JPWO2022271972A5 - - Google Patents

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Publication number
JPWO2022271972A5
JPWO2022271972A5 JP2023577564A JP2023577564A JPWO2022271972A5 JP WO2022271972 A5 JPWO2022271972 A5 JP WO2022271972A5 JP 2023577564 A JP2023577564 A JP 2023577564A JP 2023577564 A JP2023577564 A JP 2023577564A JP WO2022271972 A5 JPWO2022271972 A5 JP WO2022271972A5
Authority
JP
Japan
Prior art keywords
nucleotides
antisense strand
dsrna agent
flna
nucleotide
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023577564A
Other languages
English (en)
Japanese (ja)
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JP2024528417A5 (https=
JP2024528417A (ja
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/034765 external-priority patent/WO2022271972A1/en
Publication of JP2024528417A publication Critical patent/JP2024528417A/ja
Publication of JPWO2022271972A5 publication Critical patent/JPWO2022271972A5/ja
Publication of JP2024528417A5 publication Critical patent/JP2024528417A5/ja
Pending legal-status Critical Current

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JP2023577564A 2021-06-23 2022-06-23 フィラミンａ（ｆｌｎａ）をサイレンシングするためのｉｒｎａ組成物および方法 Pending JP2024528417A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202163214220P 2021-06-23 2021-06-23
US63/214,220 2021-06-23
US202163274248P 2021-11-01 2021-11-01
US63/274,248 2021-11-01
PCT/US2022/034765 WO2022271972A1 (en) 2021-06-23 2022-06-23 Irna compositions and methods for silencing filamin a (flna)

Publications (3)

Publication Number Publication Date
JP2024528417A JP2024528417A (ja) 2024-07-30
JPWO2022271972A5 true JPWO2022271972A5 (https=) 2025-07-01
JP2024528417A5 JP2024528417A5 (https=) 2025-07-01

Family

ID=84545942

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023577564A Pending JP2024528417A (ja) 2021-06-23 2022-06-23 フィラミンａ（ｆｌｎａ）をサイレンシングするためのｉｒｎａ組成物および方法

Country Status (4)

Country Link
US (1) US20240301418A1 (https=)
EP (1) EP4359522A4 (https=)
JP (1) JP2024528417A (https=)
WO (1) WO2022271972A1 (https=)

Family Cites Families (7)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2014110205A1 (en) * 2013-01-11 2014-07-17 Children's Medical Center Corporation Methods and compositions for the production of sirnas
WO2016014808A1 (en) * 2014-07-24 2016-01-28 Memorial Sloan Kettering Cancer Center Method and composition for targeted delivery of therapeutic agents
KR101734652B1 (ko) * 2015-06-10 2017-05-11 성균관대학교산학협력단 독소루비신 내성 관련 유전자 및 이의 용도
US20190262469A1 (en) * 2015-09-04 2019-08-29 C. Jeffrey Brinker Protocells to treat microbial infection and for synergistic delivery
WO2019217459A1 (en) * 2018-05-07 2019-11-14 Alnylam Pharmaceuticals, Inc. Extrahepatic delivery
EP4073251A1 (en) * 2019-12-13 2022-10-19 Alnylam Pharmaceuticals, Inc. Human chromosome 9 open reading frame 72 (c9orf72) irna agent compositions and methods of use thereof
JP7721130B2 (ja) * 2020-01-15 2025-08-12 国立大学法人東海国立大学機構 進行性核上性麻痺の治療

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