AR104972A1 - COMPOSITIONS OF HYDROXIPROPIL b-CYCLODEXTRINE AND METHODS - Google Patents

COMPOSITIONS OF HYDROXIPROPIL b-CYCLODEXTRINE AND METHODS

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Publication number
AR104972A1
AR104972A1 ARP160101742A ARP160101742A AR104972A1 AR 104972 A1 AR104972 A1 AR 104972A1 AR P160101742 A ARP160101742 A AR P160101742A AR P160101742 A ARP160101742 A AR P160101742A AR 104972 A1 AR104972 A1 AR 104972A1
Authority
AR
Argentina
Prior art keywords
methods
mixtures
hydroxipropil
cyclodextrine
compositions
Prior art date
Application number
ARP160101742A
Other languages
Spanish (es)
Original Assignee
Vtesse Inc
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Vtesse Inc filed Critical Vtesse Inc
Publication of AR104972A1 publication Critical patent/AR104972A1/en

Links

Abstract

Mezclas de moléculas de b-ciclodextrinas sustituidas en una o más posiciones hidroxilo con grupos hidroxipropilo, donde la mezcla, incluye moléculas de b-ciclodextrinas no sustituidas, para el uso como un ingrediente farmacéuticamente activo; métodos de elaboración de dichas mezclas; métodos de calificación de dichas mezclas para el uso en una composición farmacéutica adecuada para la administración intratecal o intracerebroventricular; composiciones farmacéuticas adecuadas para la administración intratecal o intracerebroventricular que comprenden dichas mezclas; y métodos de uso de las composiciones farmacéuticas para el tratamiento de la enfermedad de Niemann-Pick Tipo C.Mixtures of substituted b-cyclodextrin molecules in one or more hydroxyl positions with hydroxypropyl groups, where the mixture includes unsubstituted b-cyclodextrin molecules, for use as a pharmaceutically active ingredient; methods of making said mixtures; qualification methods of said mixtures for use in a pharmaceutical composition suitable for intrathecal or intracerebroventricular administration; pharmaceutical compositions suitable for intrathecal or intracerebroventricular administration comprising said mixtures; and methods of using pharmaceutical compositions for the treatment of Niemann-Pick Type C disease.

ARP160101742A 2015-06-10 2016-06-10 COMPOSITIONS OF HYDROXIPROPIL b-CYCLODEXTRINE AND METHODS AR104972A1 (en)

Applications Claiming Priority (1)

Application Number Priority Date Filing Date Title
US201562173889P 2015-06-10 2015-06-10

Publications (1)

Publication Number Publication Date
AR104972A1 true AR104972A1 (en) 2017-08-30

Family

ID=59724568

Family Applications (1)

Application Number Title Priority Date Filing Date
ARP160101742A AR104972A1 (en) 2015-06-10 2016-06-10 COMPOSITIONS OF HYDROXIPROPIL b-CYCLODEXTRINE AND METHODS

Country Status (1)

Country Link
AR (1) AR104972A1 (en)

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