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Application filed by Biomarin Pharm IncfiledCriticalBiomarin Pharm Inc
Publication of AR120461A1publicationCriticalpatent/AR120461A1/en
Medicines That Contain Protein Lipid Enzymes And Other Medicines
(AREA)
Medicines Containing Material From Animals Or Micro-Organisms
(AREA)
Abstract
Aquí se proporcionan composiciones y métodos para tratar una deficiencia del inhibidor de la esterasa C1 normalizando los niveles de la proteína inhibidora de las esterasa C1 en un sujeto que tiene HAE.Provided herein are compositions and methods for treating a C1 esterase inhibitor deficiency by normalizing C1 esterase inhibitor protein levels in a subject having HAE.
ARP200103150A2019-11-142020-11-13
TREATMENT OF HEREDITARY ANGIOEDEMA WITH LIVER-SPECIFIC GENE THERAPY VECTORS
AR120461A1
(en)