JPWO2023009622A5 - - Google Patents

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Publication number
JPWO2023009622A5
JPWO2023009622A5 JP2024502616A JP2024502616A JPWO2023009622A5 JP WO2023009622 A5 JPWO2023009622 A5 JP WO2023009622A5 JP 2024502616 A JP2024502616 A JP 2024502616A JP 2024502616 A JP2024502616 A JP 2024502616A JP WO2023009622 A5 JPWO2023009622 A5 JP WO2023009622A5
Authority
JP
Japan
Prior art keywords
nucleic acid
sequence
aav
plasmid
stuffer sequence
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024502616A
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English (en)
Japanese (ja)
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JP2024529369A5 (https=
JP2024529369A (ja
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/038520 external-priority patent/WO2023009622A1/en
Publication of JP2024529369A publication Critical patent/JP2024529369A/ja
Publication of JP2024529369A5 publication Critical patent/JP2024529369A5/ja
Publication of JPWO2023009622A5 publication Critical patent/JPWO2023009622A5/ja
Pending legal-status Critical Current

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JP2024502616A 2021-07-28 2022-07-27 Aavトランスファープラスミド Pending JP2024529369A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163226410P 2021-07-28 2021-07-28
US63/226,410 2021-07-28
PCT/US2022/038520 WO2023009622A1 (en) 2021-07-28 2022-07-27 Aav transfer plasmids

Publications (3)

Publication Number Publication Date
JP2024529369A JP2024529369A (ja) 2024-08-06
JP2024529369A5 JP2024529369A5 (https=) 2025-07-08
JPWO2023009622A5 true JPWO2023009622A5 (https=) 2025-07-08

Family

ID=85087966

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024502616A Pending JP2024529369A (ja) 2021-07-28 2022-07-27 Aavトランスファープラスミド

Country Status (8)

Country Link
US (1) US20250099617A1 (https=)
EP (1) EP4377471A4 (https=)
JP (1) JP2024529369A (https=)
CN (1) CN118043474A (https=)
AU (1) AU2022319723A1 (https=)
CA (1) CA3225271A1 (https=)
IL (1) IL310145A (https=)
WO (1) WO2023009622A1 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2025176847A1 (en) * 2024-02-21 2025-08-28 Ags Therapeutics Sas Ocular delivery of active agents via microalgae extracellular vesicles

Family Cites Families (8)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US7868149B2 (en) * 1999-07-20 2011-01-11 Monsanto Technology Llc Plant genome sequence and uses thereof
US20050244851A1 (en) * 2004-01-13 2005-11-03 Affymetrix, Inc. Methods of analysis of alternative splicing in human
US10059983B2 (en) * 2012-09-10 2018-08-28 Genesky Diagnostics (Suzhou) Inc. Multiplex nucleic acid analysis
MX384795B (es) * 2013-03-15 2025-03-14 Childrens Hospital Philadelphia Vectores que comprenden secuencias de polinucleotidos rellenadoras/de relleno y metodos de uso.
WO2017161273A1 (en) * 2016-03-18 2017-09-21 The Children's Hospital Of Philadelphia Therapeutic for treatment of diseases including the central nervous system
US10240205B2 (en) * 2017-02-03 2019-03-26 Population Bio, Inc. Methods for assessing risk of developing a viral disease using a genetic test
EP3870148A4 (en) * 2018-10-25 2022-11-09 Takeda Pharmaceutical Company Limited AAV TRIPLE PLASMID SYSTEM
CA3136117A1 (en) * 2019-04-10 2020-10-15 Prevail Therapeutics, Inc. Gene therapies for lysosomal disorders

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