JPWO2023220502A5 - - Google Patents

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Publication number
JPWO2023220502A5
JPWO2023220502A5 JP2024566373A JP2024566373A JPWO2023220502A5 JP WO2023220502 A5 JPWO2023220502 A5 JP WO2023220502A5 JP 2024566373 A JP2024566373 A JP 2024566373A JP 2024566373 A JP2024566373 A JP 2024566373A JP WO2023220502 A5 JPWO2023220502 A5 JP WO2023220502A5
Authority
JP
Japan
Prior art keywords
aav
expression construct
intron
coding region
seq
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024566373A
Other languages
English (en)
Japanese (ja)
Other versions
JP2025516599A5 (https=
JP2025516599A (ja
Publication date
Application filed filed Critical
Priority claimed from PCT/US2023/064152 external-priority patent/WO2023220502A1/en
Publication of JP2025516599A publication Critical patent/JP2025516599A/ja
Publication of JPWO2023220502A5 publication Critical patent/JPWO2023220502A5/ja
Publication of JP2025516599A5 publication Critical patent/JP2025516599A5/ja
Pending legal-status Critical Current

Links

JP2024566373A 2022-05-12 2023-03-10 組換えパルボウイルス生成のための組成物及び方法 Pending JP2025516599A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202263341201P 2022-05-12 2022-05-12
US63/341,201 2022-05-12
PCT/US2023/064152 WO2023220502A1 (en) 2022-05-12 2023-03-10 Compositions and methods for recombinant parvovirus production

Publications (3)

Publication Number Publication Date
JP2025516599A JP2025516599A (ja) 2025-05-30
JPWO2023220502A5 true JPWO2023220502A5 (https=) 2026-02-03
JP2025516599A5 JP2025516599A5 (https=) 2026-02-03

Family

ID=85781807

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024566373A Pending JP2025516599A (ja) 2022-05-12 2023-03-10 組換えパルボウイルス生成のための組成物及び方法

Country Status (7)

Country Link
US (1) US20230365991A1 (https=)
EP (1) EP4522729A1 (https=)
JP (1) JP2025516599A (https=)
KR (1) KR20250009975A (https=)
CN (1) CN119487183A (https=)
AU (1) AU2023269763A1 (https=)
WO (1) WO2023220502A1 (https=)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2024211780A1 (en) * 2023-04-07 2024-10-10 Regenxbio Inc. Compositions and methods for recombinant aav production
WO2025090962A1 (en) * 2023-10-25 2025-05-01 Regenxbio Inc. Compositions and methods for recombinant aav production
TW202548023A (zh) * 2024-03-14 2025-12-16 美商雅菲納治療公司 用於生產重組腺相關病毒的質體系統

Family Cites Families (8)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US5139941A (en) 1985-10-31 1992-08-18 University Of Florida Research Foundation, Inc. AAV transduction vectors
US5945335A (en) * 1995-11-09 1999-08-31 Avigen, Inc. Adenovirus helper-free system for producing recombinant AAV virions lacking oncogenic sequences
US6114148C1 (en) 1996-09-20 2012-05-01 Gen Hospital Corp High level expression of proteins
DE60336736D1 (de) 2002-07-16 2011-05-26 VGX Pharmaceuticals LLC Codon-optimierte synthetische plasmide
US20130095558A1 (en) * 2011-07-19 2013-04-18 Wenlin Huang Process for producing recombinant human endostatin adenovirus
EP3870148A4 (en) * 2018-10-25 2022-11-09 Takeda Pharmaceutical Company Limited AAV TRIPLE PLASMID SYSTEM
EP3722434B1 (en) * 2019-04-12 2022-07-27 Freeline Therapeutics Limited Plasmid system
EP4085143B1 (en) * 2019-12-31 2025-08-13 Swanbio Therapeutics Limited Improved aav-abcd1 constructs and use for treatment or prevention of adrenoleukodystrophy (ald) and/or adrenomyeloneuropathy (amn)

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