JPWO2023108159A5 - - Google Patents

Info

Publication number
JPWO2023108159A5
JPWO2023108159A5 JP2024534647A JP2024534647A JPWO2023108159A5 JP WO2023108159 A5 JPWO2023108159 A5 JP WO2023108159A5 JP 2024534647 A JP2024534647 A JP 2024534647A JP 2024534647 A JP2024534647 A JP 2024534647A JP WO2023108159 A5 JPWO2023108159 A5 JP WO2023108159A5
Authority
JP
Japan
Prior art keywords
nucleic acid
seq
raav
sequence
nos
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024534647A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024545183A5 (https=
JP2024545183A (ja
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/081323 external-priority patent/WO2023108159A1/en
Publication of JP2024545183A publication Critical patent/JP2024545183A/ja
Publication of JPWO2023108159A5 publication Critical patent/JPWO2023108159A5/ja
Publication of JP2024545183A5 publication Critical patent/JP2024545183A5/ja
Pending legal-status Critical Current

Links

JP2024534647A 2021-12-10 2022-12-09 ウイルスベクターによりbag-3関連心筋症を処置するための方法および組成物 Pending JP2024545183A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163288520P 2021-12-10 2021-12-10
US63/288,520 2021-12-10
PCT/US2022/081323 WO2023108159A1 (en) 2021-12-10 2022-12-09 Methods and compositions for treating bag-3 related cardiomyopathy with a viral vector

Publications (3)

Publication Number Publication Date
JP2024545183A JP2024545183A (ja) 2024-12-05
JPWO2023108159A5 true JPWO2023108159A5 (https=) 2025-12-17
JP2024545183A5 JP2024545183A5 (https=) 2025-12-17

Family

ID=86731334

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024534647A Pending JP2024545183A (ja) 2021-12-10 2022-12-09 ウイルスベクターによりbag-3関連心筋症を処置するための方法および組成物

Country Status (8)

Country Link
US (1) US20250041453A1 (https=)
EP (1) EP4444364A1 (https=)
JP (1) JP2024545183A (https=)
KR (1) KR20240118855A (https=)
AU (1) AU2022407655A1 (https=)
CA (1) CA3242351A1 (https=)
IL (1) IL313427A (https=)
WO (1) WO2023108159A1 (https=)

Families Citing this family (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CA3254775A1 (en) * 2022-03-18 2023-09-21 University Of Florida Research Foundation, Incorporated METHODS AND COMPOSITIONS FOR TREATING TNNT2-RELATED CARDIOMYOPATHY WITH A VIRAL VECTOR
EP4665749A1 (en) * 2023-02-13 2025-12-24 Astrazeneca Ireland Limited Nucleic acids encoding bcl2-associated athanogene 3 (bag3) for gene therapy
WO2024215655A1 (en) * 2023-04-10 2024-10-17 Tenaya Therapeutics, Inc. Cardioprotective bag3 therapies
AU2024265705A1 (en) * 2023-05-02 2025-11-20 Research Institute At Nationwide Children's Hospital Gene therapy for treatment of protein misfolding diseases

Family Cites Families (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP3099333B8 (en) * 2014-01-31 2020-12-30 Temple University of the Commonwealth System of Higher Education Bag3 as a target for therapy of heart failure
WO2015153889A2 (en) * 2014-04-02 2015-10-08 University Of Florida Research Foundation, Incorporated Materials and methods for the treatment of latent viral infection
EP3452101A2 (en) * 2016-05-04 2019-03-13 CureVac AG Rna encoding a therapeutic protein
US20190328836A1 (en) * 2017-01-09 2019-10-31 Duke University Methods for treating ischemic injury
KR20210112339A (ko) * 2019-01-04 2021-09-14 울트라제닉스 파마수티컬 인코포레이티드 윌슨병을 치료하기 위한 유전자 요법 구축물
WO2021154923A2 (en) * 2020-01-29 2021-08-05 Voyager Therapeutics, Inc. Methods and systems for producing aav particles

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