JPWO2023102242A5 - - Google Patents
Info
- Publication number
- JPWO2023102242A5 JPWO2023102242A5 JP2024532968A JP2024532968A JPWO2023102242A5 JP WO2023102242 A5 JPWO2023102242 A5 JP WO2023102242A5 JP 2024532968 A JP2024532968 A JP 2024532968A JP 2024532968 A JP2024532968 A JP 2024532968A JP WO2023102242 A5 JPWO2023102242 A5 JP WO2023102242A5
- Authority
- JP
- Japan
- Prior art keywords
- seq
- nos
- oligonucleotide
- compound
- formula
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (15)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163285628P | 2021-12-03 | 2021-12-03 | |
| US202163285933P | 2021-12-03 | 2021-12-03 | |
| US202163285786P | 2021-12-03 | 2021-12-03 | |
| US202163285631P | 2021-12-03 | 2021-12-03 | |
| US63/285,631 | 2021-12-03 | ||
| US63/285,933 | 2021-12-03 | ||
| US63/285,786 | 2021-12-03 | ||
| US63/285,628 | 2021-12-03 | ||
| US202263350206P | 2022-06-08 | 2022-06-08 | |
| US63/350,206 | 2022-06-08 | ||
| US202263398987P | 2022-08-18 | 2022-08-18 | |
| US202263398992P | 2022-08-18 | 2022-08-18 | |
| US63/398,992 | 2022-08-18 | ||
| US63/398,987 | 2022-08-18 | ||
| PCT/US2022/051740 WO2023102242A2 (en) | 2021-12-03 | 2022-12-02 | Splice switcher antisense oligonucleotides with modified backbone chemistries |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2024545052A JP2024545052A (ja) | 2024-12-05 |
| JP2024545052A5 JP2024545052A5 (https=) | 2026-01-19 |
| JPWO2023102242A5 true JPWO2023102242A5 (https=) | 2026-01-19 |
Family
ID=86613046
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024532968A Pending JP2024545052A (ja) | 2021-12-03 | 2022-12-02 | 修飾骨格化学を有するスプライススイッチャーアンチセンスオリゴヌクレオチド |
Country Status (9)
| Country | Link |
|---|---|
| EP (1) | EP4441226A2 (https=) |
| JP (1) | JP2024545052A (https=) |
| KR (1) | KR20240129626A9 (https=) |
| CN (1) | CN119522282A (https=) |
| AU (1) | AU2022402929A1 (https=) |
| CA (1) | CA3241870A1 (https=) |
| IL (1) | IL313141A (https=) |
| MX (1) | MX2024006612A (https=) |
| WO (1) | WO2023102242A2 (https=) |
Families Citing this family (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| AU2023356317A1 (en) * | 2022-10-05 | 2025-05-15 | Trace Neuroscience, Inc. | Unc13a antisense oligonucleotides and uses thereof |
| WO2024178223A1 (en) * | 2023-02-24 | 2024-08-29 | Northwestern University | Antisense oligonucleotides for preventing unc13a misplicing |
| GB202315883D0 (en) * | 2023-10-17 | 2023-11-29 | Univ Oxford Innovation Ltd | Method |
| WO2025186619A1 (en) * | 2024-03-05 | 2025-09-12 | Takeda Pharmaceutical Company Limited | Compositions and methods for splicing modulation of unc13a |
Family Cites Families (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| AU2003232071A1 (en) * | 2002-05-06 | 2003-11-17 | Genelabs Technologies, Inc. | Nucleoside derivatives for treating hepatitis c virus infection |
| EP3260540A1 (en) * | 2010-11-12 | 2017-12-27 | The General Hospital Corporation | Polycomb-associated non-coding rnas |
| WO2020150290A2 (en) * | 2019-01-14 | 2020-07-23 | President And Fellows Of Harvard College | Methods and compositions for restoring stmn2 levels |
| JP7795914B2 (ja) * | 2019-06-03 | 2026-01-08 | クラリス コーポレーション | 神経学的疾患を処置するためのオリゴヌクレオチドおよびその使用方法 |
-
2022
- 2022-12-02 AU AU2022402929A patent/AU2022402929A1/en active Pending
- 2022-12-02 KR KR1020247021691A patent/KR20240129626A9/ko active Pending
- 2022-12-02 EP EP22902271.0A patent/EP4441226A2/en active Pending
- 2022-12-02 CA CA3241870A patent/CA3241870A1/en active Pending
- 2022-12-02 IL IL313141A patent/IL313141A/en unknown
- 2022-12-02 CN CN202280090925.2A patent/CN119522282A/zh active Pending
- 2022-12-02 JP JP2024532968A patent/JP2024545052A/ja active Pending
- 2022-12-02 WO PCT/US2022/051740 patent/WO2023102242A2/en not_active Ceased
- 2022-12-02 MX MX2024006612A patent/MX2024006612A/es unknown
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