AR117861A1 - Métodos de reducción de eventos cerebrovasculares en pacientes con enfermedad de fabry - Google Patents

Métodos de reducción de eventos cerebrovasculares en pacientes con enfermedad de fabry

Info

Publication number
AR117861A1
AR117861A1 ARP200100155A ARP200100155A AR117861A1 AR 117861 A1 AR117861 A1 AR 117861A1 AR P200100155 A ARP200100155 A AR P200100155A AR P200100155 A ARP200100155 A AR P200100155A AR 117861 A1 AR117861 A1 AR 117861A1
Authority
AR
Argentina
Prior art keywords
fabry
patients
disease
reduction methods
cerebrovascular event
Prior art date
Application number
ARP200100155A
Other languages
English (en)
Spanish (es)
Inventor
Hjalmar Lagast
Nina Skuban
Original Assignee
Amicus Therapeutics Inc
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Family has litigation
First worldwide family litigation filed litigation Critical https://patents.darts-ip.com/?family=69726736&utm_source=google_patent&utm_medium=platform_link&utm_campaign=public_patent_search&patent=AR117861(A1) "Global patent litigation dataset” by Darts-ip is licensed under a Creative Commons Attribution 4.0 International License.
Application filed by Amicus Therapeutics Inc filed Critical Amicus Therapeutics Inc
Publication of AR117861A1 publication Critical patent/AR117861A1/es

Links

Classifications

    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K31/00—Medicinal preparations containing organic active ingredients
    • A61K31/33—Heterocyclic compounds
    • A61K31/395—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins
    • A61K31/435—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having six-membered rings with one nitrogen as the only ring hetero atom
    • A61K31/44—Non condensed pyridines; Hydrogenated derivatives thereof
    • A61K31/445—Non condensed piperidines, e.g. piperocaine
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P25/00—Drugs for disorders of the nervous system
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P9/00—Drugs for disorders of the cardiovascular system
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P9/00—Drugs for disorders of the cardiovascular system
    • A61P9/10—Drugs for disorders of the cardiovascular system for treating ischaemic or atherosclerotic diseases, e.g. antianginal drugs, coronary vasodilators, drugs for myocardial infarction, retinopathy, cerebrovascula insufficiency, renal arteriosclerosis

Landscapes

  • Health & Medical Sciences (AREA)
  • Veterinary Medicine (AREA)
  • Public Health (AREA)
  • General Health & Medical Sciences (AREA)
  • Animal Behavior & Ethology (AREA)
  • Chemical & Material Sciences (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Medicinal Chemistry (AREA)
  • Engineering & Computer Science (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • Organic Chemistry (AREA)
  • Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
  • General Chemical & Material Sciences (AREA)
  • Chemical Kinetics & Catalysis (AREA)
  • Heart & Thoracic Surgery (AREA)
  • Cardiology (AREA)
  • Epidemiology (AREA)
  • Urology & Nephrology (AREA)
  • Vascular Medicine (AREA)
  • Biomedical Technology (AREA)
  • Neurology (AREA)
  • Neurosurgery (AREA)
  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
  • Medicines Containing Material From Animals Or Micro-Organisms (AREA)
  • Enzymes And Modification Thereof (AREA)
ARP200100155A 2019-01-22 2020-01-22 Métodos de reducción de eventos cerebrovasculares en pacientes con enfermedad de fabry AR117861A1 (es)

Applications Claiming Priority (1)

Application Number Priority Date Filing Date Title
US201962795524P 2019-01-22 2019-01-22

Publications (1)

Publication Number Publication Date
AR117861A1 true AR117861A1 (es) 2021-09-01

Family

ID=69726736

Family Applications (1)

Application Number Title Priority Date Filing Date
ARP200100155A AR117861A1 (es) 2019-01-22 2020-01-22 Métodos de reducción de eventos cerebrovasculares en pacientes con enfermedad de fabry

Country Status (17)

Country Link
US (1) US20220087993A1 (enExample)
EP (2) EP4523750A3 (enExample)
JP (2) JP7680356B2 (enExample)
AR (1) AR117861A1 (enExample)
DK (1) DK3914247T3 (enExample)
ES (1) ES3007212T3 (enExample)
FI (1) FI3914247T3 (enExample)
HR (1) HRP20250078T1 (enExample)
HU (1) HUE069934T2 (enExample)
LT (1) LT3914247T (enExample)
PL (1) PL3914247T3 (enExample)
PT (1) PT3914247T (enExample)
RS (1) RS66410B1 (enExample)
SI (1) SI3914247T1 (enExample)
SM (1) SMT202500034T1 (enExample)
TW (1) TW202042812A (enExample)
WO (1) WO2020154354A1 (enExample)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
LT3840753T (lt) * 2018-08-20 2024-11-11 Amicus Therapeutics, Inc. Migalastatas skirtas naudoti fabry ligos gydymo būdui, pacientams turintiems gla geno mutaciją
KR20220044560A (ko) 2019-08-07 2022-04-08 아미쿠스 세라퓨틱스, 인코포레이티드 Gla 유전자에 돌연변이를 갖는 환자에서 파브리 질병을 치료하는 방법

Family Cites Families (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6274597B1 (en) 1998-06-01 2001-08-14 Mount Sinai School Of Medicine Of New York University Method of enhancing lysosomal α-Galactosidase A
EP2142197A4 (en) 2007-03-30 2010-11-10 Amicus Therapeutics Inc METHOD FOR THE TREATMENT OF MORBUS FABRY WITH PHARMACOLOGICAL CHAPTERONES
US9999618B2 (en) * 2007-04-26 2018-06-19 Amicus Therapeutics, Inc. Dosing regimens for the treatment of lysosomal storage diseases using pharmacological chaperones
WO2009102895A2 (en) 2008-02-12 2009-08-20 Amicus Therapeutics, Inc. Method to predict response to pharmacological chaperone treatment of diseases
WO2018017721A1 (en) * 2016-07-19 2018-01-25 Amicus Therapeutics, Inc. Treatment of fabry disease in ert-naïve and ert-experienced patients

Also Published As

Publication number Publication date
HUE069934T2 (hu) 2025-04-28
ES3007212T3 (en) 2025-03-19
LT3914247T (lt) 2025-01-27
EP3914247A1 (en) 2021-12-01
EP4523750A2 (en) 2025-03-19
PT3914247T (pt) 2025-01-23
JP2022518733A (ja) 2022-03-16
FI3914247T3 (fi) 2025-02-16
RS66410B1 (sr) 2025-02-28
US20220087993A1 (en) 2022-03-24
WO2020154354A1 (en) 2020-07-30
PL3914247T3 (pl) 2025-04-14
EP4523750A3 (en) 2025-06-11
SI3914247T1 (sl) 2025-03-31
JP2025128105A (ja) 2025-09-02
HRP20250078T1 (hr) 2025-03-28
EP3914247B1 (en) 2024-11-13
JP7680356B2 (ja) 2025-05-20
SMT202500034T1 (it) 2025-03-12
DK3914247T3 (da) 2025-01-27
TW202042812A (zh) 2020-12-01

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