
- 239000000375 suspending agent Substances 0.000 description 1
- 208000011580 syndromic disease Diseases 0.000 description 1
- 238000007910 systemic administration Methods 0.000 description 1
- 150000003512 tertiary amines Chemical class 0.000 description 1
- RAOIDOHSFRTOEL-UHFFFAOYSA-N tetrahydrothiophene Chemical compound C1CCSC1 RAOIDOHSFRTOEL-UHFFFAOYSA-N 0.000 description 1
- 125000000383 tetramethylene group Chemical group [H]C([H])([*:1])C([H])([H])C([H])([H])C([H])([H])[*:2] 0.000 description 1
- 210000001103 thalamus Anatomy 0.000 description 1
- GVIJJXMXTUZIOD-UHFFFAOYSA-N thianthrene Chemical compound C1=CC=C2SC3=CC=CC=C3SC2=C1 GVIJJXMXTUZIOD-UHFFFAOYSA-N 0.000 description 1
- RTKIYNMVFMVABJ-UHFFFAOYSA-L thimerosal Chemical compound [Na+].CC[Hg]SC1=CC=CC=C1C([O-])=O RTKIYNMVFMVABJ-UHFFFAOYSA-L 0.000 description 1
- 229940033663 thimerosal Drugs 0.000 description 1
- 150000007970 thio esters Chemical class 0.000 description 1
- JADVWWSKYZXRGX-UHFFFAOYSA-M thioflavine T Chemical group [Cl-].C1=CC(N(C)C)=CC=C1C1=[N+](C)C2=CC=C(C)C=C2S1 JADVWWSKYZXRGX-UHFFFAOYSA-M 0.000 description 1
- 125000003396 thiol group Chemical group [H]S* 0.000 description 1
- ANRHNWWPFJCPAZ-UHFFFAOYSA-M thionine Chemical compound [Cl-].C1=CC(N)=CC2=[S+]C3=CC(N)=CC=C3N=C21 ANRHNWWPFJCPAZ-UHFFFAOYSA-M 0.000 description 1
- QERYCTSHXKAMIS-UHFFFAOYSA-N thiophene-2-carboxylic acid Chemical compound OC(=O)C1=CC=CS1 QERYCTSHXKAMIS-UHFFFAOYSA-N 0.000 description 1
- RYYWUUFWQRZTIU-UHFFFAOYSA-K thiophosphate Chemical compound [O-]P([O-])([O-])=S RYYWUUFWQRZTIU-UHFFFAOYSA-K 0.000 description 1
- 210000001685 thyroid gland Anatomy 0.000 description 1
- 210000002105 tongue Anatomy 0.000 description 1
- 125000002088 tosyl group Chemical group [H]C1=C([H])C(=C([H])C([H])=C1C([H])([H])[H])S(*)(=O)=O 0.000 description 1
- 230000009466 transformation Effects 0.000 description 1
- 238000011830 transgenic mouse model Methods 0.000 description 1
- 229940108519 trasylol Drugs 0.000 description 1
- 150000003852 triazoles Chemical class 0.000 description 1
- ITMCEJHCFYSIIV-UHFFFAOYSA-M triflate Chemical compound [O-]S(=O)(=O)C(F)(F)F ITMCEJHCFYSIIV-UHFFFAOYSA-M 0.000 description 1
- JBWKIWSBJXDJDT-UHFFFAOYSA-N triphenylmethyl chloride Chemical compound C=1C=CC=CC=1C(C=1C=CC=CC=1)(Cl)C1=CC=CC=C1 JBWKIWSBJXDJDT-UHFFFAOYSA-N 0.000 description 1
- 238000001665 trituration Methods 0.000 description 1
- 201000008827 tuberculosis Diseases 0.000 description 1
- 210000002700 urine Anatomy 0.000 description 1
- 229940070710 valerate Drugs 0.000 description 1
- NQPDZGIKBAWPEJ-UHFFFAOYSA-N valeric acid Chemical compound CCCCC(O)=O NQPDZGIKBAWPEJ-UHFFFAOYSA-N 0.000 description 1
- 230000003612 virological effect Effects 0.000 description 1
Landscapes
- Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
- Medicines Containing Antibodies Or Antigens For Use As Internal Diagnostic Agents (AREA)
Abstract
One aspect of the present invention relates to compounds, compositions and methods for diagnosis and/or treatment of a subject suffering from an amyloidosis-associated pathological condition. In certain embodiments, the imaging and/or therapeutic agents of the instant invention may be administered to a subject for identification and/or treatment of amyloid deposits. A specific imaging method detects amyloid deposits by administering the imaging agent to the subject and detecting the spatial distribution of the agent. Differential accumulation of the agent is indicative of AD or an amyloidosis-associated pathological condition and can be monitored by using a PET or SPECT camera.
Description
WO 2009/117728 PCT/US2009/037928 Compounds and Compositions for the Detection and Treatment of Alzheimer's Disease and Related Disorders RELATED APPLICATIONS This application claims the benefit of priority to United States Provisional Patent 5 Application serial number 61/038,571 filed March 21, 2008, which is hereby incorporated by reference in its entirety. BACKGROUND Millions of Americans suffer from dementia and other cognitive deficits as a result of Alzheimer's disease (AD), a neurodegenerative disease. Due to its occurrence in the 10 brain, it is difficult to diagnose the condition and to determine its cause without dangerous brain biopsy. Scientists believe that as many as 4.5 million Americans suffer from AD. AD usually begins after age 60 and its risk goes up with age. The cause of AD is unknown and, at present, no cure has been found. AD can only be definitely confirmed after an autopsy, which prevents early accurate 15 diagnosis and treatment of the condition. Neuropathologically, AD is characterized by the presence of neuritic plaques, neurofibrillary tangles and neuronal loss. See Mann. Mech. Ageing Dev. 1985, 3(1), 213. Doctors can diagnose AD correctly up to 90 percent using several tools to diagnose "probable" AD, namely, (1) questions about the person's general health, past medical problems, and ability to carry out daily activities; (2) tests of memory, 20 problem solving, attention, counting, and language; (3) medical tests, such as tests of blood, urine, or spinal fluid; and (4) brain scans. Postmortem brain tissues of AD victims show the presence of amyloid cores of neuritic plaques that are composed of amyloid p-(A P-) protein being predominantly arranged in beta-pleated sheet configuration. See J. Biol. Chem. 1992, 267(24), 17082; and 25 Proc. Natl. Acad. Sci., USA 1986, 83(2), 503. Deposition of amyloid 0-(A P-) protein occurs, however, not only in individuals that have AD, but it also frequent among individuals who are undergoing the aging process. Thus, it is very critical to distinguish the AP production due to the normal aging process or to AD or other dementia-causing diseases such as DLB dementia associaed with Louis 30 Body. In the normal aging process, non-compact or diffuse amyloid plaques containing less - 1 - WO 2009/117728 PCT/US2009/037928 fibrillar AP are deposited primarily in the brain. In contrast, AD patients have brains that are characterized by an unanatomically widespread process of amyloid deposition and neurite plaque formation containing dense amyloid fibrils. Clinical tests to determine the onset of AD and its progression are not presently 5 sensitive and several agents are reported as potential PET and SPECT imaging tracers. Some of the developmental research on imaging agents useful for the diagnosis of AD and other related diseases are discussed below. U.S. Patent Publication Application No. 2006/0018825 Al, assigned to BF Research Institute, hereby incorporated by reference, describes a series of BF compounds or a salt or 10 solvate thereof that can be used as a probe for the imaging and diagnosis of diseases in which amyloid P-protein accumulates. These compounds have high specificity for diffuse plaques and act as early indicators of AD. In addition, they have rapid clearance from the brain. Okamura et al. (in J. Neurosci. 2004, 24(10), 2535) describes a labeled 15 sterylbenzoxazole derivative compound, 18 F-radio labeled 6-(2-fluoroethoxy)-2-[2-(4 methylaminophenyl)ethenyl]-benzoxazole (BF-168), that demonstrated abundant initial brain uptake (3.9% injected dose/gm at 2 min after injection) and fast clearance (t = 24.7 min) after intravenous (iv) administration in normal mice. In addition, autoradiograms of brain sections from APP23 transgenic mice at 180 min after iv injection of 18 F-radio labeled 20 BF-168 showed selective labeling of brain amyloid deposits with little non-specific binding. More recently, Kudo et al. (in J. Nucl. Med. 2007, 48553) have demonstrated the use of a novel compound, F- 18 labeled 2-(2- [2-diethylaminothiazo 1-5 -yl] -ethenyl)-6-(2 [fluoro])ethoxybenzoxazol (eB F-227) as a promising PET probe for in vivo detection of dense amyloid deposits in AD patients. 25 U.S. Patent Nos. 6,001,331 and 6,696,039 B2, issued December 14, 1999 and February 24, 2004, respectively, hereby incorporated by reference, describe the use of several radiolabeled benzothiazole compounds for imaging amyloid deposits. U.S. Patent Nos. 6,168,776 and 6,133,259, issued January 2, 2001 and October 17, 2000, respectively, hereby incorporated by describe amyloid-binding compounds such as 30 Chrysamine G and their use in identifying AD in vivo and other pathological conditions characterized by amyloidosis. -2- 5 One promising amyloid imaging agent is an analogue of thioflavin T, also known as the Pittsburgh Compound-B or "PIB compound." PIB is also known as [N methyl-("C)]-2-(4'-methylaminophenyl)-6-hydroxybenzothiazole (or [" C]6-OH-BTA I). PET imaging with 11 C-PIB can discriminate AD from frontotemporal lobar degeneration (FTLD). See J. Med. Chem. 2003, 46(13), 2740; and Neurology 2007, 68, 10 1205. However, use of a C-11 labeled tracer limits imaging to medical centers with a cyclotron. It is well known that 2,8-diazaspiro[4,5]decane-1,3-dione (RS-86) derivatives are active and centrally effective muscarinic cholinergic agonists, with analgesic and sedative properties in animals when given orally. In addition, it has been shown that 15 the C-11 radiolabeled version of 2,8-diazaspiro[4,5]decane-1,3-dione can be used as a tracer, though the reported study describes brain distribution results with a very low specific activity. Further, the biodistribution of the C-11 radiolabeled 2,8 diazaspiro[4,5]decane-1,3-dione in rats, as a function of time, showed that the initial brain uptake was about 1.1%, with high concentrations of percent dose per gram in 20 areas rich with muscarinic receptors such as caudate, putamen and thalamus. However, as discussed above with respect to 11 C-PIB, the utility of a C-11 labeled tracer is limited to medical centers with a cyclotron. Accordingly, there is a need to provide compounds and methods for imaging and treating AD and amyloidosis-associated pathological conditions that are easily 25 available and cost effective. There is a continuing need to seek novel imaging tracers that are accurate and used in early detection of AD and other related pathological conditions. Any discussion of documents, acts, materials, devices, articles or the like which has been included in the present specification is not to be taken as an admission that 30 any or all of these matters form part of the prior art base or were common general knowledge in the field relevant to the present disclosure as it existed before the priority date of each claim of this application. Throughout this specification the word "comprise", or variations such as 'comprises" or "comprising", will be understood to imply the inclusion of a stated 35 element, integer or step, or group of elements, integers or steps, but not the exclusion of any other element, integer or step, or group of elements, integers or steps. 3 5 SUMMARY In a first aspect there is provided a compound, or a pharmaceutically acceptable salt thereof, represented by formula II: R7 R7 L-O R 7
R
7
R
7 II 10 wherein, independently for each occurrence, L is -C(=O)R 3 , -C(=O)[C(R 1 )2]pR 3 , -C(=O)[C(R)2]pC(=O)R 3 , [C(R)2]pC(=O)R 3 , -C(=O)[C1_10alkylene]R 3 , -[C1_0alkylene]C(=O)R 3 or
-C(=O)[C
1
_
1 0alkylene]C(=O)R3 15 R 1 is hydrogen; R 4 R 4 R4 'R4 0 0 R1 R 3 is R1
R
4 is hydrogen, halo, hydroxy, alkoxy, aryloxy, heteroaryloxy, aralkyloxy, heteroaralkyloxy, or -OR5;
R
5 is hydrogen, alkyl, heteroalkyl, cycloalkyl, heterocycloalkyl, aryl, heteroaryl, 20 aralkyl, or heteroaralkyl;
R
7 is halo, hydroxy, alkoxy, aryloxy, heteroaryloxy, aralkyloxy, heteroaralkyloxy, -OR 5 ; and p is 1-10 inclusive. 3a 5 In another aspect there is provided a compound selected from the group consisting of: ao osn 1-deoxy-1-fluoro-scyllo-inositol, 1-deoxy-1-fluoro-myo-inositol, HG OH HB AcO 00 ai NOAc AcO OAC OAc OH 1 8 F OH HO ~OH and OH 10 In another aspect a method for amyloid imaging a subject suffering from an amyloidosis-associated pathological condition comprising the step of: administering a compound, or a composition comprising a pharmaceutically acceptable carrier and the compound or a pharmaceutically acceptable form thereof, OH 18 F - _ -t\JOH HOO wherein the compound is o or OH 15 One aspect of the present invention relates to compounds, compositions and methods for diagnosis and/or treatment of a subject suffering from an amyloidosis-associated pathological condition. In certain embodiments, the imaging and/or therapeutic agents of the instant invention may be administered to a subject for identification and/or treatment of amyloid deposits. A specific imaging method detects amyloid deposits by 20 administering the imaging agent to the subject and detecting the spatial distribution of the agent. Differential accumulation of the agent is indicative of AD or an amyloidosis associated pathological condition and can be monitored by using a PET or SPECT camera. One aspect of the invention relates to the preparation of fluorinated or radiofluorinated 25 2,8-diazaspiro[4,5]decane- 1,3-diones, and their diagnostic and/or 3b WO 2009/117728 PCT/US2009/037928 therapeutic use in brain disorders associated with aging, such as, senile dementia and Alzheimer's disease. Another aspect of the invention relates to the preparation of fluorinated or radiofluorinated inositols (such as 1-deoxy-1-fluoro-scyllo-inositol and 1-deoxy-1-fluoro 5 myo-inositol), and their diagnostic and/or therapeutic use in brain disorders associated with aging, such as, senile dementia and Alzheimer's disease. Another aspect of the invention relates to compounds which are a combination of an inositol and a 2,8-diazaspiro[4,5]decane-1,3-dione (e.g., wherein the inositol is covalently linked by a cross-linker to the 2,8-diazaspiro[4,5]decane-1,3-dione), and their diagnostic 10 and/or therapeutic use in brain disorders associated with aging, such as, senile dementia and Alzheimer's disease. Another aspect of the invention relates to optionally fluorinated or radio fluorinated combinations of 2,8-diazaspiro[4,5]decane-1,3-diones and D-glucose (e.g. [F-18]-2-fluoro 2-deoxy-D-glucose), and their diagnostic and/or therapeutic use in brain disorders 15 associated with aging, such as, senile dementia and Alzheimer's disease. In certain embodiments, the 2,8-diazaspiro[4,5]decane-1,3-dione improves the selectivity and.or uptake of the glucose. Another aspect of the invention relates to the optionally fluorinated or radiofluorinated combination of an inositol with D-glucose (e.g. [F-18]-2-fluoro-2-deoxy 20 D-glucose), and their diagnostic and/or therapeutic use in brain disorders associated with aging, such as, senile dementia and Alzheimer's disease. In certain embodiments, the inositol improves the selectivity and/or uptake of the glucose. Other aspects, features, objects, and advantages of the present invention are apparent in the detailed description that follows. It should be understood, however, that the 25 detailed description is given by way of illustration only, not limitation. Various changes and modifications within the scope of the invention will become apparent to those skilled in the art from the detailed description. BRIEF DESCRIPTION OF THE FIGURES Figure 1 depicts a table showing the biodistribution in rats following the injection 30 of [F-i 8]-N-2-fluoroethyl-2,8-diazaspiro[4,5]decane- 1,3-dione at three different time points. -4- WO 2009/117728 PCT/US2009/037928 Figure 2 depicts a table showing the biodistribution in rats following the injection of [F-18]-N-2-fluoropropyl-2,8-diazaspiro[4,5]decane-1,3-dione at two different time points. Figure 3 depicts one approach to the synthesis of two fluorinated 2,8 5 diazaspiro[4,5]decane-1,3-dione derivatives. Figure 4 depicts one approach to the synthesis of N-2-ethyl-2,8 diazaspiro[4,5]decane- 1,3-dione. Figure 5 depicts three examples of combinations of 2,8-diazaspiro[4,5]decane-1,3 dione and inositol structures. 10 Figure 6 depicts one approach to the synthesis of 6-0-[N-(N-2-ethyl-2,8 diazaspiro[4,5]decane-1,3-dione)aminocarbonyl]-a,p-D-glucopyranose. Figure 7 depicts one approach to the synthesis of 1,2,3,4,5-penta-O-benzyl-scyllo inositol. Figure 8 depicts one approach to the synthesis of 1-deoxy-1-F-18-fluoro-scyllo 15 inositol Figure 9 depicts one approach to the synthesis of 6-0-[(p-D-glucopyranose-6-yl) succinyl]-scyllo-inositol. Figure 10 depicts a table showing the some of the effects of amyloid buildup. DETAILED DESCRIPTION 20 One aspect of the present invention provides embodiments of compounds, compositions and methods for effective administration to a subject suffering from amylodiosis-associated pathological conditions, such as Alzheimer's disease (AD). In certain embodiments of the invention, the compounds are reversible choline esterase inhibitors that show high brain uptake. In certain embodiments, the compounds inhibit p 25 (A j-)protein folding that causes amyloid plaque formation. Further, in certain embodiments, the compounds are labeled with a PET or SPECT radionuclide, and can be used for diagnosing amyloid deposits in patients suffering from Alzheimer's disease and/or pathological conditions characterized by the presence of amyloid deposits. In certain embodiments, the novel imaging compounds act on both potential Alzheimer disease 30 progressions. -5- WO 2009/117728 PCT/US2009/037928 One aspect of the invention relates to the preparation of fluorinated or radiofluorinated 2,8-diazaspiro[4,5]decane-1,3-diones, and their diagnostic and/or therapeutic use in amylodiosis-associated pathological conditions. For example in brain disorders associated with aging, such as, senile dementia and Alzheimer's disease. In 5 certain embodiments, the compositions comprise an effective amount of a fluorinated 2,8 diazaspiro[4,5]decane-1,3-dione, in combination with a pharmaceutical carrier in an appropriate dosage. In certain embodiments, the compositions comprise a diagnostic radioimaging amount of a 18 F-labeled fluorinated 2,8-diazaspiro[4,5]decane-1,3-dione, in combination with a pharmaceutical carrier in an appropriate dosage. 10 Another aspect of the invention relates to compounds which are a combination of a scyllo-inositol and a 2,8-diazaspiro[4,5]decane-1,3-dione (e.g., wherein a scyllo-inositol is covalently linked by a cross-linker to a 2,8-diazaspiro[4,5]decane-1,3-dione). Some of such compounds may be reversible acetyl choline esterase inhibitors and/or A p-amyloid plaque formation inhibitors; in addition, as such, some compounds may be useful for imaging and 15 treating brain disorders associated with aging, such as, for example, senile dementia and Alzheimer's disease. In certain embodiments, certain compounds which are combinations of a scyllo-inositol and a 2,8-diazaspiro[4,5]decane-1,3-dione may show improved brain uptake and/or brain bioavailability compared to the scyllo-inositol and/or the 2,8 diazaspiro[4,5]decane-1,3-dione. Therefore, such compounds may improve the effective 20 action of the compound comprising the combination over one or both of the individual compounds. In certain embodiments, certain compositions of the invention comprise a therapeutically and/or diagnostically effective amount of a composition comprising a compound which is a combination of scyllo-inositol and a radiofluorinated 2,8 diazaspiro[4,5]decane-1,3-dione, and a pharmaceutical carrier in an appropriate dosage. 25 Another aspect of the invention relates to combinations of 2,8 diazaspiro[4,5]decane-1,3-diones and D-glucose for therapy; and combinations with [F-18] 2-fluoro-2-deoxy-D-glucose for diagnosis. In certain embodiments, compositions of the invention comprise a therapeutically and/or diagnostically effective amount of a composition comprising a compound which is a combination of D-glucose or [F-18]-2 30 fluoro-2-deoxy-D-glucose and a 2,8-diazaspiro[4,5]decane-1,3-dione, and a pharmaceutical carrier in an appropriate dosage. Another aspect of the invention relates to the combination of scyllo-inositol with D glucose for improving uptake and therapy; and combinations with [F-18]-2-fluoro-2-deoxy - 6- WO 2009/117728 PCT/US2009/037928 D-glucose for diagnosis. In certain embodiments, compositions of the invention comprise a therapeutically and/or diagnostically effective amount of a composition comprising a compound which is a combination of D-glucose or [F-18]-2-fluoro-2-deoxy-D-glucose and a scyllo-inositol, and a pharmaceutical carrier, in an appropriate dosage. 5 In certain embodiments, imaging and/or therapeutic agents of the instant invention may be administered to a subject for identification of amyloid deposits. A specific imaging method detects amyloid deposits by administering the imaging agent to the subject and detecting the spatial distribution of the agent. Differential accumulation of the agent is indicative of AD or an amyloidosis-associated pathological condition and can be monitored 10 by using a PET or SPECT camera. Definitions Herein a number of terms are used extensively. The following definitions are provided to facilitate understanding of the invention. The indefinite articles "a" and "an," as used herein in the specification and in the 15 claims, unless clearly indicated to the contrary, should be understood to mean "at least one." The phrase "and/or," as used herein in the specification and in the claims, should be understood to mean "either or both" of the elements so conjoined, i.e., elements that are conjunctively present in some cases and disjunctively present in other cases. Multiple 20 elements listed with "and/or" should be construed in the same fashion, i.e., "one or more" of the elements so conjoined. Other elements may optionally be present other than the elements specifically identified by the "and/or" clause, whether related or unrelated to those elements specifically identified. Thus, as a non-limiting example, a reference to "A and/or B", when used in conjunction with open-ended language such as "comprising" can refer, in 25 one embodiment, to A only (optionally including elements other than B); in another embodiment, to B only (optionally including elements other than A); in yet another embodiment, to both A and B (optionally including other elements); etc. As used herein in the specification and in the claims, "or" should be understood to have the same meaning as "and/or" as defined above. For example, when separating items 30 in a list, "or" or "and/or" shall be interpreted as being inclusive, i.e., the inclusion of at least one, but also including more than one, of a number or list of elements, and, optionally, additional unlisted items. Only terms clearly indicated to the contrary, such as "only one -7- WO 2009/117728 PCT/US2009/037928 of' or "exactly one of," or, when used in the claims, "consisting of," will refer to the inclusion of exactly one element of a number or list of elements. In general, the term "or" as used herein shall only be interpreted as indicating exclusive alternatives (i.e., "one or the other but not both") when preceded by terms of exclusivity, such as "either," "one of," 5 "only one of," or "exactly one of." "Consisting essentially of," when used in the claims, shall have its ordinary meaning as used in the field of patent law. As used herein in the specification and in the claims, the phrase "at least one," in reference to a list of one or more elements, should be understood to mean at least one element selected from any one or more of the elements in the list of elements, but not 10 necessarily including at least one of each and every element specifically listed within the list of elements and not excluding any combinations of elements in the list of elements. This definition also allows that elements may optionally be present other than the elements specifically identified within the list of elements to which the phrase "at least one" refers, whether related or unrelated to those elements specifically identified. Thus, as a non 15 limiting example, "at least one of A and B" (or, equivalently, "at least one of A or B," or, equivalently "at least one of A and/or B") can refer, in one embodiment, to at least one, optionally including more than one, A, with no B present (and optionally including elements other than B); in another embodiment, to at least one, optionally including more than one, B, with no A present (and optionally including elements other than A); in yet 20 another embodiment, to at least one, optionally including more than one, A, and at least one, optionally including more than one, B (and optionally including other elements); etc. It should also be understood that, unless clearly indicated to the contrary, in any methods claimed herein that include more than one step or act, the order of the steps or acts of the method is not necessarily limited to the order in which the steps or acts of the method 25 are recited. In the claims, as well as in the specification above, all transitional phrases such as "comprising," "including," "carrying," "having," "containing," "involving," "holding," "composed of," and the like are to be understood to be open-ended, i.e., to mean including but not limited to. Only the transitional phrases "consisting of' and "consisting essentially 30 of' shall be closed or semi-closed transitional phrases, respectively, as set forth in the United States Patent Office Manual of Patent Examining Procedures, Section 2111.03. -8- WO 2009/117728 PCT/US2009/037928 Amyloidosis is a condition characterized by the accumulation of various insoluble, fibrillar proteins in the tissues of a patient. An amyloid deposit is formed by the aggregation of amyloid proteins, followed by the further combination of aggregates and/or amyloid proteins. 5 As used herein, "amylodiosis-associated pathological conditions" refers to a group of disorders caused by abnormal folding of proteins leading to fibril formation in one or more body organs, systems or soft tissues. These clumps of protein are called amyloid deposits and the accumulation of amyloid deposits causes the progressive malfunction and eventual failure of the affected organ. Normally, proteins are broken down at about the 10 same rate as they are produced, but these unusually stable amyloid deposits are deposited more rapidly than they can be broken down. The accumulation may be localized in one organ or may be systemic such that several organs are affected. Amyloidosis causes few or no symptoms in some people, while producing severe symptoms and fatal complications in other people. The severity of the disease depends on 15 which organs are affected by amyloid deposits. Amyloidosis is twice as common in men as in women and is more common among older people. Many forms of amyloidosis exist, and the disease can be classified into four groups: primary amyloidosis, secondary amyloidosis, hereditary amyloidosis, and amyloidosis associated with normal aging. 20 Primary amyloidosis (light chain amyloidosis) occurs with abnormalities of plasma cells, and some people with primary amyloidosis also have multiple myeloma (cancer of the plasma cells). Typical sites of amyloid buildup in primary amyloidosis are the heart, lungs, skin, tongue, thyroid gland, intestines, liver, kidneys, and blood vessels. Secondary amyloidosis may develop in response to various diseases that cause 25 persistent infection or inflammation, such as tuberculosis, rheumatoid arthritis, and familial Mediterranean fever. Typical sites of amyloid buildup in secondary amyloidosis are the spleen, liver, kidneys, adrenal glands, and lymph nodes. Hereditary amyloidosis has been noted in some families, particularly those from Portugal, Sweden, and Japan. The amyloid-producing defect occurs because of mutations in 30 specific proteins in the blood. Typical sites for amyloid buildup in hereditary amyloidosis are the nerves, heart, blood vessels, and kidneys. -9- WO 2009/117728 PCT/US2009/037928 Amyloidosis associated with normal aging usually affects the heart. What causes amyloid to build up in the heart, other than age, usually is not known. Amyloid also accumulates in the brain of people with Alzheimer's disease and is thought to play a role in causing Alzheimer's. See Figure 10 for a table showing the effects of amyloid buildup. 5 Besides its presence in Alzheimer's disease, amyloid deposits has also been shown in diseases such as Mediterranean fever, Muckle-Wells syndrome, idiopathetic myeloma, amyloid polyneuropathy, amyloid cardiomyopathy, systemic senile amyloidosis, amyloid polyneuropathy, hereditary cerebral hemorrhage with amyloidosis, Down's syndrome, Scrapie, Creutzfeldt-Jacob disease, Kum, Gerstamnn-Straussler-Scheinker syndrome, 10 medullary carcinoma of the thyroid, Isolated atrial amyloid, p 2 -microglobulin amyloid in dialysis patients, inclusion body myositis, p 2 -amyloid deposits in muscle wasting disease, and Islets of Langerhans diabetes Type Il insulinoma. The term "heteroatom" is art-recognized and refers to an atom of any element other than carbon or hydrogen. Illustrative heteroatoms include boron, nitrogen, oxygen, 15 phosphorus, sulfur and selenium. The term "alkyl" is art-recognized, and includes saturated aliphatic groups, including straight-chain alkyl groups, branched-chain alkyl groups, cycloalkyl (alicyclic) groups, alkyl substituted cycloalkyl groups, and cycloalkyl substituted alkyl groups. In certain embodiments, a straight chain or branched chain alkyl has about 80 or fewer carbon 20 atoms in its backbone (e.g., C 1
-C
80 for straight chain, C 3
-C
80 for branched chain), and alternatively, about 30 or fewer. Likewise, cycloalkyls have from about 3 to about 10 carbon atoms in their ring structure, and alternatively about 5, 6 or 7 carbons in the ring structure. As used herein, "fluoroalkyl" denotes an alkyl where one or more hydrogens have been replaced with fluorines; "perfluoroallyl" denotes an alkyl where all the 25 hydrogens have been replaced with fluorines. Unless the number of carbons is otherwise specified, "lower alkyl" refers to an alkyl group, as defined above, but having from one to about ten carbons, alternatively from one to about six carbon atoms in its backbone structure. Likewise, "lower alkenyl" and "lower alkynyl" have similar chain lengths. 30 The term "alkylene," is art-recognized, and as used herein, pertains to a bidentate moiety obtained by removing two hydrogen atoms, either both from the same carbon atom, or one from each of two different carbon atoms, of a hydrocarbon compound, which may be - 10 - WO 2009/117728 PCT/US2009/037928 aliphatic or alicyclic, or a combination thereof, and which may be saturated, partially unsaturated, or fully unsaturated. Examples of linear saturated CI_oalkylene groups include, but are not limited to, -(CH 2 )n 1 - where n is an integer from I to 10, for example, CH 2 - (methylene), -CH 2
CH
2 - (ethylene), -CH 2
CH
2
CH
2 - (propylene), -CH 2
CH
2
CH
2
CH
2 5 (butylene), -CH 2
CH
2
CH
2
CH
2
CH
2 - (pentylene) and -CH 2
CH
2
CH
2
CH
2
CH
2
CH
2 - (hexylene). Examples of branched saturated CI_10alkylene groups include, but are not limited to,
-CH(CH
3 )-, -CH(CH 3
)CH
2 -, -CH(CH 3
)CH
2
CH
2 -, -CH(CH 3
)CH
2
CH
2
CH
2 -, CH 2
CH(CH
3
)CH
2 -, -CH 2
CH(CH
3
)CH
2
CH
2 -, -CH(CH 2
CH
3 )-, -CH(CH 2
CH
3
)CH
2 -, and CH 2
CH(CH
2
CH
3
)CH
2 -. Examples of linear partially unsaturated C1I10alkylene groups 10 include, but are not limited to,-CH=CH- (vinylene), -CH=CH-CH 2 -, -CH=CH-CH 2
-CH
2 -, CH=CH-CH 2
-CH
2
-CH
2 -, -CH=CH-CH=CH-, -CH=CH-CH=CH-CH 2 -, -CH=CH-CH=CH
CH
2
-CH
2 -, -CH=CH-CH 2 -CH=CH-, and -CH=CH-CH 2
-CH
2 -CH=CH-. Examples of branched partially unsaturated CI_oalkylene groups include, but are not limited to,
-C(CH
3 )=CH-, -C(CH 3
)=CH-CH
2 -, and -CH=CH-CH(CH 3 )-. Examples of alicyclic 15 saturated CI_10alkylene groups include, but are not limited to, cyclopentylene (e.g., cyclopent-1,3-ylene), and cyclohexylene (e.g., cyclohex-1,4-ylene). Examples of alicyclic partially unsaturated CI_10alkylene groups include, but are not limited to, cyclopentenylene (e.g., 4-cyclopenten-1,3-ylene), and cyclohexenylene (e.g., 2-cyclohexen-1,4-ylene, 3 cyclohexen-1,2-ylene, and 2,5-cyclohexadien-1,4-ylene). 20 The term "aralkyl" is art-recognized and refers to an alkyl group substituted with an aryl group (e.g., an aromatic or heteroaromatic group). The terms "alkenyl" and "alkynyl" are art-recognized and refer to unsaturated aliphatic groups analogous in length and possible substitution to the alkyls described above, but that contain at least one double or triple bond respectively. 25 The term "aryl" is art-recognized and refers to 5-, 6- and 7-membered single-ring aromatic groups that may include from zero to four heteroatoms, for example, benzene, naphthalene, anthracene, pyrene, pyrrole, furan, thiophene, imidazole, oxazole, thiazole, triazole, pyrazole, pyridine, pyrazine, pyridazine and pyrimidine, and the like. Those aryl groups having heteroatoms in the ring structure may also be referred to as "aryl 30 heterocycles" or "heteroaromatics." The aromatic ring may be substituted at one or more ring positions with such substituents as described herein, for example, halogen, azide, alkyl, aralkyl, alkenyl, alkynyl, cycloalkyl, hydroxyl, alkoxyl, amino, nitro, sulfhydryl, imino, amido, phosphonate, phosphinate, carbonyl, carboxyl, silyl, alkylthio, sulfonyl, - 11 - WO 2009/117728 PCT/US2009/037928 sulfonamido, ketone, aldehyde, ester, heterocyclyl, aromatic or heteroaromatic moieties, trifluoromethyl, cyano, or the like. The term "aryl" also includes polycyclic ring systems having two or more cyclic rings in which two or more carbons are common to two adjoining rings (the rings are "fused rings") wherein at least one of the rings is aromatic, 5 e.g., the other cyclic rings may be cycloalkyls, cycloalkenyls, cycloalkynyls, aryls and/or heterocyclyls. The terms ortho, meta and para are art-recognized and refer to 1,2-, 1,3- and 1,4 disubstituted benzenes, respectively. For example, the names 1,2-dimethylbenzene and ortho-dimethylbenzene are synonymous. 10 The terms "heterocyclyl", "heteroaryl", or "heterocyclic group" are art-recognized and refer to 3- to about 1 0-membered ring structures, alternatively 3- to about 7-membered rings, whose ring structures include one to four heteroatoms. Heterocycles may also be polycycles. Heterocyclyl groups include, for example, thiophene, thianthrene, furan, pyran, isobenzofuran, chromene, xanthene, phenoxanthene, pyrrole, imidazole, pyrazole, 15 isothiazole, isoxazole, pyridine, pyrazine, pyrimidine, pyridazine, indolizine, isoindole, indole, indazole, purine, quinolizine, isoquinoline, quinoline, phthalazine, naphthyridine, quinoxaline, quinazoline, cinnoline, pteridine, carbazole, carboline, phenanthridine, acridine, pyrimidine, phenanthroline, phenazine, phenarsazine, phenothiazine, furazan, phenoxazine, pyrrolidine, oxolane, thiolane, oxazole, piperidine, piperazine, morpholine, 20 lactones, lactams such as azetidinones and pyrrolidinones, sultams, sultones, and the like. The heterocyclic ring may be substituted at one or more positions with such substituents as described above, as for example, halogen, alkyl, aralkyl, alkenyl, alkynyl, cycloalkyl, hydroxyl, amino, nitro, sulfhydryl, imino, amido, phosphonate, phosphinate, carbonyl, carboxyl, silyl, alkylthio, sulfonyl, ketone, aldehyde, ester, a heterocyclyl, an aromatic or 25 heteroaromatic moiety, trifluoromethyl, cyano, or the like. The term "nitro" is art-recognized and refers to -NO 2 ; the term "halo" or "halogen" is art-recognized and refers to -F, -Cl, -Br or -I, and as used herein also refers to radioactive forms thereof, such as 18F, 76Br, 7Br, m 12 4 j and 1251; the term "sulfhydryl" is art recognized and refers to -SH; the term "hydroxyl" means -OH; and the term "sulfonyl" is 30 art-recognized and refers to -S0 2 _. The terms "amine" and "amino" are art-recognized and refer to both unsubstituted and substituted amines, e.g., a moiety that may be represented by the general formulas: - 12 - WO 2009/117728 PCT/US2009/037928 R50 R50 N N- R53 R51 R52 wherein R50, R5 1, R52 and R53 each independently represent a hydrogen, an alkyl, an alkenyl, -(CH 2 )m-R61, or R50 and R51 or R52, taken together with the N atom to which they are attached complete a heterocycle having from 4 to 8 atoms in the ring structure; R61 5 represents an aryl, a cycloalkyl, a cycloalkenyl, a heterocycle or a polycycle; and m is zero or an integer in the range of 1 to 8. In other embodiments, R50 and R51 (and optionally R52) each independently represent a hydrogen, an alkyl, an alkenyl, or -(CH 2 )m-R61. Thus, the term "alkylamine" includes an amine group, as defined above, having a substituted or unsubstituted alkyl attached thereto, i.e., at least one of R50 and R51 is an alkyl group. 10 The term "acylamino" is art-recognized and refers to a moiety that may be represented by the general formula: 0 -N- R54 R50 wherein R50 is as defined above, and R54 represents a hydrogen, an alkyl, an alkenyl or
-(CH
2 )m-R61, where m and R61 are as defined above. 15 The term "amido" is art recognized as an amino-substituted carbonyl and includes a moiety that may be represented by the general formula: 0 R51 R50 wherein R50 and R51 are as defined above. Certain embodiments of the amide in the present invention will not include imides which may be unstable. 20 The term "alkylthio" refers to an alkyl group, as defined above, having a sulfur radical attached thereto. In certain embodiments, the "alkylthio" moiety is represented by - 13 - WO 2009/117728 PCT/US2009/037928 one of -S-alkyl, -S-alkenyl, -S-alkynyl, and -S-(CH 2 )m-R61, wherein m and R61 are defined above. Representative alkylthio groups include methylthio, ethyl thio, and the like. The term "carboxyl" is art recognized and includes such moieties as may be represented by the general formulas: 0 0 5 X50 R55 X50 R56 wherein X50 is a bond or represents an oxygen or a sulfur, and R55 and R56 represents a hydrogen, an alkyl, an alkenyl, -(CH 2 )m-R61or a pharmaceutically acceptable salt, R56 represents a hydrogen, an alkyl, an alkenyl or -(CH 2 )m-R61, where m and R61 are defined above. Where X50 is an oxygen and R55 or R56 is not hydrogen, the formula represents an 10 "ester". Where X50 is an oxygen, and R55 is as defined above, the moiety is referred to herein as a carboxyl group, and particularyl when R55 is a hydrogen, the formula represents a "carboxylic acid". Where X50 is an oxygen, and R56 is hydrogen, the formula represents a "formate". In general, where the oxygen atom of the above formula is replaced by sulfur, the formula represents a "thiolcarbonyl" group. Where X50 is a sulfur and R55 or R56 is 15 not hydrogen, the formula represents a "thiolester." Where X50 is a sulfur and R55 is hydrogen, the formula represents a "thiolcarboxylic acid." Where X50 is a sulfur and R56 is hydrogen, the formula represents a "thiolformate." On the other hand, where X50 is a bond, and R55 is not hydrogen, the above formula represents a "ketone" group. Where X50 is a bond, and R55 is hydrogen, the above formula represents an aldehydee" group. 20 The term "carbamoyl" refers to -O(C=O)NRR', where R and R' are independently H, aliphatic groups, aryl groups or heteroaryl groups. The term "oxo" refers to a carbonyl oxygen (=0). The terms "oxime" and "oxime ether" are art-recognized and refer to moieties that may be represented by the general formula: OR N 25 R75 - 14 - WO 2009/117728 PCT/US2009/037928 wherein R75 is hydrogen, alkyl, cycloalkyl, alkenyl, alkynyl, aryl, aralkyl, or -(CH 2 )m-R61. The moiety is an "oxime" when R is H; and it is an "oxime ether" when R is alkyl, cycloalkyl, alkenyl, alkynyl, aryl, aralkyl, or -(CH 2 )m-R61. The terms "alkoxyl" or "alkoxy" are art-recognized and refer to an alkyl group, as 5 defined above, having an oxygen radical attached thereto. Representative alkoxyl groups include methoxy, ethoxy, propyloxy, tert-butoxy and the like. An "ether" is two hydrocarbons covalently linked by an oxygen. Accordingly, the substituent of an alkyl that renders that alkyl an ether is or resembles an alkoxyl, such as may be represented by one of -0-alkyl, -0-alkenyl, -0-alkynyl, -0-(CH 2 )m-R61, where m and R61 are described above. 10 The term "sulfonate" is art recognized and refers to a moiety that may be represented by the general formula: O || S-OR57 0 in which R57 is an electron pair, hydrogen, alkyl, cycloalkyl, or aryl. The term "sulfate" is art recognized and includes a moiety that may be represented 15 by the general formula: O 0-S-OR57 II 0 in which R57 is as defined above. The term "sulfonamido" is art recognized and includes a moiety that may be represented by the general formula: O N-S-OR56 I 1 20 R50 0 in which R50 and R56 are as defined above. - 15 - WO 2009/117728 PCT/US2009/037928 The term "sulfamoyl" is art-recognized and refers to a moiety that may be represented by the general formula: 0 || R50 _S--N || IR51 0 in which R50 and R51 are as defined above. 5 The term "sulfonyl" is art-recognized and refers to a moiety that may be represented by the general formula: 0 S--R58 0 in which R58 is one of the following: hydrogen, alkyl, alkenyl, alkynyl, cycloalkyl, heterocyclyl, aryl or heteroaryl. 10 The term "sulfoxido" is art-recognized and refers to a moiety that may be represented by the general formula: 0 S R58 in which R58 is defined above. The term "phosphoryl" is art-recognized and may in general be represented by the 15 formula: Q50 OR59 wherein Q50 represents S or 0, and R59 represents hydrogen, a lower alkyl or an aryl. When used to substitute, e.g., an alkyl, the phosphoryl group of the phosphorylalkyl may be represented by the general formulas: - 16 - WO 2009/117728 PCT/US2009/037928 Q50 Q50 -Q51-p -Q51-p-R59 OR59 OR59 wherein Q50 and R59, each independently, are defined above, and Q51 represents 0, S or N. When Q50 is S, the phosphory moiety is a "phosphorothioate". The term "phosphoramidite" is art-recognized and may be represented in the general 5 formulas: 0 O -Q51---o -Q51-P-OR59 | | R50 R51 R50 R51 wherein Q51, R50, R5 1 and R59 are as defined above. The term "phosphonamidite" is art-recognized and may be represented in the general formulas: R60 R60 -Q51-P1-- -Q51-p-R59 N N / ?14\ /' \ 10 R50 R51 R50 R51 wherein Q51, R50, R5 1 and R59 are as defined above, and R60 represents a lower alkyl or an aryl. Analogous substitutions may be made to alkenyl and alkynyl groups to produce, for example, aminoalkenyls, aminoalkynyls, amidoalkenyls, amidoalkynyls, iminoalkenyls, 15 iminoalkynyls, thioalkenyls, thioalkynyls, carbonyl-substituted alkenyls or alkynyls. The term "selenoalkyl" is art-recognized and refers to an alkyl group having a substituted seleno group attached thereto. Exemplary "selenoethers" which may be substituted on the alkyl are selected from one of -Se-alkyl, -Se-alkenyl, -Se-alkynyl, and Se-(CH 2 )m-R61, m and R61 being defined above. - 17 - WO 2009/117728 PCT/US2009/037928 The terms triflyl, tosyl, mesyl, and nonaflyl are art-recognized and refer to trifluoromethanesulfonyl, p-toluenesulfonyl, methanesulfonyl, and nonafluorobutanesulfonyl groups, respectively. The terms triflate, tosylate, mesylate, and nonaflate are art-recognized and refer to trifluoromethanesulfonate ester, p-toluenesulfonate 5 ester, methanesulfonate ester, and nonafluorobutanesulfonate ester functional groups and molecules that contain said groups, respectively. The definition of each expression, e.g., alkyl, m, n, and the like, when it occurs more than once in any structure, is intended to be independent of its definition elsewhere in the same structure. 10 The abbreviations Me, Et, Ph, Tf, Nf, Ts, and Ms represent methyl, ethyl, phenyl, trifluoromethanesulfonyl, nonafluorobutanesulfonyl, p-toluenesulfonyl and methanesulfonyl, respectively. A more comprehensive list of the abbreviations utilized by organic chemists of ordinary skill in the art appears in the first issue of each volume of the Journal of Organic Chemistry; this list is typically presented in a table entitled Standard List 15 of Abbreviations. Certain compounds contained in compositions of the present invention may exist in particular geometric or stereoisomeric forms. In addition, polymers of the present invention may also be optically active. The present invention contemplates all such compounds, including cis- and trans-isomers, R- and S-enantiomers, diastereomers, (D)-isomers, (L) 20 isomers, the racemic mixtures thereof, and other mixtures thereof, as falling within the scope of the invention. Additional asymmetric carbon atoms may be present in a substituent such as an alkyl group. All such isomers, as well as mixtures thereof, are intended to be included in this invention. If, for instance, a particular enantiomer of compound of the present invention is 25 desired, it may be prepared by asymmetric synthesis, or by derivation with a chiral auxiliary, where the resulting diastereomeric mixture is separated and the auxiliary group cleaved to provide the pure desired enantiomers. Alternatively, where the molecule contains a basic functional group, such as amino, or an acidic functional group, such as carboxyl, diastereomeric salts are formed with an appropriate optically-active acid or base, followed 30 by resolution of the diastereomers thus formed by fractional crystallization or chromatographic means well known in the art, and subsequent recovery of the pure enantiomers. - 18 - WO 2009/117728 PCT/US2009/037928 It will be understood that "substitution" or "substituted with" includes the implicit proviso that such substitution is in accordance with permitted valence of the substituted atom and the substituent, and that the substitution results in a stable compound, e.g., which does not spontaneously undergo transformation such as by rearrangement, cyclization, 5 elimination, or other reaction. The term "substituted" is also contemplated to include all permissible substituents of organic compounds. In a broad aspect, the permissible substituents include acyclic and cyclic, branched and unbranched, carbocyclic and heterocyclic, aromatic and nonaromatic substituents of organic compounds. Illustrative substituents include, for example, those 10 described herein above. The permissible substituents may be one or more and the same or different for appropriate organic compounds. For purposes of this invention, the heteroatoms such as nitrogen may have hydrogen substituents and/or any permissible substituents of organic compounds described herein which satisfy the valences of the heteroatoms. This invention is not intended to be limited in any manner by the permissible 15 substituents of organic compounds. For purposes of this invention, the chemical elements are identified in accordance with the Periodic Table of the Elements, CAS version, "Handbook of Chemistry and Physics", 67th Ed., 1986-87, inside cover. As used herein, the term "subject" or "individual" refers to a human or other 20 vertebrate animal. It is intended that the term encompass "patients." As used herein, a "combination" of two compounds indicates one compound wherein the two compounds have been linked by a cross linker. For example, examples of combinations between 2,8-diazaspiro[4,5]decane-1,3-diones and inositol are shown in Figure 5. 25 The term "diagnosis" as used herein refers to methods by which the skilled artisan can estimate and/or determine whether or not a patient is suffering from a given disease or condition. The skilled artisan often makes a diagnosis on the basis of one or more diagnostic indicators, i.e., a marker, the presence, absence, amount, or change in amount of which is indicative of the presence, severity, or absence of the condition. 30 The kit may also include at least one chelating structure and/or an auxillary molecule such as mannitol, gluconate, glucoheptonate and tartrate and a tin containing reducing agent. - 19 - WO 2009/117728 PCT/US2009/037928 The term "conjugated" refers to ionically or covalently attached (e.g., via a crosslinking agent). A "chelating structure" refers to any molecule or complex of molecules that bind to a metal as well as the structure bound to a metal. In some embodiments, the metal can be 5 radioactive (such as 9 9 mTc, 6 8 Cu, 64 Cu and 68 Ga). Examples of chelating structures include
N
2
S
2 structure, a HYNIC (hydrazinonicotinic acid) group-containing structure, a 2 methylthiolnicotinic acid groupcontaining structure, a carboxylate group-containing structure and the like. Additional discussion of chelating structures is below. A "radioimaging agent" refers to a composition capable of generating a detectable 18 76 '77 10 image upon binding with a target and shall include radionuclides such as 1 F, Br, Br, 123 1,124 1 25 1,99mTC 68C 64Can G m, I4 99mIc, 8Cu, 4Cu and 68 Ga. A "fluorescence imaging agent" refers to a composition capable of generating a detectable optical imaging upon binding with a target with or without specific wave length of light activation and shall include fluorophores. The preferred fluorescence agents are 15 near infra red light absorbing agents. A "target" refers to an in vivo site to which imaging compounds binds. A preferred target is a brain tissue from a subject suffering from AD or an amyloidosis-associated pathological condition. A "targeting molecule" is any molecule or biological entity that specifically 20 accumulates in brain tissue from a subject suffering from AD or an amyloidosis-associated pathological condition. Radioimaging methods that may be employed in accordance with the present inventions are known in the art. See Patent No. 6,187,286 and U.S. Patent Publication No. 2006/0140859; both of which are hereby incorporated by reference. 25 In accordance with the invention, the targeting molecule is in association with (spatial proximity to) the radionuclide. Spatial proximity between the targeting molecule and the radionuclide may be effected in any manner which preserves the specificity of the targeting molecule for its target tissue. For example, spatial proximity between the radionuclide and the targeting molecule may be effected by a covalent or non-covalent 30 chemical bond. Such a chemical bond may be effected through a chelating substance and/or an auxiliary molecule such as mannitol, gluconate, glucoheptonate, tartrate, and the like. - 20 - WO 2009/117728 PCT/US2009/037928 Alternatively, spatial proximity between the nuclide and the targeting molecule may be effected by incorporating the radionuclide and the targeting molecule in a micelle or liposome, in such a way that the affinity of the targeting molecule for its target tissue is maintained. Spatial proximity between the radionuclide and the targeting molecule may 5 also be effected by attaching the radionuclide and the targeting molecule to a matrix such, as a microsphere or liposomes. A radionuclide may be incorporated into the imaging agent by covalent bonding directly to an atom of the targeting molecule, or the radionuclide may be noncovalently or covalently associated with the targeting molecule through a chelating structure or through 10 an auxiliary molecule such as mannitol, gluconate, glucoheptonate, tartrate, and the like. When a chelating structure is used to provide spatial proximity between the radionuclide and the targeting molecule, the chelating structure may be directly associated with the targeting molecule or it may be associated with the targeting molecule through an auxiliary molecule such as mannitol, gluconate, glucoheptonate, tartrate, and the like. 15 Any suitable chelating structure may be used to provide spatial proximity between the radionuclide and the targeting molecule of the agent through covalent or noncovalent association. Many such chelating structures are known in the art. Preferably, the chelating structure is an N 2
S
2 structure, an NS 3 structure, an N 4 structure, an isonitrilecontaining structure, a hydrazine containing structure, a HYNIC (hydrazinonicotinic acid) group 20 containing structure, a 2-methylthiolnicotinic acid group-containing structure, a carboxylate group containing structure, and the like. In some cases, chelation can be achieved without including a separate chelating structure, because the radionuclide chelates directly to atom(s) in the targeting moiety, for example to oxygen atoms in the phosphate group(s) or in carboxylate group(s). 25 The chelating structure, auxiliary molecule, or radionuclide may be placed in spatial proximity to any position of the targeting molecule which does not interfere with the interaction of the targeting molecule with its receptor in tumors. The chelating structure, auxiliary molecule, or radionuclide may be covalently or non-covalently associated with any moiety of the targeting molecule except the receptor-binding moiety. For example, the 30 chelating structure, auxiliary molecule, or radionuclide may be associated with the phosphate moiety of the targeting molecule, with the --X-- moiety of the targeting molecule. - 21 - WO 2009/117728 PCT/US2009/037928 After the labeling reaction is complete, the reaction mixture may optionally be purified using one or more high performance liquid chromatography (HPLC) steps. Any suitable HPLC system may be used if a purification step is performed, and the yield of imaging agent obtained from the HPLC step may be optimized by varying the parameters of 5 the HPLC system, as is known in the art. Any HPLC parameter may be varied to optimize the yield of the imaging agent of the invention. For example, the pH may be varied, e.g., raised, to decrease the elution time of the peak corresponding to the imaging agent of the invention. The invention as embodied in a kit for radioimaging comprises a radioimaging agent 10 described above, in combination with a pharmaceutically acceptable carrier such as human serum albumin. Human serum albumin for use in the kit of the invention may be made in any way, for example, through purification of the protein from human serum or though recombinant expression of a vector containing a gene encoding human serum albumin. Other substances may also be used as carriers in accordance with this embodiment of the 15 invention, for example, detergents, dilute alcohols, carbohydrates, auxiliary molecules, and the like. The kit of the invention may of course also contain such other items as may facilitate its use, such as syringes, instructions, reaction vials, and the like. In one embodiment, a kit according to the invention contains from about 1 to about 30 mCi of the radionuclide-labeled amyloid imaging agent described herein, in combination 20 with a pharmaceutically-acceptable carrier. The amyloid imaging agent and carrier may be provided in solution or in lyophilized form. When the amyloid imaging agent and carrier of the kit are in lyophilized form, the kit may optionally contain a sterile and physiologically acceptable reconstitution medium such as water, saline, buffered saline, and the like. The radioimaging agents of the invention may be used in accordance with the 25 methods of the invention by those of skill in the art, e.g., by specialists in nuclear medicine, to image tissue in a mammal. Any mammalian tumor may be imaged the imaging agents of the invention. Images are generated by virtue of differences in the spatial distribution of the imaging agents which accumulate in the various tissues and organs of the mammal. The spatial distribution of the imaging agent accumulated in a mammal, in an organ, or in a 30 tissue may be measured using any suitable means, for example, a PET or single photon emission computer tomography (SPECT) imaging camera apparatus, and the like. - 22 - WO 2009/117728 PCT/US2009/037928 PET imaging is accomplished with the aid of tracer compounds labeled with a positron-emitting isotope (Goodman, M. M. Clinical Positron Emission Tomography, Mosby Yearbook, 1992, K. F. Hubner et al., Chapter 14). These tracer compounds can be labeled with a positron-emitting radionuclide that includes 1 8 F and 76 Br. In general, a PET 5 label, is a label which is covalently attached to the remainder of a molecule and should have a half life of at least about 5-20 minutes, preferably about 60 minutes or more. Examples of 18 13 76 7 PET labels include F, N, Br (half life = 16.1 hrs), 77 Br, 150, 68 Ga (half life = 68.3 min), 6 2 Cu (half life = 9.74 min), 64 Cu (half life = 12.7 hrs), 82 Rb (half life = 78 sec), and 24I (half life = 4.18 days) 10 The use of 18 F-labeled compounds in PET has thus far been limited to a few analog compounds. Most notably, 18-fluorodeoxyglucose has been widely used in studies of glucose metabolism and localization of glucose uptake associated with brain activity. More recently, other analogs, such as ' 8 F-methyl choline (for prostate cancers; see Cancer Res. 2001, 6, 110), 18 F-fluorothymidine (for lung tumors; see J. Nucl. Med. 2003, 44, 1426; and 15 Eur. J. Nuc. Mol. Imaging 2003, 30, 1407) and O-(2- [ 18 F]fluoroethyl)-L-tyrosine (U.S. Patent No. 7,138,540; hereby incorporated by reference), have also been employed in PET imaging. For examples of 18 F-labeling imaging agents see: Eur. J. Med. Chem. 1994, 29, 115; Eur. J. Med. Chem. 1994, 29, 955; J. Heterocyclic Chem. 1993, 30, 1337; Organic Process Research & Development 2005, 9(6), 774; J. Med. Chem. 2005, 48(16), 5290; J. 20 Med. Chem. 1990, 33, 1482; Nuclear Medicine and Biology 2001, 28(6), 683; and Nuclear Medicine and Biology 2004, 31(4), 483. For SPECT imaging, the inventive compound can be labeled with a y-emitting nuclide, such as, 99 mTC, In, 67Ga, 20 1 T1, , 33Xe and others. For fluorescence tomography imaging, the inventive compound can be conjugated 25 to a near infra red moiety, such as CY5 (Cyanine dye). Fluorescence tomography is under development. The imaging agents of the instant invention are used in the following manner. An effective amount of an imaging agent comprising at least one targeting molecule and a nuclide (from 1 to 50 mCi) may be combined with a pharmaceutically-acceptable carrier for 30 use in imaging studies. In accordance with the invention, "an effective amount" of the imaging agent of the invention is defined as an amount sufficient to yield an acceptable image using equipment which is available for clinical use. An effective amount of the - 23 - WO 2009/117728 PCT/US2009/037928 imaging agent of the invention may be administered in more than one injection. Effective amounts of the imaging agent of the invention will vary according to factors such as the degree of susceptibility of the individual, the age, sex, and weight of the individual, idiosyncratic responses of the individual, and the dosimetry. Effective amounts of the 5 imaging agent of the invention will also vary according to instrument and film-related factors. Optimization of such factors is well within the level of skill in the art. As used herein, "pharmaceutically-acceptable carrier" includes any and all solvents, dispersion media, coatings, antibacterial and antifungal agents, isotonic agents, absorption delaying agents, and the like. Pharmaceutically-acceptable carriers are materials, useful for 10 the purpose of administering the compounds in the method of the present invention, which are preferably non-toxic, and may be solid, liquid, or gaseous materials, which are otherwise inert and pharmaceutically acceptable, and are compatible with the compounds of the present invention. Examples of such carriers include oils such as corn oil, buffers such as PBS, saline, polyethylene glycol, glycerin, polypropylene glycol, dimethylsulfoxide, an 15 amide such as dimethylacetamide, a protein such as albumin, and a detergent such as Tween 80, mono- and oligopolysaccharides such as glucose, lactose, cyclodextrins and starch. The formulation used in the present invention may also contain stabilizers, preservatives, buffers, antioxidants, or other additives known to those of skill in the art. The 20 use of such media and agents for pharmaceutically-active substances is well known in the art. Supplementary active compounds can also be incorporated into the imaging agent of the invention. The imaging agent of the invention may further be administered to an individual in an appropriate diluent or adjuvant, co-administered with enzyme inhibitors or in an appropriate carrier such as human serum albumin or liposomes. Pharmaceutically 25 acceptable diluents include sterile saline and other aqueous buffer solutions. Adjuvants contemplated herein include resorcinols, non-ionic surfactants such as polyoxyethylene oleyl ether and n-hexadecyl polyethylene ether. Enzyme inhibitors include pancreatic trypsin inhibitor, diethylpyrocarbonate, and trasylol. Liposomes inhibitors include water-in oil-in-water CGF emulsions, as well as conventional liposomes (see J Neuroimmunol. 30 1984, 7, 27). As described herein, certain embodiments of the present compounds may contain a basic functional group, such as amino or alkylamino, and are, thus, capable of forming pharmaceutically-acceptable salts with pharmaceutically-acceptable acids. The term - 24 - WO 2009/117728 PCT/US2009/037928 "pharmaceutically-acceptable salts" in this respect, refers to the relatively non-toxic, inorganic and organic acid addition salts of compounds of the present invention. These salts can be prepared in situ in the administration vehicle or the dosage form manufacturing process, or by separately reacting a purified compound of the invention in its free base form 5 with a suitable organic or inorganic acid, and isolating the salt thus formed during subsequent purification. Representative salts include the hydrobromide, hydrochloride, sulfate, bisulfate, phosphate, nitrate, acetate, valerate, oleate, palmitate, stearate, laurate, benzoate, lactate, phosphate, tosylate, citrate, maleate, fumarate, succinate, tartrate, napthylate, mesylate, glucoheptonate, lactobionate, and laurylsulphonate salts and the like. 10 See J. Pharm. Sci. 1977, 66, 1-19. The pharmaceutically acceptable salts of the subject compounds include the conventional nontoxic salts or quaternary ammonium salts of the compounds, e.g., from non-toxic organic or inorganic acids. For example, such conventional nontoxic salts include those derived from inorganic acids such as hydrochloride, hydrobromic, sulfuric, 15 sulfamic, phosphoric, nitric, and the like; and the salts prepared from organic acids such as acetic, propionic, succinic, glycolic, stearic, lactic, malic, tartaric, citric, ascorbic, palmitic, maleic, hydroxymaleic, phenylacetic, glutamic, benzoic, salicyclic, sulfanilic, 2 acetoxybenzoic, fumaric, toluenesulfonic, methanesulfonic, ethane disulfonic, oxalic, isothionic, and the like. 20 In other cases, the compounds of the present invention may contain one or more acidic functional groups and, thus, are capable of forming pharmaceutically-acceptable salts with pharmaceutically-acceptable bases. The term "pharmaceutically-acceptable salts" in these instances refers to the relatively non-toxic, inorganic and organic base addition salts of compounds of the present invention. These salts can likewise be prepared in situ in the 25 administration vehicle or the dosage form manufacturing process, or by separately reacting the purified compound in its free acid form with a suitable base, such as the hydroxide, carbonate or bicarbonate of a pharmaceutically-acceptable metal cation, with ammonia, or with a pharmaceutically-acceptable organic primary, secondary or tertiary amine. Representative alkali or alkaline earth salts include the lithium, sodium, potassium, 30 calcium, magnesium, and aluminum salts and the like. Representative organic amines useful for the formation of base addition salts include ethylamine, diethylamine, ethylenediamine, ethanolamine, diethanolamine, piperazine and the like. (See, for example, J. Pham. Sci. 1977., supra) - 25 - WO 2009/117728 PCT/US2009/037928 Preferably, the imaging agent of the present invention is administered intravenously, and the imaging agent will be formulated as a sterile, pyrogen-free, parenterally-acceptable aqueous solution. The preparation of such parenterally-acceptable solutions, having due regard to pH, isotonicity, stability, and the like, is within the skill in the art. A preferred 5 formulation for intravenous injection should contain, in addition to the imaging agent, an isotonic vehicle such as Sodium Chloride Injection, Ringer's Injection, Dextrose Injection, Dextrose and Sodium Chloride Injection, Lactated Ringer's Injection, or other vehicle as known in the art. The amount of imaging agent used for diagnostic purposes and the duration of the 10 imaging study will depend upon the nature and severity of the condition being treated, on the nature of therapeutic treatments which the patient has undergone, and on the idiosyncratic responses of the patient. Ultimately, the attending physician will decide the amount of imaging agent to administer to each individual patient and the duration of the imaging study. 15 The diagnostic imaging amounts are preferably about 3 to 15 millicuries (mCi) for a 70 kg normal adult, more preferably being about 1 - 25 mCi for a 70 kg normal adult. The ultimate solution form is preferably sterile. Sterilization can be accomplished by any art recognized technique, including but not limited to, addition of antibacterial of antifungal agents, for example, paraben, chlorobutanol, phenol, sorbic acid, thimerosal, and 20 the like. More specifically, the compounds that can be formulated into a pharmaceutical composition include a therapeutically-effective amount of the compound and a pharmaceutically-acceptable carrier. The therapeutically-effective amount of the compound and the specific pharmaceutically-acceptable carrier will vary depending upon, e.g., the age, 25 weight, sex of the subject, the mode of administration, and the type of viral condition being treated. In a particular aspect, the pharmaceutical composition which can be used includes the compounds of the present invention in effective unit dosage form. As used herein, the term "effective unit dosage" or "effective unit dose" is used herein to mean a predetermined 30 amount sufficient to be effective against AD or the like. The pharmaceutical compositions may contain the compound used in the method of this invention in an amount of from 0.01 to 99% by weight of the total composition, - 26 - WO 2009/117728 PCT/US2009/037928 preferably 0.1 to 80% by weight of the total composition. For oral administration, the compound is generally administered in an amount of 0.1 g/body to 15 g/body, preferably 0.5 g/body to 5 g/body. For intravenous injection, the dose may be about 0.1 to about 30 mg/kg/day, preferably about 0.5 to about 10 mg/kg/day. If applied topically as a liquid, 5 ointment, or cream, the compound may be present in an amount of about 0.1 to about 50 mg/mL, preferably about 0.5 to 30 mg/mL of the composition. Fluorescence agents will be administered in several jig/kg to several mg/kg. For example, 1-10 mg/kg. When the compounds according to the invention are formulated for injection, the dose may be presented in unit dose form in ampoules or in multi-dose containers with 10 added pharmaceutically-acceptable adjuvants such as a preservative. In addition, the compositions may take forms such as suspensions, solutions, or emulsions in oily or aqueous vehicles, and may contain formulating agents, such as suspending, stabilizing, or dispersing agents, isotonic agents and/or dissolving co-solvents conventionally cited in the pharmaceutical art. 15 For systemic administration, the daily dosage as employed for adult human treatment will range from about 0.1 mg/kg to about 150 mg/kg, preferably about 0.2 mg/kg to about 80 mg/kg. One aspect of the invention relates to a compound, or a pharmaceutically acceptable salt thereof, represented by formula I:
[C(R)
2 ]m X L-N [C(R')2 N R2 20 X wherein, independently for each occurrence, X is -0- or -S-; Y is -0-, -S-, -C(R) 2 -,- N(R 5 )- or -N[(C=0)R']-; 25 L is -R3, -C(=O)R 3 , -C(=O)[C(R) 2 ]pR 3 , -C(=0)[C(R) 2 ]pC(=O)R 3 , -[C(RI)2]pC(=0)R3, -[C(R')2]pR3, -[C1_10alkylene]R3, -C(=0)[C1_10alkylene]R3, -[C1_ ioalkylene]C(=O)R 3 , -C(=O)[C1_1oalkylene]C(=O)R 3 , an unsubstituted alkyl, or alkyl - 27 - WO 2009/117728 PCT/US2009/037928 substituted with one or more substituents selected from the group consisting of halo, azido, hydroxy, alkoxy, aryloxy, heteroaryloxy, amino, alkylamino, arylamino, acylamino, heteroarylamino, nitro, sulfhydryl, imino, amido, phosphonate, phosphinate, oxycarbonyl, acyloxy, silyl, thioether, sulfo, sulfonate, sulfonyl, sulfonamido, formyl, cyano, isocyano, 5 (C(R) 2 )qC(R) 3 or a chelating structure;
R
1 is hydrogen, halo, azido, alkyl, haloalkyl, perhaloalkyl, fluoroalkyl, perfluoroalkyl, aralkyl, alkenyl, alkynyl, cycloalkyl, heterocyclyl, aryl, heteroaryl, aralkyl, heteroaralkyl, hydroxy, alkoxy, aryloxy, heteroaryloxy, aralkyloxy, heteroaralkyloxy, amino, alkylamino, arylamino, acylamino, heteroarylamino, nitro, sulfhydryl, imino, amido, 10 phosphonate, phosphinate, acyl, carboxyl, oxycarbonyl, acyloxy, silyl, thioether, sulfo, sulfonate, sulfonyl, sulfonamido, formyl, cyano, isocyano or a chelating structure;
R
2 is -R, -C(=O)R 3 , -C(=O)[C(R) 2 ]pR 3 , -C(=O)[C(R) 2 ]pC(=O)R, -[C(RI)2]pC(=0)R', -[C(R')2],RW, -[C1_10alkylene]R3, -C(=0)[C1_10alkylene]R3, -[C1_ ioalkylene]C(=O)R 3 , -C(=O)[C 1
_
10 alkylene]C(=O)R 3 , an unsubstituted alkyl, or alkyl 15 substituted with one or more substituents selected from the group consisting of halo, azido, hydroxy, alkoxy, aryloxy, heteroaryloxy, amino, alkylamino, arylamino, acylamino, heteroarylamino, nitro, sulfhydryl, imino, amido, phosphonate, phosphinate, oxycarbonyl, acyloxy, silyl, thioether, sulfo, sulfonate, sulfonyl, sulfonamido, formyl, cyano, isocyano, (C(R) 2 )qC(R) 3 or a chelating structure; 20 R 3 is hydrogen, alkyl, heteroalkyl, cycloalkyl, heterocycloalkyl, aryl, heteroaryl, R 4 R 4 R4-0 aralkyl, heteroarakyl, R4 R4 - 28 - WO 2009/117728 PCT/US2009/037928 R 4 R 4 R 4 0- R4 ' 0-- R4 R4 o 0 R4 Rl R4 R1 R R O R 4 R 4 R 4 R4 ' R4 ---- R4 o 0 R4 Rl R4 Rl RI R ,or R 4 R 4 R4 ' R4 0 -- RI
RI
R
4 is hydrogen, halo, azido, alkyl, haloalkyl, perhaloalkyl, fluoroalkyl, 5 perfluoroalkyl, aralkyl, alkenyl, alkynyl, cycloalkyl, heterocyclyl, aryl, heteroaryl, aralkyl, heteroaralkyl, hydroxy, alkoxy, aryloxy, heteroaryloxy, aralkyloxy, heteroaralkyloxy, amino, alkylamino, arylamino, acylamino, heteroarylamino, nitro, sulfhydryl, imino, amido, phosphonate, phosphinate, acyl, carboxyl, oxycarbonyl, acyloxy, silyl, thioether, sulfo, sulfonate, sulfonyl, sulfonamido, formyl, cyano, isocyano, -OR , -SR 5 , -N(R 5
)
2 , 10 (C(R) 2 )qC(R) 3 or a chelating structure; R' is hydrogen, alkyl, heteroalkyl, cycloalkyl, heterocycloalkyl, aryl, heteroaryl, aralkyl, heteroaralkyl, acyl, -(C(RI) 2 )qC(R) 3 or a chelating structure; - 29 - WO 2009/117728 PCT/US2009/037928 m is 1, 2 or 3; n is 1, 2 or 3; m plus n is 3 or 4 p is 1-10 inclusive; and 5 q is 0-10 inclusive; provided that when R 2 is an unsubstituted alkyl, or alkyl substituted with one or more substituents selected from the group consisting of halo, azido, hydroxy, alkoxy, aryloxy, heteroaryloxy, amino, alkylamino, arylamino, acylamino, heteroarylamino, nitro, sulfhydryl, imino, amido, phosphonate, phosphinate, oxycarbonyl, acyloxy, silyl, thioether, 10 sulfo, sulfonate, sulfonyl, sulfonamido, formyl, cyano, isocyano, -(C(R) 2 )qC(R) 3 or a chelating structure, then L is -R 3 , -C(=O)R 3 , -C(=O)[C(R) 2 ]pR 3 , -C(=O)[C(R) 2 ]pC(=O)R 3 , -[C(R')2]pC(=0)R3, -[C(R')2]pR3, -[C1_10alkylene]R3, -C(=0)[C1_10alkylene]R3, -[C1_ ioalkylene]C(=O)R 3 , -C(=O)[C1_1oalkylene]C(=O)R 3 ; and when L is an unsubstituted alkyl, or alkyl substituted with one or more substituents selected from the group consisting of 15 halo, azido, hydroxy, alkoxy, aryloxy, heteroaryloxy, amino, alkylamino, arylamino, acylamino, heteroarylamino, nitro, sulfhydryl, imino, amido, phosphonate, phosphinate, oxycarbonyl, acyloxy, silyl, thioether, sulfo, sulfonate, sulfonyl, sulfonamido, formyl, cyano, isocyano, -(C(R) 2 )qC(RI) 3 or a chelating structure, then R 2 is -R 3 , -C(=O)R 3 , C(=0)[C(R')2]pR3, -C(=0)[C(R')2]pC(=0)R3, -[C(R')2]pC(=0)R3, -[C(R')2]pR3, -[C1_ 20 1oalkylcnc]R 3 , -C(=O)[C1_1oalkylcne]R 3 , -[C1-ioalkylcnc]C(=O)R 3 , -C(=O)[C1ioalkylene]C(=O)R 3 . In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein said compound comprises at least one 18 F, 76 Br, 7 Br, , 124I or 12s. 25 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein said compound comprises at least one 18 F. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein said compound comprises 30 only one chelating structure. - 30 - WO 2009/117728 PCT/US2009/037928 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein said compound comprises only one chelating structure; and 99 mTc, 6 Cu, 64Cu or 6 8 Ga chelated to the chelating structure. 5 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein X is -0-. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein Y is -C(R) 2 -. In certain embodiments, the present invention relates to any one of the 10 aforementioned compounds and attendant definitions, wherein Y is -CH 2 -. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein Y is -0-. For examples of 4 oxa-analogs of the muscarinic agonist 2-ethyl-8-methyl-2,8-diazaspiro[4,5]decane-1,3 dione, see J. Med. Chem. 1993, 36, 2292, which is hereby incorporated by reference. 15 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein R 1 is hydrogen. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein m is 1; and n is 2. In certain embodiments, the present invention relates to any one of the 20 aforementioned compounds and attendant definitions, wherein m is 1; and n is 3. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein m is 2; and n is 2. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein X is -0-; Y is -CH 2 -; R' is 25 hydrogen; m is 2; and n is 2. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein R2 is unsubstituted alkyl. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein R2 is -CH 3 , -CH 2
CH
3 , 30 CH 2
CH
2
CH
3 , or -CH(CH 3
)CH
3 . -31 - WO 2009/117728 PCT/US2009/037928 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein R2 is alkyl substituted with F, -Cl, -Br or -I. In certain embodiments, the present invention relates to any one of the 5 aforementioned compounds and attendant definitions, wherein R2 is alkyl substituted with F. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein R2 is alkyl substituted with 1 8 F. 10 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein R2 is -CH 2
CH
2 18F or CH 2
CH"FCH
3 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein X is -0-; Y is -CH 2 -; R, is 15 hydrogen; m is 2; n is 2; and R2 is alkyl substituted with -F, -Cl, -Br or -I. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein X is -0-; Y is -CH 2 -; R is hydrogen; m is 2; n is 2; and R2 is alkyl substituted with -F. In certain embodiments, the present invention relates to any one of the 20 aforementioned compounds and attendant definitions, wherein X is -0-; Y is -CH 2 -; R1 is hydrogen; m is 2; n is 2; and R2 is alkyl substituted with - 18 F. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein X is -0-; Y is -CH 2 -; R1 is hydrogen; m is 2; n is 2; and R2 is -CH 2
CH
2 18F or -CH 2 CH 18FCH 3 25 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein L is R3. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein L is R3; and R3 is alkyl. In certain embodiments, the present invention relates to any one of the 30 aforementioned compounds and attendant definitions, wherein L is R3; and R3 is -CH 3 . - 32 - WO 2009/117728 PCT/US2009/037928 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein X is -0-; Y is -CH 2 -; R, is hydrogen; m is 2; n is 2; R 2 is alkyl substituted with -F, -Cl, -Br or -I; L is R 3 ; and R 3 is alkyl. 5 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein X is -0-; Y is -CH 2 -; R, is hydrogen; m is 2; n is 2; R 2 is alkyl substituted with -F; L is R 3 ; and R 3 is alkyl. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein X is -0-; Y is -CH 2 -; R, is 10 hydrogen; m is 2; n is 2; R 2 is alkyl substituted with -"F; L is R 3 ; and R 3 is alkyl. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein X is -0-; Y is -CH 2 -; R 1 is hydrogen; m is 2; n is 2; R2 is -CH 2
CH
2 1 F or -CH 2 CH FCH 3 ; L is R 3 ; and R 3 is -CH 3 . One aspect of the invention relates to a fluorinated 2,8-diazaspiro[4,5]decane-1,3 15 dione compound, or pharmaceutically acceptable salt thereof One aspect of the invention relates to a 'RF-fluorinated 2,8-diazaspiro[4,5]decane 1,3-dione compound, or a pharmaceutically acceptable salt thereof One aspect of the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein the compound is [F-18]-N-2-fluoroethyl-2,8 20 diazaspiro[4,5]decane-1,3-dione or [F-18]-N-2-fluoroethyl-2,8-diazaspiro[4,5]decane-1,3 dione. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein L is -C(=0)R 3 , C(=0)[CH 2 ]pR 3 , -C(=O)[CH 2 ]pC(=O)R 3 , or -[CH 2 ]pC(=O)R 3 . 25 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein L is -C(=O)R 3 or
-C(=O)CH
2
CH
2
C(=O)R
3 . - 33 - WO 2009/117728 PCT/US2009/037928 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, R3 is R 4 R 4 R4 * 0 R4 R4. In certain embodiments, the present invention relates to any one of the 5 aforementioned compounds and attendant definitions, R 3 is R 4 R 4 R4 0- R4 R4 ; and R 4 is -H, -F, -Cl, -Br, -I, or -OR5. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, R3 is R 4 R 4 R4 0- R4 R4 ;and R 4 is -OR 5 . 10 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, R3 is R 4 R 4 R4 * 0 R4 R4 ;and R 4 is -OH. - 34 - WO 2009/117728 PCT/US2009/037928 In certain embodiments, the present invention relates to any one of the OH 0 0 OH HO aforementioned compounds and attendant definitions, R 3 is OH , or OH O 0 H OH HO ,0 In certain embodiments, the present invention relates to any one of the 5 aforementioned compounds and attendant definitions, wherein L is -C(=0)R 3 , C(=O)ICH 2 ]pR 3 , -C(=O)[CH 2 ]pC(=O)R 3 , or -[CH 2 ]pC(=O)R 3 ; and R 3 is R 4 R 4 R4 * 0 R4 R4. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein L is -C(=0)R 3 , 10 C(=O)[CH 2 ]pR 3 , -C(=O)[CH 2 ]pC(=O)R 3 , or -[CH 2 ]pC(=O)R 3 ; R3 is R 4 R 4 R4 * 0 R4 R4 ;and R 4 is -OR 5 . - 35 - WO 2009/117728 PCT/US2009/037928 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein L is -C(=0)R 3 ; and R 3 is OH 0| 0 OH HO OH In certain embodiments, the present invention relates to any one of the 5 aforementioned compounds and attendant definitions, wherein L is OH 0FV0KH OH HO
-C(=O)CH
2
CH
2
C(=O)R
3 ; and R 3 is In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein X is -0-; Y is -CH 2 -; R, is hydrogen; m is 2; n is 2; R2 is alkyl substituted with -18F; L is -C(=0)R3, -C(=0)[CH2]pR3 R 4 R 4 R4 0- 10 -C(=O)[CH 2 ]pC(=O)R 3 , or -[CH 2 ]pC(=O)R 3 ; and R 3 is R4 R4 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein X is -0-; Y is -CH 2 -; R 1 is hydrogen; m is 2; n is 2; R2 is alkyl substituted with -18F; L is -C(=0)R3, -C(=0)[CH2]pR3, R 4 R 4 R4 0-
-C(=O)[CH
2 ]pC(=0)R 3 , or -[CH 2 ]pC(=O)R 3 ; R 3 is R4 R4; and R 4 15 is -OR. - 36 - WO 2009/117728 PCT/US2009/037928 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein X is -0-; Y is -CH 2 -; R, is hydrogen; m is 2; n is 2; R2 is -CH 2
CH
2 1 F or -CH 2 CH FCH 3 ; L is -C(=O)R 3 ; and R3 is O H 0| 0 OH HO OH 5 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein X is -0-; Y is -CH 2 -; R, is hydrogen; m is 2; n is 2; R2 is -CH 2
CH
2 "F or -CH 2 CH 1FCH 3 ; and R 3 is OH O 0 H OH HO ,0 In certain embodiments, the present invention relates to any one of the 10 aforementioned compounds and attendant definitions, R 3 is R4 R4 R4 R4 0 R1 - 37 - WO 2009/117728 PCT/US2009/037928 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, R3 is R 4 R 4 R4 ' R4 0 O R and R 4 is -H, -F, -Cl, -Br, -I, or -OR.. In certain embodiments, the present invention relates to any one of the 5 aforementioned compounds and attendant definitions, R 3 is R4 R4 0 R4 R O R1 ;and R is -OR.. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, R 3 is R4 R4 R4 ' R4 0 S 0H O H H ; and R 4 is -OH.. - 38 - WO 2009/117728 PCT/US2009/037928 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, R3 is R 4 R 4 R4 'W 0 S 0H O H H ;Wis -F, -Cl, -Br or -I; and R 4 is -OR. In certain embodiments, the present invention relates to any one of the 5 aforementioned compounds and attendant definitions, R 3 is R4 R4 R4 'W 0 S 0H O H H ;Wis -F; and R 4 is -OR'. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, R 3 is R4 R4 R4 'W 0 S 0H O H H ; W is - 1 8 F; and R 4 is -OH. 10 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein X is -0-; Y is -CH 2 -; R 1 is hydrogen; m is 2; n is 2; R2 is unsubstituted alkyl or alkyl substituted with -F, -Cl, -Br, or - 39 - WO 2009/117728 PCT/US2009/037928 I; L is -C(=O)R 3 , -C(=O)[CH 2 ]pR 3 , -C(=O)[CH 2 ]pC(=O)R 3 , or -[CH 2 ]pC(=O)R 3 ; and R 3 is R 4 R 4 R4 R4 0 O 0 R In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein X is -0-; Y is -CH 2 -; R 1 is 5 hydrogen; m is 2; n is 2; R2 is alkyl; L is -C(=0)R3 or -C(=O)[CH 2 ]pC(=O)R 3 ; R3 is R 4 R 4 R4 ' R4 0 O R and R 4 is -H, -F, -C, -Br, -I, or -OR 5 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein X is -0-; Y is -CH 2 -; R, is hydrogen; m is 2; n is 2; R 2 is unsubstituted alkyl or alkyl substituted with -F, -Cl, -Br, or R 4 R 4 R4 ' R4 0 0 R1 10 I; L is -C(=O)CH 2
CH
2
C(=O)R
3 ; R 3 is ; and R 4 is -OR 5 . In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein X is -0-; Y is -CH 2 -; R, is - 40 - WO 2009/117728 PCT/US2009/037928 hydrogen; m is 2; n is 2; R 2 is alkyl substituted with -F; L is -C(=O)CH 2
CH
2
C(=O)R
3 ; R 3 is R4 R4 R4 R4 0 O R and R 4 is -OH.. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein X is -0-; Y is -CH 2 -; R 1 is 5 hydrogen; m is 2; n is 2; R2 is alkyl substituted with -18F; L is -C(=0)CH 2
CH
2 C(=0)R 3 ; R 3 R 4 R 4 R4 ' R4 0 0 R1 is R1 ;and R 4 is -OH. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein X is -0-; Y is -CH 2 -; R, is hydrogen; m is 2; n is 2; R2 is -CH 2
CH
2 1 F or -CH 2 CH 8FCH 3 ; L is R 4 R4 R4 ' R4 0 S 0H o H 10 -C(=0)CH 2
CH
2 C(=0)R 3 ; R3 is H ; and R4 is -OH.. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein X is -O-; Y is -CH 2 -; R, is - 41 - WO 2009/117728 PCT/US2009/037928 hydrogen; m is 2; n is 2; R2 is ; L is -C(=O)R 3 or -C(=O)[CH 2 ]pC(=O)-; R3 is R 4 R 4 R4 'W 0 # 0H O H H ;Wis -F; and R 4 is -OR. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein X is -0-; Y is -CH 2 -; R 1 is 5 hydrogen; m is 2; n is 2; R2 is unsubstituted alkyl; L is -C(=O)R 3 or -C(=O)CH 2
CH
2 C(=O)-; R 4 R 4 R4 'W 0 H
R
3 is H W is - 8 F; and R 4 is -OH. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein the compound comprises a radio imaging agent. 10 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein Ri comprises the radio imaging agent. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein R 1 comprises the 15 radio imaging agent; and the radio imaging agent is 18F. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein R2 comprises the radio imaging agent. - 42 - WO 2009/117728 PCT/US2009/037928 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein R 2 comprises the radioimaging agent; and the radioimaging agent is 18F. In certain embodiments, the present invention relates to any one of the 5 aforementioned compounds and attendant definitions, wherein R3 comprises the radio imaging agent. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein R3 comprises the radioimaging agent; and the radioimaging agent is 18F. 10 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein R4 comprises the radio imaging agent. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein R4 comprises the 15 radioimaging agent; and the radioimaging agent is 18F. One aspect of the invention relates to a compound, or a pharmaceutically acceptable salt thereof, represented by formula II: R7 R 7 L--O R7
R
7
R
7 II 20 wherein, independently for each occurrence, L is -H, -C(=O)R3, -C(=O)[C(R) 2 ]pR 3 , -C(=O)[C(R) 2 ]pC(=O)R 3 -[C(RI)2]pC(=0)R3, -[C(R')2]pR3, -[C1_10alkylene]R3, -C(=0)[C1_10alkylene]R3, -[C1_ ioalkylene]C(=O)R 3 or -C(=O)[C 1 _1oalkylene]C(=0)R;
R
1 is hydrogen, halo, azido, alkyl, haloalkyl, perhaloalkyl, fluoroalkyl, 25 perfluoroalkyl, aralkyl, alkenyl, alkynyl, cycloalkyl, heterocyclyl, aryl, heteroaryl, aralkyl, heteroaralkyl, hydroxy, alkoxy, aryloxy, heteroaryloxy, aralkyloxy, heteroaralkyloxy, - 43 - WO 2009/117728 PCT/US2009/037928 amino, alkylamino, arylamino, acylamino, heteroarylamino, nitro, sulfhydryl, imino, amido, phosphonate, phosphinate, acyl, carboxyl, oxycarbonyl, acyloxy, silyl, thioether, sulfo, sulfonate, sulfonyl, sulfonamido, formyl, cyano, or isocyano; R 4 R 4 R 4 0- R4 ' 0-- R4 R4 0 0 R4 Rl R4 Rl
R
3 is R R O R 4 R 4 R 4 R4 ' R4 --- O R4 0 0 R4 Rl R4 Rl 5 R R ,or R 4 R 4 R4 R4 0 Rl R4 is hydrogen, halo, azido, alkyl, haloalkyl, perhaloalkyl, fluoroalkyl, perfluoroalkyl, aralkyl, alkenyl, alkynyl, cycloalkyl, heterocyclyl, aryl, heteroaryl, aralkyl, heteroaralkyl, hydroxy, alkoxy, aryloxy, heteroaryloxy, aralkyloxy, heteroaralkyloxy, 10 amino, alkylamino, arylamino, acylamino, heteroarylamino, nitro, sulfhydryl, imino, amido, phosphonate, phosphinate, acyl, carboxyl, oxycarbonyl, acyloxy, silyl, thioether, sulfo, - 44 - WO 2009/117728 PCT/US2009/037928 sulfonate, sulfonyl, sulfonamido, formyl, cyano, isocyano, -OR 5 , -SR 5 , -N(R 5
)
2 , (C(R) 2 )qC(R) 3 or a chelating structure; R' is hydrogen, alkyl, heteroalkyl, cycloalkyl, heterocycloalkyl, aryl, heteroaryl, aralkyl, heteroaralkyl, acyl, -(C(RI) 2 )qC(R) 3 or a chelating structure. 5 R 7 is hydrogen, halo, azido, alkyl, haloalkyl, perhaloalkyl, fluoroalkyl, perfluoroalkyl, aralkyl, alkenyl, alkynyl, cycloalkyl, heterocyclyl, aryl, heteroaryl, aralkyl, heteroaralkyl, hydroxy, alkoxy, aryloxy, heteroaryloxy, aralkyloxy, heteroaralkyloxy, amino, alkylamino, arylamino, acylamino, heteroarylamino, nitro, sulfhydryl, imino, amido, phosphonate, phosphinate, acyl, carboxyl, oxycarbonyl, acyloxy, silyl, thioether, sulfo, 10 sulfonate, sulfonyl, sulfonamido, formyl, cyano, isocyano, -OR', -SR 5 , -N(R) 2 , (C(R) 2 )qC(R) 3 or a chelating structure; p is 1-10 inclusive; and q is 0-10 inclusive; provided that when L is -H, one R7 is fluoro; and the other R7 are hydroxy, alkoxy, 15 aryloxy, heteroaryloxy, aralkyloxy, or heteroaralkyloxy. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein said compound comprises at least one 18 F, 76 Br, 77Br, 1231, 124I or 1251 In certain embodiments, the present invention relates to any one of the 20 aforementioned compounds and attendant definitions, wherein said compound comprises at least one 18 F. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein said compound comprises only one chelating structure. 25 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein said compound comprises only one chelating structure; and 99 mTc, 68Cu, 64Cu or 68 Ga chelated to the chelating structure. In certain embodiments, the present invention relates to any one of the 30 aforementioned compounds and attendant definitions, wherein L is -C(=O)R 3 or C(=0) [C(R1)2]pC(=0)R3 - 45 - WO 2009/117728 PCT/US2009/037928 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein L is -C(=O)R 3 . In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein L is -C(=O)[CH 2 ]pC(=O)R 3 . 5 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein L is -C(=0)CH 2
CH
2
C(=O)R
3 . In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein R7 is -H, -F, -Cl, -Br, -I, or 10 -OR . In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein RI is -H, -F, -Cl, -Br, -I, or -OH. In certain embodiments, the present invention relates to any one of the 15 aforementioned compounds and attendant definitions, wherein R7 is -F or -OH. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein RI is -18F or -OH; provided that only one R 7 is -"F. In certain embodiments, the present invention relates to any one of the 20 aforementioned compounds and attendant definitions, wherein L is -C(=0)R 3 or 5
C(=O)[C(R)
2 ]pC(=O)R 3 ; and R7 is -H, -F, -Cl, -Br, -1, or -OR . In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein L is -C(=O)R 3 ; and R 7 is -H, 5 -F, -Cl, -Br, -I, or -OR . 25 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein L is -C(=O)[CH 2 ]pC(=O)R 3 5 and R7 is -H, -F, -Cl, -Br, -I, or -OR. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein L is -C(=0)R 3 ; and RI is 30 -OH. -46- WO 2009/117728 PCT/US2009/037928 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein L is -C(=O)CH 2
CH
2
C(=O)R
3 ; and R' is OH. In certain embodiments, the present invention relates to any one of the 5 aforementioned compounds and attendant definitions, wherein L is -C(=O)R 3 ; and R 7 is R 7 is -F or -OH; provided that only one R 7 is -F. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein L is -C(=O)CH 2
CH
2
C(=O)R
3 ; and R7 is -F or -OH; provided that only one R7 is -F. 10 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein L is -C(=O)R 3 ; and R 7 is R 7 is - 18 F or -OH; provided that only one R' is - 18 F. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein L is -C(=O)CH 15 2
CH
2
C(=O)R
3 ; and R' is -18F or -OH; provided that only one R7 is -8F. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein R3 is R 4 R 4 R4 R4 0 O - 47 - WO 2009/117728 PCT/US2009/037928 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, R3 is R 4 R 4 R4 ' R4 0 O R and R 4 is -H, -F, -Cl, -Br, -I, or -OR.. In certain embodiments, the present invention relates to any one of the 5 aforementioned compounds and attendant definitions, R 3 is R4 R4 0 R4 R O R1 ;and R is -OR.. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, R 3 is R4 R4 R4 ' R4 0 S 0H O H H ; and R 4 is -OH.. - 48 - WO 2009/117728 PCT/US2009/037928 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, R3 is R 4 R 4 R4 'W 0 S 0H O H H ;Wis -F, -Cl, -Br or -I; and R 4 is -OR. In certain embodiments, the present invention relates to any one of the 5 aforementioned compounds and attendant definitions, R 3 is R4 R4 R4 'W 0 S 0H O H H ;Wis -F; and R 4 is -OR'. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, R 3 is R4 R4 R4 'W 0 S 0H O H H ; W is - 1 8 F; and R 4 is -OH. 10 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein L is -C(=0)R 3 or - 49 - WO 2009/117728 PCT/US2009/037928
C(=O)[C(R)
2 ]pC(=O)R 3 ; R 7 is -H, -F, -Cl, -Br, -I, or -OR'; and R 3 is R 4 R 4 R4 R4 0 R1 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein L is -C(=0)R 3 or 5 C(=O)[C(R) 2 ]pC(=O)R 3 ; R 7 is -H, -F, -Cl, -Br, -I, or -OR 5 ; and R 3 is R 4 R 4 R4 ' R4 0
-
R and R 4 is -H, -F, -C, -Br, -I, or -OR 5 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein L is -C(=O)R 3 or C(=O)[C(R) 2 ]pC(=O)R 3 ; R 7 is -H, -F, -Cl, -Br, -I, or -OR 5 ; R 3 is R 4 R 4 R4 ' R4 0
-
R 10 ;and R 4 is -OR. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein L is -C(=O)R 3 or - 50 - WO 2009/117728 PCT/US2009/037928
C(=O)[C(R
1
)
2 ]pC(=O)R 3 ; R 7 is -H, -F, -Cl, -Br, -I, or -OR'; R 3 is R 4 R 4 R4 ' R4 0 S 0H -- O H H ;and R 4 is -OH In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein L is -C(=O)R 3 or 5 C(=O)[C(R) 2 ]pC(=O)R 3 ; R 7 is -H, -F, -Cl, -Br, -I, or -OR 5 ; R 3 is R 4 R 4 R4 'W 0 S 0H -- O H 4 5 H ;Wis -F, -C], -Br or -T; and R is -OR. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein L is -C(=0)R 3 or C(=O)[C(R) 2 ]pC(=O)R 3 ; R 7 is -H, -F, -Cl, -Br, -I, or -OR 5 ; R 3 is R 4 R 4 R4 'W 0 S 0H -- O H 10 H ;Wis -F; and R 4 is -OR. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein L is -C(=0)R 3 or - 51 - WO 2009/117728 PCT/US2009/037928
C(=O)[C(R
1
)
2 ]pC(=O)R 3 ; R 7 is -H, -F, -Cl, -Br, -I, or -OR; R3 is R 4 R 4 R4 'W 0 S 0H O H H ;Wis - 18 F; and R 4 is -OH. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein L is -H, one R 7 is fluoro; and 5 the other R7 are hydroxy, alkoxy, aryloxy, heteroaryloxy, aralkyloxy, or heteroaralkyloxy. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein the compound is 1 -deoxy- 1 fluoro-scyllo-inostiol or 1-deoxy-1-fluoro-myo-inositol. In certain embodiments, the present invention relates to any one of the 10 aforementioned compounds and attendant definitions, wherein the compound comprises a radioimaging agent. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein Ri comprises the radioimaging agent. 15 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein R 1 comprises the radioimaging agent; and the radioimaging agent is 18F. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein R4 comprises the 20 radioimaging agent. In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein R4 comprises the radioimaging agent; and the radioimaging agent is 18F. - 52 - WO 2009/117728 PCT/US2009/037928 In certain embodiments, the present invention relates to any one of the aforementioned compounds and attendant definitions, wherein R7 comprises the radioimaging agent. In certain embodiments, the present invention relates to any one of the 5 aforementioned compounds and attendant definitions, wherein R7 comprises the radioimaging agent; and the radioimaging agent is 18F. One aspect of the present invention relates to a pharmaceutical composition comprising a pharmaceutically acceptable carrier and a compound, or a pharmaceutically acceptable form thereof; wherein the compound is any of the compound described herein. 10 In certain embodiments, the present invention relates to any one of the aforementioned pharmaceutical composition and attendant definitions, wherein said compound is a compound of formula I or II and attendant definitions thereto. One aspect of the present invention relates to a method for amyloid imaging a subject suffering from an amylodiosis-associated pathological condition, or treating a 15 subject suffering fromamylodiosis-associated pathological condition, comprising the step of: administering a compound, or a composition comprising a pharmaceutically acceptable carrier and the compound or a pharmaceutically acceptable form thereof, wherein the compound is represented by any of the compound described herein. 20 In certain embodiments, the present invention relates to any one of the aforementioned methods and attendant definitions, wherein said compound is a compound of formula I or II and attendant definitions thereto. In certain embodiments, the present invention relates to any one of the aforementioned methods and attendant definitions, wherein said amylodiosis-associated 25 pathological condition is Alzheimer's disease. In certain embodiments, the present invention relates to any one of the aforementioned methods and attendant definitions, wherein said compound comprises at least one 18 F, 76 Br, 7 7Br, , 1I or 1I. - 53 - WO 2009/117728 PCT/US2009/037928 In certain embodiments, the present invention relates to any one of the aforementioned methods and attendant definitions, wherein the compound is OH 18F OH N N- 8F N N OH 0 ,or 0 One aspect of the present invention relates to a method for treating a subject 5 suffering from an amylodiosis-associated pathological condition, comprising the step of: administering a compound, or a composition comprising a pharmaceutically acceptable carrier and the compound or a pharmaceutically acceptable form thereof, wherein the compound is represented by any of the compounds described herein. In certain embodiments, the present invention relates to any one of the 10 aforementioned methods and attendant definitions, wherein said compound is a compound of formula I or II and attendant definitions thereto. In certain embodiments, the present invention relates to any one of the aforementioned methods and attendant definitions, wherein said amylodiosis-associated pathological condition is Alzheimer's disease. 15 In certain embodiments, the present invention relates to any one of the aforementioned methods and attendant definitions, wherein said treatment inhibits the formation of plaque. In certain embodiments, the present invention relates to any one of the aforementioned methods and attendant definitions, wherein said compound is a 20 combination of RS-86 and inositol, a combination of RS-86 and glucose, a combination of inositol and glucose, or a disaccharide comrpising inositiol and glucose. In certain embodiments, the present invention relates to any one of the aforementioned methods and attendant definitions, wherein said combination shows increased uptake over one or both of the consitutents thereof. 25 In certain embodiments, the present invention relates to any one of the aforementioned methods and attendant definitions, wherein said combination shows increased uptake over one or both of the consitutents thereof, in cells of the blood, heart, lung, liver, spleen, kidney, adrenal gland, stomach, gi tract, gonads, skeletal muscle, bone, or brain. - 54 - WO 2009/117728 PCT/US2009/037928 In certain embodiments, the present invention relates to any one of the aforementioned methods and attendant definitions, wherein said combination shows increased uptake over one or both of the consitutents thereof, in the brain. In certain embodiments, the present invention relates to any one of the 5 aforementioned methods and attendant definitions, wherein said compound is fluoronated. In certain embodiments, the present invention relates to any one of the aforementioned methods and attendant definitions, wherein the compound is 0 O OH O OH ,or NN OH 0N OH 00 H H OHO OH, 10 EXEMPLIFICATION It should be understood that the above-described embodiments and the following examples are given by way of illustration, not limitation. Various changes and modifications within the scope of the present invention will become apparent to those skilled in the art from the present description. 15 General Reaction Materials and Methods of Analysis All reactions were carried out in dry glassware (oven at 150 'C for 12 hrs) unless otherwise noted and a steady stream of dry N 2 gas was used to prevent moisture-air off the reaction system. All chemicals and solvents for moisture-sensitive reactions were purchased from Aldrich chemical company and used as supplied. Ethyl ether was distilled 20 from sodium-benzophenone immediately prior to use. Dichloromethane was distilled from CaH or P 2 0 5 prior to use. DMF was distilled under reduced pressure onto activated 4 angstrom molecular sieves or purchased as dry solvent for immediate use. Syringes possessing Teflon or rubber seals/plungers were dried (24h) using an evacuated Abderhalden drying apparatus at 56 'C (acetone) with KOH as the desiccant and the same - 55 - WO 2009/117728 PCT/US2009/037928 Abderhalden drying apparatus at 64 'C (methyl alcohol) with P 2 0 5 was used for sample drying purpose. Reactions carried out at -50 'C employed the frozen slurry of 50% CaCl 2 solution with powdered dry-ice. I H NMR spectra were recorded on a 300 MHz Varian Mercury instrument and reported in parts per million (ppm), with residual CDC 3 5 referenced at 7.26 ppm and Me 4 Si at 0.00 ppm. Multiplicity, coupling constant (Hz), and proton count follow each peak assignment. Elemental analyses were performed by Robertson Laboratories, Madison, NJ, and were within +/- 0.4% of theoretical values unless otherwise indicated. Analytic polyester TLC plates were purchased from Aldrich (Silica gel thickness: 250 jim, pore size 60 angstroms, 20 x 20 cm, Fluorescent indicator, 10 Cat. No. Z122785). TLC plates were visualized using a 254 nm / 366 nm UV lamp and 5% ethanol solution of phosphomolybdic acid or an iodine/silica gel mixture. Preparative TLC plates were purchased from Sigma-Aldrich (silica gel on glass, 2000 pim, 20 x 20 cm, fl. Ind. Cat No. Z513040). Chromatographic separations were made using Silia-P Flask silica gel (Silicycle Chemical Division, Quebec, QC, Canada), particle size: 40-63 pm, 15 60 angstroms. HRMS determinations were done by Molecular Biology Core Facilities, DFCI, MA in the electron-impact (EI) or fast-atom bombardment (FAB) mode. EXAMPLE 1 Figure 3 depicts one approach to the synthesis of two novel fluorinated 2,8 diazaspiro[4,5]decane-1,3-dione derivatives. Synthetic protocols for the synthesis of the 20 compounds depicted in Figure 3 are presented below. [A] Synthesis of ethyl (1-methyl-4-piperidylidene)cyanoacetate (1; Figure 3). See United States Patent No. 3,056,796, hereby incorporated by reference; Bioorganic & Medicinal Chemistry Letters 2002, 12, 1103; and J. Med. Chem. 2004, 47 (8), 2037. To a stirred solution of 1-methyl-4-piperidone (10.0g, 88.3 mmol) and ethyl cyanoacetate (13.0g, 25 115.2 mmol) in CH 2 Cl 2 (100 mL) was added Et 3 N (17.9g, 177.0 mmol). Then, crushed 4 angstrom molecular sieves (9.0 g) were added and the mixture was stirred at room temperature overnight. The reaction mixture was filtered through Celite, and the filtrate was concentrated to give the product as a clear red syrup (15 g; yield 82%). 'HNMR (CDC 3 -d) 6 1.31 (t, 3H, CH 2
CH
3 ), 2.28 (s, 3H, N-CH 3 ), 2.50 (t, 2H, Jab = 5.7 Hz, CH2N), 2.57 (t, 2H, 30 Jab = 6.0 Hz, CH 2 N), 2.77 (t, 2H, Jab = 6.0 Hz, CH 2 C=C), 3.12 (t, 2H, Jab = 5.7Hz,
CH
2 C=C). It was used directly in the following step without further purification. [B] Synthesis of 1-methyl-4-cyanomethylpiperidine-4-carbonitrile (2; Figure 3). The - 56 - WO 2009/117728 PCT/US2009/037928 ethyl ester 1 (15 g, 72.1 mmol) obtained from previous step was dissolved in ethanol (150 ml). A solution of KCN (28.7 g, 442 mmol) in H 2 0 (60 mL). The red solution was heated to reflux for 4 h, then solvent was evaporated under the reduced pressure to a dark-red syrup which was extracted with EtOAc (4 x 100). The combined organic extract was 5 washed with brine, dried over MgSO 2 , and concentrated to yield a red clear oil. Chromatography using 10% methanol in CH 2 Cl 2 furnished pure dinitrile compound (8.8g; yield 74.9%). 1 HNMR (CDCl 3 -d) 6 1.75 (in, 2H, CH 2 N), 2.06 (d, 2H, CH 2 N), 2.30 (in, 2H,
CH
2 C=N), 2.33 (s, 3H, NCH 3 ), 2.73 (s, 2H, CH 2 CN), 2.87 (d, 2H, CH2C=N). [C] Synthesis of 1-methyl-4-carboxymethylpiperidine-4-carboxylic acid 10 hydrochloride (3; Figure 3). See .. Med. Chem. 2004, 47 (8), 2037. A suspension of dinitrile 2 (14.4 g, 88.3 mmol) in concentrated HCl (250 mL) was refluxed for 36 h. Then the pale yellow solution was concentrated under the reduced pressure to dryness to afford the diacid 3 as an off-white solid, as its hydrochloride salt (19.lg; yield 91%). 1 HNMR (DMSO-d6) 61.92 (t, 2H, CH 2 N), 2.17 (t, 2H, CH 2 N), 2.46 (s, 1H, CH 2
CCO
2 H), 2.72 (s, 15 3H, NCH 3 ), 2.84 (in, 2H, CH 2
CCO
2 H), 3.24 (q, 1H, CH 2
CCO
2 H), 3.33 (s, 2H,
CH
2
CO
2 H), 10.88 (m, 2H, COOH). [D] Synthesis of 8-methyl-2,8-diazaspiro[4,5]decane-1,3-dione (4; Figure 3). See J. Med. Chem. 1988, 31(8), 1598. The diacid HCl 3 (16.4 g, 69 mmol) was dissolved in 30 mL conc. NH 4 0H and heated to reflux for 1 hour and then the volatile components of the 20 solution were distilled off at normal pressure, the residue was heated at 250 'C for 5 h. After cooling, the residue was treated with hot water (10 mL), 50% K 2 C0 3 (28 mL), and using 50% NaOH (1 mL) the pH of the solution was adjusted to 12. Then the mixture was extracted with chloroform (3 x 100 mL) and concentrated under the reduced pressure to provide a slight brown solid. The crude product was purified by crystallization in 2 25 propanol to give a yellow crystal (7.6g; yield 60%). 1 1HNMR (CDCl 3 -d) 6 1.55 (d, 2H,
CH
2 N), 2.03 (t, 2H, CH 2 C), 2.12 (t, 2H, CH 2 N), 2.28 (s, 3H, NCH 3 ), 2.56 (s, 2H, CH 2 CO), 2.87 (d, 2H, CH 2 C). Note: For the preparation of compound 4, the product was easy to decompose and had caused lower yield under the condition cited from literature, higher temperature 230 30 280 'C in vacuo. The condition was modified by controlling the temperature at 250 'C at the normal pressure to increase the yield from literature 310% to 60%. [E] Synthesis of 2-(2-hydroxyethyl)-8-methyl-2,8-diazaspiro[4,5]decane-1,3-dione - 57 - WO 2009/117728 PCT/US2009/037928 (5; Figure 3). See J. Med. Chem. 1988, 31(8), 1598. A solution of compound 4 (1.8 g, 10 mmol) dissolved in fresh distilled DMF (10 mL) was treated with 95% NaH (0.28 g, 11 mmol) in mineral oil and the mixture was stirred for 1.5 h at 50 'C and then there was added a solution of 2-bromoethanol (1.58 g, 12 mmol) in DMF (6 mL) over the period of 5 50 min and the mixture was stirred for 4 h at 75 to 80 'C. Then the mixture was filtered with 1 g active charcoal carbon and the filtrate was evaporated in vacuo. The residue was extracted with chloroform (3 x 50 mL) and the precipitated salts were filtered off, the filtrate was filtered through a layer of neutral A1 2 0 3 (activity II). The solvent was evaporated under the reduced pressure to give a colorless semi-solid. The crude product 10 can't be perfectly purified by crystallization with a mixture of 2-propanol : hexanes (20:5). The pure product was obtained as a colorless powder by flash chromatography with 15% methanol in CH 2 Cl 2 (1.12 g; yield 50%). 1 H NMR (CDCl 3 -d) 6 1.49 (d, 2H, CH 2 N), 1.98 (t, 2H, CH 2 C), 2.08 (t, 2H, CH 2 N), 2.25 (s, 3H, NCH 3 ), 2.51 (s, 2H, CH 2 CO), 2.81 (d, 2H,
CH
2 C), 3.63 (t, 2H, NCH 2
CH
2 ), 3.69 (t, 2H, CH 2 OH). 15 Note: In the preparation of spiro-compound 5, using the same purification method provided in literature was failed to obtain a pure product, a need for flash chromatography was required. Elution with 15% methanol in CH 2 Cl 2 afforded a 50% yield that was lower than that (76%) reported in literature. The product has a weak UV absorption so its TLC detection is difficult too. 1 2 /Silical gel was used for chromatography detection of the 20 product. [F] Synthesis of 2-(2-methanesulfonylethyl)-8-methyl-2,8-diazaspiro[4,5]decane 1,3-done (6; Figure 3). In a 25-ml round-bottom flask was dissolved compound 5 (0.3 g, 1.3 mmol) in anhydrous dichloromethane (5 mL). To this solution was added triethylamine (0.27 g, 2.6 mmol), the reaction mixture was cooled to 0 C with an ice-NaCl bath. 25 Methanesulfonyl chloride was added dropwise, and the reaction mixture was stirred under nitrogen for 2 h, allowing the ice bath to expire and stirred at room temperature for 1 h. Then the reaction mixture was diluted with dichloromethane (20 mL), washed with a sat. solution of NaHCO 3 , then brine, dried over MgSO 4 , and the solvent was evaporated under the reduced pressure to provide a yellow clear oil. The product was purified by flash 30 chromatography eluted with a mixture of 10% methanol in dichloromethane to give a colorless clear syrup which evaporated under high vacuum to obtain a colorless semi-solid (144 mg; yield 36%). 1 HNMR (CDCl 3 -d) 61.48 (d, 2H, CH 2 N), 1.93 (t, 2H, CH 2 C), 2.05 (t, 2H, CH 2 N), 2.23 (s, 3H, NCH 3 ), 2.51 (s, 2H, CH 2 CO), 2.78(d, 2H, CH 2 C), 2.94(s, 3H, - 58 - WO 2009/117728 PCT/US2009/037928
CH
3
SO
3 ), 3.76 (t, 2H, NCH 2
CH
2 ), 4.34 (t, 2H, CH 2
OSO
2
CH
3 ). [G] Synthesis of 2-(2-hydroxypropyl)-8-methyl-2,8-diazaspiro[4,5]decane-1,3-dione (7; Figure 3). To a solution of compound 4 (1.8 g, 10 mmol) in DMF (10 mL) was slowly added 95% NaH in mineral oil (0.28 g, 11 mmol), which produced a lot of bubbles and 5 additional DMF (5 mL) was added. The mixture was stirred at 65 'C for 1 h. To the mixture a solution of 1-bromo-2-propanol (1.2 g, 12 mmol) in DMF (6 mL) was added over 80 min until the brown bubbles all dissolved and the mixture became a clear yellow solution, then the temperature of the oil bath was raised up to 70 'C and kept overnight. The mixture was added charcoal carbon (0.1 g) and filtered through a layer of Celite. The 10 filtrate was evaporated to dryness under the reduced pressure and the residue was extracted with chloroform (3 x 60 mL). The collected chloroform was filtered off the insoluble materials and then filtered through a layer of neutral A1 2 0 3 (activity II). The filtrate was evaporated in the reduced pressure to give a yellow solid. The crude product was purified by crystallization after trituration with a mixture of hexanes and 2-propanol (4:1) to provide 15 a colorless powder (1.3 g; yield 54%). 1 H NMR (CDCl 3 -d) 6 1.13 (d, 3H, CH 3 CH), 1.47 (t, 2H, CH 2 N), 1.99 (t, 2H, CH 2 N), 2.08 (t, 2H, CH 2 C), 2.24 (s, 3H, NCH 3 ), 2.53 (s, 2H,
CH
2 CO), 2.82 (t, 2H, CH 2 C), 3.48 (d, 2H, NCH 2 CH), 3.94 (m, 1H, CHOH). Note: In the preparation of compound 7, the addition of NaH (95%) will cause a large amount of bubbles and heat to be released, so the suggestion is to use a ice bath at the 20 beginning of the reaction, then take it away after finishing the NaH addition. After the overnight reaction, charcoal addition is necessary to remove any conjugation or dehydration by-products and Filtration through A1 2 0 3 layer is to remove possible acidic by-products. Attempts to react compound 4 with propylene oxide and sodium hydride in DMF to prepare the product 7 have been unsuccessful. Although the commercial starting material, 1 25 bromo-2-propanol, contains 30% of its isomer, 2-bromo-1-propanol, it appears that this isomer did not have any negative effect on the separation of a pure product in the procedure outlined above. [H] Synthesis of 2-(2-methanesulfonylpropyl)-8-methyl-2,8-diazaspiro[4,5]decane 1,3-done (8; Figure 3). To a solution of compound 7 (1.3 g, 5.4 mmol) dissolved in freshly 30 distilled CH 2 Cl 2 (20 ml) in an ice-salt bath (0 'C) was added triethylamine (1.09 g, 6.6 mmol) and then methanesulfonyl chloride was added dropwise. The reaction mixture was stirred under nitrogen for 1.5 h, allowing the ice-bath to expire, and stirring continued at room temperature for 1 h. The mixture was diluted with CH 2 Cl 2 (20 mL), and then washed - 59 - WO 2009/117728 PCT/US2009/037928 with sat. NaHCO 3 , brine, and dried over MgSO 4 . The solution was evaporated under the reduced pressure to give a yellow solid. The crude product was purified by chromatography eluted with 15% methanol in CH 2 Cl 2 to obtain a colorless powder (0.9 g; yield 52%). 1 H NMR (CDCl 3 -d) 6 1.40 (d, 3H, CH 3 CH), 1.58 (d, 2H, CH 2 N), 2.01 (t, 2H, CH 2 N), 2.10 (t, 5 2H, CH 2 C), 2.28 (s, 3H, NCH 3 ), 2.53 (s, 2H, CH 2 CO), 2.82 (d, 2H, CH 2 C), 2.94 (s, 3H,
CH
3
SO
2 0), 3.44 (dd, 1H, NCH 2 CH), 3.79 (q, 1H, NCH 2 CH), 5.04 (in, 1H, CHOMs). Elemental Analysis: (C 13
H
2 2
N
2 0 5 S) Cal: C 49.04; H 6.96; N 8.80, S 10.07. Found: C 48.84, H 6.75, N 8.51, S 10.37. [I] Synthesis of 2-(2-fluoroethyl)-8-methyl-2,8-diazaspiro [4,5] decane- 1,3 -dione (9; 10 Figure 3). A solution of compound 4 (0.3 g, 1.65 mmol) dissolved in fresh distilled DMF (2 mL) was treated with 95% NaH (0.05 g, 1.90 mmol) in mineral oil and the mixture was stirred for 1.5 h at 50 'C and then there was added a solution of 1-bromo-2-fluoroethane (0.33 g, 2.6 mmol) in DMF (2 mL) over the period of 50 min and the mixture was stirred for 4 h at 75 to 80 'C. Then the mixture was filtered with active charcoal carbon (0.01 g) 15 and the filtrate was evaporated in vacuo. The residue was extracted with chloroform (3 x 50 mL) and the precipitated salts were filtered off, the filtrate was filtered through a layer of neutral A1 2 0 3 (activity II). The solvent was evaporated under the reduced pressure to give a colorless solid. The pure product was obtained as a colorless powder by flash chromatography with 15% methanol in CH 2 Cl 2 (175 mg; yield 46%). 1 H NMR (CDCl 3 -d) 20 6 1.48 (d, 2H, CH 2 N), 1.96 (t, 2H, CH 2 C), 2.08 (t, 2H, CH 2 N), 2.24 (s, 3H, NCH 3 ), 2.52 (s, 2H, CH 2 CO), 2.81 (d, 2H, CH 2 C), 3.75 (tt, 2H, NCH 2 ), 4.48 (tt, 2H, CH 2 F). Elemental Analysis: (Cn H 1 7
FN
2 0 2 ) Cal: C 57.88; H 7.51; N 12.27; F 8.32. Found: C 57.61; H 7.79; N 12.13; F 7.73. Note: In the preparation of compound 9, the method of using compound 6 reacted 25 with TBAF (tetrabutylammonium fluoride in THF) in order to replace the Ms-group with a fluoro-group was unsuccessful due to excess TBAF which could not be separated from the product 9, both have an overlap Rf values in TLC and flash chromatography in elution systems such as 10-20% methanol in CH 2 Cl 2 . See Nucl. Med. Biol. 1993, 20(1), 81. [J] Synthesis of 2-(2-fluoropropyl)-8-methyl-2,8-diazaspiro[4,5]decane-1,3-dione 30 (10; Figure 3). To a solution of compound 4 (1.2 g, 6.5 mmol) in DMF (10 mL) was slowly added 95% NaH in mineral oil (0.2g, 7.8 mmol). The mixture was stirred at 65 'C for 1 h. To the mixture, a solution of 1-bromo-2-fluoropropane (1.1 g, 7.8 mmol) in DMF (6 mL) was added over 80 min until the brown bubbles all dissolved and the mixture became a - 60 - WO 2009/117728 PCT/US2009/037928 clear yellow solution, then the temperature of the oil bath was raised up to 70 'C and kept overnight. After cooling to room temperature, the mixture was added charcoal carbon (0.1 g) and filtered through a layer of Celite. The filtrate was evaporated to dryness under the reduced pressure and the residue was extracted with chloroform (3 x 60 mL). The collected 5 chloroform was filtered off the insoluble materials and then filtered through a layer of neutral A1 2 0 3 (activity II). The filtrate was evaporated in the reduced pressure to give a yellow solid. The crude product was purified by crystallization in hexanes to provide a colorless powder (1.2 g; yield 76%). 1 H NMR (CDCl 3 -d) 6 1.33 (q, 3H, CH 3 CH), 1.49 (d, 2H, CH 2 N), 1.99 (t, 2H, CH 2 N), 2.13 (t, 2H, CH 2 C), 2.28 (s, 3H, NCH 3 ), 2.57 (s, 2H, 10 CH 2 CO), 2.83 (d, 2H, CH 2 C), 3.48 (d-q, 1H, NCH 2 CHF), 3.78 (d-t, 1H, NCH 2 CHF), 4.84 (d-m, 1H, CHF). Elemental Analysis: (C 12
H
19
FN
2 0 2 ) Cal: 59.49; H 7.90; N 11.56; F 7.84. Found: C 59.49; H 8.06; N 11.55; F 7.69. Note: In the preparation of compound 10, the method of using compound 7 directly reacted with DAST (diethylaminosulfur trifluoride) in CH 2 Cl 2 has been proved to provide 15 the product 10 only with poor yield 10-20%. See J. Org. Chem. 1975, 40(5), 574. [K] Synthesis of 1-bromo-2-fluoroethane. See J. Org. Chem. 1975, 40(5), 574. 1-Bromoethanol (1.65 g, 12.5 mmol) was added dropwise to a solution of dimethylaminosulfur trifluoride (DAST) (2.0 g, 12.5 mmol) in diglyme (8 mL) cooled to 50 'C in a bath of dry-ice and acetone. The reaction mixture was warmed to room 20 temperature, and continued to stirring at room temperature for 1 h. The most volatile portion was distilled at 68-75 'C for collection in dry-ice traps by a hood vacuum. The distillate was washed with water (4 mL), 5% sodium bicarbonate solution, dried over MgSO 4 , and redistilled to give product as a colorless oil (1.4 g; yield 88%). 1 H NMR (CDCl 3 -d) 6 3.50 (t-t, 2H, CH 2 Br), 4.62 (t-t, 2H, CH 2 F). 25 [L] Synthesis of 1-bromo-2-fluoropropane. This compound was synthesized as reported in the literature; see Organic Syntheses 2004, 10, 128; and Organic Syntheses 1999, 76, 159. 1 H NMR (CDCl 3 -d) 6 1.41 (d-d, 3H, CH 3 CH), 3.44 (d-d, 2H, CH 2 Br), 4.80 (m-rn, 1H, CHF). Example 2 30 Figure 4 depicts one approach to the synthesis of N-2-ethyl-2,8 diazaspiro[4,5]dccanc-1,3-dione (6; Figure 4). The preparation of 2-ethyl-2,8 diazaspiro[4,5]decane-1,3-dione 6 was done according to a modified version of a known - 61 - WO 2009/117728 PCT/US2009/037928 procedure. See Irie, 0., Iwasaki, G. et al., WO 2004/076455; which is hereby incorporated by reference in its entirety. Synthetic protocols for the synthesis of the compounds depicted in Figure 4 are presented below. [A] Synthesis of 1-benzyl-piperidin-4-ylidene)-cyanoacetate (2; Figure 4). A 5 solution of 1-benzyl-piperidin-4-one (75.1 g, 0.40 mol) in toluene (9400 mL), ethyl cyanoacetate (50.6 mL, 0.48 mol) and acetic acid (918.2 mL, 0.32 mol) was refluxed for 4 hr. The mixture was quenched with ice-water and extracted with diethyl ether. The combined extracts were washed with water, brine and dried over Na 2
SO
4 to give ethyl (1 benzyl-piperidin-4-ylidene)cyanoacetate in quantitative yield. Rf=0.53 10 (hexane:AcOEt=1:1). [B] Synthesis of 1-benzyl-4-cyanomethylpiperidine-4-carbonitrile (3; Figure 4). A solution of (1-benzyl-piperidin-4-ylidene)cyanoacetate (112.9 g, 0.40 mol) in ethanol (500 mL) and water (100 mL), potassium cyanide (64.6 g, 0.99 mol) heated at 65'C for 24 h. After removal of ethanol, water was added to the residue. The water phase was extracted 15 with ether and the combined ether extract was washed with water, brine and dried over Na2SO4 to give 77.7 g of 1-benzyl-4-cyanomethylpiperidine-4-carbonitrile. Rf=0.38 (hexane:AcOEt=1:1). [C] Synthesis of 8-benzyl-2,8-diazaspiro[4,5]decane-1,3-dione (4; Figure 4). 1 Benzyl-4-cyanomethylpiperidine-4-carbonitrile (27.2 g, 0.114 mol), acetic acid (56.8 mL) 20 and sulfuric acid (11.8 mL) were heated at 125 'C for 1 hr. The mixture was cooled to 25'C and sat. NaOH was used to adjust the pH to 6. The mixture was extracted with dichloromethane. The combined extracts were washed with water, brine, dried over Na 2
SO
4 and evaporated to give 8-benzyl-2,8-diazaspiro[4,5]decane-1,3-dione. R=0.40
(CH
2 Cl 2 :MeOH=10:1). 25 [D] Synthesis of 8-benzyl- N-2-ethyl-2,8-diazaspiro[4,5]decane-1,3-dione (5; Figure 4). 8-Benzyl-2,8-diazaspiro[4,5]decane-1,3-dione in DMF was treated with NaH (1.2 eq) and 2-bromeethane was added. The mixture was heated at 100 'C for 2 hr. The mixture was cooled to 25 'C and poured over ice-water and extracted with dichloromethane. The combined dichloromethane extract was washed with water, brine, dried over Na 2
SO
4 and 30 evaporated to give 8-benzyl-N-2-ethyl-2,8-diazaspiro[4,5]decane-1,3-dione. [E] Synthesis ofN-2-ethyl-2,8-diazaspiro[4,5]decane-1,3-dione (6; Figure 4). 8 Benzyl-N-2-ethyl-2,8-diazaspiro[4,5]decane-1,3-dione (2.8 g) and Pd(OH) 2 (0.8 g) in - 62 - WO 2009/117728 PCT/US2009/037928 ethanol (50 mL) and acetic acid (0.5 mL) was stirred under H 2 at 25 'C for 15 hr. The catalyst was removed by filtration and ethanol was evaporated to give N-2-ethyl-2,8 diazaspiro[4,5]decane-1,3-dione. Example 3 5 One approach to the synthesis of 6-0-[N-(N-2-ethyl-2,8-diazaspiro[4,5]decane- 1,3 dione)aminocarbonyl]-a,p-D-glucopyranose (13; Figure 6) is depicted in Figure 6. 1-0 Benzyl- 3-D-Glucoside 7 is commercially available or it can be made in one step from almond p-D-glucosidase-catalyzed glycosidation of -D-glucose and benzyl alcohol. See Carbohydrate Res. 1995, 279, 315. In addition, benzyl 2,3,4-tri-O-benzyl-6-0 10 imidazolylcarbonyl- p-D-glucopyranoside (11; Figure 6) can be prepared via a known procedure. See Org. Biomol. Chen. 2003, 1, 767-771. Synthetic protocols for the synthesis of the compounds depicted in Figure 6 are presented below. [A] Synthesis of benzyl 6-0-trityl-3-D-glucopyranside (8; Figure 6). A solution of 1 (1.71 g, 6.33 mmol) in pyridine (14 mL) is treated with trityl chloride (2.65 g, 9.5 mmol) 15 and DMAP (155 mg, 1.27 mmol) at 60 'C for 7 hr. The reaction mixture is cooled at room temperature, MeOH (4 mL) added, and the solvents were evaporated. The residue is purified by flash chromatography (hexane-AcOEt, 5:1 to give benzyl 6-0-trityl-p-D glucopyranside as a solid. Rf= 0.22 (hexane-AcOEt, 1:2); m.p. 72-74 'C; [ca]D 20 - 52.0 (c 1, CHCl 3 ). 20 [B] Synthesis of benzyl 2,3,4-tri-O-benzyl-6-0-trityl-p-D-glucopyranoside (9; Figure 6). A solution of benzyl 6-0-trityl-p-D-glucopyranside (3.58 g, 6.99 mmol) in dry DMF (23 mL) is treated with 950% NaH (630 mg, 26.2 mmol) at 0 0 C. After 10 min, benzyl bromide (2.74 mL, 23.1 mmol) is added and the reaction is allowed to proceed at room temperature overnight. The reaction mixture is quenched with methanol and concentrated. 25 The residue is dissolved in ether (50 mL), washed with water (4 x 30 mL), dried (Na 2
SO
4 ), and concentrated. The residue is purified by flash chromatography (hexane-AcOEt, 20:1; 10:1) to give benzyl 2,3,4-tri-O-benzyl-6-0-trityl- p-D-glucopyranoside as a syrup. Rf = 0.29 (hexane-AcOEt, 10:1). [C] Synthesis of benzyl 2,3,4-tri-O-benzyl-p-D-glucopyranoside (10; Figure 6). A 30 solution of benzyl 2,3,4-tri-O-benzyl-6-0-trityl-p-D-glucopyranoside (4.41 g, 5.64 mmol) in CH 2 Cl 2 -MeOH (1:2, 56.4 mL) is treated with pTsOH (0.21 g, 1.13 mmol) at room temperature for 6 hr. After this time, triethylamine (0.16 mL, 1.13 mmol) is added, the - 63 - WO 2009/117728 PCT/US2009/037928 mixture concentrated and the residue dissolved in ether (60 mL). The organic solution is washed with water (2 x 30 mL), brine (30 mL), dried (Na 2
SO
4 ), and concentrated. The residue is fractionated by flash chromatography (hexane-AcOEt, 8:1; 5:1; 3:1) to give benzyl 2,3,4-tri-O-benzyl- P-D-glucopyranoside as a solid. Rf= 0.21 (hexane-AcOEt, 3:1); 5 m.p. 99-101 'C; [a]D 20 -10.4 0 (c 1, CHC1 3 ). [D] Synthesis of benzyl 2,3,4-tri-O-benzyl-6-0-imidazolylcarbonyl-p-D glucopyranoside (11; Figure 6). A solution of benzyl 2,3,4-tri-O-benzyl-p-D glucopyranoside (2.53 g, 4.69 mmol) in dioxane (5.3 mL) and N,N-carbonyldiimidazol (0.91 g, 5.63 mmol) is stirred at room temperature for lhr. After this time, the mixture is 10 concentrated and the residue purified by flash chromatography (hexane-AcOEt 3:1) to give benzyl 2,3,4-tri-O-benzyl-6-0-imidazolylcarbonyl-p-D-glucopyranoside as a solid. Rf= 0.22 (hexane-AcOEt, 2:1); m.p. 105-108 'C; [a]D 2 0 +28.9 0 (c 1, CHC1 3 ). [E] Synthesis of benzyl 2,3,4-tri-O-benzyl-6-0-[N-2-ethyl-2,8 diazaspiro[4,5]decane-1,3-dione) aminocarbony] -p-D-glucopyranoside (12; Figure 6). A 15 mixture of benzyl 2,3,4-tri-O-benzyl-6-0-imidazo lylcarbonyl- -D-glucopyranoside (2.78 g, 4.39 mmol), N-2-ethyl-2,8-diazaspiro[4,5]decane-1,3-dione (1.63 g, 3.65 nimol), triethylamine (5mL), and THF (15 mL) is stirred at 80 0 C for 8 hr. After this time, the solvents were removed and the residue was purified by flash chromatography to give benzyl 2,3,4-tri-O-benzyl-6-0-[N-2-ethyl-2,8-diazaspiro[4,5]decane-1,3-dione) 20 aminocarbony]- p-D-glucopyranoside. [F] Synthesis of 6-0-[N-2-ethyl-2,8-diazaspiro[4,5]decane-1,3 dione)aminocarbony]-a,-D-glucopyranose (13; Figure 6). A solution of the glycoconjugate (0.01M) in AcOEt-MeOH-toluene (4:3:3) was hydrogenolyzed over 10% Pd/C (1.1 g per mmol) for 1-5 hr, when TLC (AcOEt-AcOH-MeOH, 4:1:1) shows the complete conversion 25 product. The reaction mixture is filtered through Celite, and concentrated. The residue is dissolved in methanol/water (95:5) and freeze-dried, to give 6-0-[N-2-ethyl-2,8 diazaspiro[4,5]decane- 1,3-dione)aminocarbony]-ap-D-glucopyranose. Example 4 One approach to the synthesis of 1,2,3,4,5-penta-O-benzyl-scyllo-inositol is shown 30 in Figure 7. Preparation of 1,2-0-Cyclohexylidene myo-inositol was done using a modified version of the method described by Angyal. See J. Chem. Soc. 1961, 4116. 1,2,3,4,5, Penta-O-benzylmyo-inositol was synthesized according to a known procedure of Lowe. - 64 - WO 2009/117728 PCT/US2009/037928 See J. Chem. Soc. Perkin Trans 1. 1991, 1249. Synthetic protocols for the synthesis of the compounds depicted in Figure 7 are presented below. [A] Synthesis of 1,2-0-cyclohexylidene myo-inositol (2; Figure 7). Myo-inositol (5 g, 28 mmol) cyclohexanone (50 mL), p-toluene sulfonic acid (36 mg), DMF (5 mL), and 5 benzene (25 mL) were refluxed in a Dean-Stark apparatus for 16 hr. The clear solution was cooled to 40'C and benzene (25 mL), petroleum ether (25 mL), and ethanol (12 mL) were added. To this solution was added p-toluene sulfonic acid (0.3 g) and the mixture was stirred at 4'C for 2 hr. Triethylamine (0.3 mL) was added and the mixture was allowed to stand at -20'C for 16 hr. The suspension was filtered and the filtrate was heated in ethanol 10 (100 mL) and triethylamine (0.5 mL) at 80'C for 1 hr. After cooling, crystalline (±)-cis-1,2 0-cyclohexylidene myo-inositol was collected by filtration and dried (5.3 g, 74%), m.p. 175-180-C (Lit 178-C). [B] Synthesis of 1,4,5,6-tetra-O-benzyl-2,3-0-cyclohexylidene myo-inositol. 1,2 0-cyclohexylidene myo-inositol is treated with benzyl bromide and sodium hydride in 15 DMF heated for 16 hr. The solution is poured over ice-water and extracted with ether. The combined extracts are washed with water, brine and dried. The solvent is evaporated in vacuo and the residue is chromatographed on silica gel to give 1,4,5,6-tetra-O-benzyl-2,3 0-cyclohexylidene myo-inositol; mp 113-115'C. [C] Synthesis of 1,4,5,6-Tetra-O-benzylmyo-inositol. 1,4,5,6-tetra-O-benzyl-2,3-0 20 cyclohexylidene myo-inositol is heated for 4 hr at 1 00 0 C with glacial acetic acid (20 mL) and water (5 mL). The solution is evaporated in vacuo and the residue is chromatographed on silica gel to give 1,4,5,6-tetra-O-benzylmyo-inositol. [D] Synthesis of 1,3,4,5,6-Penta-O-benzylmyo-inositol. A solution of 1,4,5,6-tetra O-benzyllmyo-inositol in benzene is treated with benzyl bromide and sodium hydride. The 25 mixture was stirred at 100 'C for 2 hr. The reaction mixture is poured over ice-water and extracted with ether. The organic layer was separated and washed successively with saturated aqueous NaHCO 3 and brine. The solution was evaporated in vacuo and the residue was chromatographed on silica gel to give 1,3,4,5,6-penta-O-benzylmyo-inositol. [E] Synthesis of 1,2,3,4,5-penta-O-benzyl-scyllo-inositol. 1,3,4,5,6-penta-O 30 benzylmyo-inositol in anhydrous and methylene chloride (20 mL) and dry pyridine is treated with trifluoromethylsulfonyl anhydride at -60 'C. The reaction mixture is allowed to - 65 - WO 2009/117728 PCT/US2009/037928 warm to 25 'C and kept for 2 hr. The solution is quenched with water, diluted with methylene chloride and washed with saturated aqueous NaHCO 3 . Solvent is evaporated in vacuo and the residue is chromatographed on silica gel to give 1,2,3,4,5-penta-O-benzyl scyllo-inositol. 5 Example 5 One approach to the synthesis of 1-deoxy-1-[18F]fluoro-scyllo-inositol is presented in Figure 8. Preparation of 1,4,5,6-tetra-O-acetyl-myo-inositol (4; Figure 8) was done using a modified version of the method described by Angyal. See J. Chem. Soc. 1961, 4116. 1,3,4,5,6-Penta-O-acetylmyo-inositol (5; Figure 8) was synthesized according to a known 10 procedure of Hosoda. See Bioorg. Med. Chem. 2002, 10, 1855. Synthetic protocols for the synthesis of the compounds depicted in Figure 8 are presented below. [A] Synthesis of 1,2-0-cyclohexylidene myo-inositol (2; Figure 8). Myo-inositol (5 g, 28 mmol) cyclohexanone (50 mL), p-toluene sulfonic acid (36 mg), DMF (5 mL), and benzene (25 mL) were refluxed in a Dean-Stark apparatus for 16 hr. The clear solution was 15 cooled to 40 'C and benzene (25 mL), petroleum ether (25 mL), and ethanol (12 mL) were added. To this solution was added p-toluene sulfonic acid (0.3 g) and the mixture was stirred at 4 'C for 2 hr. Triethylamine (0.3 mL) was added and the mixture was allowed to stand at -20 'C for 16 hr. The suspension was filtered and the filtrate was heated in ethanol (100 mL) and triethylamine (0.5 mL) at 80 'C for 1 hr. After cooling, crystalline (±)-cis 20 1,2-0-cyclohexylidene myo-inositol was collected by filtration and dried (5.3 g, 74%), m.p. 175-180-C (Lit 178-C). [B] Synthesis of 1,4,5,6-tetra-O-acetyl-2,3-0-cyclohexylidene myo-inositol (3; Figure 8). 1,2-0-cyclohexylidene myo-inositol (4.8 g, 17.4 mmol) was heated at 90 'C for 2 hr with anhydrous pyridine (30 mL) and acetic anhydride (32 mL). The solution was 25 evaporated in vacuo and the residue was chromatographed on silica gel using 96:4 methylene chloride/methanol to give 1,4,5,6-tetra-O-acetyl-2,3-0-cyclohexylidene myo inositol (6.8 g, 85%), mp 112-114C (lit 118'C). [C] Synthesis of 1,4,5,6-tetra-O-acetylmyo-inositol (4; Figure 8). 1,4,5,6-tetra-O acetyl-2,3-0-cyclohexylidene myo-inositol (5 g, 11.7 mmol) was heated for 4 hr at 100 'C 30 with glacial acetic acid (20 mL) and water (5 mL). The solution was evaporated in vacuo - 66 - WO 2009/117728 PCT/US2009/037928 and the residue was chromatographed on silica gel to give 1,3,4,5,6-penta-O-acetylmyo inositol as a monohydrate. [D] Synthesis of 1,3,4,5,6-penta-O-acetylmyo-inositol (5; Figure 8). To a solution of 1,3,4,5,6-penta-O-acetylmyo-inositol (2 g, 5.7 mmol) in anhydrous pyridine (5 mL) and 5 methylene chloride (20 mL) was added successively 4-(dimethylamino)pyridine (2 mg) and acetyl chloride (0.9 g,11.5 mmol). The mixture was stirred at 25 'C for 16 hr. Water was added to the reaction mixture and the organic layer was separated and washed successively with saturated aqueous NaHCO; and brine. The solution was evaporated in vacuo and the residue was chromatographed on silica gel to give 1,3,4,5,6-penta-O-acetylmyo-inositol. 10 [E] Synthesis of 1,3,4,5,6-penta-O-acetyl-2-0-methanesulfonyl myo-inositol (6; Figure 8). 1,3,4,5,6-penta-O-acetylmyo-inositol (1 g, 2.6 mmol) in anhydrous pyridine (5 mL) and methylene chloride (20 mL) was treated with 4-(dimethylamino)pyridine (2 mg) and methanesulfonyl chloride (0.6 g, 5.2 mmol) at 25'C for 16 hr. The solution was evaporated in vacuo and the residue was chromatographed on silica gel to give 1,3,4,5,6 15 penta-O-acetyl-2-0-methanesulfonyl myo-inositol. [F] Synthesis of 1-deoxy-1-[18F]fluoro-scyllo-inositol (8; Figure 8). A Wheaton 5 mL reaction vial containing fluorine-18 (100 mCi) in 1 mL of 18 0-enriched water, Kryptofix 2.2.2. (8 mg), and potassium carbonate (2 mg) was heated at 120'C and water was evaporated with the aid of a nitrogen gas flow. The KISF/Kryptofix complex was dried 20 three successive times by the addition of 1 mL acetonitrile followed by evaporation of the solvent using a nitrogen flow. A solution of 2 mg of mesylate 6 in 0.1 mL acetonitrile was added to the sealed vial and fluorination was performed at 140 'C for 10 min. After cooling to room temperature, the reaction mixture was passed through a silica gel Sep-Pak using methylene chloride (3 mL) and the solvent removed using a nitrogen flow. A mixture of 0.5 25 mL 1 M lithium hydroxide and 1 mL methanol was added to the reaction vial and the vial heated at 80 'C for 20 min. Solvent was removed, and 1-deoxy-1-[L 1 F]fluoro-scyllo-inositol was purified on a C18 Sep-Pak using saline and filtered (MillexGV 0.22 [Lm). Example 6 One approach to the synthesis of 6-0-[(B-D-glucopyranose 6-yl)-succinyl]-scyllo 30 inositol is shown in Figure 9. Benzyl 2,3,4-tri-O-benzyl- p-D-glucopyranoside 6-(hydrogen succinate) is prepared from a known procedure. See Org. Biomol. Chem. 2003, 1, 767-771. - 67 - WO 2009/117728 PCT/US2009/037928 Synthetic protocols for the synthesis of the compounds depicted in Figure 9 are presented below. [A] Synthesis of benzyl 2,3 ,4-tri-0-benzyl- f-D-glucopyranoside 6-(hydrogen succinate). A solution of benzyl 2,3,4-tri-O-benzyl- p-D-glucopyranoside (10; Figure 9) in 5 pyridine is treated with succinic anhydride and DMAP and stirred at room temperature for 16 h. The mixture is concentrated and the residue dissolved in CH 2 Cl 2 and washed successively with 5% aqueous HCl (3 x 15 mL), sat. aqueous NaHCO 3 (3 x 15 mL), and water (3 x 15 mL). The organic solution is dried (Na 2
SO
4 ), and concentrated to give benzyl 2,3,4-tri-O-benzyl-p-D-glucopyranoside 6-(hydrogen succinate) as a solid. Rf= 0.56 10 (hexane-AcOEt, 2:1); m.p. 75-80 0 C; [a]D 20 -7.7 0 (c 1, CHC1 3 ). [B] Synthesis of benzyl-[(benzyl 2,3,4-tri-O-benzyl- P-D-glucopyranoside 6-yl) succinyl]-scyllo-inositol. A solution of benzyl 2,3,4-tri-O-benzyl- -D-glucopyranoside 6 (hydrogen succinate) in CH 2 Cl 2 (2.5 mL) is added dropwise to a solution of 1,2,3,4,5, penta-O-benzyl-scyllo-inositol and N,N'-diisopropylcarbodiimide in CH 2 Cl 2 (10 ml) at 0 15 0 C. The mixture is allowed to stir 24 h at room temperature, then, diluted with CH 2 Cl 2 (15 mL), washed with IN KHSO 4 (2 x 10 mL), sat. aqueous NaHCO 3 (2 x 10 mL), water (2 x 10 mL), and sat. NaCl (10 mL). The organic solution is dried (Na 2
SO
4 ), the solvent removed under reduced pressure, and the residue purified by flash chromatography to give benzyl-[(benzyl 2,3,4-tri-O-benzyl- P-D-glucopyranoside 6-yl)-succinyl]-scyllo-inositol. 20 [C] Synthesis of 6-0-[(p-D-glucopyranose 6-yl)-succinyl]-scyllo-inositol. Benzyl [(benzyl 2,3,4-tri-0-benzyl- p-D-glucopyranoside 6-yl)-succinyl]-scyllo-inositol in 1:1 AcOEt-MeOH is treated with TFA and Pd/C and stirring under hydrogen for 12 h. The reaction mixture is filtered and concentrated, and the residue is dissolved in CH 3
NO
2 -water (95:5) and freeze-dried, to give 6-0-[(p-D-glucopyranose 6-yl)-succinyl]-scyllo-inositol. 25 Example 7 RS-86 (2-ethyl-8-methyl-2,8-diazaspiro[4,5]decane-1,3-dione), a M1 muscarinic receptor agonist, was radiofluorinated and brain accumulation evaluated and compared to that of its C-I1 labeled analog. Alzheimer's disease (AD) is associated with reductions in the presynaptic marker choline acetyltransferase activity and M2 muscarine receptors which 30 precedes other pathologic changes. A number of M1 agonists have been developed to treat AD that increase acetylcholine transmission in the brain alleviating memory loss. M1 postsynaptic receptors are thought to be upregulated. Therefore, a M1 specific radioligand - 68 - WO 2009/117728 PCT/US2009/037928 may show higher than normal accumulation in patients, and hence, serve as a potential early diagnostic method for AD. As described above, 2-(2-methanesulfonylethyl)-8-methyl-2,8 diazaspiro[4,5]decane-1,3-dione was prepared in five steps. The RS-86 mesylate (2 mg) in 5 acetonitrile (0.1 mL) was added to a sealed vial containing dried K 1 "F/kryptofix and heated at 120'C for 10 min. The mixture was diluted with water (0.2 mL) and purified by HPLC (C-18 column 250 x 10 mm, flow 6 mL/min, PBS/acetonitrile (95:5). The fraction containing [ 18 F]fluoro-RS 86 was evaporated to dryness and the activity dissolved in PBS before filtering. Biodistribution was performed in rats at 5, 30 and 60 min. 10 [ 18 F]fluoro-RS 86 was prepared in 20% yield (EOS) with 95% chemical and 98% radio purity. Brain uptake at 5, 30 and 60 min was 0.27, 0.54, 0.48, respectively. Blood, liver and stomach were 0.3%, 0.64% and 0.90% with the greatess uptake in the kidneys (2.5%) at 30 min. Defluorination was minimal (0.42% in bone at 30 min). The lower brain uptake of ["F]fluoro-RS 86 compared to ["C]RS-86 (0.54% vs. 15 1%) may be due to the location of the fluoride label on the ligand. These preliminary results suggest that [ 1 "F]fluoro-RS 86 accumulates in rat brain, however further studies are needed to determine whether the distribution in the brain reflects M1 mAChR concentration. INCORPORATION BY REFERENCE All of the U.S. patents and U.S. patent application publications cited herein are 20 hereby incorporated by reference. EQUIVALENTS Those skilled in the art will recognize, or be able to ascertain using no more than routine experimentation, many equivalents to the specific embodiments of the invention described herein. Such equivalents are intended to be encompassed by the following claims. - 69 -
Claims (55)
1. A compound, or a pharmaceutically acceptable salt thereof, represented by formula II: R 7 R 7 L-O R 7 R 7 R 7 II wherein, independently for each occurrence, L is -C(=O)R 3 , -C(=O)[C(R 1 )2]pR 3 , -C(=O)[C(R)2]pC(=O)R 33 _3 [C(R) 2 ]pC(=O)R', -C(=O)[C 1 _ 1 0alkylene]R , -[C 1 1 oalkylene]C(=O)R or C(=O)[C1_1oalkylene]C(=O)R 3 ; R 1 is hydrogen, or alkyl; R 4 R 4 R4 'R4 0 0 R1 R 3 is R1 R 4 is hydrogen, halo, hydroxy, alkoxy, aryloxy, heteroaryloxy, aralkyloxy, heteroaralkyloxy, or -OR5; R 5 is hydrogen, alkyl, heteroalkyl, cycloalkyl, heterocycloalkyl, aryl, heteroaryl, aralkyl, or heteroaralkyl; R 7 is halo, hydroxy, alkoxy, aryloxy, heteroaryloxy, aralkyloxy, heteroaralkyloxy, or -OR 5 ; and p is 1-10 inclusive. 70
2. The compound of claim 1, wherein said compound comprises at least one 18F, 76 77 123 124 125 Br, Br, 1, 1 or 1.
3. The compound of claim 1, wherein said compound comprises at least one 18F.
4. The compound of claim 1, wherein L is -C(=O)R 3 or -C(=O)[C(R ) 2 ]pC(=O)R 3 .
5. The compound of claim 1, wherein L is -C(=O)R 3 . 3
6. The compound of claim 1, wherein L is -C(=O)[CH 2 ]C(=O)R.
7. The compound of claim 1, wherein L is -C(=O)CH 2 CH 2 C(=O)R.
8. The compound of claim 1, wherein R7 is -F, -Cl, -Br, -5, or -OR5.
9. The compound of claim 1, wherein R7 is, -F, -Cl, -Br, -I, or -OH.
10. The compound of claim 1, wherein R 7 is -F or -OH.
11. The compound of claim 1, wherein R 7 is - 1 8 F or -OH; provided that only one R7 is -18F.
12. The compound of claim 1, wherein L is -C(=O)R 3 or -C(=O)[C(R 1 )2]pC(=O)R 3 ; and R7 is -F, -Cl, -Br, -I, or -OR5.
13. The compound of claim 1, wherein L is -C(=O)R 3; and R7 is -F, -Cl, -Br, -I, or OR 5 .
14. The compound of claim 1, wherein L is -C(=O)[CH 2 ]pC(=O)R 3; and R7 is -F, 5 Cl, -Br, -I, or -OR .
15. The compound of claim 1, wherein L is -C(=O)R 3 ; and R 7 is -OH.
16. The compound of claim 1, wherein L is -C(=O)CH 2 CH 2 C(=O)R 3 ; and R7 is OH.
17. The compound of claim 1, wherein L is -C(=O)R 3 ; and R 7 is -F or -OH; provided that only one R 7 is -F.
18. The compound of claim 1, wherein L is -C(=O)CH 2 CH 2 C(=O)R 3 ; and R 7 is -F or -OH; provided that only one R7 is -F.
19. The compound of claim 1, wherein L is -C(=O)R 3; and R7 is -18 F or -OH; provided that only one R7 is -18 F.
20. The compound of claim 1, wherein L is -C(=O)CH 2 CH 2 C(=O)R 3; and R7 is -18 F or -OH; provided that only one R7 is -18 F. 71 4 5
21. The compound of claim 1, wherein R4 is -H, -F, -Cl, -Br, -I, or -OR . 4 i 5
22. The compound of claim 1, wherein R4 is -OR.
23. The compound of claim 1, wherein R 4 is-OH. R4 R4 R4 'W 0 S 0H -- O H
24. The compound of claim 1, wherein R 3 is H ; W is -F, -Cl, -Br or -I; and R4 is -OR5. R4 R4 R4 'W 0 S 0H -- O H
25. The compound of claim 1, wherein R 3 is H ; W is -F; and R4 is -OR5. R4 R4 R4 'W 0 S 0H O H
26. The compound of claim 1, wherein R 3 is H ; W is -18F; and R4 is -OH.
27. The compound of claim 1, wherein L is -C(=O)R 3 or -C(=O)[C(R 1 ) 2 ]pC(=O)R 3 ; R7 is, -F, -Cl, -Br, -I, or -OR ; and R4 is -F, -Cl, -Br, -I, or -OR5. 72
28. The compound of claim 1, wherein L is -C(=O)R 3 or -C(=O)[C(R 1 )2]pC(=O)R 3 ; R7 is -F, -Cl, -Br, -I, or -OR ; and R4 is -OR5.
29. The compound of claim 1, wherein L is -C(=O)R 3 or -C(=O)[C(R 1 )2]pC(=O)R 3 ; R 7 is -H, -F, -Cl, -Br, -I, or -OR 5 ; and R 4 is -OH.
30. The compound of claim 1, wherein L is -C(=O)R 3 or -C(=O)[C(R 1 )2]pC(=O)R 3 ; R4 R4 R4 'W 0 - H R 7 is, -F, -Cl, -Br, -I, or -OR 5 ; R 3 is H ; W is -F, -Cl, -Br or -I; and R4 is -OR5.
31. The compound of claim 1, wherein L is -C(=O)R 3 or -C(=0)[C(R )2]pC(=0)R3 R4 R4 R4 'W 0 -O H R 7 is -F, -Cl, -Br, -I, or -OR 5 ; R 3 is H ;W is -F; and R 4 is -OR . 73
32. The compound of claim 1, wherein L is -C(=O)R 3 or -C(=O)[C(R 1 )2]pC(=O)R 3 ; R4 R4 R4 'W 0 H R7 is -F, -Cl, -Br, -I, or -OR5; R3 is H ;W is 18 F; and R4 is -OH.
33. The compound of claim 1, wherein the compound comprises a radioimaging agent.
34. The compound of claim 33, wherein R 4 comprises the radioimaging agent.
35. The compound of claim 33, wherein R 4 comprises the radioimaging agent; and the radioimaging agent is 18F.
36. The compound of claim 33, wherein R 7 comprises the radioimaging agent.
37. The compound of claim 33, wherein R 7 comprises the radioimaging agent; and the radioimaging agent is 18F.
38. A pharmaceutical composition comprising a pharmaceutically acceptable carrier and a compound represented by a compound of any one of claims 1-37.
39. A method for amyloid imaging a subject suffering from an amyloidosis associated pathological condition comprising the step of: administering a compound, or a composition comprising a pharmaceutically acceptable carrier and the compound or a pharmaceutically acceptable form thereof, wherein the compound is a compound of any one of claims 1-37.
40. The method of claim 39, wherein said amyloidosis associated pathological condition is Alzheimer's disease.
41. The method of claim 39, wherein said compound comprises at least one 18F, 76 77 123 124 125 Br, Br, 1, 1I or 1.
42. A method for treating a subject suffering from an amyloidosis associated pathological condition, comprising the step of: 74 administering a compound, or a composition comprising a pharmaceutically acceptable carrier and the compound or a pharmaceutically acceptable form thereof, wherein the compound is a compound of any one of claims 1-37.
43. The method of claim 42, wherein said amyloidosis associated pathological condition is Alzheimer's disease.
44. The method of claim 42, wherein said treatment inhibits the formation of plaque.
45. The method of claim 42, wherein said compound is a combination of inositol and glucose, or a disaccharide comprising inositol and glucose.
46. The method of claim 45, wherein said combination shows increased uptake over one or both of the constituents thereof.
47. The method of claim 42, wherein said compound is fluorinated.
48. The compound of claim 1, wherein the compound is 0 B n0 O B OBn Bgo - OBO~n OBn or
49. A compound having the following structure:
50. A pharmaceutical composition comprising a pharmaceutically acceptable carrier and a compound represented by a compound of claim 49.
51. A method for amyloid imaging a subject suffering from an amyloidosis associated pathological condition comprising the step of: administering a compound, or a composition comprising a pharmaceutically acceptable carrier and the compound or a pharmaceutically acceptable form thereof, wherein the compound is one 75
52. The method of claim 51, wherein said amyloidosis-associated pathological condition is Alzheimer's disease.
53. A method for treating a subject suffering from an amyloidosis-associated pathological condition, comprising the step of: administering a compound, or a composition comprising a pharmaceutically acceptable carrier and the compound or a pharmaceutically acceptable form thereof, wherein the compound is the compound of claim 49.
54. The method of claim 53, wherein said amyloidosis-associated pathological condition is Alzheimer's disease.
55. The method of claim 53, wherein said treatment inhibits the formation of plaque. 76
Priority Applications (2)
Application Number | Priority Date | Filing Date | Title |
---|---|---|---|
AU2013248197A AU2013248197B2 (en) | 2008-03-21 | 2013-10-23 | Compounds and compositions for the detection and treatment of Alzheimer's disease and related disorders |
AU2016213801A AU2016213801A1 (en) | 2008-03-21 | 2016-08-11 | Compounds and compositions for the detection and treatment of Alzheimer's disease and related disorders |
Applications Claiming Priority (3)
Application Number | Priority Date | Filing Date | Title |
---|---|---|---|
US61/038,571 | 2008-03-21 | ||
AU2009225407A AU2009225407B2 (en) | 2008-03-21 | 2009-03-23 | Compounds and compositions for the detection and treatment of Alzheimer's disease and related disorders |
AU2013248197A AU2013248197B2 (en) | 2008-03-21 | 2013-10-23 | Compounds and compositions for the detection and treatment of Alzheimer's disease and related disorders |
Related Parent Applications (1)
Application Number | Title | Priority Date | Filing Date |
---|---|---|---|
AU2009225407A Division AU2009225407B2 (en) | 2008-03-21 | 2009-03-23 | Compounds and compositions for the detection and treatment of Alzheimer's disease and related disorders |
Related Child Applications (1)
Application Number | Title | Priority Date | Filing Date |
---|---|---|---|
AU2016213801A Division AU2016213801A1 (en) | 2008-03-21 | 2016-08-11 | Compounds and compositions for the detection and treatment of Alzheimer's disease and related disorders |
Publications (2)
Publication Number | Publication Date |
---|---|
AU2013248197A1 AU2013248197A1 (en) | 2013-11-14 |
AU2013248197B2 true AU2013248197B2 (en) | 2016-05-12 |
Family
ID=49552483
Family Applications (1)
Application Number | Title | Priority Date | Filing Date |
---|---|---|---|
AU2013248197A Ceased AU2013248197B2 (en) | 2008-03-21 | 2013-10-23 | Compounds and compositions for the detection and treatment of Alzheimer's disease and related disorders |
Country Status (1)
Country | Link |
---|---|
AU (1) | AU2013248197B2 (en) |
Citations (3)
Publication number | Priority date | Publication date | Assignee | Title |
---|---|---|---|---|
WO2007041855A1 (en) * | 2005-10-13 | 2007-04-19 | Waratah Pharmaceuticals, Inc. | Scyllo-inositol derivatives and their use in the treatment of diseases characterised by abnormal protein folding or aggregation or amyloid formation, deposition, accumulation or persistence |
US20070197452A1 (en) * | 2006-02-17 | 2007-08-23 | Mclaurin Joanne | Treatment of amyloid-related diseases |
WO2009014203A1 (en) * | 2007-07-26 | 2009-01-29 | Hokko Chemical Industry Co., Ltd. | Method for producing (1,3,5/2,4,6)-1-fluoro-2,3,4,5,6-cyclohexanepentol |
-
2013
- 2013-10-23 AU AU2013248197A patent/AU2013248197B2/en not_active Ceased
Patent Citations (3)
Publication number | Priority date | Publication date | Assignee | Title |
---|---|---|---|---|
WO2007041855A1 (en) * | 2005-10-13 | 2007-04-19 | Waratah Pharmaceuticals, Inc. | Scyllo-inositol derivatives and their use in the treatment of diseases characterised by abnormal protein folding or aggregation or amyloid formation, deposition, accumulation or persistence |
US20070197452A1 (en) * | 2006-02-17 | 2007-08-23 | Mclaurin Joanne | Treatment of amyloid-related diseases |
WO2009014203A1 (en) * | 2007-07-26 | 2009-01-29 | Hokko Chemical Industry Co., Ltd. | Method for producing (1,3,5/2,4,6)-1-fluoro-2,3,4,5,6-cyclohexanepentol |
Non-Patent Citations (7)
Title |
---|
HOSODA, A. et al, "Synthesis of Feruloyl-myo-inositol Derivatives and their Inhibitory Effects on Phorbol Ester-Induced Superoxide Generation and Epstein-Barr Virus Activation." Bioorganic and Medicinal Chemistry, 2002, 10(6), 1855-1863. * |
KOZIKOWSKI, A. et al, "Synthesis and Biological Activity of the D-3-Deoxy-3-fluoro and D-3-Chloro-3-deoxy Analogues of Phosphatidylinositol." Journal of Organic Chemistry, 1994, 59, 963-971. * |
KOZIKOWSKI, A. et al, Bioorganic and Medicinal Chemistry Letters, 1995, 5(12), 1295-1300. * |
LAMPE, D. et al, Journal of the Chemical Society, Perkin Transactions 1: Organic and Bio-Organic Chemistry, 1996, 14, 1717-1727. * |
MARTIN, S. et al, "General Method for the Synthesis of Phospholipid Derivatives of 1,2-O-Diacyl-sn-glycerols." Journal of Organic Chemistry, 1994, 59(17), 4805-4820. * |
OFFER, J. et al, "Synthesis and Tritium Radiolabelling of Fluorinated Analogues of myo-lnositol." Journal of the Chemical Society, Perkin Transactions 1: Organic and Bio-Organic Chemistry, 1992, 8, 953-960. * |
SOLOMONS, K. et al, "Synthesis of D-1,2-dideoxy-1,2-difluoro-myo-inositol 3,4,5,6-tetrakisphosphate and its enantiomer as analogues of myo-inositol 3,4,5,6-tetrakisphosphate." Carbohydrate Research, 1998, 309, 337-343. * |
Also Published As
Publication number | Publication date |
---|---|
AU2013248197A1 (en) | 2013-11-14 |
Similar Documents
Publication | Publication Date | Title |
---|---|---|
US10857247B2 (en) | Compounds and compositions for the detection and treatment of Alzheimer's disease and related disorders | |
US8558003B2 (en) | Imaging tracers for early detection and treatment of amyloid plaques caused by Alzheimer's disease and related disorders | |
JP2011512354A (en) | A novel contrast agent for detecting neurological dysfunction | |
CA2617319A1 (en) | Radiolabeled-pegylation of ligands for use as imaging agents | |
KR20080105766A (en) | Heterocyclic indene derivatives and their radioisotope labeled compounds for imaging beta;-amyloid deposition | |
JP2010520275A (en) | Novel 2-heteroaryl substituted indole 695 | |
AU2013248197B2 (en) | Compounds and compositions for the detection and treatment of Alzheimer's disease and related disorders | |
AU2016213801A1 (en) | Compounds and compositions for the detection and treatment of Alzheimer's disease and related disorders | |
WO2012017891A1 (en) | Pyridyl benzofuran derivative | |
JPWO2013027694A1 (en) | Molecular imaging probe for conformation disease diagnosis | |
JP2021102593A (en) | New compound imaging tau | |
RU2472789C2 (en) | Novel 2-heteroaryl-substituted benzothiophenes and benzofurans 709 | |
JP2009203166A (en) | Diagnostic composition containing diphenyloxadiazole derivative |
Legal Events
Date | Code | Title | Description |
---|---|---|---|
PC1 | Assignment before grant (sect. 113) |
Owner name: THE GENERAL HOSPITAL CORPORATION Free format text: FORMER APPLICANT(S): THE GENERAL HOSPITAL CORPORATION; FLUOROPHARMA, INC. |
|
FGA | Letters patent sealed or granted (standard patent) | ||
MK14 | Patent ceased section 143(a) (annual fees not paid) or expired |