JPWO2023198663A5 - - Google Patents

Info

Publication number
JPWO2023198663A5
JPWO2023198663A5 JP2024560444A JP2024560444A JPWO2023198663A5 JP WO2023198663 A5 JPWO2023198663 A5 JP WO2023198663A5 JP 2024560444 A JP2024560444 A JP 2024560444A JP 2024560444 A JP2024560444 A JP 2024560444A JP WO2023198663 A5 JPWO2023198663 A5 JP WO2023198663A5
Authority
JP
Japan
Prior art keywords
sequence
rna
nucleic acid
sequence encoding
expression cassette
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024560444A
Other languages
English (en)
Japanese (ja)
Other versions
JP2025512061A (ja
JP2025512061A5 (https=
Publication date
Application filed filed Critical
Priority claimed from PCT/EP2023/059361 external-priority patent/WO2023198663A1/en
Publication of JP2025512061A publication Critical patent/JP2025512061A/ja
Publication of JPWO2023198663A5 publication Critical patent/JPWO2023198663A5/ja
Publication of JP2025512061A5 publication Critical patent/JP2025512061A5/ja
Pending legal-status Critical Current

Links

JP2024560444A 2022-04-12 2023-04-11 Sncaの核酸調節 Pending JP2025512061A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
EP22168001.0 2022-04-12
EP22168001 2022-04-12
PCT/EP2023/059361 WO2023198663A1 (en) 2022-04-12 2023-04-11 Nucleic acid regulation of snca

Publications (3)

Publication Number Publication Date
JP2025512061A JP2025512061A (ja) 2025-04-16
JPWO2023198663A5 true JPWO2023198663A5 (https=) 2026-03-26
JP2025512061A5 JP2025512061A5 (https=) 2026-03-26

Family

ID=81580388

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024560444A Pending JP2025512061A (ja) 2022-04-12 2023-04-11 Sncaの核酸調節

Country Status (4)

Country Link
US (1) US20250297252A1 (https=)
EP (1) EP4508216A1 (https=)
JP (1) JP2025512061A (https=)
WO (1) WO2023198663A1 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2025160429A1 (en) * 2024-01-26 2025-07-31 Genzyme Corporation Artificial micrornas targeting snca

Family Cites Families (12)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6103526A (en) 1998-10-08 2000-08-15 Protein Sciences Corporation Spodoptera frugiperda single cell suspension cell line in serum-free media, methods of producing and using
EP2311967B1 (en) 2005-10-20 2017-09-20 UniQure IP B.V. Improved AAV vectors produced in insect cells
KR101589259B1 (ko) 2006-06-21 2016-02-01 유니큐어 아이피 비.브이. 곤충세포 내 aav의 생산에 유용한 aav-rep78의 번역을 위한 변형된 개시 코돈을 갖는 벡터
SI3093345T1 (sl) 2007-07-26 2019-08-30 Uniqure Ip B.V. Bakulovirusni vektorji, ki vsebujejo ponavljajoča kodirna zaporedja z različnimi kodonskimi preferencami
EP3257937B1 (en) 2008-02-19 2022-08-03 uniQure IP B.V. Optimisation of expression of parvoviral rep and cap proteins in insect cells
WO2011122950A1 (en) 2010-04-01 2011-10-06 Amsterdam Molecular Therapeutics (Amt) Ip B.V. Monomeric duplex aav vectors
WO2012027558A2 (en) * 2010-08-25 2012-03-01 The Trustees Of Columbia University In The City Of New York OPTIMIZED miRNA CONSTRUCTS
PT2744895E (pt) 2011-09-08 2016-02-08 Uniqure Ip Bv Remoção de vírus contaminantes de preparações de aav
WO2015137802A1 (en) 2014-03-10 2015-09-17 Uniqure Ip B.V. Further improved aav vectors produced in insect cells
AU2015370903B2 (en) 2014-12-24 2021-06-17 Uniqure Ip B.V. RNAi induced huntingtin gene suppression
JP7666922B2 (ja) 2017-07-20 2025-04-22 ユニキュアー アイピー ビー.ブイ. 昆虫細胞における向上したaavカプシド産生
EP3850098A1 (en) * 2018-09-12 2021-07-21 uniQure IP B.V. Rnai induced c9orf72 suppression for the treatment of als/ftd

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