JPWO2023015304A5 - - Google Patents
Info
- Publication number
- JPWO2023015304A5 JPWO2023015304A5 JP2024501135A JP2024501135A JPWO2023015304A5 JP WO2023015304 A5 JPWO2023015304 A5 JP WO2023015304A5 JP 2024501135 A JP2024501135 A JP 2024501135A JP 2024501135 A JP2024501135 A JP 2024501135A JP WO2023015304 A5 JPWO2023015304 A5 JP WO2023015304A5
- Authority
- JP
- Japan
- Prior art keywords
- composition
- intrathecal
- meters
- effective amount
- itr
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163229936P | 2021-08-05 | 2021-08-05 | |
| US63/229,936 | 2021-08-05 | ||
| US202163239881P | 2021-09-01 | 2021-09-01 | |
| US63/239,881 | 2021-09-01 | ||
| PCT/US2022/074622 WO2023015304A1 (en) | 2021-08-05 | 2022-08-05 | Adeno-associated virus particles and methods of use thereof |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2024527742A JP2024527742A (ja) | 2024-07-26 |
| JP2024527742A5 JP2024527742A5 (https=) | 2025-08-14 |
| JPWO2023015304A5 true JPWO2023015304A5 (https=) | 2025-08-14 |
Family
ID=85156338
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024501135A Pending JP2024527742A (ja) | 2021-08-05 | 2022-08-05 | アデノ随伴ウイルス粒子及びその使用方法 |
Country Status (8)
| Country | Link |
|---|---|
| US (1) | US20250041450A1 (https=) |
| EP (1) | EP4380626A4 (https=) |
| JP (1) | JP2024527742A (https=) |
| KR (1) | KR20240045203A (https=) |
| AU (1) | AU2022325165A1 (https=) |
| CA (1) | CA3224482A1 (https=) |
| MX (1) | MX2024001634A (https=) |
| WO (1) | WO2023015304A1 (https=) |
Families Citing this family (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2025250909A1 (en) | 2024-05-31 | 2025-12-04 | Sarepta Therapeutics, Inc. | Muscle-tropic recombinant aav |
| CN119144658A (zh) * | 2024-09-13 | 2024-12-17 | 南京鼓楼医院 | 一种调控平滑肌收缩的aav载体及其构建方法和应用 |
Family Cites Families (10)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US9624282B2 (en) * | 2012-11-26 | 2017-04-18 | The Curators Of The University Of Missouri | Microdystrophin peptides and methods for treating muscular dystrophy using the same |
| EP3097197B1 (en) * | 2014-01-21 | 2020-12-16 | Vrije Universiteit Brussel | Muscle-specific nucleic acid regulatory elements and methods and use thereof |
| CA2971303C (en) * | 2016-06-21 | 2026-03-03 | Bamboo Therapeutics, Inc. | Optimized mini-dystrophin genes and expression cassettes and their use |
| MX2019011046A (es) * | 2017-03-17 | 2019-10-17 | Res Inst Nationwide Childrens Hospital | Administracion de vectores del virus adenoasociado de microdistrofina especifica del musculo para tratar la distrofia muscular. |
| CA3063464A1 (en) * | 2017-05-19 | 2018-11-22 | Encoded Therapeutics, Inc. | High activity regulatory elements |
| US20200405824A1 (en) * | 2019-06-26 | 2020-12-31 | University Of Washington | Use of ribonucleotide reductase alone or in combination with micro-dystrophin to treat duchenne muscular dystrophy striated muscle disease |
| EP3990030A1 (en) * | 2019-06-27 | 2022-05-04 | Pfizer Inc. | Methods of treating duchenne muscular dystrophy using aav mini-dystrophin gene therapy |
| AU2020368539A1 (en) * | 2019-10-16 | 2022-04-28 | Massachusetts Institute Of Technology | Engineered muscle targeting compositions |
| WO2022029543A1 (en) * | 2020-08-06 | 2022-02-10 | Intas Pharmaceuticals Ltd. | Adeno-associated virus vector delivery of micro-dystrophin to treat muscular dystrophy |
| CA3172481A1 (en) * | 2020-11-12 | 2022-05-19 | Precision Biosciences, Inc. | Engineered meganucleases having specificity for recognition sequences in the dystrophin gene |
-
2022
- 2022-08-05 JP JP2024501135A patent/JP2024527742A/ja active Pending
- 2022-08-05 KR KR1020247002648A patent/KR20240045203A/ko active Pending
- 2022-08-05 MX MX2024001634A patent/MX2024001634A/es unknown
- 2022-08-05 AU AU2022325165A patent/AU2022325165A1/en active Pending
- 2022-08-05 US US18/294,792 patent/US20250041450A1/en active Pending
- 2022-08-05 WO PCT/US2022/074622 patent/WO2023015304A1/en not_active Ceased
- 2022-08-05 EP EP22854128.0A patent/EP4380626A4/en active Pending
- 2022-08-05 CA CA3224482A patent/CA3224482A1/en active Pending