AR120461A1 - TREATMENT OF HEREDITARY ANGIOEDEMA WITH LIVER-SPECIFIC GENE THERAPY VECTORS - Google Patents

TREATMENT OF HEREDITARY ANGIOEDEMA WITH LIVER-SPECIFIC GENE THERAPY VECTORS

Info

Publication number
AR120461A1
AR120461A1 ARP200103150A ARP200103150A AR120461A1 AR 120461 A1 AR120461 A1 AR 120461A1 AR P200103150 A ARP200103150 A AR P200103150A AR P200103150 A ARP200103150 A AR P200103150A AR 120461 A1 AR120461 A1 AR 120461A1
Authority
AR
Argentina
Prior art keywords
liver
treatment
gene therapy
specific gene
therapy vectors
Prior art date
Application number
ARP200103150A
Other languages
Spanish (es)
Inventor
Peter Colosi
Original Assignee
Biomarin Pharm Inc
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Biomarin Pharm Inc filed Critical Biomarin Pharm Inc
Publication of AR120461A1 publication Critical patent/AR120461A1/en

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  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
  • Medicines Containing Material From Animals Or Micro-Organisms (AREA)

Abstract

Aquí se proporcionan composiciones y métodos para tratar una deficiencia del inhibidor de la esterasa C1 normalizando los niveles de la proteína inhibidora de las esterasa C1 en un sujeto que tiene HAE.Provided herein are compositions and methods for treating a C1 esterase inhibitor deficiency by normalizing C1 esterase inhibitor protein levels in a subject having HAE.

ARP200103150A 2019-11-14 2020-11-13 TREATMENT OF HEREDITARY ANGIOEDEMA WITH LIVER-SPECIFIC GENE THERAPY VECTORS AR120461A1 (en)

Applications Claiming Priority (1)

Application Number Priority Date Filing Date Title
US201962935359P 2019-11-14 2019-11-14

Publications (1)

Publication Number Publication Date
AR120461A1 true AR120461A1 (en) 2022-02-16

Family

ID=80782256

Family Applications (1)

Application Number Title Priority Date Filing Date
ARP200103150A AR120461A1 (en) 2019-11-14 2020-11-13 TREATMENT OF HEREDITARY ANGIOEDEMA WITH LIVER-SPECIFIC GENE THERAPY VECTORS

Country Status (1)

Country Link
AR (1) AR120461A1 (en)

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